Trial Outcomes & Findings for Comparative Efficacy & Safety Study of D961H Versus Placebo for the Prevention of Gastric and Duodenal Ulcers With Low-dose Aspirin (NCT NCT01069939)

NCT ID: NCT01069939

Last Updated: 2012-11-22

Results Overview

Assessments for occurrence of gastric and/or duodenal ulcers were performed every 12 weeks after randomisation. The numbers of participants with recurrence of gastric and/or duodeal ulcers were analysed every 12 weeks up to 48 weeks.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

427 participants

Primary outcome timeframe

From randomisation to up to 48 weeks (Maximum follow-up period at the interim analysis)

Results posted on

2012-11-22

Participant Flow

First participant enrolled on 4 February 2010. On 20 May 2011, the efficacy analysis was completed based on positive results of an interim analysis so that the efficacy data in this report are at the interim analysis. To evaluate the safety, the study was continued. The last participant completed the study on 9 November 2011.

Out of 914 enrolled participants, 430 participants were assigned , but 484 participants were not assigned. The major reasons of no assignment were 'Did not meet eligibility criteria' (462 participants) and 'Voluntary discontinuation by participant' (21 participants). After 366 participants were randomised, the interim analysis was done.

Participant milestones

Participant milestones
Measure
Esomeprazole 20mg
Esomeprazole 20mg once daily oral
Placebo
Placebo once daily oral
Randomised and Included in the Analyses
STARTED
213
214
Randomised and Included in the Analyses
COMPLETED
164
137
Randomised and Included in the Analyses
NOT COMPLETED
49
77
At Data Cut Off Date (26 Feb 2011)
STARTED
213
214
At Data Cut Off Date (26 Feb 2011)
COMPLETED
182
182
At Data Cut Off Date (26 Feb 2011)
NOT COMPLETED
31
32

Reasons for withdrawal

Reasons for withdrawal
Measure
Esomeprazole 20mg
Esomeprazole 20mg once daily oral
Placebo
Placebo once daily oral
Randomised and Included in the Analyses
Adverse Event
17
22
Randomised and Included in the Analyses
Withdrawal by Subject
15
12
Randomised and Included in the Analyses
Lost to Follow-up
1
1
Randomised and Included in the Analyses
Protocol Violation
0
1
Randomised and Included in the Analyses
Lack of Efficacy
0
1
Randomised and Included in the Analyses
Study-specific withdrawal criteria
7
33
Randomised and Included in the Analyses
Eligibility criteria not fulfilled
4
3
Randomised and Included in the Analyses
Use of prohibited concomitant drug
4
2
Randomised and Included in the Analyses
Physician Decision
0
2
Randomised and Included in the Analyses
Removal
1
0

Baseline Characteristics

Comparative Efficacy & Safety Study of D961H Versus Placebo for the Prevention of Gastric and Duodenal Ulcers With Low-dose Aspirin

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Esomeprazole 20mg
n=213 Participants
Esomeprazole 20mg once daily oral
Placebo
n=214 Participants
Placebo once daily oral
Total
n=427 Participants
Total of all reporting groups
Age, Customized
<=64years
85 Participants
n=5 Participants
71 Participants
n=7 Participants
156 Participants
n=5 Participants
Age, Customized
Between 65 and 74 years
82 Participants
n=5 Participants
89 Participants
n=7 Participants
171 Participants
n=5 Participants
Age, Customized
>=75 years
46 Participants
n=5 Participants
54 Participants
n=7 Participants
100 Participants
n=5 Participants
Sex: Female, Male
Female
43 Participants
n=5 Participants
46 Participants
n=7 Participants
89 Participants
n=5 Participants
Sex: Female, Male
Male
170 Participants
n=5 Participants
168 Participants
n=7 Participants
338 Participants
n=5 Participants
Region of Enrollment
Taiwan
22 Participants
n=5 Participants
21 Participants
n=7 Participants
43 Participants
n=5 Participants
Region of Enrollment
Japan
160 Participants
n=5 Participants
160 Participants
n=7 Participants
320 Participants
n=5 Participants
Region of Enrollment
Korea, Republic of
31 Participants
n=5 Participants
33 Participants
n=7 Participants
64 Participants
n=5 Participants
Helicobacter pylori status
Positive
93 Participants
n=5 Participants
93 Participants
n=7 Participants
186 Participants
n=5 Participants
Helicobacter pylori status
Negative
117 Participants
n=5 Participants
116 Participants
n=7 Participants
233 Participants
n=5 Participants

PRIMARY outcome

Timeframe: From randomisation to up to 48 weeks (Maximum follow-up period at the interim analysis)

Population: Participants not taking investigational drug were not included. In total 364 participants were included in the efficacy evaluation at the interim analysis. 24 of the 364 total participants had an occurrence of gastric and/or duodenal ulcers by the 48-week assessment.

Assessments for occurrence of gastric and/or duodenal ulcers were performed every 12 weeks after randomisation. The numbers of participants with recurrence of gastric and/or duodeal ulcers were analysed every 12 weeks up to 48 weeks.

Outcome measures

Outcome measures
Measure
Esomeprazole 20mg
n=182 Participants
Esomeprazole 20mg once daily oral
Placebo
n=182 Participants
Placebo once daily oral
Time From Randomization to Occurrence of Gastric and/or Duodenal Ulcers up to Data Cut-off Date for Interim Analysis.
0 - 12 weeks
1 Participants
16 Participants
Time From Randomization to Occurrence of Gastric and/or Duodenal Ulcers up to Data Cut-off Date for Interim Analysis.
13 - 24 weeks
1 Participants
4 Participants
Time From Randomization to Occurrence of Gastric and/or Duodenal Ulcers up to Data Cut-off Date for Interim Analysis.
25 - 36 weeks
0 Participants
2 Participants
Time From Randomization to Occurrence of Gastric and/or Duodenal Ulcers up to Data Cut-off Date for Interim Analysis.
37 - 48 weeks
0 Participants
0 Participants

SECONDARY outcome

Timeframe: Up to 48 weeks (Baseline to last measurement)

Population: Participants who had LANZA scores at both baseline and post-dose were included into this analysis.

Modified Lanza scale attributes the degree of gastric mucosal lesion, graded on a 5 point scale (0=No hemorrhage, no erosion, 1=One hemorrhage or one erosions, 2=2-10 hemorrhages or erosions, 3=11-25 hemorrhages or erosions, 4=More than 25 hemorrhages or erosions, or ulcer). Higher scores indicate greater severity of gastric mucosal lesion.

Outcome measures

Outcome measures
Measure
Esomeprazole 20mg
n=144 Participants
Esomeprazole 20mg once daily oral
Placebo
n=145 Participants
Placebo once daily oral
Change in Degree of Gastric Mucosal Lesion by Modified Lanza Scale From Baseline to Last Measurement up to Week 48
-0.4 Scores on a scale
Standard Deviation 0.6
1.3 Scores on a scale
Standard Deviation 1.6

SECONDARY outcome

Timeframe: 12, 24, 36 and 48 weeks

Population: Patients with endoscopy were included in the analyses at 12, 24, 36 and 48 weeks after randomisation.

Endoscopy was conducted at 12, 24, 36 and 48 weeks after randomisation. At the endoscopy, participants was evaluated whether they have reflux esophagitis or not.

Outcome measures

Outcome measures
Measure
Esomeprazole 20mg
n=141 Participants
Esomeprazole 20mg once daily oral
Placebo
n=138 Participants
Placebo once daily oral
Number of Participants With Reflux Esophagitis Evaluated by the LA Classification up to Week 48.
12 weeks
0 Participants
9 Participants
Number of Participants With Reflux Esophagitis Evaluated by the LA Classification up to Week 48.
24 weeks
1 Participants
6 Participants
Number of Participants With Reflux Esophagitis Evaluated by the LA Classification up to Week 48.
36 weeks
0 Participants
3 Participants
Number of Participants With Reflux Esophagitis Evaluated by the LA Classification up to Week 48.
48 weeks
0 Participants
0 Participants

SECONDARY outcome

Timeframe: Up to 48 weeks (Baseline to last measurement)

Population: Participants who had the measurements of epigastric pain at baseline and post-dose up to 48 weeks were included in this analysis.

The severity of epigastric pain at baseline and the last measurement up to 48 weeks was obtained (None, Mild, Moderate, Severe). If the value at the last was better in a participant, the participant was categorized into "Improved". If the value was same, categorised into "Unchanged". If the value was worsened, categorise into "Worsened".

Outcome measures

Outcome measures
Measure
Esomeprazole 20mg
n=168 Participants
Esomeprazole 20mg once daily oral
Placebo
n=172 Participants
Placebo once daily oral
Change in the Severity of Epigastric Pain From Baseline to Last Measurement up to Week 48
Improved
11 Participants
16 Participants
Change in the Severity of Epigastric Pain From Baseline to Last Measurement up to Week 48
Unchanged
153 Participants
145 Participants
Change in the Severity of Epigastric Pain From Baseline to Last Measurement up to Week 48
Worsened
4 Participants
11 Participants

SECONDARY outcome

Timeframe: Up to 48 weeks (Baseline to last measurement)

Population: Participants who had the measurements of heartburn at baseline and post-dose up to 48 weeks were included in this analysis.

The severity of heartburn at baseline and the last measurement up to 48 weeks was obtained (None, Mild, Moderate, Severe). If the value at the last was better in a participant, the participant was categorized into "Improved". If the value was same, categorised into "Unchanged". If the value was worsened, categorise into "Worsened".

Outcome measures

Outcome measures
Measure
Esomeprazole 20mg
n=168 Participants
Esomeprazole 20mg once daily oral
Placebo
n=172 Participants
Placebo once daily oral
Change in the Severity of Heartburn From Baseline to Last Measurement up to Week 48.
Improved
7 Participants
6 Participants
Change in the Severity of Heartburn From Baseline to Last Measurement up to Week 48.
Unchanged
158 Participants
154 Participants
Change in the Severity of Heartburn From Baseline to Last Measurement up to Week 48.
Worsened
3 Participants
12 Participants

SECONDARY outcome

Timeframe: Up to 48 weeks (Baseline to last measurement)

Population: Participants who had the measurements of anorexia at baseline and post-dose up to 48 weeks were included in this analysis.

The severity of anorexia at baseline and the last measurement up to 48 weeks was obtained (None, Mild, Moderate, Severe). If the value at the last was better in a participant, the participant was categorized into "Improved". If the value was same, categorised into "Unchanged". If the value was worsened, categorise into "Worsened".

Outcome measures

Outcome measures
Measure
Esomeprazole 20mg
n=168 Participants
Esomeprazole 20mg once daily oral
Placebo
n=172 Participants
Placebo once daily oral
Change in the Severity of Anorexia From Baseline to Last Measurement up to Week 48
Improved
9 Participants
10 Participants
Change in the Severity of Anorexia From Baseline to Last Measurement up to Week 48
Unchanged
156 Participants
153 Participants
Change in the Severity of Anorexia From Baseline to Last Measurement up to Week 48
Worsened
3 Participants
9 Participants

SECONDARY outcome

Timeframe: Up to 48 weeks (Baseline to last measurement)

Population: Participants who had the measurements of abdomen enlarged feeling at baseline and post-dose up to 48 weeks were included in this analysis.

The severity of abdomen enlarged feeling at baseline and the last measurement up to 48 weeks was obtained (None, Mild, Moderate, Severe). If the value at the last was better in a participant, the participant was categorized into "Improved". If the value was same, categorised into "Unchanged". If the value was worsened, categorise into "Worsened".

Outcome measures

Outcome measures
Measure
Esomeprazole 20mg
n=168 Participants
Esomeprazole 20mg once daily oral
Placebo
n=172 Participants
Placebo once daily oral
Change in the Severity of Abdomen Enlarged Feeling From Baseline to Last Measurement up to Week
Improved
18 Participants
24 Participants
Change in the Severity of Abdomen Enlarged Feeling From Baseline to Last Measurement up to Week
Unchanged
141 Participants
141 Participants
Change in the Severity of Abdomen Enlarged Feeling From Baseline to Last Measurement up to Week
Worsened
9 Participants
7 Participants

SECONDARY outcome

Timeframe: Up to 48 weeks (Baseline to last measurement)

Population: Participants who had the measurements of Nausea and/or Vomiting at baseline and post-dose up to 48 weeks were included in this analysis.

The severity of Nausea and/or Vomiting at baseline and the last measurement up to 48 weeks was obtained (None, Mild, Moderate, Severe). If the value at the last was better in a participant, the participant was categorized into "Improved". If the value was same, categorised into "Unchanged". If the value was worsened, categorise into "Worsened".

Outcome measures

Outcome measures
Measure
Esomeprazole 20mg
n=168 Participants
Esomeprazole 20mg once daily oral
Placebo
n=172 Participants
Placebo once daily oral
Change in the Severity of Nausea and/or Vomiting From Baseline to Last Measurement up to Week 48
Improved
8 Participants
5 Participants
Change in the Severity of Nausea and/or Vomiting From Baseline to Last Measurement up to Week 48
Unchanged
160 Participants
154 Participants
Change in the Severity of Nausea and/or Vomiting From Baseline to Last Measurement up to Week 48
Worsened
0 Participants
13 Participants

SECONDARY outcome

Timeframe: Up to 48 weeks (Baseline to last measurement)

The severity of Discomfort in the stomach at baseline and the last measurement up to 48 weeks was obtained (None, Mild, Moderate, Severe). If the value at the last was better in a participant, the participant was categorized into "Improved". If the value was same, categorised into "Unchanged". If the value was worsened, categorise into "Worsened".

Outcome measures

Outcome measures
Measure
Esomeprazole 20mg
n=168 Participants
Esomeprazole 20mg once daily oral
Placebo
n=172 Participants
Placebo once daily oral
Change in the Severity of Discomfort in the Stomach From Baseline to Last Measurement up to Week 48
Improved
13 Participants
15 Participants
Change in the Severity of Discomfort in the Stomach From Baseline to Last Measurement up to Week 48
Unchanged
150 Participants
148 Participants
Change in the Severity of Discomfort in the Stomach From Baseline to Last Measurement up to Week 48
Worsened
5 Participants
9 Participants

SECONDARY outcome

Timeframe: Up to 70 weeks at the longest

Population: All participants who received any study drug were included in this analysis.

Participants who had at least adverse events (AE) which occurred after receiving study drug were counted.

Outcome measures

Outcome measures
Measure
Esomeprazole 20mg
n=214 Participants
Esomeprazole 20mg once daily oral
Placebo
n=213 Participants
Placebo once daily oral
Number of Participants With Adverse Events
Adverse event
155 Participants
139 Participants
Number of Participants With Adverse Events
Adverse event (Frequency>=5%)
70 Participants
53 Participants
Number of Participants With Adverse Events
Death
0 Participants
0 Participants
Number of Participants With Adverse Events
Serious adverse event other than death
17 Participants
15 Participants
Number of Participants With Adverse Events
Adverse event leading to discontinuation of study
17 Participants
22 Participants
Number of Participants With Adverse Events
Drug-related adverse event
31 Participants
29 Participants
Number of Participants With Adverse Events
Severe adverse event
7 Participants
10 Participants

Adverse Events

Esomeprazole 20mg

Serious events: 17 serious events
Other events: 70 other events
Deaths: 0 deaths

Placebo

Serious events: 15 serious events
Other events: 53 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Esomeprazole 20mg
n=214 participants at risk
Esomeprazole 20mg once daily oral
Placebo
n=213 participants at risk
Placebo once daily oral
Metabolism and nutrition disorders
Dehydration
0.00%
0/214
0.47%
1/213
Surgical and medical procedures
Cholecystectomy
0.47%
1/214
0.00%
0/213
Respiratory, thoracic and mediastinal disorders
Sleep Apnoea Syndrome
0.47%
1/214
0.00%
0/213
Reproductive system and breast disorders
Epididymitis
0.47%
1/214
0.00%
0/213
Renal and urinary disorders
Renal Infarct
0.47%
1/214
0.00%
0/213
Musculoskeletal and connective tissue disorders
Intervertebral Disc Protrusion
0.47%
1/214
0.00%
0/213
Musculoskeletal and connective tissue disorders
Lumbar Spinal Stenosis
0.47%
1/214
0.00%
0/213
Investigations
Prostatic Specific Antigen Increased
0.47%
1/214
0.00%
0/213
Injury, poisoning and procedural complications
Hip Fracture
0.00%
0/214
0.47%
1/213
Injury, poisoning and procedural complications
In-Stent Coronary Artery Restenosis
0.47%
1/214
0.00%
0/213
Infections and infestations
Infective Exacerbation Of Chronic Obstructive Airways Disease
0.00%
0/214
0.47%
1/213
Infections and infestations
Pneumonia
0.00%
0/214
0.47%
1/213
Infections and infestations
Gastroenteritis
0.00%
0/214
0.47%
1/213
Infections and infestations
Urinary Tract Infection
0.47%
1/214
0.00%
0/213
Hepatobiliary disorders
Cholangitis Acute
0.47%
1/214
0.00%
0/213
Gastrointestinal disorders
Gastritis Erosive
0.00%
0/214
0.47%
1/213
Gastrointestinal disorders
Diverticulum Intestinal Haemorrhagic
0.00%
0/214
0.47%
1/213
Gastrointestinal disorders
Haemorrhoids
0.47%
1/214
0.00%
0/213
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Cardiac Myxoma
0.00%
0/214
0.47%
1/213
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Lung Neoplasm Malignant
0.00%
0/214
0.47%
1/213
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Malignant Ascites
0.47%
1/214
0.00%
0/213
Neoplasms benign, malignant and unspecified (incl cysts and polyps)
Gastric Cancer
0.47%
1/214
0.47%
1/213
Nervous system disorders
Epilepsy
0.00%
0/214
0.47%
1/213
Nervous system disorders
Cerebral Infarction
0.47%
1/214
0.00%
0/213
Nervous system disorders
Brain Stem Haemorrhage
0.93%
2/214
0.00%
0/213
Cardiac disorders
Ventricular Tachycardia
0.00%
0/214
0.47%
1/213
Cardiac disorders
Acute Myocardial Infarction
0.00%
0/214
0.94%
2/213
Cardiac disorders
Coronary Artery Stenosis
0.47%
1/214
0.00%
0/213
Cardiac disorders
Arteriosclerosis Coronary Artery
0.47%
1/214
0.00%
0/213
Cardiac disorders
Angina Pectoris
0.47%
1/214
0.47%
1/213

Other adverse events

Other adverse events
Measure
Esomeprazole 20mg
n=214 participants at risk
Esomeprazole 20mg once daily oral
Placebo
n=213 participants at risk
Placebo once daily oral
Gastrointestinal disorders
Duodenitis
1.9%
4/214
5.2%
11/213
Gastrointestinal disorders
Gastric Polyps
5.1%
11/214
0.47%
1/213
Gastrointestinal disorders
Constipation
5.6%
12/214
5.2%
11/213
Infections and infestations
Nasopharyngitis
20.1%
43/214
14.1%
30/213

Additional Information

Gerard Lynch

AstraZeneca

Results disclosure agreements

  • Principal investigator is a sponsor employee All PIs were prohibited to disclose all information related to this study without AZ approval before this study was completed.
  • Publication restrictions are in place

Restriction type: OTHER