Trial Outcomes & Findings for A Study to Assess the Effect of Ustekinumab (Stelara®) and Etanercept (Enbrel®) in Participants With Moderate to Severe Psoriasis (MK-0000-206) (NCT NCT01276847)

NCT ID: NCT01276847

Last Updated: 2015-01-26

Results Overview

Skin biopsies were collected from participants at baseline and after treatment with ustekinumab for 1,2,4 and 16 weeks. The expression of messenger RNA (mRNA) from three pre-defined IL-12 pathway related genes, modulated by interferon gamma (IFN-γ), namely IFN-γ, inducible nitric oxide synthase(iNOS) and CXC motif chemokine 10(CXCL10) was quantitated by real-time polymerase chain reaction (qPCR), with the data normalized by the delta-delta Ct method. The expression score for each gene, showing the percentage difference from baseline, was calculated as follows : \[(baseline - post baseline)/baseline\] x 100. Composite gene expression scores were derived for each individual by summing the expression scores of the individual genes. Positive composite scores denote a decrease from baseline in gene expression.

Recruitment status

COMPLETED

Study phase

PHASE1

Target enrollment

40 participants

Primary outcome timeframe

Baseline and Weeks 1, 2, 4, and 16

Results posted on

2015-01-26

Participant Flow

Participant milestones

Participant milestones
Measure
Etanercept
Etanercept : Etanercept 50 mg twice weekly by self-administered subcutaneous injection for 12 weeks, then once weekly for 4 weeks
No Treatment
No treatment administered
Ustekinumab
Ustekinumab : Ustekinumab 45 mg per dose, administered subcutaneously for participants weighing ≤ 100 kg, and ustekinumab 90 mg per dose administered subcutaneously for participants weighing \> 100 kg on Day 1, and Weeks 4 and 16
Overall Study
STARTED
10
10
20
Overall Study
COMPLETED
9
10
20
Overall Study
NOT COMPLETED
1
0
0

Reasons for withdrawal

Reasons for withdrawal
Measure
Etanercept
Etanercept : Etanercept 50 mg twice weekly by self-administered subcutaneous injection for 12 weeks, then once weekly for 4 weeks
No Treatment
No treatment administered
Ustekinumab
Ustekinumab : Ustekinumab 45 mg per dose, administered subcutaneously for participants weighing ≤ 100 kg, and ustekinumab 90 mg per dose administered subcutaneously for participants weighing \> 100 kg on Day 1, and Weeks 4 and 16
Overall Study
Withdrawal by Subject
1
0
0

Baseline Characteristics

A Study to Assess the Effect of Ustekinumab (Stelara®) and Etanercept (Enbrel®) in Participants With Moderate to Severe Psoriasis (MK-0000-206)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Etanercept
n=10 Participants
Etanercept : Etanercept 50 mg twice weekly by self-administered subcutaneous injection for 12 weeks, then once weekly for 4 weeks
No Treatment
n=10 Participants
No treatment administered
Ustekinumab
n=20 Participants
Ustekinumab : Ustekinumab 45 mg per dose, administered subcutaneously for participants weighing ≤ 100 kg, and ustekinumab 90 mg per dose administered subcutaneously for participants weighing \> 100 kg on Day 1, and Weeks 4 and 16
Total
n=40 Participants
Total of all reporting groups
Age, Continuous
39.5 years
STANDARD_DEVIATION 12.5 • n=5 Participants
53.4 years
STANDARD_DEVIATION 13.0 • n=7 Participants
45.7 years
STANDARD_DEVIATION 12.1 • n=5 Participants
46.1 years
STANDARD_DEVIATION 13.1 • n=4 Participants
Sex: Female, Male
Female
4 Participants
n=5 Participants
1 Participants
n=7 Participants
7 Participants
n=5 Participants
12 Participants
n=4 Participants
Sex: Female, Male
Male
6 Participants
n=5 Participants
9 Participants
n=7 Participants
13 Participants
n=5 Participants
28 Participants
n=4 Participants

PRIMARY outcome

Timeframe: Baseline and Weeks 1, 2, 4, and 16

Population: Pre-specified to be collected only in participants treated with Ustekinumab. One participant treated with Ustekinumab with extreme outlying data, likely due to mislabeling of lesional and nonlesional tissues, was excluded from the analysis.

Skin biopsies were collected from participants at baseline and after treatment with ustekinumab for 1,2,4 and 16 weeks. The expression of messenger RNA (mRNA) from three pre-defined IL-12 pathway related genes, modulated by interferon gamma (IFN-γ), namely IFN-γ, inducible nitric oxide synthase(iNOS) and CXC motif chemokine 10(CXCL10) was quantitated by real-time polymerase chain reaction (qPCR), with the data normalized by the delta-delta Ct method. The expression score for each gene, showing the percentage difference from baseline, was calculated as follows : \[(baseline - post baseline)/baseline\] x 100. Composite gene expression scores were derived for each individual by summing the expression scores of the individual genes. Positive composite scores denote a decrease from baseline in gene expression.

Outcome measures

Outcome measures
Measure
Ustekinumab
n=19 Participants
Ustekinumab : Ustekinumab 45 mg per dose, administered subcutaneously for participants weighing ≤ 100 kg, and ustekinumab 90 mg per dose administered subcutaneously for participants weighing \> 100 kg on Day 1, and Weeks 4 and 16
Change From Baseline in Composite Gene Expression Score Based on IL-12 Pathway Related Interferon Gamma (IFN-γ)-Modulated Genes in Psoriatic Lesions of Participants Treated With Ustekinumab
Week 1
53.68 Gene expression score
Interval 19.9 to 96.34
Change From Baseline in Composite Gene Expression Score Based on IL-12 Pathway Related Interferon Gamma (IFN-γ)-Modulated Genes in Psoriatic Lesions of Participants Treated With Ustekinumab
Week 2
130.54 Gene expression score
Interval 38.47 to 158.0
Change From Baseline in Composite Gene Expression Score Based on IL-12 Pathway Related Interferon Gamma (IFN-γ)-Modulated Genes in Psoriatic Lesions of Participants Treated With Ustekinumab
Week 4
180.19 Gene expression score
Interval 130.5 to 189.38
Change From Baseline in Composite Gene Expression Score Based on IL-12 Pathway Related Interferon Gamma (IFN-γ)-Modulated Genes in Psoriatic Lesions of Participants Treated With Ustekinumab
Week 16
240.29 Gene expression score
Interval 139.44 to 257.76

SECONDARY outcome

Timeframe: Baseline and Weeks 1, 2, 4, and 16

Population: Pre-specified to be collected only in participants treated with Ustekinumab. One participant treated with Ustekinumab with extreme outlying data, likely due to mislabeling of lesional and nonlesional tissues, was excluded from the analysis.

Skin biopsies were collected from participants at baseline and after treatment with ustekinumab for 1,2,4 and 16 weeks. The mRNA expression of eight pre-defined IL-23 pathway related genes, namely beta 4 defensin (DEFB4), CXC motif chemokine 8 (CXCL8), Interleukins 17A, 17F, 20, 22, 23A (IL-17, IL-17F, IL-20, IL-22, IL-23A) and cyclic AMP dependent protein kinase (CAMP) was quantitated by qPCR, with the data normalized by the delta-delta Ct method. The expression score for each gene, showing the percentage difference from baseline, was calculated as follows : \[(baseline - post baseline)/baseline\] x 100. Composite gene expression scores were derived for each individual by summing the expression scores of the individual genes. Positive composite scores denote a reduction from baseline in gene expression.

Outcome measures

Outcome measures
Measure
Ustekinumab
n=19 Participants
Ustekinumab : Ustekinumab 45 mg per dose, administered subcutaneously for participants weighing ≤ 100 kg, and ustekinumab 90 mg per dose administered subcutaneously for participants weighing \> 100 kg on Day 1, and Weeks 4 and 16
Change From Baseline in Composite Gene Expression Score Based on Interleukin 23 (IL-23) Pathway Related Genes in Psoriatic Lesions of Participants Treated With Ustekinumab
Week 1
44.24 Gene expression score
Interval -170.81 to 185.43
Change From Baseline in Composite Gene Expression Score Based on Interleukin 23 (IL-23) Pathway Related Genes in Psoriatic Lesions of Participants Treated With Ustekinumab
Week 2
399.31 Gene expression score
Interval 96.66 to 442.98
Change From Baseline in Composite Gene Expression Score Based on Interleukin 23 (IL-23) Pathway Related Genes in Psoriatic Lesions of Participants Treated With Ustekinumab
Week 4
412.79 Gene expression score
Interval 304.55 to 550.96
Change From Baseline in Composite Gene Expression Score Based on Interleukin 23 (IL-23) Pathway Related Genes in Psoriatic Lesions of Participants Treated With Ustekinumab
Week 16
716.14 Gene expression score
Interval 358.51 to 746.78

SECONDARY outcome

Timeframe: Baseline and Weeks 1, 2, 4, and 16

Population: Pre-specified to be collected only in participants treated with Etanercept.

Participants had skin biopsies performed at baseline and after treatment with etanercept for 1,2,4 and 16 weeks. The expression of IL-17 mRNA was quantitated by qPCR, with the data normalized by the delta-delta Ct method. The expression score, showing the percentage difference from baseline, was calculated as follows : \[(baseline - post baseline)/baseline\] x 100.

Outcome measures

Outcome measures
Measure
Ustekinumab
n=10 Participants
Ustekinumab : Ustekinumab 45 mg per dose, administered subcutaneously for participants weighing ≤ 100 kg, and ustekinumab 90 mg per dose administered subcutaneously for participants weighing \> 100 kg on Day 1, and Weeks 4 and 16
Change From Baseline in Gene Expression Score for Interleukin 17 (IL-17) in Psoriatic Lesions of Participants Treated With Etanercept
Week 1
5.17 Gene expression score
Interval -118.88 to 15.68
Change From Baseline in Gene Expression Score for Interleukin 17 (IL-17) in Psoriatic Lesions of Participants Treated With Etanercept
Week 2
17.75 Gene expression score
Interval -154.28 to 44.76
Change From Baseline in Gene Expression Score for Interleukin 17 (IL-17) in Psoriatic Lesions of Participants Treated With Etanercept
Week 4
65.50 Gene expression score
Interval -10.94 to 84.78
Change From Baseline in Gene Expression Score for Interleukin 17 (IL-17) in Psoriatic Lesions of Participants Treated With Etanercept
Week 16
52.77 Gene expression score
Interval -24.74 to 91.7

Adverse Events

Etanercept

Serious events: 1 serious events
Other events: 3 other events
Deaths: 0 deaths

No Treatment

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

Ustekinumab

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Etanercept
n=10 participants at risk
Etanercept : Etanercept 50 mg twice weekly by self-administered subcutaneous injection for 12 weeks, then once weekly for 4 weeks
No Treatment
n=10 participants at risk
No treatment administered
Ustekinumab
n=20 participants at risk
Ustekinumab : Ustekinumab 45 mg per dose, administered subcutaneously for participants weighing ≤ 100 kg, and ustekinumab 90 mg per dose administered subcutaneously for participants weighing \> 100 kg on Day 1, and Weeks 4 and 16
Pregnancy, puerperium and perinatal conditions
Foetal Distress Syndrome
10.0%
1/10
0.00%
0/10
0.00%
0/20

Other adverse events

Other adverse events
Measure
Etanercept
n=10 participants at risk
Etanercept : Etanercept 50 mg twice weekly by self-administered subcutaneous injection for 12 weeks, then once weekly for 4 weeks
No Treatment
n=10 participants at risk
No treatment administered
Ustekinumab
n=20 participants at risk
Ustekinumab : Ustekinumab 45 mg per dose, administered subcutaneously for participants weighing ≤ 100 kg, and ustekinumab 90 mg per dose administered subcutaneously for participants weighing \> 100 kg on Day 1, and Weeks 4 and 16
Eye disorders
Vitreous Detachment
0.00%
0/10
10.0%
1/10
0.00%
0/20
General disorders
Cyst
0.00%
0/10
10.0%
1/10
0.00%
0/20
Infections and infestations
Nasopharyngitis
0.00%
0/10
0.00%
0/10
15.0%
3/20
Infections and infestations
Pharyngitis Streptococcal
10.0%
1/10
0.00%
0/10
0.00%
0/20
Infections and infestations
Upper Respiratory Tract Infection
0.00%
0/10
10.0%
1/10
10.0%
2/20
Injury, poisoning and procedural complications
Procedural Site Reaction
0.00%
0/10
0.00%
0/10
5.0%
1/20
Pregnancy, puerperium and perinatal conditions
Gestational Diabetes
10.0%
1/10
0.00%
0/10
0.00%
0/20
Skin and subcutaneous tissue disorders
Dermatitis Contact
0.00%
0/10
0.00%
0/10
5.0%
1/20
Skin and subcutaneous tissue disorders
Pruritus
10.0%
1/10
10.0%
1/10
0.00%
0/20

Additional Information

Senior Vice President, Global Clinical Development

Merck Sharp & Dohme Corp.

Phone: 1-800-672-6372

Results disclosure agreements

  • Principal investigator is a sponsor employee The SPONSOR must have the opportunity to review all proposed abstracts, manuscripts or presentations regarding this study 60 days prior to submission for publication/presentation. Any information identified by the SPONSOR as confidential must be deleted prior to submission.
  • Publication restrictions are in place

Restriction type: OTHER