PALACE 3: Efficacy and Safety Study of Apremilast to Treat Active Psoriatic Arthritis

NCT ID: NCT01212770

Last Updated: 2020-05-06

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

505 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-09-30

Study Completion Date

2017-02-09

Brief Summary

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The purpose of this study is to determine whether apremilast is safe and effective in the treatment of patients with psoriatic arthritis and a qualifying psoriasis lesion.

Apremilast is proposed to improve signs and symptoms of psoriatic arthritis (tender and swollen joints, pain, physical function) in treated patients.

Detailed Description

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Psoriatic arthritis (PsA) is an inflammatory arthritis that occurs in 6-39% of psoriasis patients. The immunopathogenesis of PsA, which mirrors but is not identical to that seen in psoriatic plaques, reflects a complex interaction among resident dendritic, fibroblastic and endothelial cells, and inflammatory cells attracted to the synovium by cytokines and chemokines. Apremilast (CC-10004) is a novel oral agent that modulates multiple inflammatory pathways through targeted phosphodiesterase type 4 (PDE4) enzyme inhibition. Therefore, apremilast has the potential to be effective in the treatment of PsA.

Conditions

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Psoriatic Arthritis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Apremilast 20 mg

20 mg Apremilast tablets administered twice daily for 24 weeks during the placebo-controlled phase followed by 20 mg Apremilast tablets administered twice daily for up to 4.5 years in the active treatment / long-term safety phase

Group Type EXPERIMENTAL

Apremilast 20mg

Intervention Type DRUG

Apremilast 20 mg twice daily, orally

Apremilast 30 mg

30 mg Apremilast tablets administered twice a day for 24 weeks during the placebo-controlled phase followed by 30 mg Apremilast tablets administered twice a day for up to 4.5 years in the active treatment / long-term safety phase orally twice daily

Group Type EXPERIMENTAL

Apremilast 30mg

Intervention Type DRUG

Apremilast 30 mg twice daily, orally

Placebo + 20 mg Apremilast

Placebo + 20 mg Apremilast tablets administered twice daily for 24 weeks during the placebo-controlled phase followed by 20 mg Apremilast tablets administered twice daily for up to 4.5 years in the active treatment / long-term safety phase. Subjects who do not have at least 20% improvement in their swollen and tender joint counts at Week 16 will escape to 20 mg Apremilast twice daily at Week 16

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo + 30 mg Apremilast

Placebo + 30 mg Apremilast tablets administered twice daily for 24 weeks during the placebo-controlled phase followed by 30 mg Apremilast tablets administered twice daily for up to 4.5 years in the active treatment / long-term safety phase. Subjects who do not have at least 20% improvement in their swollen and tender joint counts at Week 16 will escape to 30 mg Apremilast twice daily at Week 16.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Interventions

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Apremilast 20mg

Apremilast 20 mg twice daily, orally

Intervention Type DRUG

Apremilast 30mg

Apremilast 30 mg twice daily, orally

Intervention Type DRUG

Placebo

Intervention Type DRUG

Other Intervention Names

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CC-10004 CC-10004

Eligibility Criteria

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Inclusion Criteria

* Males or females, aged ≥ 18 years at time of consent.
* Have a diagnosis of Psoriatic Arthritis (PsA, by any criteria) of ≥ 6 months duration.
* Meet the Classification Criteria for Psoriatic Arthritis (CASPAR) criteria for PsA at time of screening.
* Must have been inadequately treated by disease-modifying antirheumatic drugs (DMARDs)
* May not have axial involvement alone
* Concurrent Tx allowed with methotrexate, leflunomide, or sulfasalazine
* Have ≥ 3 swollen AND ≥ 3 tender joints.
* Males \& Females must use contraception
* Stable dose of NSAIDs, narcotics and low dose oral corticosteroids allowed.
* Have at least one ≥2 cm psoriasis lesion

Exclusion Criteria

* Pregnant or breast feeding.
* History of allergy to any component of the investigational product Hepatitis B surface antigen and/or Hepatitis C antibody positive at screening.
* Therapeutic failure on \> 3 agents for PsA or \> 1 biologic tumor necrosis factor (TNF) blocker
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Amgen

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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MD

Role: STUDY_DIRECTOR

Amgen

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Elite Clinical Studies, LLC

Phoenix, Arizona, United States

Site Status

Catalina Pointe Clinical Research Incorporated

Tucson, Arizona, United States

Site Status

Bakersfield Dermatology and Skin Cancer Medical Group

Bakersfield, California, United States

Site Status

Dermatology Research Associates

Los Angeles, California, United States

Site Status

Desert Medical Advances

Palm Desert, California, United States

Site Status

Joao Nascimento, MD

Bridgeport, Connecticut, United States

Site Status

In Vivo Clinical Research

Doral, Florida, United States

Site Status

Suncoast Clinical Research

New Port Richey, Florida, United States

Site Status

Rheumatology Associates of Long Island

Orlando, Florida, United States

Site Status

Advent Clinical Research

Pinellas Park, Florida, United States

Site Status

Rockford Orthopedic Associates, LLC

Rockford, Illinois, United States

Site Status

Dawes Fretzin Clinical Research Group, LLC

Indianapolis, Indiana, United States

Site Status

DermResearch, PLLC

Louisville, Kentucky, United States

Site Status

Clinical Pharmacology Study Group

Worcester, Massachusetts, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

STAT Research, Inc.

Dayton, Ohio, United States

Site Status

West Tennessee Research Institute

Jackson, Tennessee, United States

Site Status

Austin Dermatology Associates

Austin, Texas, United States

Site Status

Austin Regional Clinic

Austin, Texas, United States

Site Status

Center for Clinical Studies

Houston, Texas, United States

Site Status

Houston Medical Research

Houston, Texas, United States

Site Status

Texas Research Center

Sugar Land, Texas, United States

Site Status

Royal Prince Alfred Hospital

Camperdown, , Australia

Site Status

Skin Cancer Foundation

Carlton, , Australia

Site Status

Coff's Clinical Trials

Coffs Harbour, , Australia

Site Status

Heidelberg Repatriation Hospital

Heidelberg, , Australia

Site Status

Menzies Centre for Population Health Research

Hobart, , Australia

Site Status

Optimus Clinical Research Pty. Ltd

Kogarah, , Australia

Site Status

Coastal Joint Care

Maroochydore, , Australia

Site Status

The Queen Elizabeth Hospital

Woodville, , Australia

Site Status

Arthritis Research Centre of Canada

Vancouver, British Columbia, Canada

Site Status

PerCuro Clinical Research

Victoria, British Columbia, Canada

Site Status

Manitoba Clinic

Winnipeg, Manitoba, Canada

Site Status

Arthritis Centre

Winnipeg, Manitoba, Canada

Site Status

Alpha Clinical Research, LLC

St. John's, Newfoundland and Labrador, Canada

Site Status

Niagara Peninsula Arthritis Centre Inc.

St. Catharines, Ontario, Canada

Site Status

Manna Research

Toronto, Ontario, Canada

Site Status

Helsingin Reumakeskus Oy

Helsinki, , Finland

Site Status

Helsingin yliopistollinen keskussairaala

Helsinki, , Finland

Site Status

Finnish Medical Research Co

Pori, , Finland

Site Status

Centre Hospitalier Sud Francilien - Site Gilles de Corbeil

Corbeil-Essonnes, , France

Site Status

Hôtel-Dieu

Nantes, , France

Site Status

Groupe Hospitalier Archet I et II

Nice, , France

Site Status

Hopital Larrey Universite Paul Sabatier

Toulouse, , France

Site Status

Charite - Universitätsmedizin Berlin

Berlin, , Germany

Site Status

Klinische Forschung Berlin - Buch GmbH

Berlin, , Germany

Site Status

Klinikum der Friedrich-Schiller-Universität Jena

Jena, , Germany

Site Status

Universitätsmedizin der Johannes Gutenberg-Universität Mainz

Mainz, , Germany

Site Status

Azienda Ospedaliero-Universitaria di Bologna - Policlinico S.Orsola-Malpighi

Bologna, , Italy

Site Status

Fondazione PTV Policlinico Tor Vergata

Roma, , Italy

Site Status

Hospital of Lithuanian University Health and Sciences

Kaunas, , Lithuania

Site Status

Klaipeda University Hospital

Klaipėda, , Lithuania

Site Status

Panevezys Hospital

Panevezys, , Lithuania

Site Status

Siauliai Hospital

Šiauliai, , Lithuania

Site Status

Gabinet Internistyczno-Reumatologiczny Piotr Adrian Klimiuk

Bialystok, , Poland

Site Status

Centrum Medyczne Silesiana Sp. z o.o.

Bytom, , Poland

Site Status

Malopolskie Centrum Medyczne S.C.

Krakow, , Poland

Site Status

Prywatna Praktyka Lekarska Pawel Hrycaj

Poznan, , Poland

Site Status

REUMATIKA-Centrum Reumatologii Niepubliczny Zaklad Opieki Zdrowotnej

Warsaw, , Poland

Site Status

Baia Mare, Emergency County Hospital "Dr. Constantin Opris"

Baia Mare, , Romania

Site Status

SC Duo Medical SRL

Bucharest, , Romania

Site Status

Sf. Maria Clinical Hospital

Bucharest, , Romania

Site Status

Emergency County Clinical Hospital

Cluj-Napoca, , Romania

Site Status

Sf Apostol Andrei Emergency Clinical County Hospital

Galati, , Romania

Site Status

C.M.I. Dr. Ciornohuz Adriana

Iași, , Romania

Site Status

Research Medical Complex Vashe Zdorovie

Kezch, , Russia

Site Status

Research Institute of Clinical and Experimental Lymphology

Novosibirsk, , Russia

Site Status

Penza Regional Clinical Hospital n.a. N.N. Burdenko

Penza, , Russia

Site Status

City Hospital 26

Saint Petersburg, , Russia

Site Status

Sverdlovsk Regional Clinical Hospital 1

Yekaterinburg, , Russia

Site Status

Narodny ustav reumatickych chorob

Piešťany, , Slovakia

Site Status

MUDr. Zuzana Cizmarikova, s.r.o.

Poprad,Spisska Sobota, , Slovakia

Site Status

REUMEX s.r.o.

Rimavská Sobota, , Slovakia

Site Status

Hallym University Sacred Heart Hospital

Anyang, Kyunggi, , South Korea

Site Status

Chungnam National University Hospital

Daejeon, , South Korea

Site Status

Inha University Hosiptal

Incheon, , South Korea

Site Status

Gachon University Gil Medical Center

Incheon, , South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Severance Hospital

Seoul, , South Korea

Site Status

Ajou University Hospital

Suwon, , South Korea

Site Status

Hospital Universitario a Coruna

A Coruña, , Spain

Site Status

Hospital de Basurto-Osakidetza

Bilbao, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital Universitario Central de Asturias

Oviedo, , Spain

Site Status

Hospital Infanta Sofia

San Sebastián de los Reyes, , Spain

Site Status

HFR Fribourg - Hôpital Cantonal

Fribourg, , Switzerland

Site Status

Chuv Bh-04

Lausanne, , Switzerland

Site Status

Kantonsspital St. Gallen

Sankt Gallen, , Switzerland

Site Status

Haywood Hospital

Burslem, , United Kingdom

Site Status

Southampton General Hospital

Southampton, , United Kingdom

Site Status

Countries

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United States Australia Canada Finland France Germany Italy Lithuania Poland Romania Russia Slovakia South Korea Spain Switzerland United Kingdom

References

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Edwards CJ, Blanco FJ, Crowley J, Birbara CA, Jaworski J, Aelion J, Stevens RM, Vessey A, Zhan X, Bird P. Apremilast, an oral phosphodiesterase 4 inhibitor, in patients with psoriatic arthritis and current skin involvement: a phase III, randomised, controlled trial (PALACE 3). Ann Rheum Dis. 2016 Jun;75(6):1065-73. doi: 10.1136/annrheumdis-2015-207963. Epub 2016 Jan 20.

Reference Type RESULT
PMID: 26792812 (View on PubMed)

Mease PJ, Hatemi G, Paris M, Cheng S, Maes P, Zhang W, Shi R, Flower A, Picard H, Stein Gold L. Apremilast Long-Term Safety Up to 5 Years from 15 Pooled Randomized, Placebo-Controlled Studies of Psoriasis, Psoriatic Arthritis, and Behcet's Syndrome. Am J Clin Dermatol. 2023 Sep;24(5):809-820. doi: 10.1007/s40257-023-00783-7. Epub 2023 Jun 14.

Reference Type DERIVED
PMID: 37316690 (View on PubMed)

Mease PJ, Gladman DD, Kavanaugh A, McGonagle D, Nash P, Guerette B, Nakasato P, Brunori M, Teng L, McInnes IB. Articular and Extra-Articular Benefits in ACR20 Non-responders at Week 104 Treated With Apremilast: Pooled Analysis of Three Randomized Controlled Trials. Rheumatol Ther. 2021 Dec;8(4):1677-1691. doi: 10.1007/s40744-021-00369-x. Epub 2021 Sep 18.

Reference Type DERIVED
PMID: 34536218 (View on PubMed)

Mease PJ, Gladman DD, Ogdie A, Coates LC, Behrens F, Kavanaugh A, McInnes I, Queiro R, Guerette B, Brunori M, Teng L, Smolen JS. Treatment-to-Target With Apremilast in Psoriatic Arthritis: The Probability of Achieving Targets and Comprehensive Control of Disease Manifestations. Arthritis Care Res (Hoboken). 2020 Jun;72(6):814-821. doi: 10.1002/acr.24134. Epub 2020 May 8.

Reference Type DERIVED
PMID: 31909868 (View on PubMed)

Kavanaugh A, Gladman DD, Edwards CJ, Schett G, Guerette B, Delev N, Teng L, Paris M, Mease PJ. Long-term experience with apremilast in patients with psoriatic arthritis: 5-year results from a PALACE 1-3 pooled analysis. Arthritis Res Ther. 2019 May 10;21(1):118. doi: 10.1186/s13075-019-1901-3.

Reference Type DERIVED
PMID: 31077258 (View on PubMed)

Gladman DD, Kavanaugh A, Gomez-Reino JJ, Wollenhaupt J, Cutolo M, Schett G, Lespessailles E, Guerette B, Delev N, Teng L, Edwards CJ, Birbara CA, Mease PJ. Therapeutic benefit of apremilast on enthesitis and dactylitis in patients with psoriatic arthritis: a pooled analysis of the PALACE 1-3 studies. RMD Open. 2018 Jun 27;4(1):e000669. doi: 10.1136/rmdopen-2018-000669. eCollection 2018.

Reference Type DERIVED
PMID: 30018799 (View on PubMed)

Other Identifiers

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CC-10004-PSA-004

Identifier Type: -

Identifier Source: org_study_id

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