Trial Outcomes & Findings for Ketoconazole and Dexamethasone in Prostate Cancer (NCT NCT01036594)

NCT ID: NCT01036594

Last Updated: 2020-06-29

Results Overview

The number of participants who experience a ≥30% decline in PSA between the time of first progression on ketoconazole and hydrocortisone and eight weeks after dexamethasone therapy was initiated.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

32 participants

Primary outcome timeframe

Up to 5 years

Results posted on

2020-06-29

Participant Flow

Participants were recruited through the Urologic Oncology Program at University of California, San Francisco

All participants were prescribed ketoconazole for a 7 day run-in phase, then hydrocortisone + ketoconazole treatment. Participants not achieving \>=30% PSA decline at 12 weeks were taken off study. Participants continued treatment until progression at which time, hydrocortisone was discontinued and ketoconazole + dexamethasone treatment began.

Participant milestones

Participant milestones
Measure
Ketoconazole + Hydrocortisone
po = oral, tid = 3 times per day, qam = every morning, qom = every evening, bid = twice daily, 1 cycle = 28 days * Ketoconazole: 200mg during run-in phase, then 400mg po tid * Hydrocortisone 20mg po qam and 10mg po qpm: If participant has ≥ 30% PSA decline at 12 week evaluation, treatment continues until progressive disease (by RECIST criteria OR by Prostate Specific Antigen Working Group (PSAWG) criteria) is documented. After that, drug will be discontinued. If participant has \< 30% PSA decline at 12 week evaluation, participant goes off study.
Ketoconazole + Dexamethasone
Ketoconazole: 400mg po tid Dexamethasone 0.5mg po bid: If ≥ 30% PSA decline (Prostate-specific antigen) at 12 week evaluation, administration starts when disease progression on Ketoconazole + Hydrocortisone (by RECIST criteria OR by PSAWG criteria) is documented.
Run-In: Ketoconazole Only (200 mg)
STARTED
32
0
Run-In: Ketoconazole Only (200 mg)
COMPLETED
31
0
Run-In: Ketoconazole Only (200 mg)
NOT COMPLETED
1
0
First Treatment Regimen
STARTED
31
0
First Treatment Regimen
COMPLETED
30
0
First Treatment Regimen
NOT COMPLETED
1
0
Week 12 Evaluation
STARTED
30
0
Week 12 Evaluation
COMPLETED
24
0
Week 12 Evaluation
NOT COMPLETED
6
0
Treatment Regiments Post Week 12
STARTED
15
9
Treatment Regiments Post Week 12
COMPLETED
13
5
Treatment Regiments Post Week 12
NOT COMPLETED
2
4

Reasons for withdrawal

Reasons for withdrawal
Measure
Ketoconazole + Hydrocortisone
po = oral, tid = 3 times per day, qam = every morning, qom = every evening, bid = twice daily, 1 cycle = 28 days * Ketoconazole: 200mg during run-in phase, then 400mg po tid * Hydrocortisone 20mg po qam and 10mg po qpm: If participant has ≥ 30% PSA decline at 12 week evaluation, treatment continues until progressive disease (by RECIST criteria OR by Prostate Specific Antigen Working Group (PSAWG) criteria) is documented. After that, drug will be discontinued. If participant has \< 30% PSA decline at 12 week evaluation, participant goes off study.
Ketoconazole + Dexamethasone
Ketoconazole: 400mg po tid Dexamethasone 0.5mg po bid: If ≥ 30% PSA decline (Prostate-specific antigen) at 12 week evaluation, administration starts when disease progression on Ketoconazole + Hydrocortisone (by RECIST criteria OR by PSAWG criteria) is documented.
Run-In: Ketoconazole Only (200 mg)
Adverse Event
1
0
First Treatment Regimen
Withdrawal by Subject
1
0
Week 12 Evaluation
Adverse Event
5
0
Week 12 Evaluation
Physician Decision
1
0
Treatment Regiments Post Week 12
Physician Decision
1
1
Treatment Regiments Post Week 12
Withdrawal by Subject
1
0
Treatment Regiments Post Week 12
Adverse Event
0
1
Treatment Regiments Post Week 12
Non-Cancer Disease Complications
0
1
Treatment Regiments Post Week 12
Lack of Efficacy
0
1

Baseline Characteristics

This measure presents data for the 9 participants that were subsequently randomized to the second treatment arm

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
All Patients Who Received Treatment
n=32 Participants
po = oral, tid = 3 times per day, qam = every morning, qom = every evening, bid = twice daily, 1 cycle = 28 days * Ketoconazole: 200mg during first week of study (run-in phase), then 400mg po tid * Hydrocortisone 20mg po qam and 10mg po qpm: If patient has ≥ 30% PSA decline at 12 week evaluation, treatment continues until progressive disease (by RECIST criteria OR by PSAWG criteria) is documented. After that, drug will be discontinued. If participant has \< 30% PSA decline at 12 week evaluation, participant goes off study. Based on the results of evaluation at 12 weeks , participants were offered to either stay on this regimen or receive -Ketoconazole: 400mg po tid Dexamethasone 0.5mg po bid: If ≥ 30% PSA decline (Prostate-specific antigen) at 12 week evaluation, administration starts when disease progression on Ketoconazole + Hydrocortisone (by RECIST criteria OR by PSAWG criteria) is documented.
Age, Customized
50-59 years old
7 Participants
n=32 Participants
Age, Customized
60-69 years old
11 Participants
n=32 Participants
Age, Customized
70-79 years old
10 Participants
n=32 Participants
Age, Customized
80-89 years old
4 Participants
n=32 Participants
Age, Customized
50-59 years
1 Participants
n=9 Participants • This measure presents data for the 9 participants that were subsequently randomized to the second treatment arm
Age, Customized
60-69 years
6 Participants
n=9 Participants • This measure presents data for the 9 participants that were subsequently randomized to the second treatment arm
Age, Customized
70-79 years
2 Participants
n=9 Participants • This measure presents data for the 9 participants that were subsequently randomized to the second treatment arm
Sex: Female, Male
Female
0 Participants
n=32 Participants
Sex: Female, Male
Male
32 Participants
n=32 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
2 Participants
n=9 Participants • This measure presents data for the participants that were subsequently randomized to the second treatment arm
Ethnicity (NIH/OMB)
Not Hispanic or Latino
6 Participants
n=9 Participants • This measure presents data for the participants that were subsequently randomized to the second treatment arm
Ethnicity (NIH/OMB)
Unknown or Not Reported
1 Participants
n=9 Participants • This measure presents data for the participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=9 Participants • This measure presents data for the participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
Asian
3 Participants
n=9 Participants • This measure presents data for the participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=9 Participants • This measure presents data for the participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
Black or African American
1 Participants
n=9 Participants • This measure presents data for the participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
White
5 Participants
n=9 Participants • This measure presents data for the participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
More than one race
0 Participants
n=9 Participants • This measure presents data for the participants that were subsequently randomized to the second treatment arm
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=9 Participants • This measure presents data for the participants that were subsequently randomized to the second treatment arm
Region of Enrollment
United States
32 participants
n=32 Participants

PRIMARY outcome

Timeframe: Up to 5 years

Population: Progression data for patients not enrolled to Dexamethasone arm are not used in this analysis.

The number of participants who experience a ≥30% decline in PSA between the time of first progression on ketoconazole and hydrocortisone and eight weeks after dexamethasone therapy was initiated.

Outcome measures

Outcome measures
Measure
Ketoconazole + Hydrocortisone
po = oral, tid = 3 times per day, qam = every morning, qom = every evening, bid = twice daily, 1 cycle = 28 days * Ketoconazole: 200mg during first week of study (run-in phase), then 400mg po tid * Hydrocortisone 20mg po qam and 10mg po qpm: If patient has ≥ 30% PSA decline at 12 week evaluation, treatment continues until progressive disease (by RECIST criteria OR by PSAWG criteria) is documented. After that, drug will be discontinued. If patient has \< 30% PSA decline at 12 week evaluation, patient goes off study.
Ketoconazole + Dexamethasone
n=8 Participants
Ketoconazole: 400mg po tid Dexamethasone 0.5mg po bid: If ≥ 30% PSA decline (Prostate-specific antigen) at 12 week evaluation, administration starts when disease progression on Ketoconazole + Hydrocortisone (by RECIST criteria OR by PSAWG criteria) is documented.
Number of Participants Who Achieved a Second Decline in Prostate Specific Antigen (PSA) Following Progression on First Regimen
0 Participants

SECONDARY outcome

Timeframe: Up to 5 years

Population: ACTH data not collected for this endpoint. Planned statistical analysis could not be performed.

Nonparametric Wilcoxon test for matched pairs will be used to test the difference in ACTH levels from baseline until the time of disease progression for participants taking ketoconazole/hydrocortisone for participants with evaluable laboratory values.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 2 years

Population: Data on duration of castration prior to treatment data not collected. Planned analysis could not be performed.

The Spearman rank correlation will be calculated to explore the relationship between the baseline ACTH level and the duration of castration prior to the start of any ketoconazole therapy

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 5 years

Population: Testosterone data for this endpoint not collected. Planned statistical analysis could not be performed.

For PSA responders to ketoconazole/ hydrocortisone continuing with dexamethasone treatment after initial disease progression, the overall pattern of testosterone levels will be investigated with nonparametric methods for statistical analyses. This will include Friedman's analysis of variance method using ranks for repeated measures. A key comparison using the Wilcoxon test for matched pairs will investigate the change in testosterone from progression #1 to progression #2.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 5 years

Population: Estrodiol data for this endpoint not collected. Planned statistical analysis could not be performed.

For PSA responders to ketoconazole/ hydrocortisone continuing with dexamethasone treatment after initial disease progression, the overall pattern of estrodiol levels will be investigated with nonparametric methods for statistical analyses. This will include Friedman's analysis of variance method using ranks for repeated measures. A key comparison using the Wilcoxon test for matched pairs will investigate the change in estrodiol from progression #1 to progression #2.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 5 years

Population: AA data not collected for this endpoint. Planned statistical analyses could not be performed.

For PSA responders to ketoconazole/ hydrocortisone continuing with dexamethasone treatment after initial disease progression, the overall pattern of AA levels will be investigated with nonparametric methods for statistical analyses. This will include Friedman's analysis of variance method using ranks for repeated measures. A key comparison using the Wilcoxon test for matched pairs will investigate the change in AA levels from progression #1 to progression #2.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 5 years

Population: Cortisol data not collected for this endpoint. Planned statistical analysis could not be performed

For PSA responders to ketoconazole/ hydrocortisone continuing with dexamethasone treatment after initial disease progression, the overall pattern of cortisol levels will be investigated with nonparametric methods for statistical analyses. This will include Friedman's analysis of variance method using ranks for repeated measures. A key comparison using the Wilcoxon test for matched pairs will investigate the change in cortisol levels from progression #1 to progression #2.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 5 years

Population: DHEA data was not collected for this endpoint. Planned statistical analysis could not be performed.

For PSA responders to ketoconazole/ hydrocortisone continuing with dexamethasone treatment after initial disease progression, the overall pattern of DHEA levels will be investigated with nonparametric methods for statistical analyses. This will include Friedman's analysis of variance method using ranks for repeated measures. A key comparison using the Wilcoxon test for matched pairs will investigate the change in DHEA levels from progression #1 to progression #2.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 5 years

Population: DHEA-S data was not collected for this endpoint. Planned statistical analysis could not be performed.

For PSA responders to ketoconazole/ hydrocortisone continuing with dexamethasone treatment after initial disease progression, the overall pattern of DHEA-S levels will be investigated with nonparametric methods for statistical analyses. This will include Friedman's analysis of variance method using ranks for repeated measures. A key comparison using the Wilcoxon test for matched pairs will investigate the change in DHEA-S levels from progression #1 to progression #2.

Outcome measures

Outcome data not reported

Adverse Events

Ketoconazole + Hydrocortisone

Serious events: 4 serious events
Other events: 25 other events
Deaths: 0 deaths

Ketoconazole + Dexamethasone

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Ketoconazole + Hydrocortisone
n=32 participants at risk
po = oral, tid = 3 times per day, qam = every morning, qom = every evening, bid = twice daily, 1 cycle = 28 days * Ketoconazole: 200mg during first week of study (run-in phase), then 400mg po tid * Hydrocortisone 20mg po qam and 10mg po qpm: If patient has ≥ 30% PSA decline at 12 week evaluation, treatment continues until progressive disease (by RECIST criteria OR by PSAWG criteria) is documented. After that, drug will be discontinued. If patient has \< 30% PSA decline at 12 week evaluation, patient goes off study.
Ketoconazole + Dexamethasone
n=9 participants at risk
Ketoconazole: 400mg po tid Dexamethasone 0.5mg po bid: If ≥ 30% PSA decline (Prostate-specific antigen) at 12 week evaluation, administration starts when disease progression on Ketoconazole + Hydrocortisone (by RECIST criteria OR by PSAWG criteria) is documented.
Gastrointestinal disorders
Dehydration
3.1%
1/32 • Number of events 1 • Up to 5 years
0.00%
0/9 • Up to 5 years
Vascular disorders
Peripheral arterial ischemia
3.1%
1/32 • Number of events 2 • Up to 5 years
0.00%
0/9 • Up to 5 years
Renal and urinary disorders
Renal failure
3.1%
1/32 • Number of events 2 • Up to 5 years
0.00%
0/9 • Up to 5 years
Renal and urinary disorders
Obstruction, GU - Ureter
3.1%
1/32 • Number of events 1 • Up to 5 years
0.00%
0/9 • Up to 5 years
Musculoskeletal and connective tissue disorders
Fracture
3.1%
1/32 • Number of events 1 • Up to 5 years
0.00%
0/9 • Up to 5 years
Infections and infestations
Infection with unknown ANC - Bladder (urinary)
3.1%
1/32 • Number of events 1 • Up to 5 years
0.00%
0/9 • Up to 5 years
Infections and infestations
Infection with normal ANC or Grade 1 or 2 neutrophils - Upper airway NOS
3.1%
1/32 • Number of events 1 • Up to 5 years
0.00%
0/9 • Up to 5 years
Infections and infestations
Infection with normal ANC or Grade 1 or 2 neutrophils - Bladder (urinary)
3.1%
1/32 • Number of events 1 • Up to 5 years
0.00%
0/9 • Up to 5 years
Infections and infestations
Infection - Other
3.1%
1/32 • Number of events 1 • Up to 5 years
0.00%
0/9 • Up to 5 years
Respiratory, thoracic and mediastinal disorders
Dyspnea
3.1%
1/32 • Number of events 1 • Up to 5 years
0.00%
0/9 • Up to 5 years

Other adverse events

Other adverse events
Measure
Ketoconazole + Hydrocortisone
n=32 participants at risk
po = oral, tid = 3 times per day, qam = every morning, qom = every evening, bid = twice daily, 1 cycle = 28 days * Ketoconazole: 200mg during first week of study (run-in phase), then 400mg po tid * Hydrocortisone 20mg po qam and 10mg po qpm: If patient has ≥ 30% PSA decline at 12 week evaluation, treatment continues until progressive disease (by RECIST criteria OR by PSAWG criteria) is documented. After that, drug will be discontinued. If patient has \< 30% PSA decline at 12 week evaluation, patient goes off study.
Ketoconazole + Dexamethasone
n=9 participants at risk
Ketoconazole: 400mg po tid Dexamethasone 0.5mg po bid: If ≥ 30% PSA decline (Prostate-specific antigen) at 12 week evaluation, administration starts when disease progression on Ketoconazole + Hydrocortisone (by RECIST criteria OR by PSAWG criteria) is documented.
Skin and subcutaneous tissue disorders
Dermatology - Other
25.0%
8/32 • Number of events 17 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Skin and subcutaneous tissue disorders
Dry skin
25.0%
8/32 • Number of events 13 • Up to 5 years
0.00%
0/9 • Up to 5 years
Skin and subcutaneous tissue disorders
Rash/desquamation
9.4%
3/32 • Number of events 4 • Up to 5 years
0.00%
0/9 • Up to 5 years
Skin and subcutaneous tissue disorders
Rash: hand-foot skin reaction
9.4%
3/32 • Number of events 3 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Skin and subcutaneous tissue disorders
Rash: dermatitis associated with radiation - Radiation
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Gastrointestinal disorders
Nausea
18.8%
6/32 • Number of events 9 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Gastrointestinal disorders
Constipation
9.4%
3/32 • Number of events 3 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Gastrointestinal disorders
Anorexia
6.2%
2/32 • Number of events 2 • Up to 5 years
0.00%
0/9 • Up to 5 years
Gastrointestinal disorders
Diarrhea
9.4%
3/32 • Number of events 3 • Up to 5 years
0.00%
0/9 • Up to 5 years
Gastrointestinal disorders
Dry mouth/salivary gland (xerostomia)
9.4%
3/32 • Number of events 3 • Up to 5 years
0.00%
0/9 • Up to 5 years
Gastrointestinal disorders
Vomiting
9.4%
3/32 • Number of events 3 • Up to 5 years
0.00%
0/9 • Up to 5 years
Gastrointestinal disorders
Taste alteration (dysgeusia)
3.1%
1/32 • Number of events 1 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Gastrointestinal disorders
Hemorrhoids
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Gastrointestinal disorders
Mucositis/stomatitis (clinical exam) - Oral cavity
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
General disorders
Fatigue (asthenia, lethargy, malaise)
37.5%
12/32 • Number of events 23 • Up to 5 years
22.2%
2/9 • Number of events 2 • Up to 5 years
General disorders
Insomnia
6.2%
2/32 • Number of events 3 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
General disorders
Weight gain
3.1%
1/32 • Number of events 1 • Up to 5 years
11.1%
1/9 • Number of events 2 • Up to 5 years
General disorders
Weight loss
3.1%
1/32 • Number of events 1 • Up to 5 years
11.1%
1/9 • Number of events 2 • Up to 5 years
General disorders
Edema: limb
21.9%
7/32 • Number of events 14 • Up to 5 years
22.2%
2/9 • Number of events 2 • Up to 5 years
Investigations
ALT, SGPT (serum glutamic pyruvic transaminase) increased
15.6%
5/32 • Number of events 15 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Investigations
AST, SGOT(serum glutamic oxaloacetic transaminase) increased
18.8%
6/32 • Number of events 9 • Up to 5 years
0.00%
0/9 • Up to 5 years
Metabolism and nutrition disorders
Hyperglycemia
6.2%
2/32 • Number of events 2 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Investigations
Creatinine increased
6.2%
2/32 • Number of events 3 • Up to 5 years
0.00%
0/9 • Up to 5 years
Gastrointestinal disorders
Abdomen Pain, NOS
12.5%
4/32 • Number of events 8 • Up to 5 years
0.00%
0/9 • Up to 5 years
Musculoskeletal and connective tissue disorders
Pain - Back
9.4%
3/32 • Number of events 4 • Up to 5 years
0.00%
0/9 • Up to 5 years
Musculoskeletal and connective tissue disorders
Pain - Extremity-limb
9.4%
3/32 • Number of events 4 • Up to 5 years
0.00%
0/9 • Up to 5 years
Musculoskeletal and connective tissue disorders
Pain - Joint
6.2%
2/32 • Number of events 2 • Up to 5 years
11.1%
1/9 • Number of events 2 • Up to 5 years
General disorders
Pain - Other
9.4%
3/32 • Number of events 3 • Up to 5 years
0.00%
0/9 • Up to 5 years
General disorders
Pain - Chest/thorax NOS
6.2%
2/32 • Number of events 3 • Up to 5 years
0.00%
0/9 • Up to 5 years
Respiratory, thoracic and mediastinal disorders
Dyspnea (shortness of breath)
12.5%
4/32 • Number of events 8 • Up to 5 years
0.00%
0/9 • Up to 5 years
Respiratory, thoracic and mediastinal disorders
Bronchospasm, wheezing
3.1%
1/32 • Number of events 1 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Respiratory, thoracic and mediastinal disorders
Cough
3.1%
1/32 • Number of events 2 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Respiratory, thoracic and mediastinal disorders
Pneumonitis/pulmonary infiltrates
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Renal and urinary disorders
Urinary frequency/urgency
15.6%
5/32 • Number of events 6 • Up to 5 years
0.00%
0/9 • Up to 5 years
Renal and urinary disorders
Renal/Genitourinary
6.2%
2/32 • Number of events 3 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Renal and urinary disorders
Perforation, GU - Kidney
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Infections and infestations
Infection with normal ANC or Grade 1 or 2 neutrophils - Skin (cellulitis)
3.1%
1/32 • Number of events 1 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Infections and infestations
Infection with normal ANC or Grade 1 or 2 neutrophils - Lung (pneumonia)
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Infections and infestations
Infection with unknown ANC - Joint
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Psychiatric disorders
Mood alteration - Depression
6.2%
2/32 • Number of events 2 • Up to 5 years
22.2%
2/9 • Number of events 2 • Up to 5 years
Nervous system disorders
Cognitive disturbance
6.2%
2/32 • Number of events 2 • Up to 5 years
0.00%
0/9 • Up to 5 years
Nervous system disorders
Syncope (fainting)
6.2%
2/32 • Number of events 2 • Up to 5 years
0.00%
0/9 • Up to 5 years
Vascular disorders
Hypertension
15.6%
5/32 • Number of events 11 • Up to 5 years
0.00%
0/9 • Up to 5 years
Musculoskeletal and connective tissue disorders
Fracture
6.2%
2/32 • Number of events 2 • Up to 5 years
11.1%
1/9 • Number of events 2 • Up to 5 years
Musculoskeletal and connective tissue disorders
Joint-effusion
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Musculoskeletal and connective tissue disorders
Muscle weakness, generalized or specific area (not due to neuropathy) - Whole body/generalized
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Musculoskeletal and connective tissue disorders
Osteoporosis
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Cardiac disorders
Cardiac Arrhythmia - Other
6.2%
2/32 • Number of events 3 • Up to 5 years
0.00%
0/9 • Up to 5 years
Cardiac disorders
Supraventricular and nodal arrhythmia - Sinus bradycardia
6.2%
2/32 • Number of events 3 • Up to 5 years
0.00%
0/9 • Up to 5 years
Endocrine disorders
Cushingoid appearance (e.g., moon face, buffalo hump, centripetal obesity, cutaneous striae)
6.2%
2/32 • Number of events 2 • Up to 5 years
22.2%
2/9 • Number of events 2 • Up to 5 years
Vascular disorders
Peripheral arterial ischemia
6.2%
2/32 • Number of events 2 • Up to 5 years
0.00%
0/9 • Up to 5 years
Blood and lymphatic system disorders
Thrombotic thrombocytopenic purpura [TTP] or hemolytic uremic syndrome [HUS]
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years
Hepatobiliary disorders
Hepatobiliary/Pancreas - Other
0.00%
0/32 • Up to 5 years
11.1%
1/9 • Number of events 1 • Up to 5 years

Additional Information

Dr. Terence Friedlander, MD

University of California, San Francisco

Phone: (415) 514-6380

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place