Trial Outcomes & Findings for Safety Study of Adenovirus/PNP Coupled With Fludarabine Phosphate to Treat Solid Tumors (NCT NCT01310179)

NCT ID: NCT01310179

Last Updated: 2015-06-10

Results Overview

Number of participants who had the most frequently observed undesirable effects after exposure to study drug

Recruitment status

COMPLETED

Study phase

PHASE1

Target enrollment

12 participants

Primary outcome timeframe

Entry through Study Day 56

Results posted on

2015-06-10

Participant Flow

Participant milestones

Participant milestones
Measure
Ad/PNP and Fludarabine Monophosphate
Ad/PNP will be injected three times into the tumor over 2 days followed by three daily intravenous infusions of F-araAMP (fludarabine monophosphate). Subjects in the first 3 cohorts will receive 3x10e11 VP for 3 injections and escalating dose levels of F-araAMP (15, 45, and 75 mg/m2 in each sequential cohort) daily for 3 days. The fourth cohort will receive 3x10e12 for 3 injections and 75 mg/m2 fludarabine daily for 3 days. Ad/PNP and fludarabine monophosphate: Subjects in the first 3 cohorts will receive 3x10e11 VP for 3 injections and escalating dose levels of F-araAMP (15, 45, and 75 mg/m2 in each sequential cohort) daily for 3 days. The fourth cohort will receive 3x10e12 for 3 injections and 75 mg/m2 fludarabine daily for 3 days.
Overall Study
STARTED
12
Overall Study
COMPLETED
12
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Safety Study of Adenovirus/PNP Coupled With Fludarabine Phosphate to Treat Solid Tumors

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Ad/PNP and Fludarabine Monophosphate
n=12 Participants
Ad/PNP will be injected three times into the tumor over 2 days followed by three daily intravenous infusions of F-araAMP (fludarabine monophosphate). Subjects in the first 3 cohorts will receive 3x10e11 VP for 3 injections and escalating dose levels of F-araAMP (15, 45, and 75 mg/m2 in each sequential cohort) daily for 3 days. The fourth cohort will receive 3x10e12 for 3 injections and 75 mg/m2 fludarabine daily for 3 days. Ad/PNP and fludarabine monophosphate: Subjects in the first 3 cohorts will receive 3x10e11 VP for 3 injections and escalating dose levels of F-araAMP (15, 45, and 75 mg/m2 in each sequential cohort) daily for 3 days. The fourth cohort will receive 3x10e12 for 3 injections and 75 mg/m2 fludarabine daily for 3 days.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
9 Participants
n=5 Participants
Age, Categorical
>=65 years
3 Participants
n=5 Participants
Sex: Female, Male
Female
3 Participants
n=5 Participants
Sex: Female, Male
Male
9 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
12 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=5 Participants
Race (NIH/OMB)
White
11 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Karnofsky Performance Status Score
100%
2 participants
n=5 Participants
Karnofsky Performance Status Score
90%
3 participants
n=5 Participants
Karnofsky Performance Status Score
80%
3 participants
n=5 Participants
Karnofsky Performance Status Score
70%
4 participants
n=5 Participants
Tumor Site
Neck
6 participants
n=5 Participants
Tumor Site
Cheek
1 participants
n=5 Participants
Tumor Site
Hard Palate
1 participants
n=5 Participants
Tumor Site
Tonsil
1 participants
n=5 Participants
Tumor Site
Lower Lip
1 participants
n=5 Participants
Tumor Site
Scalp
1 participants
n=5 Participants
Tumor Site
Lower Extremities
1 participants
n=5 Participants
Tumor Histology
squamous cell carcinoma
8 participants
n=5 Participants
Tumor Histology
adenoid cycstic carcinoma
2 participants
n=5 Participants
Tumor Histology
melanoma
2 participants
n=5 Participants
Recurrence
Local
7 participants
n=5 Participants
Recurrence
Regional
4 participants
n=5 Participants
Recurrence
Distant
1 participants
n=5 Participants
Non-Target Lesions
Present
7 participants
n=5 Participants
Non-Target Lesions
Not Present
5 participants
n=5 Participants

PRIMARY outcome

Timeframe: Entry through Study Day 56

Number of participants who had the most frequently observed undesirable effects after exposure to study drug

Outcome measures

Outcome measures
Measure
Ad/PNP and Fludarabine Monophosphate
n=12 Participants
Ad/PNP will be injected three times into the tumor over 2 days followed by three daily intravenous infusions of F-araAMP (fludarabine monophosphate). Subjects in the first three cohorts will receive 3x10e11 VP for 3 injections and 5, 15 or 25 mg/m2 of F-araAMP daily for 3 days. Subject in the fourth cohort will receive 3x10e12 VP for 3 injections and the highest tolerated dose of F-araAMP daily for 3 days. Ad/PNP and fludarabine monophosphate: Subjects in the first 3 cohorts will receive 3x10e11 VP for 3 injections and escalating dose levels of F-araAMP (15, 45, and 75 mg/m2 in each sequential cohort) daily for 3 days. The fourth cohort will receive 3x10e12 for 3 injections and 75 mg/m2 fludarabine daily for 3 days.
Number of Participants With Side Effects After Ad/PNP-F-araAMP Treatment
nausea
5 participants
Number of Participants With Side Effects After Ad/PNP-F-araAMP Treatment
injection site symptoms
12 participants
Number of Participants With Side Effects After Ad/PNP-F-araAMP Treatment
fatigue
8 participants
Number of Participants With Side Effects After Ad/PNP-F-araAMP Treatment
facial pain
8 participants

SECONDARY outcome

Timeframe: Entry through Study Day 56

Measurement of tumor response to study drug, as measured by the percentage of change in tumor volume as measured by a physicial measurement using a ruler

Outcome measures

Outcome measures
Measure
Ad/PNP and Fludarabine Monophosphate
n=12 Participants
Ad/PNP will be injected three times into the tumor over 2 days followed by three daily intravenous infusions of F-araAMP (fludarabine monophosphate). Subjects in the first three cohorts will receive 3x10e11 VP for 3 injections and 5, 15 or 25 mg/m2 of F-araAMP daily for 3 days. Subject in the fourth cohort will receive 3x10e12 VP for 3 injections and the highest tolerated dose of F-araAMP daily for 3 days. Ad/PNP and fludarabine monophosphate: Subjects in the first 3 cohorts will receive 3x10e11 VP for 3 injections and escalating dose levels of F-araAMP (15, 45, and 75 mg/m2 in each sequential cohort) daily for 3 days. The fourth cohort will receive 3x10e12 for 3 injections and 75 mg/m2 fludarabine daily for 3 days.
Treatment Outcome and Percent Change in Tumor Volume
Stable (+20% to -30%)
5 participants
Treatment Outcome and Percent Change in Tumor Volume
Partial Response (>-30%)
5 participants
Treatment Outcome and Percent Change in Tumor Volume
Progression (>+20%)
2 participants

Adverse Events

Ad/PNP and Fludarabine Monophosphate

Serious events: 8 serious events
Other events: 12 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Ad/PNP and Fludarabine Monophosphate
n=12 participants at risk
Ad/PNP will be injected three times into the tumor over 2 days followed by three daily intravenous infusions of F-araAMP (fludarabine monophosphate). Subjects in the first 3 cohorts will receive 3x10e11 VP for 3 injections and escalating dose levels of F-araAMP (15, 45, and 75 mg/m2 in each sequential cohort) daily for 3 days. The fourth cohort will receive 3x10e12 for 3 injections and 75 mg/m2 fludarabine daily for 3 days.. Ad/PNP and fludarabine monophosphate: Subjects in the first 3 cohorts will receive 3x10e11 VP for 3 injections and escalating dose levels of F-araAMP (15, 45, and 75 mg/m2 in each sequential cohort) daily for 3 days. The fourth cohort will receive 3x10e12 for 3 injections and 75 mg/m2 fludarabine daily for 3 days.
Metabolism and nutrition disorders
dehydration
8.3%
1/12 • 56 days
Cardiac disorders
pericardial effusion
8.3%
1/12 • 56 days
Cardiac disorders
cardiac tamponade
8.3%
1/12 • 56 days
General disorders
pain
8.3%
1/12 • 56 days
Gastrointestinal disorders
nausea/vomiting
8.3%
1/12 • 56 days
Infections and infestations
bacteremia
8.3%
1/12 • 56 days
Nervous system disorders
partial seizure
8.3%
1/12 • 56 days
Musculoskeletal and connective tissue disorders
lower extremity weakness
8.3%
1/12 • 56 days
Infections and infestations
chronic wound infection
8.3%
1/12 • 56 days

Other adverse events

Other adverse events
Measure
Ad/PNP and Fludarabine Monophosphate
n=12 participants at risk
Ad/PNP will be injected three times into the tumor over 2 days followed by three daily intravenous infusions of F-araAMP (fludarabine monophosphate). Subjects in the first 3 cohorts will receive 3x10e11 VP for 3 injections and escalating dose levels of F-araAMP (15, 45, and 75 mg/m2 in each sequential cohort) daily for 3 days. The fourth cohort will receive 3x10e12 for 3 injections and 75 mg/m2 fludarabine daily for 3 days.. Ad/PNP and fludarabine monophosphate: Subjects in the first 3 cohorts will receive 3x10e11 VP for 3 injections and escalating dose levels of F-araAMP (15, 45, and 75 mg/m2 in each sequential cohort) daily for 3 days. The fourth cohort will receive 3x10e12 for 3 injections and 75 mg/m2 fludarabine daily for 3 days.
General disorders
injection site symptoms
100.0%
12/12 • 56 days
General disorders
fatigue
66.7%
8/12 • 56 days
General disorders
facial pain
66.7%
8/12 • 56 days
Gastrointestinal disorders
nausea
41.7%
5/12 • 56 days
General disorders
flu-like symptoms
33.3%
4/12 • 56 days
Nervous system disorders
dizziness
33.3%
4/12 • 56 days
Nervous system disorders
headache
33.3%
4/12 • 56 days
Metabolism and nutrition disorders
decreased lymphocytes
33.3%
4/12 • 56 days
Metabolism and nutrition disorders
decreased hemoglobin
33.3%
4/12 • 56 days
Metabolism and nutrition disorders
decreased/loss of appetite
33.3%
4/12 • 56 days
Nervous system disorders
paresthesia
33.3%
4/12 • 56 days
General disorders
non-cardiac chest pain
25.0%
3/12 • 56 days
General disorders
facial edema
25.0%
3/12 • 56 days
Respiratory, thoracic and mediastinal disorders
cough
25.0%
3/12 • 56 days
Vascular disorders
hypertension
25.0%
3/12 • 56 days
Infections and infestations
yeast infection
25.0%
3/12 • 56 days
Respiratory, thoracic and mediastinal disorders
sore throat
25.0%
3/12 • 56 days
Musculoskeletal and connective tissue disorders
back pain
16.7%
2/12 • 56 days
General disorders
lower extremity edema
16.7%
2/12 • 56 days
Skin and subcutaneous tissue disorders
rash
16.7%
2/12 • 56 days
Skin and subcutaneous tissue disorders
pruritis
16.7%
2/12 • 56 days
Musculoskeletal and connective tissue disorders
neck stiffness
16.7%
2/12 • 56 days
Gastrointestinal disorders
dysphagia
16.7%
2/12 • 56 days
Cardiac disorders
tachycardia
16.7%
2/12 • 56 days
Vascular disorders
hypotension
16.7%
2/12 • 56 days
Respiratory, thoracic and mediastinal disorders
pneumonia
16.7%
2/12 • 56 days
Gastrointestinal disorders
constipation
16.7%
2/12 • 56 days
Nervous system disorders
syncope
16.7%
2/12 • 56 days
Musculoskeletal and connective tissue disorders
arm pain
8.3%
1/12 • 56 days
Gastrointestinal disorders
vomiting
8.3%
1/12 • 56 days
Gastrointestinal disorders
diarrhea
8.3%
1/12 • 56 days
Metabolism and nutrition disorders
increased AST
8.3%
1/12 • 56 days
General disorders
fever
8.3%
1/12 • 56 days
Renal and urinary disorders
urinary urgency
8.3%
1/12 • 56 days
Musculoskeletal and connective tissue disorders
arthralgia
8.3%
1/12 • 56 days
General disorders
chills
8.3%
1/12 • 56 days
Endocrine disorders
hypothyroidism
8.3%
1/12 • 56 days
Respiratory, thoracic and mediastinal disorders
atelectasis
8.3%
1/12 • 56 days
Cardiac disorders
pericardial effusion
8.3%
1/12 • 56 days
Infections and infestations
upper respiratory infection
8.3%
1/12 • 56 days
General disorders
localized edema
8.3%
1/12 • 56 days
Skin and subcutaneous tissue disorders
periorbital edema
8.3%
1/12 • 56 days
Respiratory, thoracic and mediastinal disorders
bronchospasm
8.3%
1/12 • 56 days
Infections and infestations
wound infection
8.3%
1/12 • 56 days
Metabolism and nutrition disorders
dehydration
8.3%
1/12 • 56 days
Respiratory, thoracic and mediastinal disorders
wheezing
8.3%
1/12 • 56 days
Renal and urinary disorders
acute renal failure
8.3%
1/12 • 56 days
Gastrointestinal disorders
oral mucositis
8.3%
1/12 • 56 days
Investigations
weight loss
8.3%
1/12 • 56 days

Additional Information

Eben Rosenthal, MD

University of Alabama at Birmingham

Phone: 205-934-9713

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place