Trial Outcomes & Findings for Pazopanib as Single Agent in Advanced NETs (NCT NCT01280201)

NCT ID: NCT01280201

Last Updated: 2019-05-29

Results Overview

Per Response Evaluation Criteria In Solid Tumor Criteria (RECIST v1.0) for target lesions and assessed by MRI: complete response (CR) considered as dissapereance of all target lesions: partial response (PR), considered as \>=30% decrease in the sum of the longest diameter of target lesions, or stable disease (SD) considered as a decrease \<30%, after pazopanib was started. Clinical benefit rate (CBR) was defined as the percentage of patients achieving CR, PR or SD.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

44 participants

Primary outcome timeframe

6 months

Results posted on

2019-05-29

Participant Flow

Between January 2011 and March 2012, a total of 44 patients were enrolled at 9 Spanish sites, belonging to Group for Neuroendocrine Tumors (GETNE).

Participant milestones

Participant milestones
Measure
Arm of Pazopanib
Single arm of pazopanib 800 mg, administered once a day as the only treatment.
Overall Study
STARTED
44
Overall Study
COMPLETED
44
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Race and Ethnicity were not collected from any participant.

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Arm of Pazopanib
n=44 Participants
Single arm of pazopanib 800 mg, administered once a day as the only treatment.
Age, Continuous
60 years
n=44 Participants
Sex: Female, Male
Female
20 Participants
n=44 Participants
Sex: Female, Male
Male
24 Participants
n=44 Participants
Region of Enrollment
Spain
44 participants
n=44 Participants
Tumor type
Pancreatic islet cell tumors
18 Participants
n=44 Participants
Tumor type
Gastrointestinal neuroendocrine tumors
15 Participants
n=44 Participants
Tumor type
Pulmonary carcinoid tumors
5 Participants
n=44 Participants
Tumor type
Thymic carcinoid tumors
3 Participants
n=44 Participants
Tumor type
Unknown primary origin tumors
3 Participants
n=44 Participants
Functional tumor status
Functional
13 participants
n=44 Participants
Functional tumor status
Nonfunctional
31 participants
n=44 Participants
Histologic status of tumor
Well differentiated
30 Participants
n=44 Participants
Histologic status of tumor
Moderately differentiated
3 Participants
n=44 Participants
Histologic status of tumor
Poorly differentiated
2 Participants
n=44 Participants
Histologic status of tumor
Unknown
9 Participants
n=44 Participants
Ki67 index
≤2%
6 participants
n=44 Participants
Ki67 index
3%-10%
13 participants
n=44 Participants
Ki67 index
>10%
5 participants
n=44 Participants
Ki67 index
Unknown
20 participants
n=44 Participants
Previous biologic treatment
Everolimus
11 Participants
n=44 Participants
Previous biologic treatment
Multitargeted agent
16 Participants
n=44 Participants
Previous biologic treatment
mTOR and multitargeted inhibitor
8 Participants
n=44 Participants
Previous biologic treatment
None
9 Participants
n=44 Participants
Previous chemotherapy
16 Participants
n=44 Participants
Previous somatostatin analogs
35 Participants
n=44 Participants
Concurrent somatostatin analogs
30 Participants
n=44 Participants

PRIMARY outcome

Timeframe: 6 months

Per Response Evaluation Criteria In Solid Tumor Criteria (RECIST v1.0) for target lesions and assessed by MRI: complete response (CR) considered as dissapereance of all target lesions: partial response (PR), considered as \>=30% decrease in the sum of the longest diameter of target lesions, or stable disease (SD) considered as a decrease \<30%, after pazopanib was started. Clinical benefit rate (CBR) was defined as the percentage of patients achieving CR, PR or SD.

Outcome measures

Outcome measures
Measure
Arm of Pazopanib
n=15 Participants
Single arm of pazopanib 800 mg, administered once a day as the only treatment.
Clinical Benefit Rate
11 Participants

SECONDARY outcome

Timeframe: 3 years

Per Response Evaluation Criteria In Solid Tumor Criteria (RECIST v1.0) for target lesions and assessed by MRI, considered as the proportion of patietnts whose target lesions have been reported with a \>=30% increase in the sum of the longest diameter of target lesions.

Outcome measures

Outcome measures
Measure
Arm of Pazopanib
n=40 Participants
Single arm of pazopanib 800 mg, administered once a day as the only treatment.
Number of Patients Who Had an Event (Disease Progression or Death)
35 Participants

SECONDARY outcome

Timeframe: 3 years

Per Response Evaluation Criteria In Solid Tumor Criteria (RECIST v1.0) for target lesions and assessed by MRI, considered as the proportion of patients whose target lessions have dissaperead after treatment.

Outcome measures

Outcome measures
Measure
Arm of Pazopanib
n=44 Participants
Single arm of pazopanib 800 mg, administered once a day as the only treatment.
Radiological Objective Complete Response Rate
4 Participants

SECONDARY outcome

Timeframe: 3 years

Defined, for the subset of patients with a confirmed CR o PR, as the time from first documented evidence of CR or PR until first documented disease progression or death due to any cause. The DR data will be censored the day after the last evaluation in those patients who did not present an objective tumoral progression and did not died during their participation in the trial. The DR will be assessed only in the subset of patients presenting objective response.

Outcome measures

Outcome measures
Measure
Arm of Pazopanib
n=44 Participants
Single arm of pazopanib 800 mg, administered once a day as the only treatment.
Duration of Response (DoR)
11.3 months
Interval 2.0 to 20.6

SECONDARY outcome

Timeframe: 3 years

Population: Number of participantes with grade 3 or 4 AEs

Security and tolerance to the study medication will be determined evaluating the type, incidence, severity, timing, seriousness and connections with the treatment of the reported adverse events, physical examinations and laboratory tests. Toxicity will be classified according to NCI-CTCAE v 4.0.

Outcome measures

Outcome measures
Measure
Arm of Pazopanib
n=44 Participants
Single arm of pazopanib 800 mg, administered once a day as the only treatment.
Safety Assessment Criteria
28 Participants

SECONDARY outcome

Timeframe: 3 years

Predictive value of the differente biomarkers included in the study was evaluated using multivariate analysis.

Outcome measures

Outcome measures
Measure
Arm of Pazopanib
n=44 Participants
Single arm of pazopanib 800 mg, administered once a day as the only treatment.
Predictive Value of Baseline CTC (Count of 0) for Response to Treatma
6.2 Odds ratio
Interval 0.45 to 86.5

Adverse Events

Arm of Pazopanib

Serious events: 19 serious events
Other events: 0 other events
Deaths: 1 deaths

Serious adverse events

Serious adverse events
Measure
Arm of Pazopanib
n=44 participants at risk
Single arm of pazopanib 800 mg, administered once a day as the only treatment.
Hepatobiliary disorders
HEPATOTOXICITY
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Endocrine disorders
DIABETIC DECOMPENSATION
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Gastrointestinal disorders
INTESTINAL SUBOCLUSION
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Metabolism and nutrition disorders
HYPERGLUCEMIA
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Psychiatric disorders
GENERALIZED CRISIS
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Hepatobiliary disorders
OBSTRUCTIVE ICTERY
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Musculoskeletal and connective tissue disorders
OLIGOARTRALGIAS
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Vascular disorders
HYPERTENSIVE CRISIS
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Infections and infestations
RESPIRATORY INFECTION BY E.COLI
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Infections and infestations
ACTIVE TUBERCULOSIS
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Vascular disorders
CEREBELLY HEMATOMY
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Hepatobiliary disorders
ALT AND AST INCREASE
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Skin and subcutaneous tissue disorders
CELLULITIS
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Vascular disorders
DISSEMINATED INTRAVASCULAR COAGULATION
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Hepatobiliary disorders
COLANGITIS
2.3%
1/44 • Number of events 3 • 4 years, 8 months
Metabolism and nutrition disorders
COMA HYPOGLYCEMIC
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Gastrointestinal disorders
Dysphagia
2.3%
1/44 • Number of events 1 • 4 years, 8 months
General disorders
ABDOMINAL PAIN
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
TUMORAL PAIN
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Hepatobiliary disorders
HEPATIC ENCEPHALOPATHY
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Hepatobiliary disorders
BILIARY STENOSIS
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Hepatobiliary disorders
HYPERTRANSAMINASEMIA
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Hepatobiliary disorders
LIVER FAILURE
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Renal and urinary disorders
RENAL INSUFFICIENCY
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Injury, poisoning and procedural complications
INJURY IN HYPOPHYSIS
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Gastrointestinal disorders
INTESTINAL OBSTRUCTION
4.5%
2/44 • Number of events 4 • 4 years, 8 months
General disorders
PROGRESSION DISEASE
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Gastrointestinal disorders
INTESTINAL BLEEDING
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Cardiac disorders
ACUTE CORONARY SYNDROME
2.3%
1/44 • Number of events 1 • 4 years, 8 months
Gastrointestinal disorders
VOMITING
2.3%
1/44 • Number of events 1 • 4 years, 8 months

Other adverse events

Adverse event data not reported

Additional Information

Dr. Enrique Grande (Hospital Universitario Ramón y Cajal)

Group for Neuroendocrine Tumors (GETNE)

Phone: 931780742

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place