Peripheral Blood Stem Cell Transplantation Using the CliniMACS Device

NCT ID: NCT01071226

Last Updated: 2021-10-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

NA

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-05-31

Study Completion Date

2020-04-28

Brief Summary

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T cell depletion utilizing the CliniMACS device will allow more precise, specific and controlled graft engineering of peripheral blood stem cells from unrelated and partially matched related donors without an increase in relapse or graft rejection and grade III or IV acute graft versus host disease (GVHD).

Detailed Description

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Conditions

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Malignant Diseases (ie, Leukemia, MDS, Lymphoma) Non-malignant Diseases (ie, Bone Marrow Failure Syndromes)

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Stratum 1

Patients receiving an unrelated donor or partially matched related donor.

Group Type EXPERIMENTAL

CliniMACS (CD+3, CD+19 depletion)

Intervention Type DEVICE

Patient's in Stratum 1 will receive grafts that have undergone CD3+, CD19+ depletion

HSCT

Intervention Type OTHER

Peripheral Blood Stem Cell Transplant

Stratum 2

For the patient's whose donors are haploidentical or a 2 antigen mismatched where one of the mismatches includes DRB1

Group Type EXPERIMENTAL

CliniMACS (CD 34+ positive selection)

Intervention Type DEVICE

Patient's in Stratum 2 will receive peripheral blood progenitor cells that have undergone CD34+ selection

HSCT

Intervention Type OTHER

Peripheral Blood Stem Cell Transplant

Interventions

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CliniMACS (CD+3, CD+19 depletion)

Patient's in Stratum 1 will receive grafts that have undergone CD3+, CD19+ depletion

Intervention Type DEVICE

CliniMACS (CD 34+ positive selection)

Patient's in Stratum 2 will receive peripheral blood progenitor cells that have undergone CD34+ selection

Intervention Type DEVICE

HSCT

Peripheral Blood Stem Cell Transplant

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* All races are eligible
* Malignant diseases: Leukemias and Lymphomas
* Non-malignant diseases: Severe Aplastic Anemia, immunodeficiencies

Exclusion Criteria

* Lansky or Karnofsky \> 70
* Echo \> 27% shortening fraction
* renal function:serum creatinine \< 1.5 x for normal age
* no active untreated infection
* DLCO \> 50% of predicted value
* Hepatic: AST and ALT \< 3x upper limit of normal; bilirubin \< 2.0.
Maximum Eligible Age

22 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Children's Hospital of Philadelphia

OTHER

Sponsor Role collaborator

Medical College of Wisconsin

OTHER

Sponsor Role lead

Responsible Party

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Julie-An M. Talano

Associate Professor of Pediatrics and Director of Clinical Pediatric BMT Research

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Julie A Talano, MD

Role: PRINCIPAL_INVESTIGATOR

Medical College of Wisconsin

Locations

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Children's Hospital of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Countries

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United States

Other Identifiers

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CHOP 07/216

Identifier Type: -

Identifier Source: org_study_id