Trial Outcomes & Findings for A Safety and Tolerability Study of Doripenem Compared With Meropenem in Children Hospitalized With Complicated Intra-abdominal Infections (NCT NCT01110382)

NCT ID: NCT01110382

Last Updated: 2014-07-15

Results Overview

The participants were considered as clinical cure if they had clinical improvement in signs and symptoms of the intra-abdominal infection such that no additional antibacterial therapy or surgical or percutaneous intervention is/was required for the treatment of the index infection, no fever, and a favorable response at End of IV visit.

Recruitment status

TERMINATED

Study phase

PHASE3

Target enrollment

41 participants

Primary outcome timeframe

TOC (7 to 14 days after the last dose of study medication therapy)

Results posted on

2014-07-15

Participant Flow

Participant milestones

Participant milestones
Measure
Doripenem
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Overall Study
STARTED
31
10
Overall Study
COMPLETED
31
8
Overall Study
NOT COMPLETED
0
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Doripenem
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Overall Study
Withdrawal by Subject
0
1
Overall Study
Protocol Violation
0
1

Baseline Characteristics

A Safety and Tolerability Study of Doripenem Compared With Meropenem in Children Hospitalized With Complicated Intra-abdominal Infections

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Doripenem
n=31 Participants
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
n=10 Participants
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Total
n=41 Participants
Total of all reporting groups
Age, Categorical
<=18 years
31 Participants
n=5 Participants
10 Participants
n=7 Participants
41 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Continuous
8.5 years
STANDARD_DEVIATION 3.40 • n=5 Participants
9.3 years
STANDARD_DEVIATION 4.52 • n=7 Participants
8.7 years
STANDARD_DEVIATION 3.66 • n=5 Participants
Age, Customized
3 months to <2 years
0 participants
n=5 Participants
0 participants
n=7 Participants
0 participants
n=5 Participants
Age, Customized
2 to <6 years
5 participants
n=5 Participants
3 participants
n=7 Participants
8 participants
n=5 Participants
Age, Customized
6 to <12 years
18 participants
n=5 Participants
4 participants
n=7 Participants
22 participants
n=5 Participants
Age, Customized
12 to <18 years
8 participants
n=5 Participants
3 participants
n=7 Participants
11 participants
n=5 Participants
Sex: Female, Male
Female
15 Participants
n=5 Participants
0 Participants
n=7 Participants
15 Participants
n=5 Participants
Sex: Female, Male
Male
16 Participants
n=5 Participants
10 Participants
n=7 Participants
26 Participants
n=5 Participants

PRIMARY outcome

Timeframe: TOC (7 to 14 days after the last dose of study medication therapy)

Population: Clinical Intent-to-Treat (CITT): All randomized participants who met the minimal disease definition of complicated intra-abdominal infection regardless if a baseline pathogen was isolated from the intra-abdominal cavity.

The participants were considered as clinical cure if they had clinical improvement in signs and symptoms of the intra-abdominal infection such that no additional antibacterial therapy or surgical or percutaneous intervention is/was required for the treatment of the index infection, no fever, and a favorable response at End of IV visit.

Outcome measures

Outcome measures
Measure
Doripenem
n=31 Participants
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
n=10 Participants
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
The Number of Participants With Clinical Cure Rate at Test Of Cure (TOC) Visit
23 participants
7 participants

SECONDARY outcome

Timeframe: EIV (within 24 hours after completion of the last dose of IV study medication therapy)

Population: Clinical Intent-to-Treat (CITT): All randomized participants who met the minimal disease definition of complicated intra-abdominal infection regardless if a baseline pathogen was isolated from the intra-abdominal cavity.

The participants were considered as clinical improved if they had clinical improvement in signs and symptoms of the intra-abdominal infection, no fever, decrease in WBC, and not received any nonstudy antibiotics for the treatment of intra-abdominal infection after IV study drug therapy had begun.

Outcome measures

Outcome measures
Measure
Doripenem
n=31 Participants
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
n=10 Participants
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
The Number of Participants With Clinical Improvement Rate at End of IV (EIV) Visit
29 participants
8 participants

SECONDARY outcome

Timeframe: LFU (28 to 42 days after the last dose of study medication therapy)

Population: Clinical Intent-to-Treat (CITT): All randomized participants who met the minimal disease definition of complicated intra-abdominal infection regardless if a baseline pathogen was isolated from the intra-abdominal cavity.

The participants were considered as clinical cure if they had clinical improvement in signs and symptoms of the intra-abdominal infection such that no additional antibacterial therapy or surgical or percutaneous intervention is/was required for the treatment of the index infection, no fever, and a favorable response at End of IV visit.

Outcome measures

Outcome measures
Measure
Doripenem
n=31 Participants
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
n=10 Participants
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
The Number of Participants With Clinical Cure Rate at Late Follow-Up (LFU) Visit
22 participants
6 participants

SECONDARY outcome

Timeframe: EIV (within 24 hours after completion of the last dose of IV study medication therapy), TOC (7 to 14 days after the last dose of study medication therapy), and LFU (28 to 42 days after the last dose of study medication therapy)

Population: Microbiological intent-to-treat - Participants of CITT with at least 1 baseline bacterial pathogen isolated from the intra-abdominal cavity that was susceptible to both doripenem and meropenem. 8 and 2 participants from doripenem and meropenem, respectively had no susceptible intra-abdominal pathogen at baseline and were excluded from this set.

Favorable per-participant microbiological response rate was evaluated at the at End of IV (EIV) visit, Test Of Cure (TOC) visit, and Late Follow-Up (LFU) visit. The favorable per-participant microbiological response was considered when all baseline pathogens were eradicated (absence) or presumed eradicated (absence of material to culture in a participant who has a positive clinical response to treatment).

Outcome measures

Outcome measures
Measure
Doripenem
n=23 Participants
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
n=8 Participants
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
The Number of Participants With Favorable Per-participant Microbiological Response
EIV visit
21 participants
6 participants
The Number of Participants With Favorable Per-participant Microbiological Response
TOC visit
17 participants
5 participants
The Number of Participants With Favorable Per-participant Microbiological Response
LFU visit
17 participants
5 participants

SECONDARY outcome

Timeframe: EIV (within 24 hours after completion of the last dose of IV study medication therapy)

Population: Microbiological intent-to-treat - Participants of CITT with at least 1 baseline bacterial pathogen isolated from the intra-abdominal cavity that was susceptible to both doripenem and meropenem. 8 and 2 participants from doripenem and meropenem, respectively had no susceptible intra-abdominal pathogen at baseline and were excluded from this set.

A total of 24 pathogens in the doripenem group and 6 pathogens in the meropenem group were isolated at baseline from the intra-abdominal culture and were susceptible to the study drug received. The most common pathogens isolated from the intra-abdominal culture are listed in the table below; the numbers in parenthesis next to each pathogen represent the number of participants with the pathogen isolated at baseline in the doripenem and meropenem treatment groups, respectively. The favorable per-pathogen microbiological outcome was considered when all baseline pathogens were eradicated (absence) or presumed eradicated (absence of material to culture in a participant who has a positive clinical response to treatment).

Outcome measures

Outcome measures
Measure
Doripenem
n=23 Participants
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
n=8 Participants
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Number of Participants With Favorable Per-pathogen Microbiological Outcome Rate at End of IV (EIV) Visit
Streptococcus anginosus (13, 0)
12 participants
NA participants
No isolates of Streptococcus anginosus observed at baseline.
Number of Participants With Favorable Per-pathogen Microbiological Outcome Rate at End of IV (EIV) Visit
Escherichia coli (19, 8)
18 participants
6 participants
Number of Participants With Favorable Per-pathogen Microbiological Outcome Rate at End of IV (EIV) Visit
Bacteroides fragilis (11, 1)
10 participants
1 participants

SECONDARY outcome

Timeframe: TOC (7 to 14 days after the last dose of study medication therapy)

Population: Microbiological intent-to-treat - Participants of CITT with at least 1 baseline bacterial pathogen isolated from the intra-abdominal cavity that was susceptible to both doripenem and meropenem. 8 and 2 participants from doripenem and meropenem, respectively had no susceptible intra-abdominal pathogen at baseline and were excluded from this set.

A total of 24 pathogens in the doripenem group and 6 pathogens in the meropenem group were isolated at baseline from the intra-abdominal culture and were susceptible to the study drug received. The most common pathogens isolated from the intra-abdominal culture are listed in the table below; the numbers in parenthesis next to each pathogen represent the number of participants with the pathogen isolated at baseline in the doripenem and meropenem treatment groups, respectively. The favorable per-pathogen microbiological outcome was considered when all baseline pathogens were eradicated (absence) or presumed eradicated (absence of material to culture in a participant who has a positive clinical response to treatment).

Outcome measures

Outcome measures
Measure
Doripenem
n=23 Participants
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
n=8 Participants
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Number of Participants With Favorable Per-pathogen Microbiological Outcome Rate at Test Of Cure (TOC) Visit
Streptococcus anginosus (13, 0)
9 participants
NA participants
No isolates of Streptococcus anginosus observed at baseline.
Number of Participants With Favorable Per-pathogen Microbiological Outcome Rate at Test Of Cure (TOC) Visit
Escherichia coli (19, 8)
15 participants
5 participants
Number of Participants With Favorable Per-pathogen Microbiological Outcome Rate at Test Of Cure (TOC) Visit
Bacteroides fragilis (11, 1)
9 participants
1 participants

SECONDARY outcome

Timeframe: LFU (28 to 42 days after the last dose of study medication therapy)

Population: Microbiological intent-to-treat - Participants of CITT with at least 1 baseline bacterial pathogen isolated from the intra-abdominal cavity that was susceptible to both doripenem and meropenem. 8 and 2 participants from doripenem and meropenem, respectively had no susceptible intra-abdominal pathogen at baseline and were excluded from this set.

A total of 24 pathogens in the doripenem group and 6 pathogens in the meropenem group were isolated at baseline from the intra-abdominal culture and were susceptible to the study drug received. The most common pathogens isolated at baseline from the intra-abdominal culture are listed in the table below; the numbers in parenthesis next to each pathogen represent the number of participants with the pathogen isolated in the doripenem and meropenem treatment groups, respectively. The favorable per-pathogen microbiological outcome was considered when all baseline pathogens were eradicated (absence) or presumed eradicated (absence of material to culture in a participant who has a positive clinical response to treatment).

Outcome measures

Outcome measures
Measure
Doripenem
n=23 Participants
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
n=8 Participants
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Number of Participants With Favorable Per-pathogen Microbiological Outcome Rate at Late Follow-Up (LFU) Visit
Streptococcus anginosus (13, 0)
9 participants
NA participants
No isolates of Streptococcus anginosus observed at baseline.
Number of Participants With Favorable Per-pathogen Microbiological Outcome Rate at Late Follow-Up (LFU) Visit
Escherichia coli (19, 8)
15 participants
5 participants
Number of Participants With Favorable Per-pathogen Microbiological Outcome Rate at Late Follow-Up (LFU) Visit
Bacteroides fragilis (11, 1)
9 participants
1 participants

Adverse Events

Doripenem

Serious events: 7 serious events
Other events: 15 other events
Deaths: 0 deaths

Meropenem

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Doripenem
n=31 participants at risk
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
n=10 participants at risk
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Gastrointestinal disorders
Abdominal Pain
9.7%
3/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks
Gastrointestinal disorders
Functional Gastrointestinal Disorder
3.2%
1/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks
Injury, poisoning and procedural complications
Overdose
3.2%
1/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks
Injury, poisoning and procedural complications
Seroma
3.2%
1/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks
Infections and infestations
Abdominal Abscess
3.2%
1/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks

Other adverse events

Other adverse events
Measure
Doripenem
n=31 participants at risk
Doripenem 20 mg/kg per dose (up to 500 mg/dose) was administered every 8 hours as 60-minutes IV (at least 3 days of IV doripenem only or IV doripenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Meropenem
n=10 participants at risk
Meropenem 20 mg/kg per dose (up to 1 g/dose) was administered every 8 hours as 30-minutes IV (at least 3 days of IV meropenem only or IV meropenem followed by oral amoxicillin/clavulanate potassium). Total duration of treatment 5 to 14 days.
Gastrointestinal disorders
Nausea
9.7%
3/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks
Gastrointestinal disorders
Abdominal Distension
6.5%
2/31 • Approximately 8 weeks
10.0%
1/10 • Approximately 8 weeks
Gastrointestinal disorders
Abdominal Pain
6.5%
2/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks
Gastrointestinal disorders
Constipation
6.5%
2/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks
Gastrointestinal disorders
Vomiting
6.5%
2/31 • Approximately 8 weeks
20.0%
2/10 • Approximately 8 weeks
Gastrointestinal disorders
Diarrhoea
3.2%
1/31 • Approximately 8 weeks
20.0%
2/10 • Approximately 8 weeks
Gastrointestinal disorders
Tongue Ulceration
0.00%
0/31 • Approximately 8 weeks
10.0%
1/10 • Approximately 8 weeks
Investigations
Alanine Aminotransferase Increased
6.5%
2/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks
Investigations
Gamma-Glutamyltransferase Increased
6.5%
2/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks
Investigations
Electrocardiogram QT Prolonged
0.00%
0/31 • Approximately 8 weeks
10.0%
1/10 • Approximately 8 weeks
Blood and lymphatic system disorders
Eosinophilia
6.5%
2/31 • Approximately 8 weeks
0.00%
0/10 • Approximately 8 weeks
Cardiac disorders
Ventricular Extrasystoles
0.00%
0/31 • Approximately 8 weeks
10.0%
1/10 • Approximately 8 weeks
Infections and infestations
Nasopharyngitis
0.00%
0/31 • Approximately 8 weeks
10.0%
1/10 • Approximately 8 weeks
Infections and infestations
Otitis Media
0.00%
0/31 • Approximately 8 weeks
10.0%
1/10 • Approximately 8 weeks
Skin and subcutaneous tissue disorders
Rash
0.00%
0/31 • Approximately 8 weeks
10.0%
1/10 • Approximately 8 weeks

Additional Information

Therapeutic Areas Director

Janssen R&D US

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: GT60