Trial Outcomes & Findings for The Farnesoid X Receptor (FXR) Ligand Obeticholic Acid in NASH Treatment Trial(FLINT) (NCT NCT01265498)

NCT ID: NCT01265498

Last Updated: 2018-04-06

Results Overview

Centrally scored histological improvement in nonalcoholic fatty liver disease (NAFLD) from baseline to the end of 72 weeks of treatment, where improvement is defined as: 1. No worsening in fibrosis; and 2. A decrease in NAFLD Activity Score (NAS) of at least 2 points

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

283 participants

Primary outcome timeframe

baseline to 72 weeks

Results posted on

2018-04-06

Participant Flow

Participant milestones

Participant milestones
Measure
Obeticholic Acid
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Overall Study
STARTED
141
142
Overall Study
Both Baseline and Week 72 Biopsy
102
98
Overall Study
COMPLETED
110
109
Overall Study
NOT COMPLETED
31
33

Reasons for withdrawal

Reasons for withdrawal
Measure
Obeticholic Acid
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Overall Study
Protocol modified to eliminate wk72 bx
31
33

Baseline Characteristics

The Farnesoid X Receptor (FXR) Ligand Obeticholic Acid in NASH Treatment Trial(FLINT)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Obeticholic Acid
n=141 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=142 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Total
n=283 Participants
Total of all reporting groups
Age, Continuous
52 years
STANDARD_DEVIATION 11 • n=5 Participants
51 years
STANDARD_DEVIATION 12 • n=7 Participants
51 years
STANDARD_DEVIATION 11 • n=5 Participants
Sex: Female, Male
Female
98 Participants
n=5 Participants
89 Participants
n=7 Participants
187 Participants
n=5 Participants
Sex: Female, Male
Male
43 Participants
n=5 Participants
53 Participants
n=7 Participants
96 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
22 Participants
n=5 Participants
21 Participants
n=7 Participants
43 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
119 Participants
n=5 Participants
121 Participants
n=7 Participants
240 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Race/Ethnicity, Customized
Asian
6 participants
n=5 Participants
10 participants
n=7 Participants
16 participants
n=5 Participants
Race/Ethnicity, Customized
Black or African-American
2 participants
n=5 Participants
4 participants
n=7 Participants
6 participants
n=5 Participants
Race/Ethnicity, Customized
White
123 participants
n=5 Participants
111 participants
n=7 Participants
234 participants
n=5 Participants
Race/Ethnicity, Customized
Other
10 participants
n=5 Participants
17 participants
n=7 Participants
27 participants
n=5 Participants
SF-36 Quality of life: Physical component summary
45 units on a scale
STANDARD_DEVIATION 11 • n=5 Participants
44 units on a scale
STANDARD_DEVIATION 11 • n=7 Participants
44 units on a scale
STANDARD_DEVIATION 11 • n=5 Participants
SF-36 Quality of life: Mental component summary
48 units on a scale
STANDARD_DEVIATION 12 • n=5 Participants
48 units on a scale
STANDARD_DEVIATION 12 • n=7 Participants
48 units on a scale
STANDARD_DEVIATION 12 • n=5 Participants
Liver enzymes: Alanine aminotransferase
83 U/L
STANDARD_DEVIATION 49 • n=5 Participants
82 U/L
STANDARD_DEVIATION 51 • n=7 Participants
83 U/L
STANDARD_DEVIATION 50 • n=5 Participants
Liver enzymes: Aspartate aminotransferase
64 U/L
STANDARD_DEVIATION 38 • n=5 Participants
58 U/L
STANDARD_DEVIATION 34 • n=7 Participants
61 U/L
STANDARD_DEVIATION 36 • n=5 Participants
Liver enzymes: Alkaline phosphatase
82 U/L
STANDARD_DEVIATION 29 • n=5 Participants
81 U/L
STANDARD_DEVIATION 25 • n=7 Participants
82 U/L
STANDARD_DEVIATION 27 • n=5 Participants
Liver enzymes: γ-glutamyl transpeptidase
78 U/L
STANDARD_DEVIATION 85 • n=5 Participants
76 U/L
STANDARD_DEVIATION 97 • n=7 Participants
77 U/L
STANDARD_DEVIATION 91 • n=5 Participants
Liver enzymes: Total bilirubin
11.5 μmol/L
STANDARD_DEVIATION 5.9 • n=5 Participants
11.3 μmol/L
STANDARD_DEVIATION 7.5 • n=7 Participants
11.4 μmol/L
STANDARD_DEVIATION 6.8 • n=5 Participants
Lipids: Total cholesterol
4.9 mmol/L
STANDARD_DEVIATION 1.2 • n=5 Participants
4.8 mmol/L
STANDARD_DEVIATION 1.2 • n=7 Participants
4.9 mmol/L
STANDARD_DEVIATION 1.2 • n=5 Participants
Lipids: HDL cholesterol
1.1 mmol/L
STANDARD_DEVIATION 0.3 • n=5 Participants
1.1 mmol/L
STANDARD_DEVIATION 0.4 • n=7 Participants
1.1 mmol/L
STANDARD_DEVIATION 0.3 • n=5 Participants
Lipids: LDL cholesterol
2.9 mmol/L
STANDARD_DEVIATION 1.0 • n=5 Participants
2.9 mmol/L
STANDARD_DEVIATION 1.1 • n=7 Participants
2.9 mmol/L
STANDARD_DEVIATION 1.0 • n=5 Participants
Lipids: Triglycerides
2.2 mmol/L
STANDARD_DEVIATION 1.5 • n=5 Participants
2.0 mmol/L
STANDARD_DEVIATION 1.7 • n=7 Participants
2.1 mmol/L
STANDARD_DEVIATION 1.6 • n=5 Participants
Haematology: Haemoglobin
140 g/L
STANDARD_DEVIATION 15 • n=5 Participants
140 g/L
STANDARD_DEVIATION 14 • n=7 Participants
140 g/L
STANDARD_DEVIATION 14 • n=5 Participants
Haematology: Haematocrit
0.41 proportion of 1·0
STANDARD_DEVIATION 0.04 • n=5 Participants
0.41 proportion of 1·0
STANDARD_DEVIATION 0.04 • n=7 Participants
0.41 proportion of 1·0
STANDARD_DEVIATION 0.04 • n=5 Participants
Haematology: Mean corpuscular volume
88.7 fL
STANDARD_DEVIATION 4.8 • n=5 Participants
89.0 fL
STANDARD_DEVIATION 5.3 • n=7 Participants
88.9 fL
STANDARD_DEVIATION 5.1 • n=5 Participants
Haematology: White blood cell count
7.3 white blood cells *10^9 per L
STANDARD_DEVIATION 1.9 • n=5 Participants
6.9 white blood cells *10^9 per L
STANDARD_DEVIATION 2.3 • n=7 Participants
7.1 white blood cells *10^9 per L
STANDARD_DEVIATION 2.1 • n=5 Participants
Haematology: Platelet count
237 platelets *10^9 per L
STANDARD_DEVIATION 59 • n=5 Participants
237 platelets *10^9 per L
STANDARD_DEVIATION 65 • n=7 Participants
237 platelets *10^9 per L
STANDARD_DEVIATION 62 • n=5 Participants
Chemistries: Bicarbonate
25.9 mmol/L
STANDARD_DEVIATION 2.5 • n=5 Participants
26.2 mmol/L
STANDARD_DEVIATION 2.6 • n=7 Participants
26.0 mmol/L
STANDARD_DEVIATION 2.5 • n=5 Participants
Chemistries: Calcium
2.4 mmol/L
STANDARD_DEVIATION 0.1 • n=5 Participants
2.4 mmol/L
STANDARD_DEVIATION 0.1 • n=7 Participants
2.4 mmol/L
STANDARD_DEVIATION 0.1 • n=5 Participants
Chemistries: Phosphate
1.1 mmol/L
STANDARD_DEVIATION 0.2 • n=5 Participants
1.1 mmol/L
STANDARD_DEVIATION 0.2 • n=7 Participants
1.1 mmol/L
STANDARD_DEVIATION 0.2 • n=5 Participants
Chemistries: Creatinine
71 μmol/L
STANDARD_DEVIATION 18 • n=5 Participants
70 μmol/L
STANDARD_DEVIATION 16 • n=7 Participants
71 μmol/L
STANDARD_DEVIATION 17 • n=5 Participants
Chemistries: Uric acid
375 μmol/L
STANDARD_DEVIATION 89 • n=5 Participants
366 μmol/L
STANDARD_DEVIATION 86 • n=7 Participants
370 μmol/L
STANDARD_DEVIATION 87 • n=5 Participants
Chemistries: Albumin
43 g/L
STANDARD_DEVIATION 4 • n=5 Participants
43 g/L
STANDARD_DEVIATION 4 • n=7 Participants
43 g/L
STANDARD_DEVIATION 4 • n=5 Participants
Chemistries: Total protein
73 g/L
STANDARD_DEVIATION 5 • n=5 Participants
74 g/L
STANDARD_DEVIATION 5 • n=7 Participants
73 g/L
STANDARD_DEVIATION 5 • n=5 Participants
Other laboratory results: Prothrombin time
11.7 s
STANDARD_DEVIATION 2.1 • n=5 Participants
11.7 s
STANDARD_DEVIATION 2.2 • n=7 Participants
11.7 s
STANDARD_DEVIATION 2.1 • n=5 Participants
Other laboratory results: International normalised ratio
1.01 ratio
STANDARD_DEVIATION 0.08 • n=5 Participants
1.00 ratio
STANDARD_DEVIATION 0.07 • n=7 Participants
1.00 ratio
STANDARD_DEVIATION 0.07 • n=5 Participants
Metabolic factors: Fasting serum glucose
6.5 mmol/L
STANDARD_DEVIATION 1.8 • n=5 Participants
6.4 mmol/L
STANDARD_DEVIATION 2.2 • n=7 Participants
6.4 mmol/L
STANDARD_DEVIATION 2.0 • n=5 Participants
Metabolic factors: Insulin
201 pmol/L
STANDARD_DEVIATION 226 • n=5 Participants
138 pmol/L
STANDARD_DEVIATION 129 • n=7 Participants
169 pmol/L
STANDARD_DEVIATION 186 • n=5 Participants
Metabolic factors: HOMA-IR
61 glucose [mmol/L] × insulin [pmol/L]/22.5
STANDARD_DEVIATION 74 • n=5 Participants
40 glucose [mmol/L] × insulin [pmol/L]/22.5
STANDARD_DEVIATION 42 • n=7 Participants
50 glucose [mmol/L] × insulin [pmol/L]/22.5
STANDARD_DEVIATION 61 • n=5 Participants
Metabolic factors: Glycated haemoglobin A1c
48 mmol/mol
STANDARD_DEVIATION 12 • n=5 Participants
47 mmol/mol
STANDARD_DEVIATION 11 • n=7 Participants
47 mmol/mol
STANDARD_DEVIATION 11 • n=5 Participants
Metabolic factors: Weight
100 kg
STANDARD_DEVIATION 23 • n=5 Participants
96 kg
STANDARD_DEVIATION 18 • n=7 Participants
98 kg
STANDARD_DEVIATION 21 • n=5 Participants
Metabolic factors: Body-mass index
35 kg/m²
STANDARD_DEVIATION 7 • n=5 Participants
34 kg/m²
STANDARD_DEVIATION 6 • n=7 Participants
35 kg/m²
STANDARD_DEVIATION 6 • n=5 Participants
Metabolic factors: Waist circumference
112 cm
STANDARD_DEVIATION 15 • n=5 Participants
109 cm
STANDARD_DEVIATION 14 • n=7 Participants
111 cm
STANDARD_DEVIATION 15 • n=5 Participants
Metabolic factors: Waist-to-hip ratio
0.96 ratio
STANDARD_DEVIATION 0.07 • n=5 Participants
0.95 ratio
STANDARD_DEVIATION 0.09 • n=7 Participants
0.95 ratio
STANDARD_DEVIATION 0.08 • n=5 Participants
Metabolic factors: Systolic blood pressure
132 mm Hg
STANDARD_DEVIATION 17 • n=5 Participants
132 mm Hg
STANDARD_DEVIATION 15 • n=7 Participants
132 mm Hg
STANDARD_DEVIATION 16 • n=5 Participants
Metabolic factors: Diastolic blood pressure
77 mm Hg
STANDARD_DEVIATION 11 • n=5 Participants
78 mm Hg
STANDARD_DEVIATION 10 • n=7 Participants
77 mm Hg
STANDARD_DEVIATION 10 • n=5 Participants
Comorbidities: Hyperlipidaemia
87 participants
n=5 Participants
86 participants
n=7 Participants
173 participants
n=5 Participants
Comorbidities: Hypertension
87 participants
n=5 Participants
85 participants
n=7 Participants
172 participants
n=5 Participants
Comorbidities: Cardiovascular disease
7 participants
n=5 Participants
8 participants
n=7 Participants
15 participants
n=5 Participants
Comorbidities: Diabetes
75 participants
n=5 Participants
74 participants
n=7 Participants
149 participants
n=5 Participants
Concomitant medications in the past 6 months: Antilipidaemic
72 participants
n=5 Participants
64 participants
n=7 Participants
136 participants
n=5 Participants
Concomitant medications in the past 6 months: Cardiovascular
97 participants
n=5 Participants
92 participants
n=7 Participants
189 participants
n=5 Participants
Concomitant medications in the past 6 months: Antidiabetic
67 participants
n=5 Participants
73 participants
n=7 Participants
140 participants
n=5 Participants
Concomitant medications in the past 6 months: Metformin
55 participants
n=5 Participants
62 participants
n=7 Participants
117 participants
n=5 Participants
Concomitant medications in the past 6 months: Pioglitazone
1 participants
n=5 Participants
6 participants
n=7 Participants
7 participants
n=5 Participants
Concomitant medications in the past 6 months: Vitamin E
29 participants
n=5 Participants
32 participants
n=7 Participants
61 participants
n=5 Participants
Concomitant medications in the past 6 months: Thiazolidinedione
3 participants
n=5 Participants
5 participants
n=7 Participants
8 participants
n=5 Participants
Concomitant medications in the past 6 months: Aspirin (81 mg)
37 participants
n=5 Participants
33 participants
n=7 Participants
70 participants
n=5 Participants
Liver histology findings: Definite steatohepatitis
114 participants
n=5 Participants
111 participants
n=7 Participants
225 participants
n=5 Participants
Liver histology findings: Fibrosis stage
1.9 units on a scale
STANDARD_DEVIATION 1.1 • n=5 Participants
1.8 units on a scale
STANDARD_DEVIATION 1.0 • n=7 Participants
1.8 units on a scale
STANDARD_DEVIATION 1.1 • n=5 Participants
Liver histology findings: Total NAFLD activity score
5.3 units on a scale
STANDARD_DEVIATION 1.3 • n=5 Participants
5.1 units on a scale
STANDARD_DEVIATION 1.3 • n=7 Participants
5.2 units on a scale
STANDARD_DEVIATION 1.3 • n=5 Participants
Liver histology findings: Hepatocellular ballooning score
1.4 units on a scale
STANDARD_DEVIATION 0.7 • n=5 Participants
1.3 units on a scale
STANDARD_DEVIATION 0.7 • n=7 Participants
1.4 units on a scale
STANDARD_DEVIATION 0.7 • n=5 Participants
Liver histology findings: Steatosis score
2.1 units on a scale
STANDARD_DEVIATION 0.8 • n=5 Participants
2.0 units on a scale
STANDARD_DEVIATION 0.8 • n=7 Participants
2.0 units on a scale
STANDARD_DEVIATION 0.8 • n=5 Participants
Liver histology findings: Lobular inflammation score
1.8 units on a scale
STANDARD_DEVIATION 0.7 • n=5 Participants
1.8 units on a scale
STANDARD_DEVIATION 0.7 • n=7 Participants
1.8 units on a scale
STANDARD_DEVIATION 0.7 • n=5 Participants
Liver histology findings: Portal inflammation score
1.2 units on a scale
STANDARD_DEVIATION 0.6 • n=5 Participants
1.1 units on a scale
STANDARD_DEVIATION 0.6 • n=7 Participants
1.1 units on a scale
STANDARD_DEVIATION 0.6 • n=5 Participants
Liver histology findings: Biopsy length
21 mm
STANDARD_DEVIATION 10 • n=5 Participants
21 mm
STANDARD_DEVIATION 10 • n=7 Participants
21 mm
STANDARD_DEVIATION 10 • n=5 Participants

PRIMARY outcome

Timeframe: baseline to 72 weeks

Population: Number of randomly assigned patients with observed or expected week 72 visit before protocol modified on Jan 6, 2014, to eliminate week 72 biopsy. 11 patients in the placebo group and eight in the obeticholic acid group had missing histological data at week 72, and the results for these patients were imputed as a lack of improvement.

Centrally scored histological improvement in nonalcoholic fatty liver disease (NAFLD) from baseline to the end of 72 weeks of treatment, where improvement is defined as: 1. No worsening in fibrosis; and 2. A decrease in NAFLD Activity Score (NAS) of at least 2 points

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=110 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=109 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Hepatic Histological Improvement in Nonalcoholic Fatty Liver Disease (NAFLD) Activity Score (NAS)
50 participants
23 participants

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

Resolution of definite nonalcoholic steatohepatitis. Resolution defined as either not NAFLD, or NAFLD but not non-alcoholic steatohepatitis on week 72 biopsy

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Resolution of NASH Diagnosis
22 participants
13 participants

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

Patients with improvement in fibrosis score. Fibrosis was assessed on a scale of 0-4, with higher scores showing more severe fibrosis.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Fibrosis: Patient With Improvement
36 participants
19 participants

SECONDARY outcome

Timeframe: baseline to 72 weeks

Change in fibrosis score. Fibrosis was assessed on a scale of 0-4, with higher scores showing more severe fibrosis.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Fibrosis: Change in Score
-0.2 units on a scale
Standard Deviation 1.0
0.1 units on a scale
Standard Deviation 0.9

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

NAFLD activity score was assessed on a scale of 0-8, with higher scores showing more severe disease (the components of this measure are steatosis \[assessed on a scale of 0-3\], lobular inflammation \[assessed on a scale of 0-3\], and hepatocellular ballooning \[assessed on a scale of 0-2\]).

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Total NAFLD Activity Score: Change in Score
-1.7 units on a scale
Standard Deviation 1.8
-0.7 units on a scale
Standard Deviation 1.8

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

Patients with improvement in hepatocellular ballooning score. Hepatocellular ballooning was assessed on a scale of 0-2, with higher scores showing more severe ballooning.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Hepatocellular Ballooning: Patients With Improvement
47 participants
30 participants

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

Change in hepatocellular ballooning score. Hepatocellular ballooning was assessed on a scale of 0-2, with higher scores showing more severe ballooning.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Hepatocellular Ballooning: Change in Score
-0.5 units on a scale
Standard Deviation 0.9
-0.2 units on a scale
Standard Deviation 0.9

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

Patients with improvement in steatosis score. Steatosis was assessed on a scale of 0-3, with higher scores showing more severe steatosis.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Steatosis: Patients With Improvement
62 participants
37 participants

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

Change in steatosis score. Steatosis was assessed on a scale of 0-3, with higher scores showing more severe steatosis.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Steatosis: Change in Score
-0.8 units on a scale
Standard Deviation 1.0
-0.4 units on a scale
Standard Deviation 0.8

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

Patients with improvement in lobular inflammation score. Lobular inflammation was assessed on a scale of 0-3, with higher scores showing more severe lobular inflammation.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Lobular Inflammation: Patients With Improvement
54 participants
34 participants

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

Change in lobular inflammation score. Lobular inflammation was assessed on a scale of 0-3, with higher scores showing more severe lobular inflammation.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Lobular Inflammation: Change in Score
-0.5 units on a scale
Standard Deviation 0.8
-0.2 units on a scale
Standard Deviation 0.9

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

Patients with improvement in portal inflammation score. Portal inflammation was assessed on a scale of 0-2, with higher scores showing more severe portal inflammation.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Portal Inflammation: Patients With Improvement
12 participants
13 participants

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: Number of patients with biopsy specimens at baseline and 72 weeks

Change in portal inflammation score. Portal inflammation was assessed on a scale of 0-3, with higher scores showing more severe portal inflammation.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=102 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=98 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Portal Inflammation: Change in Score
0.2 units on a scale
Standard Deviation 0.7
0.2 units on a scale
Standard Deviation 0.7

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Alanine Aminotransferase
-38 U/L
Standard Deviation 47
-18 U/L
Standard Deviation 44

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Asparate Aminotransferase
-27 U/L
Standard Deviation 37
-10 U/L
Standard Deviation 31

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Alkaline Phosphatase
12 U/L
Standard Deviation 26
-6 U/L
Standard Deviation 20

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in γ-glutamyl Transpeptidase
-37 U/L
Standard Deviation 70
-6 U/L
Standard Deviation 48

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Total Bilirubin
-1.0 μmol/L
Standard Deviation 4.1
0.6 μmol/L
Standard Deviation 3.7

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Total Cholesterol
0.16 mmol/L
Standard Deviation 1.07
-0.19 mmol/L
Standard Deviation 0.96

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in HDL Cholesterol
-0.02 mmol/L
Standard Deviation 0.20
0.03 mmol/L
Standard Deviation 0.19

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in LDL Cholesterol
0.22 mmol/L
Standard Deviation 0.90
-0.22 mmol/L
Standard Deviation 0.80

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Triglycerides
-0.22 mmol/L
Standard Deviation 1.27
-0.08 mmol/L
Standard Deviation 1.74

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Haemoglobin
0.6 g/L
Standard Deviation 9.6
0.3 g/L
Standard Deviation 9.5

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Haematocrit
0.00 proportion of 1.0
Standard Deviation 0.03
0.00 proportion of 1.0
Standard Deviation 0.03

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Mean Corpuscular Volume
-0.8 fL
Standard Deviation 2.6
0.3 fL
Standard Deviation 3.5

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in White Blood Cell Count
0.0 white blood cells *10^9 per L
Standard Deviation 1.5
0.0 white blood cells *10^9 per L
Standard Deviation 1.1

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Platelet Count
12 platelets *10^9 per L
Standard Deviation 33
-4 platelets *10^9 per L
Standard Deviation 46

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Bicarbonate
-0.7 mmol/L
Standard Deviation 3.2
-0.1 mmol/L
Standard Deviation 2.7

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Calcium
0.01 mmol/L
Standard Deviation 0.10
-0.01 mmol/L
Standard Deviation 0.11

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Phosphate
0.01 mmol/L
Standard Deviation 0.18
0.02 mmol/L
Standard Deviation 0.16

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Creatinine
1.5 μmol/L
Standard Deviation 11.3
-1.1 μmol/L
Standard Deviation 9.6

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Uric Acid
2 μmol/L
Standard Deviation 68
-11 μmol/L
Standard Deviation 56

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Albumin
-0.2 gl/L
Standard Deviation 3.1
0.3 gl/L
Standard Deviation 3.1

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Total Protein
0.2 gl/L
Standard Deviation 4.5
-0.5 gl/L
Standard Deviation 4.5

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Prothrombin Time
-0.1 s
Standard Deviation 2.4
0.0 s
Standard Deviation 2.2

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in International Normalised Ratio
-0.03 ratio
Standard Deviation 0.07
0.00 ratio
Standard Deviation 0.08

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Fasting Serum Glucose
0.4 mmol/L
Standard Deviation 2.1
0.2 mmol/L
Standard Deviation 2.3

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Insulin
29 pmol/L
Standard Deviation 159
10 pmol/L
Standard Deviation 111

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in HOMA-IR
15 glucose[mmol/L]× insulin[pmol/L] / 22.5
Standard Deviation 50
4 glucose[mmol/L]× insulin[pmol/L] / 22.5
Standard Deviation 29

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Glycated Haemoglobin A1c
0.5 mmol/mol
Standard Deviation 9.7
0.4 mmol/mol
Standard Deviation 8.3

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Weight
-2.3 kg
Standard Deviation 6.7
0.0 kg
Standard Deviation 6.1

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Body-mass Index
-0.7 kg/m²
Standard Deviation 2.4
0.1 kg/m²
Standard Deviation 2.2

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Waist Circumference
-1.5 cm
Standard Deviation 7.1
-0.6 cm
Standard Deviation 8.7

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Waist-to-hip Ratio
0.00 ratio
Standard Deviation 0.06
0.00 ratio
Standard Deviation 0.06

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Systolic Blood Pressure
-4 mm Hg
Standard Deviation 17
-1 mm Hg
Standard Deviation 16

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in Diastolic Blood Pressure
0 mm Hg
Standard Deviation 11
0 mm Hg
Standard Deviation 10

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Short Form (36) Health Survey The SF-36 evaluates health-related quality of life in 8 domains consisting of two components: physical and mental. The score for each domain ranges from 0 to 100. Norm based scoring (based on the general US population) is used with a mean of 50 and standard deviation of 10. Higher values represent a better outcome.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in SF-36 Quality of Life Physical Component Summary
0 units on a scale
Standard Deviation 7
-1 units on a scale
Standard Deviation 7

SECONDARY outcome

Timeframe: baseline to 72 weeks

Population: All patients who completed their final on-treatment study visit and the visit 24 weeks after stopping treatment (including those without a final biopsy due to early treatment termination) were included in the group comparisons of non-histological secondary outcomes.

Short Form (36) Health Survey The SF-36 evaluates health-related quality of life in 8 domains consisting of two components: physical and mental. The score for each domain ranges from 0 to 100. Norm based scoring (based on the general US population) is used with a mean of 50 and standard deviation of 10. Higher values represent a better outcome.

Outcome measures

Outcome measures
Measure
Obeticholic Acid
n=126 Participants
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=131 Participants
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Change in SF-36 Quality of Life Mental Component Summary
0 units on a scale
Standard Deviation 9
1 units on a scale
Standard Deviation 9

Adverse Events

Obeticholic Acid

Serious events: 13 serious events
Other events: 99 other events
Deaths: 0 deaths

Placebo

Serious events: 10 serious events
Other events: 68 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Obeticholic Acid
n=141 participants at risk
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=142 participants at risk
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Cardiac disorders
Cardiovascular death or non-fatal myocardial infarction or non-fatal stroke
2.1%
3/141 • Number of events 3
0.70%
1/142 • Number of events 2
Cardiac disorders
Other coronary artery disease or angina
1.4%
2/141 • Number of events 2
1.4%
2/142 • Number of events 2
Cardiac disorders
Other cardiovascular event
0.71%
1/141 • Number of events 1
0.70%
1/142 • Number of events 1
Nervous system disorders
Other neurological event
0.71%
1/141 • Number of events 1
1.4%
2/142 • Number of events 2
Skin and subcutaneous tissue disorders
Pruritis
0.71%
1/141 • Number of events 1
0.00%
0/142
Hepatobiliary disorders
Hepatobiliary events
0.71%
1/141 • Number of events 1
0.70%
1/142 • Number of events 1
Gastrointestinal disorders
Abdominal pain
0.00%
0/141
1.4%
2/142 • Number of events 2
Gastrointestinal disorders
Pancreatitis
0.71%
1/141 • Number of events 1
0.70%
1/142 • Number of events 1
Gastrointestinal disorders
Other gastrointestinal event
1.4%
2/141 • Number of events 2
0.00%
0/142
Renal and urinary disorders
Other renal event
0.71%
1/141 • Number of events 1
0.00%
0/142

Other adverse events

Other adverse events
Measure
Obeticholic Acid
n=141 participants at risk
obeticholic acid obeticholic acid: 25 mg daily for 72 weeks
Placebo
n=142 participants at risk
Placebo placebo: placebo capsule, 25 mg daily for 72 weeks
Cardiac disorders
Other cardiovascular event
5.0%
7/141 • Number of events 7
3.5%
5/142 • Number of events 5
Nervous system disorders
Dizziness or syncope
2.1%
3/141 • Number of events 3
2.8%
4/142 • Number of events 4
Nervous system disorders
Headache
1.4%
2/141 • Number of events 2
3.5%
5/142 • Number of events 5
Nervous system disorders
Neuralgia
2.1%
3/141 • Number of events 3
1.4%
2/142 • Number of events 2
Nervous system disorders
Other neurological event
2.8%
4/141 • Number of events 4
5.6%
8/142 • Number of events 8
Renal and urinary disorders
Urinary tract infection or cystitis
1.4%
2/141 • Number of events 2
2.1%
3/142 • Number of events 3
Renal and urinary disorders
Kidney stones
4.3%
6/141 • Number of events 6
1.4%
2/142 • Number of events 2
Renal and urinary disorders
Other renal event
0.71%
1/141 • Number of events 1
1.4%
2/142 • Number of events 2
Skin and subcutaneous tissue disorders
Pruritus
22.7%
32/141 • Number of events 32
6.3%
9/142 • Number of events 9
Gastrointestinal disorders
Abdominal pain
5.0%
7/141 • Number of events 7
4.9%
7/142 • Number of events 7
Gastrointestinal disorders
Dental or tooth pain
2.8%
4/141 • Number of events 4
0.70%
1/142 • Number of events 1
Gastrointestinal disorders
Liver pain post biopsy
0.71%
1/141 • Number of events 1
0.70%
1/142 • Number of events 1
Gastrointestinal disorders
Nausea, vomiting, or diarrhoea
8.5%
12/141 • Number of events 12
8.5%
12/142 • Number of events 12
Gastrointestinal disorders
Constipation
3.5%
5/141 • Number of events 5
0.70%
1/142 • Number of events 1
Gastrointestinal disorders
Dyspepsia
2.1%
3/141 • Number of events 3
0.70%
1/142 • Number of events 1
Gastrointestinal disorders
Pancreatitis
0.00%
0/141
0.70%
1/142 • Number of events 1
Gastrointestinal disorders
Other gastrointestinal event
5.0%
7/141 • Number of events 7
2.8%
4/142 • Number of events 4

Additional Information

Mark Van Natta

Johns Hopkins Data Coordinating Centers

Phone: 410-614-1362

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place