Trial Outcomes & Findings for 3F8/GM-CSF Immunotherapy Plus 13-Cis-Retinoic Acid for Primary Refractory Neuroblastoma in Bone Marrow (NCT NCT01183897)

NCT ID: NCT01183897

Last Updated: 2019-08-13

Results Overview

against persistent neuroblastoma in bone marrow of patients who have no other evidence of disease by standard studies.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

31 participants

Primary outcome timeframe

2 years

Results posted on

2019-08-13

Participant Flow

Participant milestones

Participant milestones
Measure
3F8/GM-CSF Immunotherapy Plus 13-Cis-Retinoic
This phase II study of the anti-GD2 murine IgG3 monoclonal antibody 3F8 combined with granulocyte-macrophage colony stimulating factor (GM-CSF) will assess response in of primary refractory neuroblastoma in bone marrow (i.e., incomplete response to standard treatment).
Overall Study
STARTED
31
Overall Study
COMPLETED
31
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

3F8/GM-CSF Immunotherapy Plus 13-Cis-Retinoic Acid for Primary Refractory Neuroblastoma in Bone Marrow

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
3F8/GM-CSF Immunotherapy Plus 13-Cis-Retinoic
n=31 Participants
This phase II study of the anti-GD2 murine IgG3 monoclonal antibody 3F8 combined with granulocyte-macrophage colony stimulating factor (GM-CSF) will assess response in of primary refractory neuroblastoma in bone marrow (i.e., incomplete response to standard treatment).
Age, Categorical
<=18 years
31 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
Sex: Female, Male
Female
9 Participants
n=5 Participants
Sex: Female, Male
Male
22 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
0 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
31 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
1 Participants
n=5 Participants
Race (NIH/OMB)
White
27 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
2 Participants
n=5 Participants
Region of Enrollment
United States
28 participants
n=5 Participants
Region of Enrollment
Greece
1 participants
n=5 Participants
Region of Enrollment
Israel
2 participants
n=5 Participants

PRIMARY outcome

Timeframe: 2 years

Population: Data were not collected

against persistent neuroblastoma in bone marrow of patients who have no other evidence of disease by standard studies.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 2 years

Population: Data were not collected

to test the hypothesis that the minimal residual disease content of bone marrow after the first treatments with 3F8/GMCSF has significant prognostic impact on progression-free survival.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: 2 years

Population: Data were not collected

to assure no side-effects or noxious sequelae develop or emerge that were not seen in the prior phase I study.

Outcome measures

Outcome data not reported

Adverse Events

3F8/GM-CSF Immunotherapy Plus 13-Cis-Retinoic

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Brian Kushner MD

Memorial Sloan Kettering Cancer Center

Phone: 212-639-6793

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place