Trial Outcomes & Findings for Trial of the Use of Antenatal Corticosteroids in Developing Countries (NCT NCT01084096)

NCT ID: NCT01084096

Last Updated: 2024-12-09

Results Overview

Neonatal deaths before 28 days per 1,000 live births among \<5th %tile birth weight infants. The \<5th %tile birth weight group was a proxy for preterm. Site-specific cutoffs from pretrial data were 2,450g-Argentina, 2,400g-Zambia, 2,267g-Guatemala, 2,000g-Belgaum, India, 2,150g-Pakistan, 2,000g-Nagpur, India, and 2,500g-Kenya. Infants were classified as \<5th %tile on the basis of measured birth weights. Estimated weights by clinical assessment were used when measured weights were unavailable; those missing weights were classified as \<5th %tile (since based on historical data, most of the missing data were for preterm infants). We used birth weight rather than gestational age (GA) for the primary analysis subgroup because many women in the registry had missing or uncertain GA, ultrasound was often unavailable, and the intervention was designed to improve estimation of GA, which could potentially bias GA-based analyses. All live births, including multiple births, are included.

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

103117 participants

Primary outcome timeframe

Birth to 28 days

Results posted on

2024-12-09

Participant Flow

18m, 2-arm, parallel, cluster-randomized trial in 7 Global Network sites from Oct 2011-Mar 2014. Health providers in intervention clusters identified women at high risk of preterm birth for antenatal corticosteroids. Overall, 349 and 360 health facilities served intervention and control clusters, respectively; most (260 in each group) were clinics.

The treatment group for each cluster (and thus all women residing in the cluster) was randomly assigned pretrial (1:1) using a stratified procedure to account for pretrial characteristics. 102 clusters were randomly assigned (51 control:51 intervention). One control cluster withdrew because of unrelated safety concerns prior to study start.

Unit of analysis: Geographic Cluster

Participant milestones

Participant milestones
Measure
Intervention Group
Women and their babies residing in geographic clusters assigned to the intervention group. If the woman was identified as high-risk for preterm birth from 24 - 36 weeks' gestational age by the intervention she received one course of four doses of 6 mg of dexamethasone every 12 hours. If identified outside the intervention, she received standard of care.
Control Group
Women and their babies residing in geographic clusters assigned to the control group. If the woman was identified as high-risk for preterm birth, she received standard of care.
Overall Study
STARTED
49744 51
53373 51
Overall Study
COMPLETED
48219 51
51523 50
Overall Study
NOT COMPLETED
1525 0
1850 1

Reasons for withdrawal

Reasons for withdrawal
Measure
Intervention Group
Women and their babies residing in geographic clusters assigned to the intervention group. If the woman was identified as high-risk for preterm birth from 24 - 36 weeks' gestational age by the intervention she received one course of four doses of 6 mg of dexamethasone every 12 hours. If identified outside the intervention, she received standard of care.
Control Group
Women and their babies residing in geographic clusters assigned to the control group. If the woman was identified as high-risk for preterm birth, she received standard of care.
Overall Study
Lost to Follow-up
1501
1833
Overall Study
Withdrawal by Subject
3
0
Overall Study
Woman had a miscarriage
21
17

Baseline Characteristics

Trial of the Use of Antenatal Corticosteroids in Developing Countries

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Intervention Group
n=48 Participants
Women and their babies residing in geographic clusters assigned to the intervention group. If the woman was identified as high-risk for preterm birth from 24 - 36 weeks' gestational age by the intervention she received one course of four doses of 6 mg of dexamethasone every 12 hours. If identified outside the intervention, she received standard of care.
Control Group
n=51 Participants
Women and their babies residing in geographic clusters assigned to the control group. If the woman was identified as high-risk for preterm birth, she received standard of care.
Total
n=99742 Participants
Total of all reporting groups
Age, Customized
<20
5,412 Participants
n=5 Participants
6,622 Participants
n=7 Participants
12034 Participants
n=5 Participants
Age, Customized
20-35
41,003 Participants
n=5 Participants
42,938 Participants
n=7 Participants
83941 Participants
n=5 Participants
Age, Customized
>35
1,741 Participants
n=5 Participants
1,895 Participants
n=7 Participants
3636 Participants
n=5 Participants
Age, Customized
Missing
63 Participants
n=5 Participants
68 Participants
n=7 Participants
131 Participants
n=5 Participants
Sex: Female, Male
Female
48,219 Participants
n=5 Participants
51,523 Participants
n=7 Participants
99742 Participants
n=5 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Region of Enrollment
Argentina
2,115 participants
n=5 Participants
2,292 participants
n=7 Participants
4407 participants
n=5 Participants
Region of Enrollment
Pakistan
7,714 participants
n=5 Participants
8,202 participants
n=7 Participants
15916 participants
n=5 Participants
Region of Enrollment
Guatemala
5,813 participants
n=5 Participants
3,960 participants
n=7 Participants
9773 participants
n=5 Participants
Region of Enrollment
Zambia
4,279 participants
n=5 Participants
5,739 participants
n=7 Participants
10018 participants
n=5 Participants
Region of Enrollment
Kenya
5,900 participants
n=5 Participants
7,103 participants
n=7 Participants
13003 participants
n=5 Participants
Region of Enrollment
India
22,398 participants
n=5 Participants
24,227 participants
n=7 Participants
46625 participants
n=5 Participants
Education
No formal schooling
11,005 Participants
n=5 Participants
11,258 Participants
n=7 Participants
22263 Participants
n=5 Participants
Education
Primary
17,686 Participants
n=5 Participants
19,515 Participants
n=7 Participants
37201 Participants
n=5 Participants
Education
Secondary
15,528 Participants
n=5 Participants
16,170 Participants
n=7 Participants
31698 Participants
n=5 Participants
Education
University
3,757 Participants
n=5 Participants
4,313 Participants
n=7 Participants
8070 Participants
n=5 Participants
Education
Missing
243 Participants
n=5 Participants
267 Participants
n=7 Participants
510 Participants
n=5 Participants
Parity
0
16,366 Participants
n=5 Participants
17,901 Participants
n=7 Participants
34267 Participants
n=5 Participants
Parity
1
13,961 Participants
n=5 Participants
14,599 Participants
n=7 Participants
28560 Participants
n=5 Participants
Parity
2
17,570 Participants
n=5 Participants
18,934 Participants
n=7 Participants
36504 Participants
n=5 Participants
Parity
Missing
322 Participants
n=5 Participants
89 Participants
n=7 Participants
411 Participants
n=5 Participants

PRIMARY outcome

Timeframe: Birth to 28 days

Neonatal deaths before 28 days per 1,000 live births among \<5th %tile birth weight infants. The \<5th %tile birth weight group was a proxy for preterm. Site-specific cutoffs from pretrial data were 2,450g-Argentina, 2,400g-Zambia, 2,267g-Guatemala, 2,000g-Belgaum, India, 2,150g-Pakistan, 2,000g-Nagpur, India, and 2,500g-Kenya. Infants were classified as \<5th %tile on the basis of measured birth weights. Estimated weights by clinical assessment were used when measured weights were unavailable; those missing weights were classified as \<5th %tile (since based on historical data, most of the missing data were for preterm infants). We used birth weight rather than gestational age (GA) for the primary analysis subgroup because many women in the registry had missing or uncertain GA, ultrasound was often unavailable, and the intervention was designed to improve estimation of GA, which could potentially bias GA-based analyses. All live births, including multiple births, are included.

Outcome measures

Outcome measures
Measure
Intervention Group
n=2 Participants
Women and their babies residing in geographic clusters assigned to the intervention group. If the woman was identified as high-risk for preterm birth from 24 - 36 weeks' gestational age by the intervention she received one course of four doses of 6 mg of dexamethasone every 12 hours. If identified outside the intervention, she received standard of care.
Control Group
n=2 Participants
Women and their babies residing in geographic clusters assigned to the control group. If the woman was identified as high-risk for preterm birth, she received standard of care.
Neonatal Mortality Rate at 28 Days in <5th Percentile Birth Weight Infants (as a Proxy Measure for Prematurity)
566 Participants
524 Participants

SECONDARY outcome

Timeframe: 48 hours after identification of risk for preterm birth

Population: Among women with a less-than-5th-percentile for birth weight infant and with data on administration of antenatal corticosteroid data available.

Antenatal corticosteroids provided antepartum assessed in women with a less-than-5th-percentile for birth weight infants. Site-specific cut offs were determined from pretrial data.

Outcome measures

Outcome measures
Measure
Intervention Group
n=2 Participants
Women and their babies residing in geographic clusters assigned to the intervention group. If the woman was identified as high-risk for preterm birth from 24 - 36 weeks' gestational age by the intervention she received one course of four doses of 6 mg of dexamethasone every 12 hours. If identified outside the intervention, she received standard of care.
Control Group
n=2 Participants
Women and their babies residing in geographic clusters assigned to the control group. If the woman was identified as high-risk for preterm birth, she received standard of care.
Use of Antenatal Corticosteroids in Women at Risk of Preterm Birth in All the Study Clusters
1,052 Participants
215 Participants

SECONDARY outcome

Timeframe: Pregnancy through 6 weeks postpartum

Population: Women with infection data available from all data sources

Maternal safety was assessed through the frequency of suspected maternal infection, a composite of process outcomes including receipt of antibiotics plus hospital admission or referral, and receipt of intravenous fluids, surgery, or other treatment related to infection. The definition also included evidence of antepartum or post-partum infection for mothers with infants with a birthweight less than 2500 g. Additionally, use of antenatal corticosteroids, neonatal and perinatal mortality, and suspected maternal infection were measured for all births, irrespective of birthweight.

Outcome measures

Outcome measures
Measure
Intervention Group
n=48 Participants
Women and their babies residing in geographic clusters assigned to the intervention group. If the woman was identified as high-risk for preterm birth from 24 - 36 weeks' gestational age by the intervention she received one course of four doses of 6 mg of dexamethasone every 12 hours. If identified outside the intervention, she received standard of care.
Control Group
n=51 Participants
Women and their babies residing in geographic clusters assigned to the control group. If the woman was identified as high-risk for preterm birth, she received standard of care.
Suspected Maternal Infection
1,207 Participants
867 Participants

SECONDARY outcome

Timeframe: Pregnancy through 42 days postpartum

Population: All maternal deaths and pregnancy ending in live birth.

The denominator for maternal deaths through 42 days is pregnancy ending in live birth + all maternal deaths. Maternal mortality includes all maternal deaths through 42 days postpartum, irrespective of cause.

Outcome measures

Outcome measures
Measure
Intervention Group
n=46 Participants
Women and their babies residing in geographic clusters assigned to the intervention group. If the woman was identified as high-risk for preterm birth from 24 - 36 weeks' gestational age by the intervention she received one course of four doses of 6 mg of dexamethasone every 12 hours. If identified outside the intervention, she received standard of care.
Control Group
n=50 Participants
Women and their babies residing in geographic clusters assigned to the control group. If the woman was identified as high-risk for preterm birth, she received standard of care.
Maternal Mortality Rate
106 participants
97 participants

SECONDARY outcome

Timeframe: Birth to 28 days

Population: All live births, including multiples

Number of neonatal deaths before 28 days per 1,000 live births

Outcome measures

Outcome measures
Measure
Intervention Group
n=47 Participants
Women and their babies residing in geographic clusters assigned to the intervention group. If the woman was identified as high-risk for preterm birth from 24 - 36 weeks' gestational age by the intervention she received one course of four doses of 6 mg of dexamethasone every 12 hours. If identified outside the intervention, she received standard of care.
Control Group
n=50 Participants
Women and their babies residing in geographic clusters assigned to the control group. If the woman was identified as high-risk for preterm birth, she received standard of care.
Neonatal Mortality Rate
1300 Participants
1211 Participants

SECONDARY outcome

Timeframe: 20 weeks' gestational age to birth

Population: All births, including multiples.

Number of stillbirths per 1,000 births

Outcome measures

Outcome measures
Measure
Intervention Group
n=48 Participants
Women and their babies residing in geographic clusters assigned to the intervention group. If the woman was identified as high-risk for preterm birth from 24 - 36 weeks' gestational age by the intervention she received one course of four doses of 6 mg of dexamethasone every 12 hours. If identified outside the intervention, she received standard of care.
Control Group
n=52 Participants
Women and their babies residing in geographic clusters assigned to the control group. If the woman was identified as high-risk for preterm birth, she received standard of care.
Stillbirth Mortality Rate
1304 Participants
1264 Participants

Adverse Events

Intervention Group

Serious events: 2932 serious events
Other events: 0 other events
Deaths: 0 deaths

Control Group

Serious events: 2774 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Intervention Group
n=48698 participants at risk
Women and their babies residing in geographic clusters assigned to the intervention group. If the woman was identified as high-risk for preterm birth from 24 - 36 weeks' gestational age by the intervention she received one course of four doses of 6 mg of dexamethasone every 12 hours. If identified outside the intervention, she received standard of care.
Control Group
n=52007 participants at risk
Women and their babies residing in geographic clusters assigned to the control group. If the woman was identified as high-risk for preterm birth, she received standard of care.
Pregnancy, puerperium and perinatal conditions
Maternal death
0.10%
50/48219 • During the period that the trial was active in a particular cluster, serious adverse events were captured on each woman from the time the woman was enrolled in the MNH registry until 6 weeks after delivery for each pregnant woman enrolled in the MNH registry and her babies.
Total number of serious adverse events is out of all participants (i.e. the number of women plus the number of babies (stillbirths and live births)).
0.10%
49/51523 • During the period that the trial was active in a particular cluster, serious adverse events were captured on each woman from the time the woman was enrolled in the MNH registry until 6 weeks after delivery for each pregnant woman enrolled in the MNH registry and her babies.
Total number of serious adverse events is out of all participants (i.e. the number of women plus the number of babies (stillbirths and live births)).
Pregnancy, puerperium and perinatal conditions
Stillbirth/neonatal death
5.3%
2604/48698 • During the period that the trial was active in a particular cluster, serious adverse events were captured on each woman from the time the woman was enrolled in the MNH registry until 6 weeks after delivery for each pregnant woman enrolled in the MNH registry and her babies.
Total number of serious adverse events is out of all participants (i.e. the number of women plus the number of babies (stillbirths and live births)).
4.8%
2475/52007 • During the period that the trial was active in a particular cluster, serious adverse events were captured on each woman from the time the woman was enrolled in the MNH registry until 6 weeks after delivery for each pregnant woman enrolled in the MNH registry and her babies.
Total number of serious adverse events is out of all participants (i.e. the number of women plus the number of babies (stillbirths and live births)).
Pregnancy, puerperium and perinatal conditions
Congenital anomaly
0.57%
278/48698 • During the period that the trial was active in a particular cluster, serious adverse events were captured on each woman from the time the woman was enrolled in the MNH registry until 6 weeks after delivery for each pregnant woman enrolled in the MNH registry and her babies.
Total number of serious adverse events is out of all participants (i.e. the number of women plus the number of babies (stillbirths and live births)).
0.48%
250/52007 • During the period that the trial was active in a particular cluster, serious adverse events were captured on each woman from the time the woman was enrolled in the MNH registry until 6 weeks after delivery for each pregnant woman enrolled in the MNH registry and her babies.
Total number of serious adverse events is out of all participants (i.e. the number of women plus the number of babies (stillbirths and live births)).

Other adverse events

Adverse event data not reported

Additional Information

Dr. Elizabeth McClure, Data Coordinating Center PI

NICHDGlobal

Phone: 919-316-3773

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place