Imatinib Mesylate With or Without Hydroxychloroquine in Treating Patients With Chronic Myeloid Leukemia

NCT ID: NCT01227135

Last Updated: 2011-11-30

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE2

Total Enrollment

66 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-03-31

Brief Summary

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RATIONALE: Imatinib mesylate may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth. Biological therapies, such as hydroxychloroquine, may stimulate the immune system in different ways and stop cancer cells from growing. It is not yet known whether imatinib mesylate is more effective when given with or without hydroxychloroquine in treating patients with chronic myeloid leukemia.

PURPOSE: This randomized phase II trial is studying the side effects of giving imatinib mesylate with or without hydroxychloroquine and to see how well it works in treating patients with chronic myeloid leukemia.

Detailed Description

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OBJECTIVES:

Primary

* To determine if imatinib mesylate versus hydroxychloroquine (HCQ) and imatinib mesylate is more effective in terms of BCR/ABL levels in patients with chronic myeloid leukemia in major cytogenetic response (MCyR) with residual BCR/ABL-positive cells detectable by quantitative polymerase chain reaction after at least one year of imatinib mesylate treatment.
* To determine the safety and tolerability of this regimen in these patients.

Secondary

* To determine whether the introduction of HCQ influences imatinib mesylate plasma levels.
* To determine if whole blood HCQ levels achieved in combination with imatinib mesylate are in the expected range.
* To determine if HCQ inhibits autophagy in vivo.
* To evaluate the effects of this regimen on residual BCR/ABL-positive primitive progenitors.

OUTLINE: This is a multicenter study. Patients are stratified according to baseline polymerase chain reaction (PCR) level (\< 3 logs below baseline vs ≥ 3 logs below baseline), time on imatinib mesylate (12 to \< 24 months vs 24 to \< 36 months), imatinib mesylate dose (\< 400 mg vs 400 mg to \< 600 mg vs 600 mg to 800 mg), and center. Patients are randomized to 1 of 2 treatment arms.

* Arm A: Patients receive oral imatinib mesylate daily. Treatment repeats every 4 weeks for up to 12 months in the absence of disease progression or unacceptable toxicity.
* Arm B: Patients receive oral imatinib mesylate daily and oral hydroxychloroquine (HCQ) twice daily. Treatment repeats every 4 weeks for up to 12 months in the absence of disease progression or unacceptable toxicity.

In both arms, patients may then receive oral imatinib mesylate daily for another 12 months during the follow up period of this study.

Consenting patients undergo blood sample and bone marrow collection at baseline, during, and after completion of study therapy for pharmacologic and other laboratory studies.

After completion of study treatment, patients are followed up at 3, 6, 9, and 12 months.

Peer Reviewed, Funded by MRC and supported by Cancer Research UK

Conditions

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Leukemia

Keywords

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chronic phase chronic myelogenous leukemia chronic myelogenous leukemia, BCR-ABL1 positive

Study Design

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Allocation Method

RANDOMIZED

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Interventions

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hydroxychloroquine

Intervention Type DRUG

imatinib mesylate

Intervention Type DRUG

cytogenetic analysis

Intervention Type GENETIC

polymerase chain reaction

Intervention Type GENETIC

laboratory biomarker analysis

Intervention Type OTHER

pharmacological study

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

DISEASE CHARACTERISTICS:

* Diagnosis of chronic myeloid leukemia (CML) in chronic phase (CP)
* Has been treated with imatinib mesylate for at least 1 year

* Receiving a stable dose for ≥ 6 months prior to randomization
* Achieved at least major cytogenetic response (MCyR) and continues to be BCR/ABL-positive by quantitative polymerase chain reaction (Q-PCR)
* Must have a fusion gene present that can be monitored by Q-PCR

PATIENT CHARACTERISTICS:

* ECOG performance status 0-2
* Absolute neutrophil count ≥ 1,500/mm³ (stable and within normal range for ≥ 2 months)
* Platelet count ≥ 100,000/mm³ (stable and within normal range for ≥ 2 months)
* Serum albumin \> 3 g/dL
* AST and/or ALT ≤ 2.5 times upper limit of normal (ULN)
* Serum bilirubin ≤ 1.5 times ULN
* Serum creatinine ≤ 1.5 times ULN OR 24-hour creatinine clearance ≥ 50 mL/min
* Serum potassium ≥ lower limit of normal with or without replacement therapy
* Not pregnant or nursing
* Negative pregnancy test
* Fertile patients must use effective double-method contraception (including a barrier method \[i.e., condom\]) during and for 3 months after completion of study therapy
* No impaired cardiac function, including any of the following:

* QTc \> 450 msec on screening ECG
* Congenital long QT syndrome
* History or presence of sustained ventricular tachycardia
* History of ventricular fibrillation or Torsades de pointes
* NYHA class III-IV congestive heart failure
* Uncontrolled hypertension
* No severe gastrointestinal (GI) disorder, uncontrolled epilepsy, known glucose-6-phosphate dehydrogenase (G6PD) deficiency, known porphyria, moderate or severe psoriasis, known myasthenia gravis, or other concurrent severe and/or uncontrolled medical conditions
* No preexisting maculopathy of the eye
* No significant history of noncompliance to medical regimens or the inability to grant a reliable informed consent

PRIOR CONCURRENT THERAPY:

* See Disease Characteristics
* At least 4 weeks since prior chemotherapy, investigational drug, or major surgery and recovered
* More than 6 months since change in imatinib mesylate dose
* No other concurrent anticancer therapy or radiotherapy
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Medical Research Council

OTHER_GOV

Sponsor Role collaborator

CRUK Trials unit Glasgow

UNKNOWN

Sponsor Role collaborator

Lynn McMahon

OTHER

Sponsor Role lead

Responsible Party

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Lynn McMahon

Project Manager

Responsibility Role SPONSOR_INVESTIGATOR

Principal Investigators

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Tessa Holyoake, MD

Role: PRINCIPAL_INVESTIGATOR

Gartnavel General Hospital

Locations

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Royal Liverpool University Hospital

Liverpool, England, United Kingdom

Site Status RECRUITING

Imperial College London

London, England, United Kingdom

Site Status RECRUITING

Gartnavel General Hospital

Glasgow, Scotland, United Kingdom

Site Status RECRUITING

Countries

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United Kingdom

Facility Contacts

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Contact Person

Role: primary

Contact Person

Role: primary

Contact Person

Role: primary

Other Identifiers

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CRUK-H135

Identifier Type: -

Identifier Source: secondary_id

ISRCTN-61568166

Identifier Type: -

Identifier Source: secondary_id

EUDRACT-2009-014373-41

Identifier Type: -

Identifier Source: secondary_id

EU-21078

Identifier Type: -

Identifier Source: secondary_id

CDR0000686729

Identifier Type: -

Identifier Source: org_study_id