Trial Outcomes & Findings for Revlimid in Transfusion Dependent Patients (NCT NCT01178814)

NCT ID: NCT01178814

Last Updated: 2024-06-24

Results Overview

The trial will be testing the Revlimid® (lenalidomide) response signature in patients who have transfusion dependent, non-del(5q), low and intermediate-1 risk myelodysplastic syndromes (MDS) in order to confirm the predictive value of the signature and to establish the boundaries of the z-score which can be used to pre-select patients in future clinical studies. Per Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0) for target lesions and assessed by MRI: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

57 participants

Primary outcome timeframe

Up to 12 weeks from baseline

Results posted on

2024-06-24

Participant Flow

Participant milestones

Participant milestones
Measure
Revlimid
Revlimid (Lenalidomide) capsule taken orally once a day Revlimid (Lenalidomide): The starting dose will be 10 mg days 1-28 with the first dose reduction going to 5 mg days 1-28 of a 28 day cycle. Therapy will cease if there is no response after 12 weeks.
Overall Study
STARTED
57
Overall Study
COMPLETED
57
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Revlimid in Transfusion Dependent Patients

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Revlimid
n=57 Participants
Revlimid (Lenalidomide) capsule taken orally once a day Revlimid (Lenalidomide): The starting dose will be 10 mg days 1-28 with the first dose reduction going to 5 mg days 1-28 of a 28 day cycle. Therapy will cease if there is no response after 12 weeks.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
15 Participants
n=5 Participants
Age, Categorical
>=65 years
42 Participants
n=5 Participants
Sex: Female, Male
Female
16 Participants
n=5 Participants
Sex: Female, Male
Male
41 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
2 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
19 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
36 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
3 Participants
n=5 Participants
Race (NIH/OMB)
White
37 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
17 Participants
n=5 Participants
Region of Enrollment
United States
57 participants
n=5 Participants

PRIMARY outcome

Timeframe: Up to 12 weeks from baseline

The trial will be testing the Revlimid® (lenalidomide) response signature in patients who have transfusion dependent, non-del(5q), low and intermediate-1 risk myelodysplastic syndromes (MDS) in order to confirm the predictive value of the signature and to establish the boundaries of the z-score which can be used to pre-select patients in future clinical studies. Per Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0) for target lesions and assessed by MRI: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions.

Outcome measures

Outcome measures
Measure
Revlimid
n=57 Participants
Revlimid (Lenalidomide) capsule taken orally once a day Revlimid (Lenalidomide): The starting dose will be 10 mg days 1-28 with the first dose reduction going to 5 mg days 1-28 of a 28 day cycle. Therapy will cease if there is no response after 12 weeks.
Response Signature in Transfusion Dependent MDS Patients
No response
24 Participants
Response Signature in Transfusion Dependent MDS Patients
Delayed response
1 Participants
Response Signature in Transfusion Dependent MDS Patients
Complete Response (CR)
17 Participants
Response Signature in Transfusion Dependent MDS Patients
Partial Response (PR)
6 Participants
Response Signature in Transfusion Dependent MDS Patients
Other response
9 Participants

Adverse Events

Revlimid

Serious events: 3 serious events
Other events: 8 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Revlimid
n=57 participants at risk
Revlimid (Lenalidomide) capsule taken orally once a day Revlimid (Lenalidomide): The starting dose will be 10 mg days 1-28 with the first dose reduction going to 5 mg days 1-28 of a 28 day cycle. Therapy will cease if there is no response after 12 weeks.
Gastrointestinal disorders
Diarrhea
1.8%
1/57 • Up to 3 months
Respiratory, thoracic and mediastinal disorders
Dyspnea
1.8%
1/57 • Up to 3 months
Blood and lymphatic system disorders
Febrile neutropenia
1.8%
1/57 • Up to 3 months

Other adverse events

Other adverse events
Measure
Revlimid
n=57 participants at risk
Revlimid (Lenalidomide) capsule taken orally once a day Revlimid (Lenalidomide): The starting dose will be 10 mg days 1-28 with the first dose reduction going to 5 mg days 1-28 of a 28 day cycle. Therapy will cease if there is no response after 12 weeks.
Musculoskeletal and connective tissue disorders
Back Pain
5.3%
3/57 • Up to 3 months
Gastrointestinal disorders
Diarrhea
7.0%
4/57 • Up to 3 months
Investigations
Platelet count abnormality
7.0%
4/57 • Up to 3 months
Skin and subcutaneous tissue disorders
Rash
7.0%
4/57 • Up to 3 months

Additional Information

Mark Heaney, MD

Columbia University Irving Medical Center

Phone: 646-317-5199

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place