Trial Outcomes & Findings for A Trial of OPC-41061 in Patients With Hepatic Edema - Investigation of the Safety of Treatment at 7.5 mg Beyond 7 Days and of the Effect of Dose Escalation to 15 mg (NCT NCT01048788)

NCT ID: NCT01048788

Last Updated: 2016-04-11

Results Overview

Changes in body weight from baseline at the end of administration

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

51 participants

Primary outcome timeframe

Baseline, Day 14 or end of administration

Results posted on

2016-04-11

Participant Flow

Participant milestones

Participant milestones
Measure
Discontinued/Terminated Before Day8
Subjects who disconrinued treatment before Day 7 or terminated by meeting the criteria on Day 7
Continued Administration at 7.5 mg/Day
Subjects who did not meet the criteria for dose escalation
Dose Escalation to 15 mg/Day
Subjects who met the criteria for dose escalation
Overall Study
STARTED
8
30
13
Overall Study
COMPLETED
3
28
11
Overall Study
NOT COMPLETED
5
2
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Discontinued/Terminated Before Day8
Subjects who disconrinued treatment before Day 7 or terminated by meeting the criteria on Day 7
Continued Administration at 7.5 mg/Day
Subjects who did not meet the criteria for dose escalation
Dose Escalation to 15 mg/Day
Subjects who met the criteria for dose escalation
Overall Study
Adverse Event
5
1
1
Overall Study
Lack of Efficacy
0
0
1
Overall Study
Withdrawal by Subject
0
1
0

Baseline Characteristics

A Trial of OPC-41061 in Patients With Hepatic Edema - Investigation of the Safety of Treatment at 7.5 mg Beyond 7 Days and of the Effect of Dose Escalation to 15 mg

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Discontinued/Terminated Before Day8
n=8 Participants
Subjects who disconrinued treatment before Day 7 or terminated by meeting the criteria on Day 7
Continued Administration at 7.5 mg/Day
n=30 Participants
Subjects who did not meet the criteria for dose escalation
Dose Escalation to 15 mg/Day
n=13 Participants
Subjects who met the criteria for dose escalation
Total
n=51 Participants
Total of all reporting groups
Age, Continuous
66.3 years
STANDARD_DEVIATION 6.8 • n=5 Participants
63.9 years
STANDARD_DEVIATION 8.2 • n=7 Participants
61.0 years
STANDARD_DEVIATION 11.4 • n=5 Participants
63.5 years
STANDARD_DEVIATION 8.9 • n=4 Participants
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=4 Participants
Age, Categorical
Between 18 and 65 years
4 Participants
n=5 Participants
14 Participants
n=7 Participants
8 Participants
n=5 Participants
26 Participants
n=4 Participants
Age, Categorical
>=65 years
4 Participants
n=5 Participants
16 Participants
n=7 Participants
5 Participants
n=5 Participants
25 Participants
n=4 Participants
Sex: Female, Male
Female
2 Participants
n=5 Participants
9 Participants
n=7 Participants
4 Participants
n=5 Participants
15 Participants
n=4 Participants
Sex: Female, Male
Male
6 Participants
n=5 Participants
21 Participants
n=7 Participants
9 Participants
n=5 Participants
36 Participants
n=4 Participants
Region of Enrollment
Japan
8 participants
n=5 Participants
30 participants
n=7 Participants
13 participants
n=5 Participants
51 participants
n=4 Participants

PRIMARY outcome

Timeframe: Baseline, Day 14 or end of administration

Changes in body weight from baseline at the end of administration

Outcome measures

Outcome measures
Measure
Discontitued/Terminated Before Day 8
n=8 Participants
Subjects who discontinued treatment before Day 7 or teiminated by meeting the criteria on Day 7
Continued Administration at 7.5 mg/Day
n=30 Participants
Subjects who did not meet the criteria for dose escalation
Dose Escalation to 15 mg/Day
n=13 Participants
Subjects who met the criteria for dose escalation
Body Weight
-0.76 Kg
Standard Deviation 0.93
-2.97 Kg
Standard Deviation 2.57
-0.05 Kg
Standard Deviation 2.30

Adverse Events

Discontinued/Terminated Before Day8

Serious events: 3 serious events
Other events: 7 other events
Deaths: 0 deaths

Continued Administration at 7.5 mg/Day

Serious events: 3 serious events
Other events: 22 other events
Deaths: 0 deaths

Dose Escalation to 15 mg/Day

Serious events: 2 serious events
Other events: 7 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Discontinued/Terminated Before Day8
n=8 participants at risk
Subjects who disconrinued treatment before Day 7 or terminated by meeting the criteria on Day 7
Continued Administration at 7.5 mg/Day
n=30 participants at risk
Subjects who did not meet the criteria for dose escalation
Dose Escalation to 15 mg/Day
n=13 participants at risk
Subjects who met the criteria for dose escalation
Ear and labyrinth disorders
Positional Vertigo
12.5%
1/8 • Number of events 1 • 14 days
0.00%
0/30 • 14 days
0.00%
0/13 • 14 days
Gastrointestinal disorders
Ascites
0.00%
0/8 • 14 days
3.3%
1/30 • Number of events 1 • 14 days
0.00%
0/13 • 14 days
Gastrointestinal disorders
Oesophageal Varices Haemorrhage
0.00%
0/8 • 14 days
3.3%
1/30 • Number of events 1 • 14 days
0.00%
0/13 • 14 days
General disorders
Hernia Obstructive
12.5%
1/8 • Number of events 1 • 14 days
0.00%
0/30 • 14 days
0.00%
0/13 • 14 days
General disorders
Pyrexia
0.00%
0/8 • 14 days
3.3%
1/30 • Number of events 1 • 14 days
0.00%
0/13 • 14 days
Infections and infestations
Peritonitis Bacterial
0.00%
0/8 • 14 days
0.00%
0/30 • 14 days
7.7%
1/13 • Number of events 1 • 14 days
Infections and infestations
Septicaemia
0.00%
0/8 • 14 days
0.00%
0/30 • 14 days
7.7%
1/13 • Number of events 1 • 14 days
Musculoskeletal and connective tissue disorders
Muscular Weakness
12.5%
1/8 • Number of events 1 • 14 days
0.00%
0/30 • 14 days
0.00%
0/13 • 14 days
Nervous system disorders
Diabetic Neuropathy
12.5%
1/8 • Number of events 1 • 14 days
0.00%
0/30 • 14 days
0.00%
0/13 • 14 days
Nervous system disorders
Hepatic Encephalopathy
12.5%
1/8 • Number of events 1 • 14 days
3.3%
1/30 • Number of events 1 • 14 days
7.7%
1/13 • Number of events 1 • 14 days
Nervous system disorders
Polyneuropathy Alcoholic
12.5%
1/8 • Number of events 1 • 14 days
0.00%
0/30 • 14 days
0.00%
0/13 • 14 days

Other adverse events

Other adverse events
Measure
Discontinued/Terminated Before Day8
n=8 participants at risk
Subjects who disconrinued treatment before Day 7 or terminated by meeting the criteria on Day 7
Continued Administration at 7.5 mg/Day
n=30 participants at risk
Subjects who did not meet the criteria for dose escalation
Dose Escalation to 15 mg/Day
n=13 participants at risk
Subjects who met the criteria for dose escalation
Gastrointestinal disorders
Abdominal Distension
12.5%
1/8 • Number of events 1 • 14 days
3.3%
1/30 • Number of events 1 • 14 days
7.7%
1/13 • Number of events 1 • 14 days
Gastrointestinal disorders
Constipation
12.5%
1/8 • Number of events 1 • 14 days
13.3%
4/30 • Number of events 4 • 14 days
0.00%
0/13 • 14 days
General disorders
Malaise
0.00%
0/8 • 14 days
0.00%
0/30 • 14 days
15.4%
2/13 • Number of events 2 • 14 days
General disorders
Pyrexia
12.5%
1/8 • Number of events 1 • 14 days
10.0%
3/30 • Number of events 3 • 14 days
15.4%
2/13 • Number of events 2 • 14 days
General disorders
Thirst
12.5%
1/8 • Number of events 1 • 14 days
33.3%
10/30 • Number of events 10 • 14 days
7.7%
1/13 • Number of events 1 • 14 days
Injury, poisoning and procedural complications
Procedural Pain
12.5%
1/8 • Number of events 1 • 14 days
0.00%
0/30 • 14 days
0.00%
0/13 • 14 days
Investigations
Blood Creatinine Increased
0.00%
0/8 • 14 days
13.3%
4/30 • Number of events 5 • 14 days
0.00%
0/13 • 14 days
Investigations
Blood Pressure Decreased
12.5%
1/8 • Number of events 1 • 14 days
10.0%
3/30 • Number of events 4 • 14 days
7.7%
1/13 • Number of events 1 • 14 days
Investigations
Blood Urea Increased
12.5%
1/8 • Number of events 1 • 14 days
10.0%
3/30 • Number of events 3 • 14 days
0.00%
0/13 • 14 days
Metabolism and nutrition disorders
Dehydration
12.5%
1/8 • Number of events 1 • 14 days
0.00%
0/30 • 14 days
0.00%
0/13 • 14 days
Nervous system disorders
Dizziness
0.00%
0/8 • 14 days
10.0%
3/30 • Number of events 4 • 14 days
7.7%
1/13 • Number of events 1 • 14 days
Nervous system disorders
Headache
0.00%
0/8 • 14 days
0.00%
0/30 • 14 days
15.4%
2/13 • Number of events 3 • 14 days
Psychiatric disorders
Delirium
12.5%
1/8 • Number of events 1 • 14 days
0.00%
0/30 • 14 days
7.7%
1/13 • Number of events 1 • 14 days
Psychiatric disorders
Insomnia
0.00%
0/8 • 14 days
13.3%
4/30 • Number of events 4 • 14 days
15.4%
2/13 • Number of events 2 • 14 days
Renal and urinary disorders
Bladder Dysfunction
12.5%
1/8 • Number of events 1 • 14 days
0.00%
0/30 • 14 days
0.00%
0/13 • 14 days
Renal and urinary disorders
Renal Impairment
12.5%
1/8 • Number of events 1 • 14 days
6.7%
2/30 • Number of events 2 • 14 days
0.00%
0/13 • 14 days
Skin and subcutaneous tissue disorders
Rash
12.5%
1/8 • Number of events 1 • 14 days
0.00%
0/30 • 14 days
0.00%
0/13 • 14 days
Gastrointestinal disorders
Abdominal Pain Upper
0.00%
0/8 • 14 days
0.00%
0/30 • 14 days
7.7%
1/13 • Number of events 1 • 14 days

Additional Information

Director of Clinical Research and Development

Otsuka Pharmaceutical Co., Ltd.

Phone: +81-3-6361-7366

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place