Trial Outcomes & Findings for Single-agent Erlotinib in Patients Previously Treated With Oral Etoposide in Protocol OSI-774-205 (NCT NCT01247922)

NCT ID: NCT01247922

Last Updated: 2024-12-06

Results Overview

Safety is monitored through AEs, which includes abnormal or clinically significant vital sign assessments, laboratory test, physical examination findings associated with signs and/or symptoms requiring withdrawal, dose modification or medical intervention. A treatment-emergent adverse event (TEAE) was defined as an adverse event observed after starting administration of the study drug. An AE was considered serious (SAE) if it resulted in death, a life-threatening situation, inpatient hospitalization or prolongation of an existing hospitalization, persistent or significant disability/incapacity, congenital anomaly/birth defect in the offspring of a patient who received study drug or other important medical events.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

4 participants

Primary outcome timeframe

From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days)

Results posted on

2024-12-06

Participant Flow

Participants recruited for this OSI-774-206 study were participants with pediatric ependymoma previously treated with oral etoposide in Study OSI-774-205 who progressed while on study or discontinued due to unacceptable toxicity.

Participants who consented to enter this OSI-774-206 study and fulfilled all the eligibility criteria (no more than 14 days prior to registration) were enrolled in this study no more than 21 days from the last dose of oral etoposide in Study OSI-774-205.

Participant milestones

Participant milestones
Measure
Erlotinib
Participants who received erlotinib in a continuous oral dose of 85 mg/m\^2 per day until dose modification, interruption or study discontinuation occurred.
Overall Study
STARTED
4
Overall Study
Treated
4
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
4

Reasons for withdrawal

Reasons for withdrawal
Measure
Erlotinib
Participants who received erlotinib in a continuous oral dose of 85 mg/m\^2 per day until dose modification, interruption or study discontinuation occurred.
Overall Study
Disease progression
4

Baseline Characteristics

Single-agent Erlotinib in Patients Previously Treated With Oral Etoposide in Protocol OSI-774-205

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Erlotinib
n=4 Participants
Participants who received erlotinib in a continuous oral dose of 85 mg/m\^2 per day until dose modification, interruption or study discontinuation occurred.
Age, Categorical
<=18 years
4 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
Sex: Female, Male
Female
1 Participants
n=5 Participants
Sex: Female, Male
Male
3 Participants
n=5 Participants
Race/Ethnicity, Customized
White
3 participants
n=5 Participants
Race/Ethnicity, Customized
Asian-Indian subcontinent
1 participants
n=5 Participants

PRIMARY outcome

Timeframe: From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days)

Population: The analysis population is the Safety Analysis Set (SAF) consisted of all enrolled patients who received at least 1 dose of study drug.

Safety is monitored through AEs, which includes abnormal or clinically significant vital sign assessments, laboratory test, physical examination findings associated with signs and/or symptoms requiring withdrawal, dose modification or medical intervention. A treatment-emergent adverse event (TEAE) was defined as an adverse event observed after starting administration of the study drug. An AE was considered serious (SAE) if it resulted in death, a life-threatening situation, inpatient hospitalization or prolongation of an existing hospitalization, persistent or significant disability/incapacity, congenital anomaly/birth defect in the offspring of a patient who received study drug or other important medical events.

Outcome measures

Outcome measures
Measure
Erlotinib
n=4 Participants
Participants who received erlotinib in a continuous oral dose of 85 mg/m\^2 per day until dose modification, interruption or study discontinuation occurred.
Safety Assessed Through Evaluation of Physical Examinations, Vital Signs, Clinical Laboratory Tests, and Adverse Events (AEs)
Any TEAE
4 participants
Safety Assessed Through Evaluation of Physical Examinations, Vital Signs, Clinical Laboratory Tests, and Adverse Events (AEs)
With at least 1 SAE
2 participants
Safety Assessed Through Evaluation of Physical Examinations, Vital Signs, Clinical Laboratory Tests, and Adverse Events (AEs)
With at least 1 treatment-related SAE
0 participants
Safety Assessed Through Evaluation of Physical Examinations, Vital Signs, Clinical Laboratory Tests, and Adverse Events (AEs)
Discontinued study due to treatment-related AEs
0 participants
Safety Assessed Through Evaluation of Physical Examinations, Vital Signs, Clinical Laboratory Tests, and Adverse Events (AEs)
Died on treatment or within 30 days
1 participants

SECONDARY outcome

Timeframe: End of treatment (The mean treatment duration was 170.5 days.)

Population: SAF

Best overall response was derived from an integrated clinical assessment by the study investigator as per institutional standards. This included radiographic assessments deemed appropriate by the investigator in the normal care of the patient. A determination of best overall response at the end of study treatment (complete response, partial response, minor response or stable disease) was only made if (1) any disease-related neurologic symptoms were stable or improving over the interval of the radiographic assessment and (2) corticosteroid dosing for the control of tumor-related signs/symptoms was stable or decreasing.If the investigator deems that a radiographic assessment is not needed, then evidence of clinical improvement may be used to determine best response provided that corticosteroid dosing for tumor-related signs/symptoms is stable or decreasing.

Outcome measures

Outcome measures
Measure
Erlotinib
n=4 Participants
Participants who received erlotinib in a continuous oral dose of 85 mg/m\^2 per day until dose modification, interruption or study discontinuation occurred.
Best Overall Response
Complete response
0 participants
Best Overall Response
Partial response
0 participants
Best Overall Response
Minor response
0 participants
Best Overall Response
Stable disease
2 participants
Best Overall Response
Disease progression
2 participants

SECONDARY outcome

Timeframe: From first dose of study drug up to last dose of study drug (The mean treatment duration was 170.5 days)

Population: SAF

Outcome measures

Outcome measures
Measure
Erlotinib
n=4 Participants
Participants who received erlotinib in a continuous oral dose of 85 mg/m\^2 per day until dose modification, interruption or study discontinuation occurred.
Median Treatment Duration
91.0 days
Interval 27.0 to 473.0

Adverse Events

Erlotinib

Serious events: 2 serious events
Other events: 4 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Erlotinib
n=4 participants at risk
Participants who received erlotinib in a continuous oral dose of 85 mg/m\^2 per day until dose modification, interruption or study discontinuation occurred.
Nervous system disorders
Convulsion
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Nervous system disorders
Neuropathy peripheral
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Nervous system disorders
VIIth nerve paralysis
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
General disorders
Brain death
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)

Other adverse events

Other adverse events
Measure
Erlotinib
n=4 participants at risk
Participants who received erlotinib in a continuous oral dose of 85 mg/m\^2 per day until dose modification, interruption or study discontinuation occurred.
Vascular disorders
Peripheral coldness
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Investigations
Blood bilirubin increased
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Investigations
Weight decreased
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Investigations
Weight increased
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Respiratory, thoracic and mediastinal disorders
Cough
50.0%
2/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Respiratory, thoracic and mediastinal disorders
Dysphonia
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Respiratory, thoracic and mediastinal disorders
Epistaxis
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Respiratory, thoracic and mediastinal disorders
Oropharyngeal pain
50.0%
2/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Nervous system disorders
Dysarthria
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Nervous system disorders
Headache
75.0%
3/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Nervous system disorders
Partial seizures
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Eye disorders
Vision blurred
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
General disorders
Fatigue
75.0%
3/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
General disorders
Pain
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
General disorders
Pyrexia
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Gastrointestinal disorders
Abdominal pain
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Gastrointestinal disorders
Abdominal pain upper
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Gastrointestinal disorders
Diarrhoea
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Gastrointestinal disorders
Dyspepsia
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Gastrointestinal disorders
Nausea
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Gastrointestinal disorders
Vomiting
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Skin and subcutaneous tissue disorders
Dermatitis acneiform
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Skin and subcutaneous tissue disorders
Ingrowing nail
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Skin and subcutaneous tissue disorders
Rash
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Skin and subcutaneous tissue disorders
Rash maculo-papular
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Skin and subcutaneous tissue disorders
Skin striae
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Musculoskeletal and connective tissue disorders
Bone pain
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Musculoskeletal and connective tissue disorders
Muscular weakness
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Musculoskeletal and connective tissue disorders
Posture abnormal
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Metabolism and nutrition disorders
Decreased appetite
50.0%
2/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Infections and infestations
Nasopharyngitis
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Infections and infestations
Pneumonia
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)
Infections and infestations
Rash pustular
25.0%
1/4 • From first dose of study drug to 30 days after last dose of study drug (The mean treatment duration was 170.5 days.)

Additional Information

Sr. Medical Director

Astellas Pharma Global Development, Inc.

Results disclosure agreements

  • Principal investigator is a sponsor employee Institute and/or Principal Investigator may publish trial data generated at their specific study site after Sponsor publication of the multi-center data. Sponsor must receive a site's manuscript at least 30 days prior to publication for review and comment. Sponsor may delay the publication for an additional to 60 days to seek patent protection.
  • Publication restrictions are in place

Restriction type: OTHER