A Study of Vemurafenib (RO5185426) in Participants With Metastatic or Unresectable Papillary Thyroid Cancer Positive for the BRAF V600 Mutation

NCT ID: NCT01286753

Last Updated: 2016-09-07

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

51 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-06-30

Study Completion Date

2015-05-31

Brief Summary

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This open-label, multi-center study will evaluate the safety and efficacy of Vemurafenib (RO5185426) in participants with metastatic or unresectable papillary thyroid cancer (PTC) positive for the BRAF V600 mutation and resistant to radioactive iodine therapy. Participants will receive vemurafenib 960 milligrams (mg) orally twice daily until progressive disease or unacceptable toxicity occurs.

Detailed Description

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Conditions

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Neoplasms

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Tyrosine Kinase Inhibitor (TKI) Naive

Vemurafenib in participants naive to any prior systemic TKI therapy.

Group Type EXPERIMENTAL

Vemurafenib

Intervention Type DRUG

Vemurafenib 960 mg orally twice daily.

TKI Experienced

Vemurafenib in participants previously treated with TKI therapy active against vascular endothelial growth factor receptor 2 (VEGFR).

Group Type EXPERIMENTAL

Vemurafenib

Intervention Type DRUG

Vemurafenib 960 mg orally twice daily.

Interventions

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Vemurafenib

Vemurafenib 960 mg orally twice daily.

Intervention Type DRUG

Other Intervention Names

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Zelboraf® RO5185426

Eligibility Criteria

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Inclusion Criteria

* Adult participants. \>/= 18 years of age
* Histologically confirmed metastatic or unresectable papillary thyroid cancer for which standard curative or palliative measures do not exist or are no longer effective; participants whose tumors exhibit areas of "other histology" may be enrolled, provided the tumor histology remains predominantly papillary
* Positive for BRAF V600 mutation (Roche Cobas 4800 BRAF V600 Mutation Test)
* Radioactive Iodine resistant disease
* Prior therapy excluding (Cohort 1, TKI Naive) or including (Cohort 2, TKI Experienced) TKI
* Clinically relevant disease progression according to RECIST criteria within the prior 14 months
* Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1
* Adequate hematological, renal and liver function

Exclusion Criteria

* Histological diagnosis other than papillary PTC, including squamous cell variants of PTC or PTC with areas of squamous metaplasia
* Active or untreated central nervous system metastases
* History of or known carcinomatous meningitis
* Anticipated or ongoing administration of any anti-cancer therapies other than those administered in the study
* Active squamous cell skin cancer that has not been excised or adequately healed post excision
* Previous treatment with any agent that specifically and selectively targets the MEK or BRAF pathway
* Prior radiotherapy to the only measurable lesion
* Clinically relevant cardio-vascular disease or event within the prior 6 months
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Torrance, California, United States

Site Status

New Haven, Connecticut, United States

Site Status

Chicago, Illinois, United States

Site Status

Baltimore, Maryland, United States

Site Status

Boston, Massachusetts, United States

Site Status

Boston, Massachusetts, United States

Site Status

New York, New York, United States

Site Status

Philadelphia, Pennsylvania, United States

Site Status

Houston, Texas, United States

Site Status

Lyon, , France

Site Status

Paris, , France

Site Status

Villejuif, , France

Site Status

Milan, Lombardy, Italy

Site Status

Pisa, Tuscany, Italy

Site Status

Groningen, , Netherlands

Site Status

Leiden, , Netherlands

Site Status

Countries

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United States France Italy Netherlands

References

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Brose MS, Cabanillas ME, Cohen EE, Wirth LJ, Riehl T, Yue H, Sherman SI, Sherman EJ. Vemurafenib in patients with BRAF(V600E)-positive metastatic or unresectable papillary thyroid cancer refractory to radioactive iodine: a non-randomised, multicentre, open-label, phase 2 trial. Lancet Oncol. 2016 Sep;17(9):1272-82. doi: 10.1016/S1470-2045(16)30166-8. Epub 2016 Jul 23.

Reference Type DERIVED
PMID: 27460442 (View on PubMed)

Other Identifiers

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2010-024133-23

Identifier Type: -

Identifier Source: secondary_id

NO25530

Identifier Type: -

Identifier Source: org_study_id

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