Trial Outcomes & Findings for Human Fetal Liver Cell Transplantation in Chronic Liver Failure (NCT NCT01013194)

NCT ID: NCT01013194

Last Updated: 2015-11-03

Results Overview

Assessment of treated and control patients survival at 1 year follow-up

Recruitment status

COMPLETED

Study phase

PHASE1/PHASE2

Target enrollment

25 participants

Primary outcome timeframe

1 year

Results posted on

2015-11-03

Participant Flow

Participant milestones

Participant milestones
Measure
Treated Patients
Cell source: Non-purified and non-selected fetal liver cells from fetuses aborted between the 16th and 26th week of gestation. Infusion technique: Isolation and incannulation of the femoral artery.Splenic artery infusion under radiological guidance. Cell infusion: between 5x10\^8 and 10x10\^8 cells. Number of sessions: up to 2.
Control Group
Cirrhotic patients in waiting list for Liver Transplantation on standard therapy
Overall Study
STARTED
9
16
Overall Study
COMPLETED
9
16
Overall Study
NOT COMPLETED
0
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Human Fetal Liver Cell Transplantation in Chronic Liver Failure

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Treated Patients
n=9 Participants
Patients with end-stage chronic liver disease in waiting list for liver transplantation treated with non-purified and non-selected fetal liver cells.
Control Patients
n=16 Participants
Patients with end-stage chronic liver disease on standard therapy in waiting list for liver transplantation.
Total
n=25 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
9 Participants
n=5 Participants
16 Participants
n=7 Participants
25 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Sex: Female, Male
Female
3 Participants
n=5 Participants
3 Participants
n=7 Participants
6 Participants
n=5 Participants
Sex: Female, Male
Male
6 Participants
n=5 Participants
13 Participants
n=7 Participants
19 Participants
n=5 Participants
Region of Enrollment
Italy
9 participants
n=5 Participants
16 participants
n=7 Participants
25 participants
n=5 Participants

PRIMARY outcome

Timeframe: 1 year

Assessment of treated and control patients survival at 1 year follow-up

Outcome measures

Outcome measures
Measure
Treated Patients
n=9 Participants
Patients with end-stage chronic liver disease in waiting list for Liver Transplantation treated with hFLCTx
Control Patients
n=16 Participants
Patients with end-stage chronic liver disease in waiting list for Liver Transplantation on standard therapy
Patient Survival
Patient survival
5 participants
6 participants
Patient Survival
Death/Transplant
4 participants
10 participants

SECONDARY outcome

Timeframe: Baseline and 1 year Follow-up

Population: Baseline Child-Pugh score vs Follow-up

Assessment of the efficacy of human fetal liver progenitor cell transplantation on Child-Pugh score. The Child-Pugh (CP) classification is a scoring system used for the classification of the severity of cirrhosis. It includes three continuous variables (bilirubin, albumin and INR) and two discrete variables (ascites and encephalopathy). Each variable is scored 1-3 with 3 indicating most severe derangement. The determination of CP score may range from 5 to 15 and the final score allows to categorize patients in Child-Pugh A (5-6 points), B (7-9 points) and C (10-15 points). The highest is the score the sickest is the patient.

Outcome measures

Outcome measures
Measure
Treated Patients
n=9 Participants
Patients with end-stage chronic liver disease in waiting list for Liver Transplantation treated with hFLCTx
Control Patients
n=16 Participants
Patients with end-stage chronic liver disease in waiting list for Liver Transplantation on standard therapy
Analysis of Child-Pugh Score From Baseline to 1 Year Follow-up
Baseline Child-Pugh score
10.11 units on a scale
Standard Deviation 1.54
10.00 units on a scale
Standard Deviation 1.26
Analysis of Child-Pugh Score From Baseline to 1 Year Follow-up
Follow-up Child-Pugh score
9.11 units on a scale
Standard Deviation 1.45
11.13 units on a scale
Standard Deviation 1.63

SECONDARY outcome

Timeframe: Baseline and 1 year Follow-up

Assessment of the efficacy of human fetal liver progenitor cell transplantation on Meld score. The Model for End-stage Liver Disease (MELD) scoring system aims at stratifying recipients by their disease severity according to a score estimating the 3-month probability of death on the waiting list. The calculation of an individual's MELD score is based on three objective lab parameters (bilirubin, serum creatinine and prothrombin time expressed as international normalized ratio, INR) and it includes logarithmic transformations and multiplication by several factors. It ranges between 6 and 40. The highest is the score the lower is the patient's survival.

Outcome measures

Outcome measures
Measure
Treated Patients
n=9 Participants
Patients with end-stage chronic liver disease in waiting list for Liver Transplantation treated with hFLCTx
Control Patients
n=16 Participants
Patients with end-stage chronic liver disease in waiting list for Liver Transplantation on standard therapy
Analysis of Meld Score From Baseline to 1 Year Follow-up
Baseline Meld score
16.00 units on a scale
Standard Deviation 2.96
15.31 units on a scale
Standard Deviation 2.50
Analysis of Meld Score From Baseline to 1 Year Follow-up
Follow-up Meld score
15.67 units on a scale
Standard Deviation 3.84
19.06 units on a scale
Standard Deviation 5.70

Adverse Events

Treated Patients

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Control Group

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Dr Giada Pietrosi

ISMETT-UPMC

Phone: +390912192111

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place