A Study to Investigate the Efficacy and Safety of Lusutrombopag (S-888711) Tablets Administered to Adults With Immune Thrombocytopenia (ITP)

NCT ID: NCT01054443

Last Updated: 2021-03-18

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

20 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-03-18

Study Completion Date

2010-11-24

Brief Summary

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The primary objective of this study was to assess the efficacy of 3 dose levels of lusutrombopag (0.5 mg, 0.75 mg, and 1.0 mg) and placebo on platelet count.

Detailed Description

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Conditions

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Immune Thrombocytopenia (ITP)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Placebo

Participants received placebo tablets orally once a day for 42 days.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Tablet

Lusutrombopag 0.5 mg

Participants received 0.5 mg lusutrombopag orally once a day for 42 days.

Group Type EXPERIMENTAL

Lusutrombopag

Intervention Type DRUG

Tablet

Lusutrombopag 0.75 mg

Participants received 0.75 mg lusutrombopag orally once a day for 42 days.

Group Type EXPERIMENTAL

Lusutrombopag

Intervention Type DRUG

Tablet

Lusutrombopag 1.0 mg

Participants received 1.0 mg lusutrombopag orally once a day for 42 days.

Group Type EXPERIMENTAL

Lusutrombopag

Intervention Type DRUG

Tablet

Interventions

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Placebo

Tablet

Intervention Type DRUG

Lusutrombopag

Tablet

Intervention Type DRUG

Other Intervention Names

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MULPLETA® S-888711

Eligibility Criteria

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Inclusion Criteria

* A signed and dated written informed consent
* Males and females ≥ 18 years of age
* All subjects must agree to use barrier contraception
* Diagnosis of ITP
* Subjects \> 60 years must have had a diagnostic bone marrow aspiration
* Relapsed persistent or chronic ITP status, with or without prior splenectomy (exception: in Hungary only splenectomized subjects will be enrolled), after having failed at least 1 prior ITP therapy (excluding TPO agonists) and have a platelet count \< 30,000/μL if not taking medications or \< 50,000/μL despite concomitant steroids or other ITP therapies, such as danazol or immunosuppressive drugs
* Subjects receiving steroid therapy must be on a stable dose
* Prothrombin time (PT) and activated partial thromboplastin time (aPTT) within 20% of the upper limit of normal (ULN)
* Subjects receiving stable dosages of cyclosporine A, mycophenolate mofetil, azathioprine, or danazol are allowed. The dosages of all these medications must be stable for at least 4 weeks prior to Visit 1 (Day 1)

Exclusion Criteria

* History of clinically important hemorrhagic clotting disorder
* Females who are pregnant, lactating, or taking oral contraceptives
* History of alcohol/drug abuse or dependence within 1 year
* Use of the following drugs or treatment prior to Visit 1 (Day 1):

* Within 12 weeks - alemtuzumab, multi-drug systemic chemotherapy, stem cell therapy;
* Within 8 weeks - rituximab
* Within 2 weeks - platelet transfusions or plasmapheresis treatment
* Within 4 weeks - use of anti-platelet or anti-coagulant drugs
* Within 1 week - Rho(D) immune globulin or intravenous immunoglobulin
* History of clinically significant cardiovascular or thromboembolic disease within 26 weeks prior to Screening
* Splenectomy within 4 weeks prior to Screening
* Clinically significant laboratory abnormalities

* Hemoglobin \< 10.0 g/dL for men or women, not clearly related to ITP
* Absolute neutrophil count \< 1000/mm\^3
* Abnormal peripheral blood smear
* Total bilirubin \> 1.5 x upper limit of normal
* Alanine aminotransferase (ALT) \> 1.5 x upper limit of normal
* Aspartate aminotransferase (AST) \> 1.5 x upper limit of normal
* Creatinine \> 1.5 x upper limit of normal
* Human immunodeficiency virus (HIV) positive
* Hepatitis A immunoglobulin M antibody (IgM HAV) positive, hepatitis B surface antigen (HbsAg) or hepatitis C antibody (HCV) positive
* Thyroid stimulating hormone (TSH) \> 1.5 x upper limit of normal
* Free thyroxine (T4) \> 1.5 x upper limit of normal
* Exposure to previous thrombopoietin (TPO) mimetics/agonists (e.g., eltrombopag,romiplostim, E5501 \[AKR-501\] or LGD-4665) within 4 weeks prior to Screening
* Subjects unresponsive to previous TPO mimetics/agonists (e.g., eltrombopag, romiplostim, E5501 \[AKR-501\] or LGD-4665)
* Exposure to an investigative medication within the past 30 days
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Shionogi

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Shionogi Clinical Trials Administrator Clinical Support Help Line

Role: STUDY_DIRECTOR

Shionogi

Locations

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Investigator

Anaheim, California, United States

Site Status

Investigator

Los Angeles, California, United States

Site Status

Investigator

Washington D.C., District of Columbia, United States

Site Status

Investigator

Boynton Beach, Florida, United States

Site Status

Investigator

Jacksonville, Florida, United States

Site Status

Investigator

Atlanta, Georgia, United States

Site Status

Investigator

Riverdale, Georgia, United States

Site Status

Investigator

Metairie, Louisiana, United States

Site Status

Investigator

Bethesda, Maryland, United States

Site Status

Investigator

Boston, Massachusetts, United States

Site Status

Investigator

Jefferson City, Missouri, United States

Site Status

Investigator

Kansas City, Missouri, United States

Site Status

Investigator

New Brunswick, New Jersey, United States

Site Status

Investigator

New York, New York, United States

Site Status

Investigator

New York, New York, United States

Site Status

Investigator

Cleveland, Ohio, United States

Site Status

Investigator

San Antonio, Texas, United States

Site Status

Investigator

Salt Lake City, Utah, United States

Site Status

Investigator

Seattle, Washington, United States

Site Status

Countries

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United States

Other Identifiers

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0913M0621

Identifier Type: -

Identifier Source: org_study_id

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