Trial Outcomes & Findings for Treatment of Older Adults With Acute Lymphoblastic Leukemia (NCT NCT00973752)

NCT ID: NCT00973752

Last Updated: 2017-03-30

Results Overview

The number of participants alive one year after baseline.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

30 participants

Primary outcome timeframe

1 years

Results posted on

2017-03-30

Participant Flow

Participant milestones

Participant milestones
Measure
Experimental
All patients treated on same arm Prednisone: Orally during Induction, Consolidation 1, CNS (central nervous system), Consolidation 2, and Continuation therapy. Vincristine: Intravenously during Induction, CNS, Consolidation 2 and Continuation Therapy Doxorubicin: Intravenously during Induction, CNS, and Consolidation 2 therapy PEG-asparaginase: Intravenously during Induction, Consolidation 1, CNS, and Consolidation 2 therapy Cytarabine: Intrathecally during Induction and CNS therapy Methotrexate: Intrathecally during Induction, CNS, and Continuation Therapy Imatinib: Orally during Induction, Consolidation 1, CNS, Consolidation 2 and Continuation Therapy Clofarabine: Intravenously during Consolidation 1 Therapy 6 Mercaptopurine: Orally during CNS, Consolidation 2 and Continuation Therapy
Overall Study
STARTED
30
Overall Study
COMPLETED
30
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Treatment of Older Adults With Acute Lymphoblastic Leukemia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Experimental
n=30 Participants
All patients treated on same arm Prednisone: Orally during Induction, Consolidation 1, CNS, Consolidation 2, and Continuation therapy. Vincristine: Intravenously during Induction, CNS, Consolidation 2 and Continuation Therapy Doxorubicin: Intravenously during Induction, CNS, and Consolidation 2 therapy PEG-asparaginase: Intravenously during Induction, Consolidation 1, CNS, and Consolidation 2 therapy Cytarabine: Intrathecally during Induction and CNS therapy Methotrexate: Intrathecally during Induction, CNS, and Continuation Therapy Imatinib: Orally during Induction, Consolidation 1, CNS, Consolidation 2 and Continuation Therapy Clofarabine: Intravenously during Consolidation 1 Therapy 6 Mercaptopurine: Orally during CNS, Consolidation 2 and Continuation Therapy
Age, Continuous
58 years
n=5 Participants
Sex: Female, Male
Female
18 Participants
n=5 Participants
Sex: Female, Male
Male
12 Participants
n=5 Participants
Race/Ethnicity, Customized
Caucasian
27 Participants
n=5 Participants
Race/Ethnicity, Customized
Not Available
3 Participants
n=5 Participants
Region of Enrollment
United States
30 Participants
n=5 Participants
White blood cell count
10.4 10^3 cell per μL
n=5 Participants
Performance status
ECOG 0
14 Participants
n=5 Participants
Performance status
ECOG 1
11 Participants
n=5 Participants
Performance status
ECOG 2
5 Participants
n=5 Participants
Chromosomal alterations
Philadelphia chromosome positive
12 Participants
n=5 Participants
Chromosomal alterations
Mixed lineage leukemia rearrangement
2 Participants
n=5 Participants
Immunophenotype
B-cell ALL
29 Participants
n=5 Participants
Immunophenotype
T-cell ALL
1 Participants
n=5 Participants

PRIMARY outcome

Timeframe: 1 years

The number of participants alive one year after baseline.

Outcome measures

Outcome measures
Measure
Experimental
n=30 Participants
All patients treated on same arm Prednisone: Orally during Induction, Consolidation 1, CNS, Consolidation 2, and Continuation therapy. Vincristine: Intravenously during Induction, CNS, Consolidation 2 and Continuation Therapy Doxorubicin: Intravenously during Induction, CNS, and Consolidation 2 therapy PEG-asparaginase: Intravenously during Induction, Consolidation 1, CNS, and Consolidation 2 therapy Cytarabine: Intrathecally during Induction and CNS therapy Methotrexate: Intrathecally during Induction, CNS, and Continuation Therapy Imatinib: Orally during Induction, Consolidation 1, CNS, Consolidation 2 and Continuation Therapy Clofarabine: Intravenously during Consolidation 1 Therapy 6 Mercaptopurine: Orally during CNS, Consolidation 2 and Continuation Therapy
Overall Survival at One Year
19 Participants

Adverse Events

Experimental

Serious events: 10 serious events
Other events: 18 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Experimental
n=30 participants at risk
All patients treated on same arm Prednisone: Orally during Induction, Consolidation 1, CNS, Consolidation 2, and Continuation therapy. Vincristine: Intravenously during Induction, CNS, Consolidation 2 and Continuation Therapy Doxorubicin: Intravenously during Induction, CNS, and Consolidation 2 therapy PEG-asparaginase: Intravenously during Induction, Consolidation 1, CNS, and Consolidation 2 therapy Cytarabine: Intrathecally during Induction and CNS therapy Methotrexate: Intrathecally during Induction, CNS, and Continuation Therapy Imatinib: Orally during Induction, Consolidation 1, CNS, Consolidation 2 and Continuation Therapy Clofarabine: Intravenously during Consolidation 1 Therapy 6 Mercaptopurine: Orally during CNS, Consolidation 2 and Continuation Therapy
Infections and infestations
Infection w/ gr. 3/4 neutropenia
23.3%
7/30
Infections and infestations
Infection - other
10.0%
3/30
Immune system disorders
Allergic Reaction
10.0%
3/30
Hepatobiliary disorders
Transaminitis
23.3%
7/30
Hepatobiliary disorders
Hyperbilirubinemia
33.3%
10/30
Renal and urinary disorders
Azotemia
3.3%
1/30
General disorders
Tumor lysis syndrome
6.7%
2/30
Gastrointestinal disorders
stomatitis
3.3%
1/30
Gastrointestinal disorders
Gastrointestinal bleeding
6.7%
2/30
Nervous system disorders
Neuropathy
3.3%
1/30
Metabolism and nutrition disorders
Hyperglycemia
23.3%
7/30

Other adverse events

Other adverse events
Measure
Experimental
n=30 participants at risk
All patients treated on same arm Prednisone: Orally during Induction, Consolidation 1, CNS, Consolidation 2, and Continuation therapy. Vincristine: Intravenously during Induction, CNS, Consolidation 2 and Continuation Therapy Doxorubicin: Intravenously during Induction, CNS, and Consolidation 2 therapy PEG-asparaginase: Intravenously during Induction, Consolidation 1, CNS, and Consolidation 2 therapy Cytarabine: Intrathecally during Induction and CNS therapy Methotrexate: Intrathecally during Induction, CNS, and Continuation Therapy Imatinib: Orally during Induction, Consolidation 1, CNS, Consolidation 2 and Continuation Therapy Clofarabine: Intravenously during Consolidation 1 Therapy 6 Mercaptopurine: Orally during CNS, Consolidation 2 and Continuation Therapy
Blood and lymphatic system disorders
Grade 2 Anemia
40.0%
12/30
Immune system disorders
Grade 2 Allergic reaction
3.3%
1/30
Cardiac disorders
Grade 2 Hypertension
3.3%
1/30
Cardiac disorders
Grade 2 hypotension
20.0%
6/30
General disorders
Grade 2 fatigue
60.0%
18/30
General disorders
Grade 2 Insomnia
6.7%
2/30
General disorders
Grade 2 weight loss
3.3%
1/30
Skin and subcutaneous tissue disorders
Grade 2 erythema multiforme
3.3%
1/30
Skin and subcutaneous tissue disorders
Grade 2 pruritis
3.3%
1/30
Skin and subcutaneous tissue disorders
Grade 2 rash
3.3%
1/30
Skin and subcutaneous tissue disorders
Grade 2 decubitus ulcer
3.3%
1/30
Gastrointestinal disorders
Grade 2 anorexia
13.3%
4/30
Gastrointestinal disorders
Grade 2 colitis
6.7%
2/30
Gastrointestinal disorders
Grade 2 constipation
10.0%
3/30
Gastrointestinal disorders
Grade 2 diarrhea
13.3%
4/30
Gastrointestinal disorders
Grade 2 stomatitis
13.3%
4/30
Gastrointestinal disorders
Grade 2 nausea
36.7%
11/30
Gastrointestinal disorders
Grade 2 taste alteration
3.3%
1/30
Gastrointestinal disorders
Grade 2 vomiting
13.3%
4/30
Infections and infestations
Grade 2 febrile neutropenia
13.3%
4/30
Infections and infestations
Grade 2 Infection
30.0%
9/30
General disorders
Grade 2 Edema
30.0%
9/30
Hepatobiliary disorders
Grade 2 transaminitis
23.3%
7/30
Hepatobiliary disorders
Grade 2 Elevated alkaline phosphatase
6.7%
2/30
Hepatobiliary disorders
Grade 2 Hyperbilirubinemia
10.0%
3/30
Renal and urinary disorders
Grade 2 azotemia
10.0%
3/30
Metabolism and nutrition disorders
Grade 2 hyperglycemia
10.0%
3/30
General disorders
Grade 2 hypoalbuminemia
13.3%
4/30
Metabolism and nutrition disorders
Grade 2 hypocalcemia
13.3%
4/30
General disorders
Grade 2 weakness
13.3%
4/30
General disorders
Grade 2 mental status change
10.0%
3/30
Nervous system disorders
Grade 2 neuropathy
3.3%
1/30
Gastrointestinal disorders
Grade 2 Abdominal pain
16.7%
5/30
General disorders
Grade 2 back pain
6.7%
2/30
General disorders
Grade 2 pain, other
10.0%
3/30
Respiratory, thoracic and mediastinal disorders
Grade 2 dyspnea
3.3%
1/30
Respiratory, thoracic and mediastinal disorders
Grade 2 hypoxia
3.3%
1/30
Renal and urinary disorders
Grade 2 ureteral obstruction
3.3%
1/30

Additional Information

Dr. Amir Fathi

Massachusetts General Hospital

Phone: 617-724-1124

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place