Trial Outcomes & Findings for Augmenting Atropine Treatment for Amblyopia in Children 3 to < 8 Years Old (NCT NCT00944710)

NCT ID: NCT00944710

Last Updated: 2019-03-06

Results Overview

The masked 10-week amblyopic eye visual acuity scores were tabulated for both treatment groups, and included data from 10-week visual acuity exams completed between 8 to 15 weeks (inclusive) with no imputation for missing data. The primary outcome analysis followed the "intent-to-treat" principle. Therefore, data from randomized participants were included in the analysis regardless of whether the assigned treatment was actually received or whether they deviated from treatment against protocol. In addition, randomized participants who were found to be ineligible upon subsequent review of enrollment data were included in the primary outcome analysis.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

73 participants

Primary outcome timeframe

10 weeks after randomization

Results posted on

2019-03-06

Participant Flow

Between November 2009 and August 2013, 73 participants from 20 sites were randomly assigned to either augmenting weekend atropine by changing the lens over the fellow eye to plano (n=33) or continuing with weekend atropine with best spectacle correction (n=40).

Prior to being considered for the randomized trial, participants who had not completed at least 12 weeks of atropine were enrolled into a run-in phase and treated with weekend atropine 1% ophthalmic solution and spectacles based upon a recent cycloplegic refraction, with follow up every 6 weeks until no improvement

Participant milestones

Participant milestones
Measure
Control
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
10-week Primary Outcome
STARTED
40
33
10-week Primary Outcome
COMPLETED
40
33
10-week Primary Outcome
NOT COMPLETED
0
0
12-week Visit (Off-treatment)
STARTED
40
33
12-week Visit (Off-treatment)
COMPLETED
40
33
12-week Visit (Off-treatment)
NOT COMPLETED
0
0
Additional Post 10-week Primary Outcome
STARTED
40
33
Additional Post 10-week Primary Outcome
Eligible to Enter Post 10-week Phase
24
26
Additional Post 10-week Primary Outcome
COMPLETED
23
22
Additional Post 10-week Primary Outcome
NOT COMPLETED
17
11

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Augmenting Atropine Treatment for Amblyopia in Children 3 to < 8 Years Old

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Total
n=73 Participants
Total of all reporting groups
Age, Categorical
<=18 years
40 Participants
n=5 Participants
33 Participants
n=7 Participants
73 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Continuous
5.8 years
STANDARD_DEVIATION 1.5 • n=5 Participants
5.8 years
STANDARD_DEVIATION 1.4 • n=7 Participants
5.8 years
STANDARD_DEVIATION 1.4 • n=5 Participants
Age, Customized
3 to <4 years
5 participants
n=5 Participants
4 participants
n=7 Participants
9 participants
n=5 Participants
Age, Customized
4 to <5 years
8 participants
n=5 Participants
6 participants
n=7 Participants
14 participants
n=5 Participants
Age, Customized
5 to <6 years
9 participants
n=5 Participants
9 participants
n=7 Participants
18 participants
n=5 Participants
Age, Customized
6 to <7 years
7 participants
n=5 Participants
5 participants
n=7 Participants
12 participants
n=5 Participants
Age, Customized
>=7 years
11 participants
n=5 Participants
9 participants
n=7 Participants
20 participants
n=5 Participants
Sex: Female, Male
Female
22 Participants
n=5 Participants
19 Participants
n=7 Participants
41 Participants
n=5 Participants
Sex: Female, Male
Male
18 Participants
n=5 Participants
14 Participants
n=7 Participants
32 Participants
n=5 Participants
Race/Ethnicity, Customized
White
33 participants
n=5 Participants
29 participants
n=7 Participants
62 participants
n=5 Participants
Race/Ethnicity, Customized
African American
3 participants
n=5 Participants
1 participants
n=7 Participants
4 participants
n=5 Participants
Race/Ethnicity, Customized
Hispanic
4 participants
n=5 Participants
3 participants
n=7 Participants
7 participants
n=5 Participants
Region of Enrollment
United States
40 participants
n=5 Participants
33 participants
n=7 Participants
73 participants
n=5 Participants
Duration of Atropine Treatment Prior to Randomization
12 to <15 weeks
11 participants
n=5 Participants
5 participants
n=7 Participants
16 participants
n=5 Participants
Duration of Atropine Treatment Prior to Randomization
15 to <21 weeks
6 participants
n=5 Participants
9 participants
n=7 Participants
15 participants
n=5 Participants
Duration of Atropine Treatment Prior to Randomization
21 to <27 weeks
13 participants
n=5 Participants
9 participants
n=7 Participants
22 participants
n=5 Participants
Duration of Atropine Treatment Prior to Randomization
27 to 84 weeks
10 participants
n=5 Participants
10 participants
n=7 Participants
20 participants
n=5 Participants
Duration of Atropine Treatment Prior to Randomization
24.0 weeks
STANDARD_DEVIATION 11.2 • n=5 Participants
26.4 weeks
STANDARD_DEVIATION 14.6 • n=7 Participants
25.0 weeks
STANDARD_DEVIATION 12.8 • n=5 Participants
Cause of Amblyopia
Strabismus
9 participants
n=5 Participants
13 participants
n=7 Participants
22 participants
n=5 Participants
Cause of Amblyopia
Anisometropia
10 participants
n=5 Participants
6 participants
n=7 Participants
16 participants
n=5 Participants
Cause of Amblyopia
Strabismus and Anisometropia
21 participants
n=5 Participants
14 participants
n=7 Participants
35 participants
n=5 Participants
Distance Visual Acuity in the Amblyopic Eye at Randomization
20/160
2 participants
n=5 Participants
1 participants
n=7 Participants
3 participants
n=5 Participants
Distance Visual Acuity in the Amblyopic Eye at Randomization
20/125
2 participants
n=5 Participants
2 participants
n=7 Participants
4 participants
n=5 Participants
Distance Visual Acuity in the Amblyopic Eye at Randomization
20/100
5 participants
n=5 Participants
1 participants
n=7 Participants
6 participants
n=5 Participants
Distance Visual Acuity in the Amblyopic Eye at Randomization
20/80
2 participants
n=5 Participants
6 participants
n=7 Participants
8 participants
n=5 Participants
Distance Visual Acuity in the Amblyopic Eye at Randomization
20/63
9 participants
n=5 Participants
8 participants
n=7 Participants
17 participants
n=5 Participants
Distance Visual Acuity in the Amblyopic Eye at Randomization
20/50
7 participants
n=5 Participants
8 participants
n=7 Participants
15 participants
n=5 Participants
Distance Visual Acuity in the Amblyopic Eye at Randomization
20/40
11 participants
n=5 Participants
6 participants
n=7 Participants
17 participants
n=5 Participants
Distance Visual Acuity in the Amblyopic Eye at Randomization
20/32
2 participants
n=5 Participants
1 participants
n=7 Participants
3 participants
n=5 Participants
Distance Visual Acuity in the Amblyopic Eye at Randomization
0.48 logMAR
STANDARD_DEVIATION 0.19 • n=5 Participants
0.48 logMAR
STANDARD_DEVIATION 0.16 • n=7 Participants
0.48 logMAR
STANDARD_DEVIATION 0.18 • n=5 Participants
Distance Visual Acuity in the Fellow Eye at Randomization
20/32
5 participants
n=5 Participants
6 participants
n=7 Participants
11 participants
n=5 Participants
Distance Visual Acuity in the Fellow Eye at Randomization
20/25
13 participants
n=5 Participants
9 participants
n=7 Participants
22 participants
n=5 Participants
Distance Visual Acuity in the Fellow Eye at Randomization
20/20
16 participants
n=5 Participants
13 participants
n=7 Participants
29 participants
n=5 Participants
Distance Visual Acuity in the Fellow Eye at Randomization
20/16
6 participants
n=5 Participants
5 participants
n=7 Participants
11 participants
n=5 Participants
Distance Visual Acuity in the Fellow Eye at Randomization
0.04 logMAR
STANDARD_DEVIATION 0.09 • n=5 Participants
0.05 logMAR
STANDARD_DEVIATION 0.10 • n=7 Participants
0.05 logMAR
STANDARD_DEVIATION 0.09 • n=5 Participants
Interocular Eye Visual Acuity Difference at Randomization
4.4 logMAR lines
STANDARD_DEVIATION 1.8 • n=5 Participants
4.4 logMAR lines
STANDARD_DEVIATION 1.7 • n=7 Participants
4.4 logMAR lines
STANDARD_DEVIATION 1.7 • n=5 Participants
Spherical Equivalent Refractive Error in Amblyopic Eye at Enrollment
0 to <+1.00 D
0 participants
n=5 Participants
0 participants
n=7 Participants
0 participants
n=5 Participants
Spherical Equivalent Refractive Error in Amblyopic Eye at Enrollment
+1.00 to <+2.00 D
0 participants
n=5 Participants
1 participants
n=7 Participants
1 participants
n=5 Participants
Spherical Equivalent Refractive Error in Amblyopic Eye at Enrollment
+2.00 to <+3.00 D
1 participants
n=5 Participants
1 participants
n=7 Participants
2 participants
n=5 Participants
Spherical Equivalent Refractive Error in Amblyopic Eye at Enrollment
+3.00 to <+4.00 D
6 participants
n=5 Participants
5 participants
n=7 Participants
11 participants
n=5 Participants
Spherical Equivalent Refractive Error in Amblyopic Eye at Enrollment
+4.00 D or more
33 participants
n=5 Participants
26 participants
n=7 Participants
59 participants
n=5 Participants
Spherical Equivalent Refractive Error in Amblyopic Eye at Enrollment
5.73 diopters
STANDARD_DEVIATION 1.62 • n=5 Participants
5.84 diopters
STANDARD_DEVIATION 1.89 • n=7 Participants
5.78 diopters
STANDARD_DEVIATION 1.74 • n=5 Participants
Spherical Equivalent Refractive Error in Fellow Eye at Enrollment
+1.50 to <+2.00 D
5 participants
n=5 Participants
5 participants
n=7 Participants
10 participants
n=5 Participants
Spherical Equivalent Refractive Error in Fellow Eye at Enrollment
+2.00 to <+3.00 D
6 participants
n=5 Participants
2 participants
n=7 Participants
8 participants
n=5 Participants
Spherical Equivalent Refractive Error in Fellow Eye at Enrollment
+3.00 to <+4.00 D
7 participants
n=5 Participants
9 participants
n=7 Participants
16 participants
n=5 Participants
Spherical Equivalent Refractive Error in Fellow Eye at Enrollment
+4.00 D or more
22 participants
n=5 Participants
17 participants
n=7 Participants
39 participants
n=5 Participants
Spherical Equivalent Refractive Error in Fellow Eye at Enrollment
3.95 diopters
STANDARD_DEVIATION 1.60 • n=5 Participants
4.55 diopters
STANDARD_DEVIATION 2.28 • n=7 Participants
4.22 diopters
STANDARD_DEVIATION 1.95 • n=5 Participants

PRIMARY outcome

Timeframe: 10 weeks after randomization

Population: The primary outcome analysis followed the intent-to-treat principle and included data from 10-week visual acuity exams completed between 8 and 15 weeks (inclusive) with no imputation for missing data.

The masked 10-week amblyopic eye visual acuity scores were tabulated for both treatment groups, and included data from 10-week visual acuity exams completed between 8 to 15 weeks (inclusive) with no imputation for missing data. The primary outcome analysis followed the "intent-to-treat" principle. Therefore, data from randomized participants were included in the analysis regardless of whether the assigned treatment was actually received or whether they deviated from treatment against protocol. In addition, randomized participants who were found to be ineligible upon subsequent review of enrollment data were included in the primary outcome analysis.

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/50
6 participants
6 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/200
0 participants
1 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/160
2 participants
0 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/125
1 participants
2 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/100
4 participants
0 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/80
5 participants
4 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/63
3 participants
4 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/40
11 participants
4 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/32
3 participants
6 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/25
3 participants
5 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/20
1 participants
1 participants
Distribution of 10-week Amblyopic-Eye Visual Acuity
20/16
0 participants
0 participants

PRIMARY outcome

Timeframe: 10 weeks after randomization

Population: The primary outcome analysis followed the intent-to-treat principle and included data from 10-week visual acuity exams completed between 8 and 15 weeks (inclusive) with no imputation for missing data.

The primary outcome analysis was a treatment group comparison of the masked 10-week amblyopic eye visual acuity using an analysis of covariance (ANCOVA) model, adjusting for visual acuity at randomization. The analysis included data from 10-week visual acuity exams completed between 8 to 15 weeks (inclusive) with no imputation for missing data. The primary outcome analysis followed the "intent-to-treat" principle. Therefore, data from randomized participants were included in the analysis regardless of whether the assigned treatment was actually received or whether they deviated from treatment against protocol. In addition, randomized participants who were found to be ineligible upon subsequent review of enrollment data were included in the primary outcome analysis.

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Mean 10-week Amblyopic-Eye Visual Acuity
0.42 logMAR
Standard Deviation 0.22
0.37 logMAR
Standard Deviation 0.23

PRIMARY outcome

Timeframe: Randomization to 10 weeks

Population: The primary outcome analysis followed the intent-to-treat principle and included data from 10-week visual acuity exams completed between 8 and 15 weeks (inclusive) with no imputation for missing data.

The change in 10-week amblyopic eye visual acuity scores since randomization was tabulated for both treatment groups, and included data from 10-week visual acuity exams completed between 8 to 15 weeks (inclusive) with no imputation for missing data. The primary outcome analysis followed the "intent-to-treat" principle. Therefore, data from randomized participants were included in the analysis regardless of whether the assigned treatment was actually received or whether they deviated from treatment against protocol. In addition, randomized participants who were found to be ineligible upon subsequent review of enrollment data were included in the primary outcome analysis.

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Distribution of the Change in Amblyopic-Eye Visual Acuity
3 or more lines worse
0 participants
0 participants
Distribution of the Change in Amblyopic-Eye Visual Acuity
2 lines worse
1 participants
2 participants
Distribution of the Change in Amblyopic-Eye Visual Acuity
1 line worse
4 participants
3 participants
Distribution of the Change in Amblyopic-Eye Visual Acuity
No change
14 participants
6 participants
Distribution of the Change in Amblyopic-Eye Visual Acuity
1 line improved
12 participants
13 participants
Distribution of the Change in Amblyopic-Eye Visual Acuity
2 lines improved
7 participants
2 participants
Distribution of the Change in Amblyopic-Eye Visual Acuity
3 or more lines improved
1 participants
7 participants

PRIMARY outcome

Timeframe: Randomization to 10 weeks

Population: The primary outcome analysis followed the intent-to-treat principle and included data from 10-week visual acuity exams completed between 8 and 15 weeks (inclusive) with no imputation for missing data.

The change in 10-week amblyopic eye visual acuity was computed for both treatment groups and included data from 10-week visual acuity exams completed between 8 to 15 weeks (inclusive) with no imputation for missing data. The primary outcome analysis followed the "intent-to-treat" principle. Therefore, data from randomized participants were included in the analysis regardless of whether the assigned treatment was actually received or whether they deviated from treatment against protocol. In addition, randomized participants who were found to be ineligible upon subsequent review of enrollment data were included in the primary outcome analysis.

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Mean Change in Amblyopic-Eye Visual Acuity at 10 Weeks From Randomization
0.6 logMAR lines
Standard Deviation 1.1
1.1 logMAR lines
Standard Deviation 1.8

SECONDARY outcome

Timeframe: 10 weeks after randomization

Population: The analysis includes data from participants who completed a 10-week exam.

The proportion of participants who achieved 20/25 or better visual acuity since randomization was computed at the 10-week outcome. The secondary outcome analysis was a treatment group comparison of the proportion of participants whose 10-week masked amblyopic eye visual acuity was 20/25 or better since randomization. The analysis included data from 10-week visual acuity exams completed between 8 to 15 weeks (inclusive) according to the principles specified in the primary outcome analysis.

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Treatment Group Comparison of the Proportion of Participants Who Achieved 20/25 or Better Visual Acuity at 10 Weeks Since Randomization
4 participants
6 participants

SECONDARY outcome

Timeframe: 10 weeks after randomization

Population: The analysis included data from 10-week visual acuity exams completed between 8 to 15 weeks (inclusive) according to the principles specified in the primary outcome analysis.

The proportion of participants who improved at least 2 logMAR lines since randomization was computed at the 10-week outcome. The secondary outcome analysis was a treatment group comparison of the proportion of participants whose 10-week masked amblyopic eye visual acuity improved at least 2 logMAR lines since randomization using logistic regression, adjusting for visual acuity at randomization. The analysis included data from 10-week visual acuity exams completed between 8 to 15 weeks (inclusive) according to the principles specified in the primary outcome analysis.

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Treatment Group Comparison of the Proportion of Participants Who Have Improved by 2 or More logMAR Visual Acuity Lines at 10 Weeks Since Randomization
8 participants
9 participants

SECONDARY outcome

Timeframe: 10 weeks after randomization

The distribution of compliance with prescribed treatment was tabulated for the 10-week outcome. Compliance was evaluated as excellent (\>75%), good (51%-75%), fair (26%-50%), or poor (\<26%) based on discussions with the parent and by reviewing study calendars maintained by the parent, who recorded the frequency of atropine administration.

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Spectacle Compliance at 10 Weeks by Treatment Group
Excellent
39 participants
30 participants
Spectacle Compliance at 10 Weeks by Treatment Group
Good
1 participants
1 participants
Spectacle Compliance at 10 Weeks by Treatment Group
Fair
0 participants
1 participants
Spectacle Compliance at 10 Weeks by Treatment Group
Poor
0 participants
1 participants

SECONDARY outcome

Timeframe: 10 weeks after randomization or later (until no further VA improvement, up to maximum of 84 weeks for one subject)

The distribution of compliance with prescribed treatment was tabulated for the 10-week outcome and as averaged scores across all study follow-up visits. Compliance was evaluated as excellent (\>75%), good (51%-75%), fair (26%-50%), or poor (\<26%) based on discussions with the parent and by reviewing study calendars maintained by the parent, who recorded the frequency of atropine administration.

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Average Spectacle Compliance by Treatment Group
Excellent
39 participants
30 participants
Average Spectacle Compliance by Treatment Group
Good
1 participants
2 participants
Average Spectacle Compliance by Treatment Group
Fair
0 participants
0 participants
Average Spectacle Compliance by Treatment Group
Poor
0 participants
1 participants

SECONDARY outcome

Timeframe: 10 weeks after randomization

The distribution of compliance with prescribed treatment was tabulated for the 10-week outcome. Compliance was evaluated as excellent (\>75%), good (51%-75%), fair (26%-50%), or poor (\<26%) based on discussions with the parent and by reviewing study calendars maintained by the parent, who recorded the frequency of atropine administration.

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Atropine Compliance at 10 Weeks by Treatment Group
Excellent
38 participants
31 participants
Atropine Compliance at 10 Weeks by Treatment Group
Good
2 participants
2 participants
Atropine Compliance at 10 Weeks by Treatment Group
Fair
0 participants
0 participants
Atropine Compliance at 10 Weeks by Treatment Group
Poor
0 participants
0 participants

SECONDARY outcome

Timeframe: 10 weeks after randomization or later (until no further VA improvement, up to maximum of 84 weeks for one subject)

The distribution of compliance with prescribed treatment was tabulated for the 10-week outcome and as averaged scores across all study follow-up visits. Compliance was evaluated as excellent (\>75%), good (51%-75%), fair (26%-50%), or poor (\<26%) based on discussions with the parent and by reviewing study calendars maintained by the parent, who recorded the frequency of atropine administration.

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Average Atropine Compliance by Treatment Group
Excellent
39 participants
29 participants
Average Atropine Compliance by Treatment Group
Good
1 participants
4 participants
Average Atropine Compliance by Treatment Group
Fair
0 participants
0 participants
Average Atropine Compliance by Treatment Group
Poor
0 participants
0 participants

SECONDARY outcome

Timeframe: 12 weeks after randomization

Distribution of Interocular Difference Between Eyes at 12-week Exam

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Distribution of Interocular Difference at 12-week Exam
0 or less lines
3 participants
2 participants
Distribution of Interocular Difference at 12-week Exam
1 line
2 participants
2 participants
Distribution of Interocular Difference at 12-week Exam
2 lines
6 participants
8 participants
Distribution of Interocular Difference at 12-week Exam
3 lines
6 participants
8 participants
Distribution of Interocular Difference at 12-week Exam
4 lines
5 participants
4 participants
Distribution of Interocular Difference at 12-week Exam
5 lines
5 participants
5 participants
Distribution of Interocular Difference at 12-week Exam
6 or more lines
12 participants
4 participants

SECONDARY outcome

Timeframe: 12 weeks after randomization

Mean Interocular Difference Between Eyes at 12-week Exam

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Mean Interocular Difference at 12-week Exam
4.3 logMAR lines
Standard Deviation 2.6
3.3 logMAR lines
Standard Deviation 2.0

SECONDARY outcome

Timeframe: 12 weeks after randomization

Following the 10-week primary outcome exam, participants discontinued the randomized treatment and returned 2 weeks later for a 12-week visit to measure off-treatment fellow-eye visual acuity.

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Distribution of 12-week Fellow-Eye Visual Acuity
20/40
1 participants
0 participants
Distribution of 12-week Fellow-Eye Visual Acuity
20/32
0 participants
4 participants
Distribution of 12-week Fellow-Eye Visual Acuity
20/25
10 participants
7 participants
Distribution of 12-week Fellow-Eye Visual Acuity
20/20
19 participants
14 participants
Distribution of 12-week Fellow-Eye Visual Acuity
20/16
10 participants
8 participants

SECONDARY outcome

Timeframe: 12 weeks after randomization

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Mean Fellow-Eye Visual Acuity at 12-week Exam
0.01 logMAR
Standard Deviation 0.09
0.02 logMAR
Standard Deviation 0.10

SECONDARY outcome

Timeframe: 12 weeks after randomization

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Distribution of Change in Fellow-Eye Visual Acuity at 12 Weeks From Randomization
3 or more lines worse
1 participants
0 participants
Distribution of Change in Fellow-Eye Visual Acuity at 12 Weeks From Randomization
2 lines worse
0 participants
0 participants
Distribution of Change in Fellow-Eye Visual Acuity at 12 Weeks From Randomization
1 line worse
1 participants
2 participants
Distribution of Change in Fellow-Eye Visual Acuity at 12 Weeks From Randomization
No change
23 participants
22 participants
Distribution of Change in Fellow-Eye Visual Acuity at 12 Weeks From Randomization
1 line improved
12 participants
7 participants
Distribution of Change in Fellow-Eye Visual Acuity at 12 Weeks From Randomization
2 lines improved
3 participants
2 participants
Distribution of Change in Fellow-Eye Visual Acuity at 12 Weeks From Randomization
3 or more lines improved
0 participants
0 participants

SECONDARY outcome

Timeframe: 12 weeks after randomization

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Mean Change in Fellow-Eye Visual Acuity at 12 Weeks From Randomization
0.4 change in lines
Standard Deviation 0.9
0.3 change in lines
Standard Deviation 0.7

SECONDARY outcome

Timeframe: 10 weeks after randomization

Population: The analysis included participants who completed 10-week exams between 8 and 15 weeks (inclusive) according to the principles specified in the primary outcome analysis.

The number of participants was tabulated by treatment group within categorical levels of prespecified baseline subgroup factors for participants with 10-week visual acuity exams completed between 8 to 15 weeks (inclusive) according to principles specified in the primary outcome analysis.

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Distribution of Baseline Characteristics at the 10-week Outcome
Atropine duration prior to randomization:15-<21wks
6 participants
9 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Atropine duration prior to randomization:21-<27wks
12 participants
9 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Atropine duration prior to randomization:27-84 wks
10 participants
10 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Fellow-eye SE RE at enrollment: <+3.00 Diopters(D)
10 participants
7 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Fellow-eye SE RE at enrollment: +3.00 to <+4.50 D
12 participants
13 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Fellow-eye SE RE at enrollment: +4.50 to +6.00 D
12 participants
4 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Fellow-eye SE RE at enrollment: >+6.00 D
5 participants
9 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Gender: Female
21 participants
19 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Gender: Male
18 participants
14 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Race/Ethnicity: White (non-Hispanic)
32 participants
29 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Race/Ethnicity: Non-White/Hispanic
7 participants
4 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Age at randomization: 3 to <4 years
5 participants
4 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Age at randomization: 4 to <5 years
7 participants
6 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Age at randomization: 5 to <6 years
9 participants
9 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Age at randomization: 6 to <7 years
7 participants
5 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Age at randomization: 7 years or older
11 participants
9 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Amblyopic-eye VA at randomization: 20/80 or worse
11 participants
10 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Amblyopic-eye VA at randomization: 20/63
9 participants
8 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Amblyopic-eye VA at randomization: 20/50
7 participants
8 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Amblyopic-eye VA at randomization: 20/40 or better
12 participants
7 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Cause of amblyopia: Strabismus
8 participants
13 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Cause of amblyopia: Anisometropia
10 participants
6 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Cause of amblyopia: Combined mechanism
21 participants
14 participants
Distribution of Baseline Characteristics at the 10-week Outcome
Atropine duration prior to randomization:12-<15wks
11 participants
5 participants

SECONDARY outcome

Timeframe: 10 weeks after randomization

Population: The analysis included participants who completed 10-week exams between 8 and 15 weeks (inclusive) according to the principles of the primary outcome analysis.

Mean amblyopic eye visual acuity at randomization was computed by treatment group within categorical levels of prespecified baseline subgroup factors. The analysis included data from participants with 10-week exams completed between 8 to 15 weeks (inclusive) according to the principles specified in the primary outcome analysis.

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Cause of amblyopia: Strabismus
0.48 logMAR
Standard Deviation 0.23
0.46 logMAR
Standard Deviation 0.16
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Atropine duration prior to randomization:21-<27wks
0.43 logMAR
Standard Deviation 0.12
0.53 logMAR
Standard Deviation 0.12
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Atropine duration prior to randomization:27-84 wks
0.46 logMAR
Standard Deviation 0.18
0.47 logMAR
Standard Deviation 0.19
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Fellow-eye SE RE at enrollment: +3.00 to <+4.50 D
0.50 logMAR
Standard Deviation 0.18
0.51 logMAR
Standard Deviation 0.16
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Fellow-eye SE RE at enrollment: +4.50 to +6.00 D
0.53 logMAR
Standard Deviation 0.17
0.45 logMAR
Standard Deviation 0.24
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Gender: Female
0.51 logMAR
Standard Deviation 0.19
0.46 logMAR
Standard Deviation 0.14
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Gender: Male
0.45 logMAR
Standard Deviation 0.19
0.51 logMAR
Standard Deviation 0.19
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Race/Ethnicity: White (non-Hispanic)
0.50 logMAR
Standard Deviation 0.19
0.49 logMAR
Standard Deviation 0.17
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Race/Ethnicity: Non-White/Hispanic
0.41 logMAR
Standard Deviation 0.18
0.43 logMAR
Standard Deviation 0.05
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Age at randomization: 3 to <4 years
0.58 logMAR
Standard Deviation 0.22
0.48 logMAR
Standard Deviation 0.17
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Age at randomization: 4 to <5 years
0.50 logMAR
Standard Deviation 0.13
0.58 logMAR
Standard Deviation 0.23
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Age at randomization: 5 to <6 years
0.46 logMAR
Standard Deviation 0.21
0.42 logMAR
Standard Deviation 0.10
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Age at randomization: 6 to <7 years
0.43 logMAR
Standard Deviation 0.18
0.50 logMAR
Standard Deviation 0.12
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Fellow-eye SE RE at enrollment: <+3.00 Diopters(D)
0.41 logMAR
Standard Deviation 0.20
0.49 logMAR
Standard Deviation 0.20
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Fellow-eye SE RE at enrollment: >+6.00 D
0.48 logMAR
Standard Deviation 0.25
0.47 logMAR
Standard Deviation 0.11
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Age at randomization: 7 years or older
0.48 logMAR
Standard Deviation 0.21
0.48 logMAR
Standard Deviation 0.18
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Cause of amblyopia: Anisometropia
0.42 logMAR
Standard Deviation 0.13
0.35 logMAR
Standard Deviation 0.11
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Cause of amblyopia: Combined mechanism
0.51 logMAR
Standard Deviation 0.20
0.56 logMAR
Standard Deviation 0.15
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Atropine duration prior to randomization:12-<15wks
0.54 logMAR
Standard Deviation 0.23
0.38 logMAR
Standard Deviation 0.11
Mean Amblyopic Eye Visual at Randomization According to Baseline Characteristics for 10-week Outcome
Atropine duration prior to randomization:15-<21wks
0.53 logMAR
Standard Deviation 0.23
0.51 logMAR
Standard Deviation 0.18

SECONDARY outcome

Timeframe: 10 weeks after randomization

Population: The analysis included participants who completed 10-week exams between 8 and 15 weeks (inclusive) according to the principles of the primary outcome analysis.

A treatment comparison of mean amblyopic eye visual acuity change since randomization was performed at the 10-week outcome according to categorical levels of prespecified baseline subgroup factors. The analysis included data from participants with 10-week exams completed between 8 to 15 weeks (inclusive) according to the principles specified in the primary outcome analysis.

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Race/Ethnicity: White (non-Hispanic)
0.5 logMAR lines
Standard Deviation 1.1
1.1 logMAR lines
Standard Deviation 1.8
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Cause of amblyopia: Anisometropia
0.8 logMAR lines
Standard Deviation 0.9
1.0 logMAR lines
Standard Deviation 1.9
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Cause of amblyopia: Combined mechanism
0.7 logMAR lines
Standard Deviation 1.1
0.6 logMAR lines
Standard Deviation 1.6
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Atropine duration prior to randomization:12-<15wks
1.1 logMAR lines
Standard Deviation 0.7
1.2 logMAR lines
Standard Deviation 1.8
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Atropine duration prior to randomization:15-<21wks
-0.3 logMAR lines
Standard Deviation 1.0
1.7 logMAR lines
Standard Deviation 2.2
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Atropine duration prior to randomization:21-<27wks
0.6 logMAR lines
Standard Deviation 1.3
1.2 logMAR lines
Standard Deviation 1.5
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Atropine duration prior to randomization:27-84 wks
0.6 logMAR lines
Standard Deviation 0.8
0.5 logMAR lines
Standard Deviation 1.6
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Fellow-eye SE RE at enrollment: <+3.00 Diopters(D)
0.7 logMAR lines
Standard Deviation 1.3
1.0 logMAR lines
Standard Deviation 2.7
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Fellow-eye SE RE at enrollment: +4.50 to +6.00 D
0.4 logMAR lines
Standard Deviation 0.9
1.3 logMAR lines
Standard Deviation 2.6
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Fellow-eye SE RE at enrollment: >+6.00 D
0.6 logMAR lines
Standard Deviation 1.1
1.3 logMAR lines
Standard Deviation 1.4
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Gender: Female
0.2 logMAR lines
Standard Deviation 1.0
1.2 logMAR lines
Standard Deviation 1.6
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Gender: Male
1.0 logMAR lines
Standard Deviation 1.0
1.1 logMAR lines
Standard Deviation 2.0
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Race/Ethnicity: Non-White/Hispanic
0.9 logMAR lines
Standard Deviation 1.2
1.0 logMAR lines
Standard Deviation 2.2
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Age at randomization: 3 to <4 years
0.2 logMAR lines
Standard Deviation 0.8
1.3 logMAR lines
Standard Deviation 1.3
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Age at randomization: 4 to <5 years
04 logMAR lines
Standard Deviation 1.5
0.7 logMAR lines
Standard Deviation 2.4
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Age at randomization: 5 to <6 years
0.8 logMAR lines
Standard Deviation 1.3
1.2 logMAR lines
Standard Deviation 1.4
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Age at randomization: 6 to <7 years
0.3 logMAR lines
Standard Deviation 0.5
2.4 logMAR lines
Standard Deviation 2.0
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Age at randomization: 7 years or older
0.9 logMAR lines
Standard Deviation 0.9
0.6 logMAR lines
Standard Deviation 1.7
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Amblyopic-eye VA at randomization: 20/80 or worse
0.5 logMAR lines
Standard Deviation 0.7
1.0 logMAR lines
Standard Deviation 2.4
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Amblyopic-eye VA at randomization: 20/63
0.4 logMAR lines
Standard Deviation 1.3
1.5 logMAR lines
Standard Deviation 1.7
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Amblyopic-eye VA at randomization: 20/50
1.0 logMAR lines
Standard Deviation 1.3
1.3 logMAR lines
Standard Deviation 1.7
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Amblyopic-eye VA at randomization: 20/40 or better
0.5 logMAR lines
Standard Deviation 1.1
0.7 logMAR lines
Standard Deviation 1.0
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Cause of amblyopia: Strabismus
0.1 logMAR lines
Standard Deviation 1.1
1.7 logMAR lines
Standard Deviation 1.8
Treatment Comparison of Mean Amblyopic Eye Visual Acuity Change at 10-weeks According to Baseline Characteristics
Fellow-eye SE RE at enrollment: +3.00 to <+4.50 D
0.7 logMAR lines
Standard Deviation 1.2
1.0 logMAR lines
Standard Deviation 1.2

SECONDARY outcome

Timeframe: 10 weeks after randomization or later (until no further VA improvement, up to maximum of 84 weeks for one subject)

Population: The analysis includes data from participants who completed the 10-week exam and/or a later visit.

Participants in both groups who have improved by one or more lines from randomization to the 10-week outcome exam will continue in the study and visits will occur every 10 weeks until no improvement of one or more lines from the previous visit. The distribution of best post-randomization (10 weeks or later) visual acuity scores in the amblyopic eye was tabulated for both treatment groups using the initial visual acuity score (if a retest was obtained.)

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/200
0 participants
1 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/80
6 participants
1 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/63
1 participants
4 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/160
2 participants
0 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/125
1 participants
0 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/100
3 participants
1 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/50
8 participants
5 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/40
10 participants
3 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/32
3 participants
10 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/25
5 participants
5 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/20
1 participants
3 participants
Distribution of Amblyopic-Eye Visual Acuity at Best Outcome Visit
20/16
0 participants
0 participants

SECONDARY outcome

Timeframe: 10 weeks after randomization or later (until no further VA improvement, up to maximum of 84 weeks for one subject)

Population: The analysis includes data from participants who completed the 10-week exam and/or a later visit.

Participants in both groups who have improved by one or more lines from randomization to the 10-week outcome exam will continue in the study and visits will occur every 10 weeks until no improvement of one or more lines from the previous visit. A treatment comparison of mean amblyopic eye visual acuity at the visit of best post-randomization visual acuity (10 weeks or later) was performed using an analysis of covariance, adjusting for amblyopic eye visual acuity at randomization.

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Mean Amblyopic-Eye Visual Acuity at Best Outcome Visit
0.40 logMAR
Standard Deviation 0.23
0.29 logMAR
Standard Deviation 0.22

SECONDARY outcome

Timeframe: Randomization to 10 weeks or later (until no further VA improvement, up to maximum of 84 weeks for one subject)

Population: The analysis includes data from participants who completed the 10-week exam and/or a later visit.

Participants in both groups who have improved by one or more lines from randomization to the 10-week outcome exam will continue in the study and visits will occur every 10 weeks until no improvement of one or more lines from the previous visit. The distribution of change in best post-randomization (10 weeks or later) visual acuity in the amblyopic eye since randomization was tabulated for both treatment groups using the initial visual acuity score (if a retest was obtained.)

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Distribution of Change in Amblyopic-Eye Visual Acuity From Randomization to Best Outcome Visit
1 line worse
4 participants
3 participants
Distribution of Change in Amblyopic-Eye Visual Acuity From Randomization to Best Outcome Visit
No change
12 participants
3 participants
Distribution of Change in Amblyopic-Eye Visual Acuity From Randomization to Best Outcome Visit
1 line improved
12 participants
6 participants
Distribution of Change in Amblyopic-Eye Visual Acuity From Randomization to Best Outcome Visit
3 or more lines worse
0 participants
0 participants
Distribution of Change in Amblyopic-Eye Visual Acuity From Randomization to Best Outcome Visit
2 lines worse
1 participants
1 participants
Distribution of Change in Amblyopic-Eye Visual Acuity From Randomization to Best Outcome Visit
2 lines improved
9 participants
6 participants
Distribution of Change in Amblyopic-Eye Visual Acuity From Randomization to Best Outcome Visit
3 or more lines improved
2 participants
14 participants

SECONDARY outcome

Timeframe: 10 weeks after randomization or later (until no further VA improvement, up to maximum of 84 weeks for one subject)

Population: The analysis includes data from participants who completed the 10-week exam and/or a later visit.

Participants in both groups who have improved by one or more lines from randomization to the 10-week outcome exam will continue in the study and visits will occur every 10 weeks until no improvement of one or more lines from the previous visit. The mean change in amblyopic eye visual acuity since randomization was computed for both treatment groups based on the visit of best post-randomization visual acuity (10 weeks or later) using the initial visual acuity score (if a retest was obtained.)

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=30 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Mean Change in Amblyopic-Eye Visual Acuity at Best Outcome Visit
0.8 logMAR lines
Standard Deviation 1.2
1.9 logMAR lines
Standard Deviation 1.8

SECONDARY outcome

Timeframe: 10 weeks after randomization or later (until no further VA improvement, up to maximum of 84 weeks for one subject)

Outcome measures

Outcome measures
Measure
Control
n=39 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Treatment Group Comparison of the Proportion of Participants Who Have Improved by 2 or More logMAR Visual Acuity Lines Based on Visual Acuity at Best Outcome Visit
11 participants
20 participants

SECONDARY outcome

Timeframe: 12 weeks after randomization

Population: The analysis includes all participants who completed the 12-week exam.

Distribution of Randot Preschool Stereoacuity Score at 12 Weeks; Participants with a Randot Preschool test of \>800 seconds of arc were classified as having a stereoacuity of 3000 seconds of arc if the Titmus fly test was positive or as nil if the Titmus fly test was negative.

Outcome measures

Outcome measures
Measure
Control
n=40 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Distribution of Randot Preschool Stereoacuity Score at 12 Weeks
Failed pretest
4 participants
2 participants
Distribution of Randot Preschool Stereoacuity Score at 12 Weeks
100 arcsec
1 participants
1 participants
Distribution of Randot Preschool Stereoacuity Score at 12 Weeks
>800 arcsec: Nil
7 participants
10 participants
Distribution of Randot Preschool Stereoacuity Score at 12 Weeks
>800 arcsec: 3000 arcsec
14 participants
12 participants
Distribution of Randot Preschool Stereoacuity Score at 12 Weeks
800 arcsec
7 participants
3 participants
Distribution of Randot Preschool Stereoacuity Score at 12 Weeks
400 arcsec
4 participants
3 participants
Distribution of Randot Preschool Stereoacuity Score at 12 Weeks
200 arcsec
0 participants
1 participants
Distribution of Randot Preschool Stereoacuity Score at 12 Weeks
60 arcsec
2 participants
1 participants
Distribution of Randot Preschool Stereoacuity Score at 12 Weeks
40 arcsec
1 participants
0 participants

SECONDARY outcome

Timeframe: 12 weeks after randomization

Population: The analysis includes participants with anisometropic amblyopia (no strabismus) who completed the 12-week exam.

Outcome measures

Outcome measures
Measure
Control
n=10 Participants
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=6 Participants
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Distribution of Randot Preschool Stereoacuity Scores at 12 Weeks for Participants With Anisometropic Amblyopia
>800 arcsec: 3000 arcsec
2 participants
2 participants
Distribution of Randot Preschool Stereoacuity Scores at 12 Weeks for Participants With Anisometropic Amblyopia
800 arcsec
3 participants
1 participants
Distribution of Randot Preschool Stereoacuity Scores at 12 Weeks for Participants With Anisometropic Amblyopia
40 arcsec
1 participants
0 participants
Distribution of Randot Preschool Stereoacuity Scores at 12 Weeks for Participants With Anisometropic Amblyopia
Failed pretest
0 participants
0 participants
Distribution of Randot Preschool Stereoacuity Scores at 12 Weeks for Participants With Anisometropic Amblyopia
>800 arcsec: Nil
1 participants
1 participants
Distribution of Randot Preschool Stereoacuity Scores at 12 Weeks for Participants With Anisometropic Amblyopia
400 arcsec
2 participants
0 participants
Distribution of Randot Preschool Stereoacuity Scores at 12 Weeks for Participants With Anisometropic Amblyopia
200 arcsec
0 participants
0 participants
Distribution of Randot Preschool Stereoacuity Scores at 12 Weeks for Participants With Anisometropic Amblyopia
100 arcsec
0 participants
1 participants
Distribution of Randot Preschool Stereoacuity Scores at 12 Weeks for Participants With Anisometropic Amblyopia
60 arcsec
1 participants
1 participants

Adverse Events

Control

Serious events: 0 serious events
Other events: 5 other events
Deaths: 0 deaths

Intensified Treatment

Serious events: 0 serious events
Other events: 9 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Control
n=40 participants at risk
Weekend atropine 1% Atropine: Weekend atropine 1%
Intensified Treatment
n=33 participants at risk
Weekend atropine 1% with plano lens over the sound eye Atropine: Weekend atropine 1% Plano lens: plano lens over the sound eye
Eye disorders
Light Sensitivity
2.5%
1/40
18.2%
6/33
Eye disorders
New ocular deviation or worsening of preexisting deviation by at least 10 PD
10.0%
4/40
9.1%
3/33

Additional Information

Raymond Kraker, M.S.P.H., Director of PEDIG Coordinating Center

Jaeb Center for Health Research

Phone: 813-975-8690

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place