Study of Telotristat Etiprate (LX1606) in Participants With Symptomatic Carcinoid Syndrome

NCT ID: NCT01104415

Last Updated: 2019-03-15

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

15 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-06-15

Study Completion Date

2014-02-12

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of the study is to evaluate the safety and tolerability of orally administered telotristat etiprate (LX1606) in participants with symptomatic carcinoid syndrome.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Carcinoid Syndrome

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Telotristat etiprate - Core Phase

Following a 2-week Run-In Period, participants received telotristat etiprate capsules at a starting dose of 150 mg, orally three times daily (TID) for 14 days in the Core Phase. Dose escalations (250 mg, 350 mg, 500 mg) occurred serially every 14 days, up to a maximum dosage of telotristat etiprate 500 mg TID, as guided by specific clinical criteria for dose escalation. Upon completion of 12 weeks of treatment, participants were eligible to receive telotristat etiprate in the optional Open-label Extension Period.

Group Type EXPERIMENTAL

Telotristat etiprate

Intervention Type DRUG

Telotristat etiprate capsules orally three times daily.

Telotristat etiprate - Extension Period

Participants received telotristat etiprate at their highest tolerated dose (250 mg or 500 mg), orally, TID for 124 weeks in the Open-label Extension Period. If neither dose was tolerated participants were discontinued from the study and completed the 2-week Follow-up Visit.

Group Type EXPERIMENTAL

Telotristat etiprate

Intervention Type DRUG

Telotristat etiprate capsules orally three times daily.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Telotristat etiprate

Telotristat etiprate capsules orally three times daily.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

LX1606 Hippurate

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Males and females, aged 18 and older
* Biopsy-proven metastatic carcinoid tumor of the gastrointestinal (GI) tract with disease extent confirmed by computed tomography (CT), magnetic resonance imaging (MRI), or radionuclide imaging
* Symptomatic carcinoid syndrome (≥4 bowel movements per day)
* Ability to provide written informed consent

Exclusion Criteria

* ≥ 12 high-volume, watery bowel movements per day
* Sponsor-unacceptable clinical laboratory values for hematology and liver function tests at screening
* Karnofsky status ≤70% - unable to care for self
* Surgery within 60 days prior to screening
* A history of short bowel syndrome
* Life expectancy \< 12 months
* History of substance or alcohol abuse within 2 years prior to screening
* Administration of any investigational drug within 30 days of screening or any therapeutic protein or antibody within 90 days of screening
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Lexicon Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Pablo LaPuerta, MD

Role: STUDY_DIRECTOR

Lexicon Pharmaceuticals, Inc.

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Lexicon Investigational Site

Bad Berka, , Germany

Site Status

Lexicon Investigational Site

Berlin, , Germany

Site Status

Lexicon Investigational Site

Halle, , Germany

Site Status

Lexicon Investigational Site

Lübeck, , Germany

Site Status

Lexicon Investigational Site

Marburg, , Germany

Site Status

Lexicon Investigational Site

Munich, , Germany

Site Status

Lexicon Investigational Site

Basingstoke, , United Kingdom

Site Status

Lexicon Investigational Site

Cambridge, , United Kingdom

Site Status

Lexicon Investigational Site

London, , United Kingdom

Site Status

Lexicon Investigational Site

Manchester, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

Germany United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Pavel M, Horsch D, Caplin M, Ramage J, Seufferlein T, Valle J, Banks P, Lapuerta P, Sands A, Zambrowicz B, Fleming D, Wiedenmann B. Telotristat etiprate for carcinoid syndrome: a single-arm, multicenter trial. J Clin Endocrinol Metab. 2015 Apr;100(4):1511-9. doi: 10.1210/jc.2014-2247. Epub 2015 Jan 30.

Reference Type DERIVED
PMID: 25636046 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

LX1606.203, LX1032

Identifier Type: OTHER

Identifier Source: secondary_id

2009-016973-13

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

LX1606.1-203-CS

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.