Trial Outcomes & Findings for Temsirolimus to Reverse Androgen Insensitivity for Castration-resistant Prostate Cancer (NCT NCT01020305)

NCT ID: NCT01020305

Last Updated: 2014-10-13

Results Overview

Proportion of subjects with \> 50% drop in serum PSA as compared to baseline, assessed at 16 weeks

Recruitment status

TERMINATED

Study phase

PHASE1/PHASE2

Target enrollment

5 participants

Primary outcome timeframe

12 weeks treatment, with primary outcome assessed at 16 weeks

Results posted on

2014-10-13

Participant Flow

Participant milestones

Participant milestones
Measure
Temsirolimus + Bicalutamide
Temsirolimus 25 mg administered intravenously (IV) once weekly for 12 weeks Casodex (bicalutamide) administered 50 mg/day orally (PO) Temsirolimus: Temsirolimus is an inhibitor of the mammalian target of rapamycin (MTOR, aka HGNC:3942) IUPAC name: (1R,2R,4S)-4-{(2R)-2-\[(3S,6R,7E,9R,10R,12R,14S,15E,17E,19E,21S,23S,26R,27R,34aS)-9,27-dihydroxy-10,21-dimethoxy-6,8,12,14,20,26-hexamethyl-1,5,11,28,29-pentaoxo-1,4,5,6,9,10,11,12,13,14,21,22,23,24,25,26,27,28,29,31,32,33,34,34a-tetracosahydro-3H-23,27-epoxypyrido\[2,1-c\]\[1,4\]oxazacyclohentriacontin-3-yl\]propyl}-2-methoxycyclohexyl 3-hydroxy-2-(hydroxymethyl)-2-methylpropanoate Casodex (bicalutamide): Casodex (bicalutamide) 50 mg/day PO
Overall Study
STARTED
5
Overall Study
COMPLETED
3
Overall Study
NOT COMPLETED
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Temsirolimus + Bicalutamide
Temsirolimus 25 mg administered intravenously (IV) once weekly for 12 weeks Casodex (bicalutamide) administered 50 mg/day orally (PO) Temsirolimus: Temsirolimus is an inhibitor of the mammalian target of rapamycin (MTOR, aka HGNC:3942) IUPAC name: (1R,2R,4S)-4-{(2R)-2-\[(3S,6R,7E,9R,10R,12R,14S,15E,17E,19E,21S,23S,26R,27R,34aS)-9,27-dihydroxy-10,21-dimethoxy-6,8,12,14,20,26-hexamethyl-1,5,11,28,29-pentaoxo-1,4,5,6,9,10,11,12,13,14,21,22,23,24,25,26,27,28,29,31,32,33,34,34a-tetracosahydro-3H-23,27-epoxypyrido\[2,1-c\]\[1,4\]oxazacyclohentriacontin-3-yl\]propyl}-2-methoxycyclohexyl 3-hydroxy-2-(hydroxymethyl)-2-methylpropanoate Casodex (bicalutamide): Casodex (bicalutamide) 50 mg/day PO
Overall Study
Adverse Event
2

Baseline Characteristics

Temsirolimus to Reverse Androgen Insensitivity for Castration-resistant Prostate Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Temsirolimus + Bicalutamide
n=5 Participants
Temsirolimus 25 mg administered intravenously (IV) once weekly for 12 weeks Casodex (bicalutamide) administered 50 mg/day orally (PO) Temsirolimus: Temsirolimus is an inhibitor of the mammalian target of rapamycin (MTOR, aka HGNC:3942) IUPAC name: (1R,2R,4S)-4-{(2R)-2-\[(3S,6R,7E,9R,10R,12R,14S,15E,17E,19E,21S,23S,26R,27R,34aS)-9,27-dihydroxy-10,21-dimethoxy-6,8,12,14,20,26-hexamethyl-1,5,11,28,29-pentaoxo-1,4,5,6,9,10,11,12,13,14,21,22,23,24,25,26,27,28,29,31,32,33,34,34a-tetracosahydro-3H-23,27-epoxypyrido\[2,1-c\]\[1,4\]oxazacyclohentriacontin-3-yl\]propyl}-2-methoxycyclohexyl 3-hydroxy-2-(hydroxymethyl)-2-methylpropanoate Casodex (bicalutamide): Casodex (bicalutamide) 50 mg/day PO
Age, Continuous
73 years
n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
Sex: Female, Male
Male
5 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
1 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
4 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
1 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
4 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
0 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 12 weeks treatment, with primary outcome assessed at 16 weeks

Proportion of subjects with \> 50% drop in serum PSA as compared to baseline, assessed at 16 weeks

Outcome measures

Outcome measures
Measure
Temsirolimus + Bicalutamide
n=3 Participants
Temsirolimus 25 mg administered intravenously (IV) once weekly for 12 weeks Casodex (bicalutamide) administered 50 mg/day orally (PO) Temsirolimus: Temsirolimus is an inhibitor of the mammalian target of rapamycin (MTOR, aka HGNC:3942) IUPAC name: (1R,2R,4S)-4-{(2R)-2-\[(3S,6R,7E,9R,10R,12R,14S,15E,17E,19E,21S,23S,26R,27R,34aS)-9,27-dihydroxy-10,21-dimethoxy-6,8,12,14,20,26-hexamethyl-1,5,11,28,29-pentaoxo-1,4,5,6,9,10,11,12,13,14,21,22,23,24,25,26,27,28,29,31,32,33,34,34a-tetracosahydro-3H-23,27-epoxypyrido\[2,1-c\]\[1,4\]oxazacyclohentriacontin-3-yl\]propyl}-2-methoxycyclohexyl 3-hydroxy-2-(hydroxymethyl)-2-methylpropanoate Casodex (bicalutamide): Casodex (bicalutamide) 50 mg/day PO
Reduction in Serum PSA
0 participants

Adverse Events

Temsirolimus + Bicalutamide

Serious events: 1 serious events
Other events: 5 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Temsirolimus + Bicalutamide
n=5 participants at risk
Temsirolimus 25 mg administered intravenously (IV) once weekly for 12 weeks Casodex (bicalutamide) administered 50 mg/day orally (PO) Temsirolimus: Temsirolimus is an inhibitor of the mammalian target of rapamycin (MTOR, aka HGNC:3942) IUPAC name: (1R,2R,4S)-4-{(2R)-2-\[(3S,6R,7E,9R,10R,12R,14S,15E,17E,19E,21S,23S,26R,27R,34aS)-9,27-dihydroxy-10,21-dimethoxy-6,8,12,14,20,26-hexamethyl-1,5,11,28,29-pentaoxo-1,4,5,6,9,10,11,12,13,14,21,22,23,24,25,26,27,28,29,31,32,33,34,34a-tetracosahydro-3H-23,27-epoxypyrido\[2,1-c\]\[1,4\]oxazacyclohentriacontin-3-yl\]propyl}-2-methoxycyclohexyl 3-hydroxy-2-(hydroxymethyl)-2-methylpropanoate Casodex (bicalutamide): Casodex (bicalutamide) 50 mg/day PO
Gastrointestinal disorders
Colitis
20.0%
1/5 • Number of events 1

Other adverse events

Other adverse events
Measure
Temsirolimus + Bicalutamide
n=5 participants at risk
Temsirolimus 25 mg administered intravenously (IV) once weekly for 12 weeks Casodex (bicalutamide) administered 50 mg/day orally (PO) Temsirolimus: Temsirolimus is an inhibitor of the mammalian target of rapamycin (MTOR, aka HGNC:3942) IUPAC name: (1R,2R,4S)-4-{(2R)-2-\[(3S,6R,7E,9R,10R,12R,14S,15E,17E,19E,21S,23S,26R,27R,34aS)-9,27-dihydroxy-10,21-dimethoxy-6,8,12,14,20,26-hexamethyl-1,5,11,28,29-pentaoxo-1,4,5,6,9,10,11,12,13,14,21,22,23,24,25,26,27,28,29,31,32,33,34,34a-tetracosahydro-3H-23,27-epoxypyrido\[2,1-c\]\[1,4\]oxazacyclohentriacontin-3-yl\]propyl}-2-methoxycyclohexyl 3-hydroxy-2-(hydroxymethyl)-2-methylpropanoate Casodex (bicalutamide): Casodex (bicalutamide) 50 mg/day PO
Blood and lymphatic system disorders
Anemia
80.0%
4/5 • Number of events 4
Cardiac disorders
Chest pain - cardiac
20.0%
1/5 • Number of events 1
Cardiac disorders
Other-Tachycardia
20.0%
1/5 • Number of events 1
Cardiac disorders
Palpitations
20.0%
1/5 • Number of events 1
Gastrointestinal disorders
Constipation
20.0%
1/5 • Number of events 1
General disorders
Diarrhea
20.0%
1/5 • Number of events 1
Gastrointestinal disorders
Nausea
20.0%
1/5 • Number of events 1
General disorders
Edema, trunk
20.0%
1/5 • Number of events 1
General disorders
Fatigue
40.0%
2/5 • Number of events 2
General disorders
Other-fall
20.0%
1/5 • Number of events 1
Investigations
Alkaline phosphatase increased
20.0%
1/5 • Number of events 1
Investigations
Cholesterol high
60.0%
3/5 • Number of events 3
Investigations
Increase ALT
40.0%
2/5 • Number of events 2
Investigations
Increase AST
40.0%
2/5 • Number of events 2
Investigations
Increase creatinine
40.0%
2/5 • Number of events 2
Investigations
Increase in HDL
40.0%
2/5 • Number of events 2
Investigations
Increase LDL
60.0%
3/5 • Number of events 3
Investigations
Platelet count decreased
40.0%
2/5 • Number of events 2
Investigations
Weight loss
60.0%
3/5 • Number of events 3
Metabolism and nutrition disorders
Anorexia
60.0%
3/5 • Number of events 3
Metabolism and nutrition disorders
Hyperglycemia
20.0%
1/5 • Number of events 1
Metabolism and nutrition disorders
Hypertriglyceridemia
40.0%
2/5 • Number of events 2
Metabolism and nutrition disorders
Hypoalbuminemia
40.0%
2/5 • Number of events 2
Metabolism and nutrition disorders
Hypocalcemia
20.0%
1/5 • Number of events 1
Metabolism and nutrition disorders
Hypokalemia
60.0%
3/5 • Number of events 3
Musculoskeletal and connective tissue disorders
Other-Bilateral Knee pain
20.0%
1/5 • Number of events 1
Musculoskeletal and connective tissue disorders
Pain in extremity
20.0%
1/5 • Number of events 1
Nervous system disorders
Dysgeusia
20.0%
1/5 • Number of events 1
Psychiatric disorders
Anxiety
20.0%
1/5 • Number of events 1
Renal and urinary disorders
Hematuria
20.0%
1/5 • Number of events 1
Renal and urinary disorders
Urinary incontinence
20.0%
1/5 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Cough
40.0%
2/5 • Number of events 2
Respiratory, thoracic and mediastinal disorders
Epistaxis
20.0%
1/5 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Other-Sinus congestion
20.0%
1/5 • Number of events 1
Skin and subcutaneous tissue disorders
Dry Skin
20.0%
1/5 • Number of events 1
Skin and subcutaneous tissue disorders
Rash maculo-papular
40.0%
2/5 • Number of events 2

Additional Information

Associate Professor of Medicine (Oncology)

Stanford University Medical Center

Phone: 650-725-2078

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place