Trial Outcomes & Findings for PhII Study STA-9090 as Second or Third-Line Therapy for Metastatic Pancreas Cancer (NCT NCT01227018)

NCT ID: NCT01227018

Last Updated: 2014-07-23

Results Overview

Per RECIST criteria v. 1.0: measurable lesions: complete response (CR) disappearance of target lesions, partial response (PR) \> 30% decrease in the sum of the longest diameter (LD) of target lesions, stable disease (SD) neither sufficient decrease nor increase of the sum of smallest sum of the LD of target lesions, and progressive disease (PD) \> 20% increase in the sum of the LD of target lesions or appearance of new lesions. Disease control is defined as CR + PR + SD after 8 weeks of therapy.

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

15 participants

Primary outcome timeframe

at 8 weeks from the start of therapy

Results posted on

2014-07-23

Participant Flow

This study opened in December 2010 and ran to April 2013

Seventeen patients consented to this study, 2 were determined ineligible to participate

Participant milestones

Participant milestones
Measure
STA-9090
175 mg/m2 STA-9090 intravenously (IV) over 1 hour once a week for 3 weeks (Day 1, Day 8 and Day 15), followed by a 1 week dose-free interval. The 4-week treatment cycle continues to disease progression or unacceptable toxicity.
Overall Study
STARTED
15
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
15

Reasons for withdrawal

Reasons for withdrawal
Measure
STA-9090
175 mg/m2 STA-9090 intravenously (IV) over 1 hour once a week for 3 weeks (Day 1, Day 8 and Day 15), followed by a 1 week dose-free interval. The 4-week treatment cycle continues to disease progression or unacceptable toxicity.
Overall Study
Disease progression
9
Overall Study
Toxicity
2
Overall Study
Withdrew after beginning treatment
4

Baseline Characteristics

PhII Study STA-9090 as Second or Third-Line Therapy for Metastatic Pancreas Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
STA-9090
n=15 Participants
175 mg/m2 STA-9090 intravenously (IV) over 1 hour once a week for 3 weeks (Day 1, Day 8 and Day 15), followed by a 1 week dose-free interval. The 4-week treatment cycle continues to disease progression or unacceptable toxicity.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
9 Participants
n=5 Participants
Age, Categorical
>=65 years
6 Participants
n=5 Participants
Age, Continuous
65 years
FULL_RANGE 11 • n=5 Participants
Sex: Female, Male
Female
4 Participants
n=5 Participants
Sex: Female, Male
Male
11 Participants
n=5 Participants
Region of Enrollment
United States
15 participants
n=5 Participants

PRIMARY outcome

Timeframe: at 8 weeks from the start of therapy

Population: Patients who received treatment and who were available for determination of response.

Per RECIST criteria v. 1.0: measurable lesions: complete response (CR) disappearance of target lesions, partial response (PR) \> 30% decrease in the sum of the longest diameter (LD) of target lesions, stable disease (SD) neither sufficient decrease nor increase of the sum of smallest sum of the LD of target lesions, and progressive disease (PD) \> 20% increase in the sum of the LD of target lesions or appearance of new lesions. Disease control is defined as CR + PR + SD after 8 weeks of therapy.

Outcome measures

Outcome measures
Measure
STA-9090
n=11 Participants
175 mg/m2 STA-9090 intravenously (IV) over 1 hour once a week for 3 weeks (Day 1, Day 8 and Day 15), followed by a 1 week dose-free interval. The 4-week treatment cycle continues to disease progression or unacceptable toxicity.
Disease Control Rate
21 percentage of participants

SECONDARY outcome

Timeframe: On-treatment date, to date of disease progression (assessed up to 1 year)

Population: All patients with best overall response data; patients are excluded if best overall response data is missing or if the patient is non-evaluable for best overall response.

Number of patients in each response category, per RECIST v1.1, summarized as follows for target lesion criteria (see RECIST v1.1 for additional details): complete response (CR),disappearance of target lesions; partial response (PR), \>=30% decrease in sum of longest diameter of target lesions; progressive disease (PD), \>=20% increase in sum of LD of target lesions or appearance of new lesions; stable disease (SD), insufficient change in target lesions or new lesions to qualify as either PD or SD. Patients are categorized according to the best response achieved prior to occurrence of progressive disease, where best response hierarchy is CR\>PR\>SD\>PD.

Outcome measures

Outcome measures
Measure
STA-9090
n=15 Participants
175 mg/m2 STA-9090 intravenously (IV) over 1 hour once a week for 3 weeks (Day 1, Day 8 and Day 15), followed by a 1 week dose-free interval. The 4-week treatment cycle continues to disease progression or unacceptable toxicity.
Best Response
Complete response
0 participants
Best Response
Partial response
0 participants
Best Response
Stable disease
3 participants
Best Response
Progressive disease
8 participants
Best Response
Not Assessed
3 participants
Best Response
Not Evaluable
1 participants

SECONDARY outcome

Timeframe: study entry to date of death or last date known alive (assessed over 2.5 yrs)

Population: All patients are included in the analysis on intention-totreat basis. Analysis is by Kaplan-Meier method, where death is an event, with censoring for non-expired patients at greater of off-study date or last known alive date.

Estimated probable duration of life from on-study date to date of death from any cause, using the Kaplan-Meier method with censoring (see analysis population description for additional details)

Outcome measures

Outcome measures
Measure
STA-9090
n=15 Participants
175 mg/m2 STA-9090 intravenously (IV) over 1 hour once a week for 3 weeks (Day 1, Day 8 and Day 15), followed by a 1 week dose-free interval. The 4-week treatment cycle continues to disease progression or unacceptable toxicity.
Overall Survival
125 days
Interval 45.0 to 148.0

SECONDARY outcome

Timeframe: On study date to 30 days following final dose of study drug

Population: Total number of patients reported with any toxicity related to study treatment. One patient withdrew before treatment. One patient did not have a toxicity related to study drug or therapy.

Count of patients according to the worst-grade toxicity experienced by each, where worst-grade toxicity is per NCI common toxicity criteria: grade 1, mild; grade 2, moderate; grade 3, severe; grade 4, life-threatening; grade 5, death

Outcome measures

Outcome measures
Measure
STA-9090
n=13 Participants
175 mg/m2 STA-9090 intravenously (IV) over 1 hour once a week for 3 weeks (Day 1, Day 8 and Day 15), followed by a 1 week dose-free interval. The 4-week treatment cycle continues to disease progression or unacceptable toxicity.
Number of Patients With Each Worst Grade Toxicity
Patients with worst grade toxicity 1
0 participants
Number of Patients With Each Worst Grade Toxicity
Patients with worst grade toxicity 2
5 participants
Number of Patients With Each Worst Grade Toxicity
Patients with worst grade toxicity 3
8 participants
Number of Patients With Each Worst Grade Toxicity
Patients with worst grade toxicity 4
0 participants
Number of Patients With Each Worst Grade Toxicity
Patients with worst grade toxicity 5
0 participants

OTHER_PRE_SPECIFIED outcome

Timeframe: Pre-treatment and 1 week post-treatment

Population: The study's interim analysis found the study drug to be ineffective. The study was terminated. No biomarkers were performed or analyzed.

Serum will be tested for biomarkers that may be predictive of response, optional per patient consent.

Outcome measures

Outcome data not reported

Adverse Events

STA-9090

Serious events: 9 serious events
Other events: 13 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
STA-9090
n=14 participants at risk
175 mg/m2 STA-9090 IV over 1 hour once a week for 3 weeks, followed by a 1 week dose-free interval. The 4-week treatment cycle continues to disease progression.
Gastrointestinal disorders
Abdominal pain
21.4%
3/14 • Number of events 3
Renal and urinary disorders
acute kidney injury
7.1%
1/14 • Number of events 1
Investigations
alanine aminotransferase increased
7.1%
1/14 • Number of events 1
Investigations
alkaline phosphatase increased
7.1%
1/14 • Number of events 1
Gastrointestinal disorders
ascites
7.1%
1/14 • Number of events 1
Investigations
aspartate aminotransferase increased
7.1%
1/14 • Number of events 1
Hepatobiliary disorders
biliary tract infection-cholangitis
7.1%
1/14 • Number of events 1
General disorders
chills
7.1%
1/14 • Number of events 1
Psychiatric disorders
confusion
7.1%
1/14 • Number of events 1
Metabolism and nutrition disorders
dehydration
14.3%
2/14 • Number of events 2
Reproductive system and breast disorders
dyspnea
7.1%
1/14 • Number of events 1
General disorders
failure to thrive
7.1%
1/14 • Number of events 1
Gastrointestinal disorders
gastric perforation
7.1%
1/14 • Number of events 1
Hepatobiliary disorders
hepatic failure
7.1%
1/14 • Number of events 1
Metabolism and nutrition disorders
hyperkalemia
7.1%
1/14 • Number of events 1
Metabolism and nutrition disorders
hypokalemia
7.1%
1/14 • Number of events 1
Metabolism and nutrition disorders
hyponatremia
7.1%
1/14 • Number of events 1
Respiratory, thoracic and mediastinal disorders
lung infection
7.1%
1/14 • Number of events 1
General disorders
malaise
7.1%
1/14 • Number of events 1
Gastrointestinal disorders
nausea
21.4%
3/14 • Number of events 3
Respiratory, thoracic and mediastinal disorders
pleural effusion
7.1%
1/14 • Number of events 1
Renal and urinary disorders
renal calculi
7.1%
1/14 • Number of events 1
Vascular disorders
thromboembolic event
7.1%
1/14 • Number of events 1
Renal and urinary disorders
urinary tract infection
7.1%
1/14 • Number of events 1
Gastrointestinal disorders
vomiting
14.3%
2/14 • Number of events 2
Hepatobiliary disorders
blood bilirubin increased
14.3%
2/14 • Number of events 2
Respiratory, thoracic and mediastinal disorders
Acute respiratory failure
7.1%
1/14 • Number of events 1
Vascular disorders
hypotension
7.1%
1/14 • Number of events 1

Other adverse events

Other adverse events
Measure
STA-9090
n=14 participants at risk
175 mg/m2 STA-9090 IV over 1 hour once a week for 3 weeks, followed by a 1 week dose-free interval. The 4-week treatment cycle continues to disease progression.
Gastrointestinal disorders
abdominal pain
64.3%
9/14 • Number of events 16
Gastrointestinal disorders
diarrhea
57.1%
8/14 • Number of events 25
Gastrointestinal disorders
constipation
50.0%
7/14 • Number of events 10
Gastrointestinal disorders
nausea
42.9%
6/14 • Number of events 16
Gastrointestinal disorders
vomiting
21.4%
3/14 • Number of events 10
Gastrointestinal disorders
flatulence
14.3%
2/14 • Number of events 2
Gastrointestinal disorders
gastrointestinal disorders-other
14.3%
2/14 • Number of events 2
Gastrointestinal disorders
ascites
7.1%
1/14 • Number of events 1
Gastrointestinal disorders
bloating
7.1%
1/14 • Number of events 1
Gastrointestinal disorders
dyspepsia
7.1%
1/14 • Number of events 2
Gastrointestinal disorders
esophageal pain
7.1%
1/14 • Number of events 1
Gastrointestinal disorders
hemorrhoids
7.1%
1/14 • Number of events 1
Gastrointestinal disorders
rectal hemorrhage
7.1%
1/14 • Number of events 1
Metabolism and nutrition disorders
hyponatremia
57.1%
8/14 • Number of events 16
Metabolism and nutrition disorders
hypokalemia
42.9%
6/14 • Number of events 8
Metabolism and nutrition disorders
anorexia
28.6%
4/14 • Number of events 4
Metabolism and nutrition disorders
dehydration
28.6%
4/14 • Number of events 4
Metabolism and nutrition disorders
hyperglycemia
28.6%
4/14 • Number of events 9
Metabolism and nutrition disorders
hypoalbuminemia
28.6%
4/14 • Number of events 10
Metabolism and nutrition disorders
hypocalcemia
14.3%
2/14 • Number of events 2
Metabolism and nutrition disorders
hyperkalemia
7.1%
1/14 • Number of events 2
Metabolism and nutrition disorders
hypomagnesemia
7.1%
1/14 • Number of events 1
Metabolism and nutrition disorders
metabolism and nutrition disorders-other
7.1%
1/14 • Number of events 2
Investigations
alkaline phosphatase increased
57.1%
8/14 • Number of events 13
Investigations
alanine aminotransferase increased
42.9%
6/14 • Number of events 9
Investigations
aspartate aminotransferase increased
35.7%
5/14 • Number of events 8
Blood and lymphatic system disorders
lymphocyte count decreased
35.7%
5/14 • Number of events 8
Hepatobiliary disorders
blood bilirubin increased
28.6%
4/14 • Number of events 7
Blood and lymphatic system disorders
platelet count decreased
28.6%
4/14 • Number of events 4
Metabolism and nutrition disorders
weight loss
21.4%
3/14 • Number of events 4
Investigations
creatinine increased
7.1%
1/14 • Number of events 1
General disorders
fatigue
64.3%
9/14 • Number of events 18
General disorders
edema limbs
21.4%
3/14 • Number of events 4
General disorders
pain
14.3%
2/14 • Number of events 2
General disorders
chills
7.1%
1/14 • Number of events 1
General disorders
edema face
7.1%
1/14 • Number of events 1
General disorders
general disorders-other
7.1%
1/14 • Number of events 2
Blood and lymphatic system disorders
anemia
50.0%
7/14 • Number of events 11
Blood and lymphatic system disorders
blood and lymphatic system disorders-other
7.1%
1/14 • Number of events 1
Nervous system disorders
dysgeusia
14.3%
2/14 • Number of events 2
Nervous system disorders
headache
14.3%
2/14 • Number of events 2
Nervous system disorders
dizziness
7.1%
1/14 • Number of events 1
Nervous system disorders
nervous system disorders-other
7.1%
1/14 • Number of events 1
Nervous system disorders
paresthesia
7.1%
1/14 • Number of events 1
Nervous system disorders
peripheral sensory neuropathy
7.1%
1/14 • Number of events 1
Nervous system disorders
tremor
7.1%
1/14 • Number of events 1
Psychiatric disorders
depression
21.4%
3/14 • Number of events 4
Psychiatric disorders
insomnia
14.3%
2/14 • Number of events 3
Psychiatric disorders
confusion
7.1%
1/14 • Number of events 2
Psychiatric disorders
psychosis
7.1%
1/14 • Number of events 1
Respiratory, thoracic and mediastinal disorders
dyspnea
14.3%
2/14 • Number of events 2
Respiratory, thoracic and mediastinal disorders
hoarseness
7.1%
1/14 • Number of events 1
Respiratory, thoracic and mediastinal disorders
laryngeal inflammation
7.1%
1/14 • Number of events 1
Respiratory, thoracic and mediastinal disorders
sleep apnea
7.1%
1/14 • Number of events 1
Musculoskeletal and connective tissue disorders
back pain
28.6%
4/14 • Number of events 5
Musculoskeletal and connective tissue disorders
musculoskeletal and connective tissue disorder-other
7.1%
1/14 • Number of events 1
Musculoskeletal and connective tissue disorders
pain-extremity
7.1%
1/14 • Number of events 2
Cardiac disorders
cardiac disorder-other
7.1%
1/14 • Number of events 1
Cardiac disorders
sinus bradycardia
7.1%
1/14 • Number of events 2
Cardiac disorders
sinus tachycardia
7.1%
1/14 • Number of events 1
Injury, poisoning and procedural complications
bruising
7.1%
1/14 • Number of events 1
Injury, poisoning and procedural complications
fall
7.1%
1/14 • Number of events 1
Renal and urinary disorders
renal and urinary disorder-other
14.3%
2/14 • Number of events 3
Renal and urinary disorders
urinary frequency
7.1%
1/14 • Number of events 1
Skin and subcutaneous tissue disorders
dry skin
7.1%
1/14 • Number of events 1
Skin and subcutaneous tissue disorders
rash maculo-papular
7.1%
1/14 • Number of events 1
Vascular disorders
hypotension
14.3%
2/14 • Number of events 2
Respiratory, thoracic and mediastinal disorders
lung infection
7.1%
1/14 • Number of events 1
General disorders
irritability
7.1%
1/14 • Number of events 1

Additional Information

Dr. Dana Cardin

Vanderbilt-Ingram Cancer Center

Phone: 615-936-8580

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place