Trial Outcomes & Findings for Effect of Treatment With Fingolimod on the Immune Response Following Seasonal Flu Vaccination and Tetanus Booster Injection in Patients With Relapsing Multiple Sclerosis (MS) (NCT NCT01199861)

NCT ID: NCT01199861

Last Updated: 2012-06-19

Results Overview

Percentage of participants who responded to treatment with the seasonal influenza vaccine 3 weeks after vaccination. Response was defined as patients fulfilling one of the following criteria for at least one of the three strains contained in the seasonal influenza vaccine: * Seroconversion: The pre-vaccination antibody titer measurement was \<1:10 and the post-vaccination measurement is ≥1:40. * Significant increase in antibody titer: The pre-vaccination antibody titer measurement was ≥1:10 and the increase in antibody titer from this to the post-vaccination measurement is ≥ 4-fold.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

138 participants

Primary outcome timeframe

Week 6 (pre-vaccination) and 3 weeks after vaccination (Study week 9)

Results posted on

2012-06-19

Participant Flow

Participants were randomized in a 2:1 ratio to fingolimod 0.5 mg once daily or matching placebo.

Participant milestones

Participant milestones
Measure
Fingolimod
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Overall Study
STARTED
95
43
Overall Study
COMPLETED
93
43
Overall Study
NOT COMPLETED
2
0

Reasons for withdrawal

Reasons for withdrawal
Measure
Fingolimod
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Overall Study
Administrative problems
1
0
Overall Study
Adverse Event
1
0

Baseline Characteristics

Effect of Treatment With Fingolimod on the Immune Response Following Seasonal Flu Vaccination and Tetanus Booster Injection in Patients With Relapsing Multiple Sclerosis (MS)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Fingolimod
n=95 Participants
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
n=43 Participants
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Total
n=138 Participants
Total of all reporting groups
Age Continuous
37.4 years
STANDARD_DEVIATION 8.37 • n=5 Participants
39.2 years
STANDARD_DEVIATION 8.67 • n=7 Participants
37.9 years
STANDARD_DEVIATION 8.48 • n=5 Participants
Age, Customized
18-30
25 participants
n=5 Participants
8 participants
n=7 Participants
33 participants
n=5 Participants
Age, Customized
31-40
35 participants
n=5 Participants
14 participants
n=7 Participants
49 participants
n=5 Participants
Age, Customized
41-55
35 participants
n=5 Participants
21 participants
n=7 Participants
56 participants
n=5 Participants
Sex: Female, Male
Female
65 Participants
n=5 Participants
29 Participants
n=7 Participants
94 Participants
n=5 Participants
Sex: Female, Male
Male
30 Participants
n=5 Participants
14 Participants
n=7 Participants
44 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Week 6 (pre-vaccination) and 3 weeks after vaccination (Study week 9)

Population: The full analysis set which includes all patients who were randomized and received at least 1 dose of study drug, and for whom data were available.

Percentage of participants who responded to treatment with the seasonal influenza vaccine 3 weeks after vaccination. Response was defined as patients fulfilling one of the following criteria for at least one of the three strains contained in the seasonal influenza vaccine: * Seroconversion: The pre-vaccination antibody titer measurement was \<1:10 and the post-vaccination measurement is ≥1:40. * Significant increase in antibody titer: The pre-vaccination antibody titer measurement was ≥1:10 and the increase in antibody titer from this to the post-vaccination measurement is ≥ 4-fold.

Outcome measures

Outcome measures
Measure
Fingolimod
n=90 Participants
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
n=43 Participants
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Immune Response 3 Weeks After Seasonal Influenza Vaccination
53.3 percentage of participants
83.7 percentage of participants

SECONDARY outcome

Timeframe: Week 6 (pre-vaccination) and 6 weeks after vaccination (Study week 12).

Population: Full analysis set for whom data were available.

Percentage of participants who responded to treatment with the seasonal influenza vaccine 6 weeks after vaccination. Response was defined as patients fulfilling one of the following criteria for at least one of the three strains contained in the seasonal influenza vaccine: * Seroconversion: The pre-vaccination antibody titer measurement was \<1:10 and the post-vaccination measurement is ≥1:40. * Significant increase in antibody titer: The pre-vaccination antibody titer measurement was ≥1:10 and the increase in antibody titer from this to the post-vaccination measurement is ≥ 4-fold.

Outcome measures

Outcome measures
Measure
Fingolimod
n=88 Participants
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
n=43 Participants
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Immune Response 6 Weeks After Seasonal Influenza Vaccination
43.2 percentage of participants
74.4 percentage of participants

SECONDARY outcome

Timeframe: Week 6 (pre-vaccination) and 3 weeks after vaccination (Study Week 9)

Population: Full analysis set for whom data were available.

Percentage of participants with an immune response to a single dose of tetanus toxoid three weeks after vaccination. A patient was considered a responder to tetanus toxoid booster vaccination if one of the following criteria was met: 1. Seroconversion: The pre-vaccination antibody titer measurement was \<0.1 IU/ml and the post-vaccination measurement was ≥0.4 IU/ml. 2. Significant increase: The pre-vaccination antibody titer measurement was ≥0.1 IU/ml and the increase in antibody titer from this to the post-vaccination measurement was ≥4- fold.

Outcome measures

Outcome measures
Measure
Fingolimod
n=90 Participants
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
n=43 Participants
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Immune Response 3 Weeks After Tetanus Toxoid Booster
40.0 percentage of participants
60.5 percentage of participants

SECONDARY outcome

Timeframe: Week 6 (pre-vaccination) and 6 weeks after vaccination (Study Week 12)

Population: Full analysis set for whom data were available.

Percentage of participants with an immune response to a single dose of tetanus toxoid six weeks after vaccination. A patient was considered a responder to tetanus toxoid booster vaccination if one of the following criteria was met: 1. Seroconversion: The pre-vaccination antibody titer measurement was \<0.1 IU/ml and the post-vaccination measurement was ≥0.4 IU/ml. 2. Significant increase: The pre-vaccination antibody titer measurement was ≥0.1 IU/ml and the increase in antibody titer from this to the post-vaccination measurement was ≥4- fold.

Outcome measures

Outcome measures
Measure
Fingolimod
n=88 Participants
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
n=43 Participants
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Immune Response 6 Weeks After Tetanus Toxoid Booster
37.5 percentage of participants
48.8 percentage of participants

SECONDARY outcome

Timeframe: Pre-vaccination (Week 6) and 3 weeks after vaccination (Study Week 9).

Population: Full analysis set for whom data were available.

Change from Baseline was expressed by the ratio of post-vaccination to pre-vaccination antibody titer for each of the three strains included in the seasonal influenza vaccine. Inhibition of an immune response to each strain included in the seasonal influenza vaccine was assessed by the relative difference of the geometric mean antibody titer ratio on fingolimod as compared to placebo three weeks after a single dose of seasonal influenza vaccine.

Outcome measures

Outcome measures
Measure
Fingolimod
n=90 Participants
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
n=43 Participants
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Change From Baseline in Seasonal Influenza Vaccine Antibody-titer 3 Weeks After Vaccination
A/California/7/09(H1N1)
2.45 ratio
4.14 ratio
Change From Baseline in Seasonal Influenza Vaccine Antibody-titer 3 Weeks After Vaccination
A/Perth/16/2009(H3N2)
0.49 ratio
0.36 ratio
Change From Baseline in Seasonal Influenza Vaccine Antibody-titer 3 Weeks After Vaccination
B/Brisbane/60/2008
1.34 ratio
2.40 ratio

SECONDARY outcome

Timeframe: Pre-vaccination (Week 6) and 6 weeks after vaccination (Study Week 12).

Population: Full analysis set for whom data were available.

Change from Baseline was expressed by the ratio of post-vaccination to pre-vaccination antibody titer for each of the three strains included in the seasonal influenza vaccine. Inhibition of an immune response to each strain included in the seasonal influenza vaccine was assessed by the relative difference of the geometric mean antibody titer ratio on fingolimod as compared to placebo six weeks after a single dose of seasonal influenza vaccine.

Outcome measures

Outcome measures
Measure
Fingolimod
n=88 Participants
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
n=43 Participants
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Change From Baseline in Seasonal Influenza Vaccine Antibody-titer 6 Weeks After Vaccination
A/California/7/09(H1N1)
1.81 ratio
2.91 ratio
Change From Baseline in Seasonal Influenza Vaccine Antibody-titer 6 Weeks After Vaccination
A/Perth/16/2009(H3N2)
0.36 ratio
0.28 ratio
Change From Baseline in Seasonal Influenza Vaccine Antibody-titer 6 Weeks After Vaccination
B/Brisbane/60/2008
1.08 ratio
2.07 ratio

SECONDARY outcome

Timeframe: From first dose of study drug until 45 days after the last dose of study drug (130 days).

Population: Safety set - all patients who received at least 1 dose of study drug.

Relationship to study drug was determined by the investigator (suspected/not suspected). A serious AE is defined as an event which fulfills one of the following criteria: * is fatal or life-threatening; * results in persistent or significant disability/incapacity; * constitutes a congenital anomaly/birth defect; * requires inpatient hospitalization or prolongation of existing hospitalization; * is medically significant, i.e., jeopardizes the patient or may require intervention to prevent one of the outcomes listed above.

Outcome measures

Outcome measures
Measure
Fingolimod
n=95 Participants
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
n=43 Participants
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Number of Participants With Adverse Events (AEs)
Any adverse event
82 participants
34 participants
Number of Participants With Adverse Events (AEs)
AE related to study drug
42 participants
11 participants
Number of Participants With Adverse Events (AEs)
Serious adverse event
1 participants
2 participants
Number of Participants With Adverse Events (AEs)
Adverse events leading to discontinuation
1 participants
0 participants

Adverse Events

Fingolimod

Serious events: 1 serious events
Other events: 51 other events
Deaths: 0 deaths

Placebo

Serious events: 2 serious events
Other events: 22 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Fingolimod
n=95 participants at risk
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
n=43 participants at risk
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Infections and infestations
Herpes zoster
0.00%
0/95
2.3%
1/43
Injury, poisoning and procedural complications
Hip fracture
0.00%
0/95
2.3%
1/43
Nervous system disorders
Paraparesis
1.1%
1/95
0.00%
0/43

Other adverse events

Other adverse events
Measure
Fingolimod
n=95 participants at risk
Participants received Fingolimod 0.5 mg capsules orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Placebo
n=43 participants at risk
Participants received placebo tablets orally once daily for 12 weeks. At Week 6 of study treatment participants received a seasonal influenza vaccination and a tetanus booster vaccination.
Blood and lymphatic system disorders
Lymphopenia
10.5%
10/95
0.00%
0/43
Gastrointestinal disorders
Diarrhoea
3.2%
3/95
7.0%
3/43
Gastrointestinal disorders
Nausea
2.1%
2/95
9.3%
4/43
General disorders
Fatigue
3.2%
3/95
7.0%
3/43
Infections and infestations
Nasopharyngitis
15.8%
15/95
18.6%
8/43
Infections and infestations
Upper respiratory tract infection
11.6%
11/95
14.0%
6/43
Infections and infestations
Urinary tract infection
5.3%
5/95
4.7%
2/43
Nervous system disorders
Headache
18.9%
18/95
9.3%
4/43
Respiratory, thoracic and mediastinal disorders
Cough
7.4%
7/95
0.00%
0/43

Additional Information

Study Director

Novartis Pharmaceuticals

Phone: 862-778-8300

Results disclosure agreements

  • Principal investigator is a sponsor employee The terms and conditions of Novartis' agreements with its investigators may vary. However, Novartis does not prohibit any investigator from publishing. Any publications from a single-site are postponed until the publication of the pooled data (i.e., data from all sites) in the clinical trial.
  • Publication restrictions are in place

Restriction type: OTHER