Cognitive Assessment Battery (CAB) Beta Study

NCT ID: NCT01290861

Last Updated: 2012-08-03

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

255 participants

Study Classification

OBSERVATIONAL

Study Start Date

2011-02-28

Brief Summary

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The overall objective of this study is to identify a 60 minute cognitive battery, for subsequent use in clinical trials, that detects cognitive deficits in early HD and late pre-manifest HD compared to controls, and that has a potential to show drug induced improvements.

Detailed Description

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Huntington's disease (HD) is an autosomal dominant genetic disease which typically manifests beginning in adulthood in the form of movement symptoms, cognitive decline, and psychiatric changes. The proposed research is undertaken in collaboration with CHDI Foundation, Inc., a not for profit organization dedicated to finding treatments for HD. CHDI's goal is to develop or help to develop both symptomatic and disease modifying treatments for HD. To enable future therapeutic trials, CHDI has sponsored several prospective, longitudinal, observational biomarker studies of pre-manifest and early HD with the goal of determining which combination of measures is the most sensitive for detecting changes over the natural progression of pre-manifest and early HD. These and other studies have demonstrated a progressive decline in cognitive function in patients with the huntingtin gene mutation beginning in the pre-manifest period and progressing throughout the course of the disease. These findings support the use of cognitive measures as endpoints in future therapeutic clinical trials. CHDI is committed to the development of a cognitive assessment battery for use in HD therapeutic trials.

There will be paper and pencil and computerized cognitive tests given over a six week period to non-HD control subjects, pre-manifest HD and early manifest HD subjects.

Conditions

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Huntington's Disease

Keywords

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Huntington's Disease Cognitive Battery Cognitive Testing Cognition pre-manifest Huntington's Disease

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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pre-manifest HD

No interventions assigned to this group

early manifest HD

No interventions assigned to this group

healthy controls

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

1. For early HD group, subjects eligible are persons who meet the following criteria:

1. Have clinical diagnostic motor features of HD; and
2. Have huntingtin CAG expansion ≥ 36; and
3. Have Stage 1 or Stage 2 HD, defined as UHDRS TFC scores between 7 and 13 inclusive.
2. For the late pre-manifest HD group, subjects eligible are persons who meet the following criteria:

1. Do not have clinical diagnostic motor features of HD; and
2. Have huntingtin CAG expansion ≥ 39; and
3. Have Burden of Pathology scores ≥ 300 .
3. For the healthy control group, subjects eligible are persons who meet the following criteria:

1. Have no known family history of HD; or,
2. Have known family history of HD but have been tested for the huntingtin CAG expansion and are not at genetic risk for HD (CAG \< 36).
4. For all groups, subjects eligible are persons who meet the following criteria:

1. Are 25 to 55 years of age inclusive;
2. Education at ISCED level 2 or higher, (see Table 5 below) and no known learning disability affecting reading ability, per investigator assessment and judgement;
3. Are capable of complying with study procedures, including cognitive testing that requires spoken, written, and computer based responding;
4. Are ambulatory and do not require skilled nursing care;
5. Have not had cognitive testing for 2 or more months prior to the participation in cognitive testing for the current study;
6. Will not have cognitive testing for other purposes during the course of the study; and,
7. Are capable of providing informed consent.

Education inclusion criterion definition based on ISCED ISCED level 2: Completion of lower secondary general

Australia: Completed junior high school/year 9

Canada: Completed junior high school or junior secondary school or year 9

United Kingdom: Completed Key Stage 3 of secondary school or 'O' levels, or Year 10/Fourth Form (England/Wales); Year 11 (Northern Ireland); 3rd year secondary (Scotland)

United States: Completed junior high school or grade 9

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Exclusion Criteria

1. Current use of investigational drugs or participation in a clinical drug trial (unless approved by the CAB Beta study principal investigator or sponsor);
2. Current intoxication, drug or alcohol abuse or dependence (see below for assessment criteria);
3. Unstable or severe psychiatric disorder, including severe depression as indicated by clinician judgment or IDS-SR score ≥ 39;
4. Significant history of or current medical condition with known or confirmed cognitive sequelae, such as moderate to severe traumatic brain injury, multiple sclerosis, etc;
5. Use of psychostimulants (except caffeine) in the 24 hours prior to site visit;
6. Use of benzodiazepines, alcohol, or other sedating drugs in the 12 hours prior to study visit;
7. If using any psychoactive, psychotropic or other medications or nutraceuticals used to treat HD, the use of inappropriate (e.g., non-therapeutically high) or unstable dose over the past 30 days prior to beginning cognitive testing or throughout the study.

Drug and Alcohol Use Assessment

1. In the past six months has your alcohol or drug use caused you to miss work (or your educational obligations, if relevant) or created significant conflicts in your personal relationships?
2. Over the past month, how many days would you estimate you have consumed more than 4 standard drinks per day (3 for women)?
3. Over the past month, how many days would you estimate that you have used recreational drugs?

Exclude patient if:

* #1 = YES or
* #2 + #3= \>18 or
* Patient appears intoxicated or if an alcohol odour is detected
Minimum Eligible Age

25 Years

Maximum Eligible Age

55 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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Monash University

OTHER

Sponsor Role collaborator

CHDI Foundation, Inc.

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Julie C Stout, Ph.D.

Role: PRINCIPAL_INVESTIGATOR

Monash University

Beth Borowsky, Ph.D.

Role: PRINCIPAL_INVESTIGATOR

CHDI Foundation, Inc.

Locations

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University of California, San Diego

La Jolla, California, United States

Site Status

University of California, Los Angeles

Los Angeles, California, United States

Site Status

University of California, San Francisco

San Francisco, California, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Rush University

Chicago, Illinois, United States

Site Status

Hereditary Neurological Disease Center, Inc

Wichita, Kansas, United States

Site Status

Albany Medical College

Albany, New York, United States

Site Status

Columbia University

New York, New York, United States

Site Status

Duke University

Durham, North Carolina, United States

Site Status

Wake Forest University Baptist Medical Center

Winston-Salem, North Carolina, United States

Site Status

The Ohio State University

Columbus, Ohio, United States

Site Status

Oregon Health and Science University

Portland, Oregon, United States

Site Status

Monash University/Bethlehem Hospital

Melbourne, , Australia

Site Status

Westmead Hospital

Sydney, , Australia

Site Status

Center for Movement Disorders

Markham, Ontario, Canada

Site Status

Department of Neuropsychiatry

Edgbaston, Birmingham, United Kingdom

Site Status

Plymouth Hospitals NHS Trust

Derriford, Plymouth, United Kingdom

Site Status

University Hospital of Wales Cardiff

Cardiff, Wales, United Kingdom

Site Status

Cambridge Center for Brain Repair

Cambridge, , United Kingdom

Site Status

University of Manchester

Manchester, , United Kingdom

Site Status

Countries

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United States Australia Canada United Kingdom

Related Links

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http://www.highqfoundation.org/

Link to funding agency for the CAB Beta study

Other Identifiers

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CAB Beta

Identifier Type: -

Identifier Source: org_study_id