A Study of Bevacizumab (Avastin®) in Combination With Temozolomide and Radiotherapy in Participants With Newly Diagnosed Glioblastoma

NCT ID: NCT00943826

Last Updated: 2017-09-25

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

921 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-06-29

Study Completion Date

2015-09-09

Brief Summary

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This 2 arm study investigated the efficacy and safety of the addition of bevacizumab to the current standard of care (multimodality therapy of concurrent radiotherapy plus temozolomide followed by adjuvant temozolomide) as compared to the current standard of care alone. Participants were randomly assigned to either the bevacizumab (10 milligrams per kilogram (mg/kg) intravenously \[IV\] once every 2 week \[q2w\]) or the placebo arm, in combination with radiation therapy (total dose 60 Gray \[Gy\], administered as 2 Gy fractions, 5 days/week) plus temozolomide (75 milligrams per meter squared \[mg/m\^2\] oral administration \[po\] daily) for 6 weeks. After a 4 week treatment break, participants continued to receive bevacizumab (10 mg/kg IV q2w) or placebo, plus temozolomide (150-200 mg/m\^2 po daily on days 1-5 of each 4 week cycle) for 6 cycles of maintenance treatment or until disease progression or unacceptable toxicity, whichever occured first. Following the maintenance phase, bevacizumab (15 mg/kg iv every 3 weeks \[q3w\]) or placebo monotherapy continued. The time on study treatment was until disease progression.

Detailed Description

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Conditions

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Glioblastoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Bevacizumab + RT + Temozolomide

In the Concurrent Phase participants will receive radiotherapy (RT) in daily fractions of 2 Gy to be given 5 days per week for 6 weeks and temozolomide 75 mg/m\^2 daily from the first day to the last day of radiotherapy (it may continue for a maximum of 49 days in case of delay to the end of radiation therapy) and bevacizumab 10 mg/kg IV every 2 weeks for 6 weeks. There will be a 4 week treatment break. Participants will then enter the Maintenance Phase where they receive six 28-day cycle of bevacizumab 10 mg/kg IV q2w and temozolomide 150 to 200 mg/m\^2 daily in the first 5 days of each cycle. The participants will then enter the Monotherapy Phase where they will receive bevacizumab 15 mg/kg IV q3w until disease progression/unacceptable toxicity.

Group Type EXPERIMENTAL

Bevacizumab

Intervention Type DRUG

10 mg/kg intravenously q2w in the Concurrent and Maintenance Phases. 15 mg/kg intravenously q3w in the Monotherapy Phase.

Temozolomide

Intervention Type DRUG

75 mg/m\^2 once daily for 6 weeks, followed by 150-200 mg/m\^2 once daily on days 1-5 of six 4 week cycles.

Radiation therapy

Intervention Type RADIATION

30 fractions of 2 Gy delivered on days 1-5 per week for 6 weeks.

Placebo + RT + Temozolomide

In the Concurrent Phase participants will receive radiotherapy in daily fractions of 2 Gy to be given 5 days per week for 6 weeks and temozolomide 75 mg/m\^2 daily from the first day to the last day of radiotherapy (it may continue for a maximum of 49 days in case of delay to the end of radiation therapy) and placebo IV every 2 weeks for 6 weeks. There will be a 4 week treatment break. Participants will then enter the Maintenance Phase where they will receive six 28-day cycle of placebo IV q2w and temozolomide 150 to 200 mg/m\^2 daily in the first 5 days of each cycle. The participants will then enter the Monotherapy Phase where they will receive placebo IV q3w until disease progression/unacceptable toxicity.

Group Type PLACEBO_COMPARATOR

Temozolomide

Intervention Type DRUG

75 mg/m\^2 once daily for 6 weeks, followed by 150-200 mg/m\^2 once daily on days 1-5 of six 4 week cycles.

Radiation therapy

Intervention Type RADIATION

30 fractions of 2 Gy delivered on days 1-5 per week for 6 weeks.

Placebo

Intervention Type DRUG

Intravenously q2w in the Concurrent and Maintenance Phases and q3w in the Monotherapy Phase.

Interventions

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Bevacizumab

10 mg/kg intravenously q2w in the Concurrent and Maintenance Phases. 15 mg/kg intravenously q3w in the Monotherapy Phase.

Intervention Type DRUG

Temozolomide

75 mg/m\^2 once daily for 6 weeks, followed by 150-200 mg/m\^2 once daily on days 1-5 of six 4 week cycles.

Intervention Type DRUG

Radiation therapy

30 fractions of 2 Gy delivered on days 1-5 per week for 6 weeks.

Intervention Type RADIATION

Placebo

Intravenously q2w in the Concurrent and Maintenance Phases and q3w in the Monotherapy Phase.

Intervention Type DRUG

Other Intervention Names

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Avastin

Eligibility Criteria

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Inclusion Criteria

* newly diagnosed glioblastoma
* World Health Organization (WHO) performance status less than or equal to (\<=2)
* stable or decreasing corticosteroid dose within 5 days prior to randomization

Exclusion Criteria

* evidence of recent hemorrhage on postoperative magnetic resonance imaging (MRI) of brain
* any prior chemotherapy or immunotherapy for glioblastomas and low grade astrocytomas
* any prior radiotherapy to brain
* clinically significant cardiovascular disease
* history of greater than or equal to (\>=) grade 2 hemoptysis within 1 month prior to randomization
* previous centralized screening for Methylguanine-DNA methyltransferase (MGMT) status for enrollment into a clinical trial
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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University of Alabama At Birmingham; Neuro-Oncology

Birmingham, Alabama, United States

Site Status

UCLA

Los Angeles, California, United States

Site Status

University of Colorado

Aurora, Colorado, United States

Site Status

Moffitt Cancer Center

Tampa, Florida, United States

Site Status

Oncology-Evanston Nthwest Healthcare Kellogg Cancer Care Ctr

Evanston, Illinois, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Hatton Research Institutes

Cincinnati, Ohio, United States

Site Status

Sarah Cannon Cancer Center and Research Institute

Nashville, Tennessee, United States

Site Status

University of Virgina

Charlottesville, Virginia, United States

Site Status

Prince of Wales Hospital; Department of Medical Oncology

Randwick, New South Wales, Australia

Site Status

North Shore Private Hospital; Northern Specialist Centre

St Leonards, New South Wales, Australia

Site Status

Royal North Shore Hospital; Department of Medical Oncology

St Leonards, New South Wales, Australia

Site Status

Princess AleXandra Hospital; Department of Medical Oncology

Woolloongabba, Queensland, Australia

Site Status

Calvary North Adelaide; North Adeliade Oncology Centre

North Adelaide, South Australia, Australia

Site Status

Royal Melbourne Hospital; Hematology and Medical Oncology

Parkville, Victoria, Australia

Site Status

Sir Charles Gairdner Hospital

Nedlands, Western Australia, Australia

Site Status

Clin Univ de Bxl Hôpital Erasme

Brussels, , Belgium

Site Status

Cliniques Universitaires St-Luc

Brussels, , Belgium

Site Status

UZ Antwerpen

Edegem, , Belgium

Site Status

AZ Sint Lucas (Sint Lucas)

Ghent, , Belgium

Site Status

CHU Sart-Tilman

Liège, , Belgium

Site Status

AZ Delta (Campus Wilgenstraat)

Roeselare, , Belgium

Site Status

Tom Baker Cancer Centre-Calgary

Calgary, Alberta, Canada

Site Status

Cross Cancer Institute ; Dept of Medical Oncology

Edmonton, Alberta, Canada

Site Status

BC Cancer Agency, Vancouver Clinic; Dept. of Medical Oncology

Vancouver, British Columbia, Canada

Site Status

CancerCare Manitoba; Neuro-Oncology

Winnipeg, Manitoba, Canada

Site Status

Hamilton Health Sciences - Juravinski Cancer Centre

Hamilton, Ontario, Canada

Site Status

Cancer Centre of Southeastern Ontario; Kingston General Hospital

Kingston, Ontario, Canada

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

Ottawa Hospital Regional Cancer Centre; Neuro-Oncology

Ottawa, Ontario, Canada

Site Status

Sunnybrook Odette Cancer Centre

Toronto, Ontario, Canada

Site Status

Princess Margaret Hospital; Pencer Brain Tumour Centre, 18-727

Toronto, Ontario, Canada

Site Status

Hopital Notre-Dame

Montreal, Quebec, Canada

Site Status

McGill University; Montreal Neurological Institute; Oncology

Montreal, Quebec, Canada

Site Status

Chuq - Hopital Hotel Dieu de Quebec

Québec, Quebec, Canada

Site Status

Saskatoon Cancer Centre; Uni of Saskatoon Campus

Saskatoon, Saskatchewan, Canada

Site Status

Aalborg Universitetshospital, Klinik Kirurgi-Kræft, Onkologisk afd.

Aalborg, , Denmark

Site Status

Righospitalet, Hæmatologisk Klinik

København Ø, , Denmark

Site Status

Odense Universitetshospital, Onkologisk Afdeling R

Odense, , Denmark

Site Status

Hopital Avicenne; Rhumatologie

Bobigny, , France

Site Status

Hopital Saint Andre; Département de Radiothérapie Et D'Oncologie Médicale

Bordeaux, , France

Site Status

Institut Bergonie; Gastro Enterologie Oncologie

Bordeaux, , France

Site Status

Hopital neurologique Pierre Wertheimer - CHU Lyon; Neurologie

Bron, , France

Site Status

Centre Jean Perrin; Hopital De Jour

Clermont-Ferrand, , France

Site Status

Hopital Beaujon; Oncologie

Clichy, , France

Site Status

Centre Georges François Leclerc

Dijon, , France

Site Status

Hopital de La Timone - CHU de Marseille; Service de neuro-oncologie - Hôpital Adultes - 12ème étage

Marseille, , France

Site Status

Centre Val Aurelle Paul Lamarque; Medecine B3

Montpellier, , France

Site Status

Hôpital Central; Departement de Neuro-Oncologie

Nancy, , France

Site Status

Hopital Pitié Salpétrière - CHU; Service de neurologie 2 - Mazarin

Paris, , France

Site Status

Universitätsklinikum "Carl Gustav Carus"; Klinik und Poliklinik für Neurochirurgie

Dresden, , Germany

Site Status

Justus-Liebig-Universität Giessen; Neurochirurgische Klinik

Giessen, , Germany

Site Status

Universitatsklinikum Hamburg-Eppendorf; Klinik und Poliklinik fur Neurochirurgie

Hamburg, , Germany

Site Status

Universitatsklinikum Heidelberg; Abteilung Neuroonkologie

Heidelberg, , Germany

Site Status

Ärztehaus Velen

Ibbenbühren, , Germany

Site Status

Klinikum der Johannes Gutenberg Uni Mainz; Studienz. Neurologie, Klinik und Poliklinik Neurologie

Mainz, , Germany

Site Status

Uni Klinikum München - Großhardern; Med. Klinik U. Poliklinik III - Abt. Onkologie u. Hämatologie

München, , Germany

Site Status

Univ General Hosp Heraklion; Medical Oncology

Heraklion, , Greece

Site Status

University Hospital of Larissa; Oncology

Larissa, , Greece

Site Status

Papageorgiou General Hospital; Medical Oncology

Thessaloniki, , Greece

Site Status

Dr Stephen Yau; Clinical oncology

Hong Kong, , Hong Kong

Site Status

Hong Kong Sanatorium & Hospital; Comprehensive Oncology Centre

Hong Kong, , Hong Kong

Site Status

Queen Mary Hospital; Microbiology Dept.

Hong Kong, , Hong Kong

Site Status

Magyar Honvedseg Egeszsegugyi Kozpont

Budapest, , Hungary

Site Status

Borsod-Abaúj-Zemplén Megyei Kórház és Egyetemi Oktató Kórház; Neurosurgery

Miskolc, , Hungary

Site Status

Pécsi Tudományegyetem Áok; Onkoterapias Intezet

Pécs, , Hungary

Site Status

Rambam Medical Center; Oncology

Haifa, , Israel

Site Status

Hadassah Hebrew University Hospital; Leslie and Michael Gaffin Center for Neuro-Oncology

Jerusalem, , Israel

Site Status

Rabin MC; Davidof Center - Oncology Institute

Petah Tikva, , Israel

Site Status

Chaim Sheba MC; Pediatric Hematology Oncology

Tel Litwinsky, , Israel

Site Status

Ausl Di Bologna-Ospedale Bellaria;U.O. Oncologia Medica

Bologna, Emilia-Romagna, Italy

Site Status

Ospedale Bufalini

Forlì, Emilia-Romagna, Italy

Site Status

Fondazione IRCCS Istituto Neurologico C. Besta; Neuro-oncologia Sperimentale e Terapia Genica

Milan, Lombardy, Italy

Site Status

Azienda Ospedaliera Le Molintte di Torino; Dipartimento Di Neurologia - Oncologia

Turin, Piedmont, Italy

Site Status

Az. Osp. S. Maria; Dept. Di Oncologia Medica

Terni, Umbria, Italy

Site Status

Ospedale di Treviso, Universita di Padova; Neurosurgery Dept

Treviso, Veneto, Italy

Site Status

Hiroshima University Hospital; Neurosurgery

Hiroshima, , Japan

Site Status

Tsukuba University Hospital; Neurology

Ibaraki, , Japan

Site Status

Kumamoto University Hospital; Neurosurgery

Kumamoto, , Japan

Site Status

Kitano Hospital; Neurosurgery

Osaka, , Japan

Site Status

Saitama Medical University International Medical Center; Clinical and Medical Oncology

Saitama, , Japan

Site Status

National Cancer Center Hospital; Neurosurgery

Tokyo, , Japan

Site Status

Komagome Hospital; Neurosurgery

Tokyo, , Japan

Site Status

Kyorin University Hospital; Neurosurgery

Tokyo, , Japan

Site Status

VU MEDISCH CENTRUM; Dept. of Medical Oncology

Amsterdam, , Netherlands

Site Status

Catharina Ziekenhuis; Dept of Internal Medicin

Eindhoven, , Netherlands

Site Status

Utrecht University Medical Centre; Dept of Medical Oncology and UPC

Utrecht, , Netherlands

Site Status

Auckland city hospital; Auckland Regional Cancer Centre and Blood Service

Auckland, , New Zealand

Site Status

Christchurch Hospital; Dept of Oncology

Christchurch, , New Zealand

Site Status

Waikato Hospital; Regional Cancer Center

Hamilton, , New Zealand

Site Status

Bialostockie Centrum Onkologii; Oddzial Onkologii Klinicznej

Bialystok, , Poland

Site Status

Centrum Onkologii;Im. Franciszka Lukaszczyka;Onkologii

Bydgoszcz, , Poland

Site Status

Samodzielny Publiczny Szpital Kliniczny nr 4 w Lublinie; Klinika Neurochirurgii i Neurochirurgii Dzi

Lublin, , Poland

Site Status

IPO de Coimbra; Servico de Oncologia Medica

Coimbra, , Portugal

Site Status

IPO de Lisboa; Servico de Neurologia

Lisbon, , Portugal

Site Status

Hospital de Santa Maria; Servico de Oncologia Medica

Lisbon, , Portugal

Site Status

Hospital de Sao Joao; Servico de Oncologia

Porto, , Portugal

Site Status

Institut Oncologic Prof. Dr. Alexandru Trestioreanu; Departament Radioterapie

Bucharest, , Romania

Site Status

Institut Oncologic Ion Chiricuta; Departament Radioterapie

Cluj-Napoca, , Romania

Site Status

Spital Clinic Judetean Mures; Oncologie

Târgu Mureş, , Romania

Site Status

N.N.Burdenko Main Military Clinical Hospital; Oncology Dept

Moscow, , Russia

Site Status

Russian Research Oncology Center n.a. N.N. Blokhin of the RAMS; Department of Neurosurgery

Moscow, , Russia

Site Status

Scientific Research Neurosurgery Institute; Dept. of Neurooncology

Moscow, , Russia

Site Status

Institution of Higher Professional Learning Military; Neurooncology

Saint Petersburg, , Russia

Site Status

Pusan National University Hospital; Neuro Sugery

Busan, , South Korea

Site Status

Kyungpook National University Hosital; Neuro Sugery

Daegu, , South Korea

Site Status

National Cancer Centre; Neurosurgery Dept

Goyang-si, , South Korea

Site Status

Chonnam National University Hwasun Hospital

Jeollanam-do, , South Korea

Site Status

Seoul National Uni Hospital; Dept. of Internal Medicine/Hematology/Oncology

Seoul, , South Korea

Site Status

Asan Medical Center; Medical Oncology

Seoul, , South Korea

Site Status

Yonsei University Severance Hospital; Medical Oncology

Seoul, , South Korea

Site Status

Samsung Medical Center; Neurosurgery Department

Seoul, , South Korea

Site Status

Hospital Clínic i Provincial; Servicio de Hematología y Oncología

Barcelona, , Spain

Site Status

Institut Catala d Oncologia Hospital Duran i Reynals

Barcelona, , Spain

Site Status

Hospital Universitari Germans Trias i Pujol; Servicio de Oncologia

Barcelona, , Spain

Site Status

Hospital Ramon y Cajal; Servicio de Oncologia

Madrid, , Spain

Site Status

Hospital Universitario La Paz; Servicio de Oncologia

Madrid, , Spain

Site Status

Hospital Regional Universitario Carlos Haya; Servicio de Oncologia

Málaga, , Spain

Site Status

Hospital Clinico Universitario de Valencia; Servicio de Onco-hematologia

Valencia, , Spain

Site Status

Sahlgrenska Universitetssjukhuset; Jubileumskliniken

Gothenburg, , Sweden

Site Status

Skånes University Hospital, Skånes Department of Onclology

Lund, , Sweden

Site Status

Norrlands Universitetssjukhus; Cancer Centrum

Umeå, , Sweden

Site Status

Akademiska sjukhuset, Onkologkliniken

Uppsala, , Sweden

Site Status

HUG; Oncologie

Geneva, , Switzerland

Site Status

Queen Elizabeth Medical Centre; Neurosurgery

Birmingham, , United Kingdom

Site Status

Bristol Haematology and Oncology Centre

Bristol, , United Kingdom

Site Status

The Royal Marsden NHS Foundation Trust; Oncology

London, , United Kingdom

Site Status

The Clatterbridge Cancer Ctr For Oncolgy

Metropolitan Borough of Wirral, , United Kingdom

Site Status

Northern Centre for Cancer Care;Oncology

Newcastle upon Tyne, , United Kingdom

Site Status

Nottingham City Hospital; Dept of Haematology

Nottingham, , United Kingdom

Site Status

Queen's Hospital; Oncology

Romford, , United Kingdom

Site Status

Weston Park Hospital; Cancer Clinical Trials Centre

Sheffield, , United Kingdom

Site Status

Royal Marsden Hospital; Dept of Medical Oncology

Sutton, , United Kingdom

Site Status

Countries

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United States Australia Belgium Canada Denmark France Germany Greece Hong Kong Hungary Israel Italy Japan Netherlands New Zealand Poland Portugal Romania Russia South Korea Spain Sweden Switzerland United Kingdom

References

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Seliger C, Oppong FB, Lefranc F, Chinot O, Stupp R, Nabors B, Gorlia T, Weller M; EORTC Brain Tumor Group. Association of antidepressant drug use with outcome of patients with glioblastoma. Int J Cancer. 2023 Apr 1;152(7):1348-1359. doi: 10.1002/ijc.34344. Epub 2022 Nov 17.

Reference Type DERIVED
PMID: 36346112 (View on PubMed)

Hagiwara A, Schlossman J, Shabani S, Raymond C, Tatekawa H, Abrey LE, Garcia J, Chinot O, Saran F, Nishikawa R, Henriksson R, Mason WP, Wick W, Cloughesy TF, Ellingson BM. Incidence, molecular characteristics, and imaging features of "clinically-defined pseudoprogression" in newly diagnosed glioblastoma treated with chemoradiation. J Neurooncol. 2022 Sep;159(3):509-518. doi: 10.1007/s11060-022-04088-3. Epub 2022 Jul 17.

Reference Type DERIVED
PMID: 35842871 (View on PubMed)

Jiguet-Jiglaire C, Boissonneau S, Denicolai E, Hein V, Lasseur R, Garcia J, Romain S, Appay R, Graillon T, Mason W, Carpentier AF, Brandes AA, Ouafik L', Wick W, Baaziz A, Gigan JP, Arguello RJ, Figarella-Branger D, Chinot O, Tabouret E. Plasmatic MMP9 released from tumor-infiltrating neutrophils is predictive for bevacizumab efficacy in glioblastoma patients: an AVAglio ancillary study. Acta Neuropathol Commun. 2022 Jan 3;10(1):1. doi: 10.1186/s40478-021-01305-4.

Reference Type DERIVED
PMID: 34980260 (View on PubMed)

Chinot OL, Nishikawa R, Mason W, Henriksson R, Saran F, Cloughesy T, Garcia J, Revil C, Abrey L, Wick W. Upfront bevacizumab may extend survival for glioblastoma patients who do not receive second-line therapy: an exploratory analysis of AVAglio. Neuro Oncol. 2016 Sep;18(9):1313-8. doi: 10.1093/neuonc/now046. Epub 2016 Mar 22.

Reference Type DERIVED
PMID: 27006178 (View on PubMed)

Saran F, Chinot OL, Henriksson R, Mason W, Wick W, Cloughesy T, Dhar S, Pozzi E, Garcia J, Nishikawa R. Bevacizumab, temozolomide, and radiotherapy for newly diagnosed glioblastoma: comprehensive safety results during and after first-line therapy. Neuro Oncol. 2016 Jul;18(7):991-1001. doi: 10.1093/neuonc/nov300. Epub 2016 Jan 24.

Reference Type DERIVED
PMID: 26809751 (View on PubMed)

Taphoorn MJ, Henriksson R, Bottomley A, Cloughesy T, Wick W, Mason WP, Saran F, Nishikawa R, Hilton M, Theodore-Oklota C, Ravelo A, Chinot OL. Health-Related Quality of Life in a Randomized Phase III Study of Bevacizumab, Temozolomide, and Radiotherapy in Newly Diagnosed Glioblastoma. J Clin Oncol. 2015 Jul 1;33(19):2166-75. doi: 10.1200/JCO.2014.60.3217. Epub 2015 May 26.

Reference Type DERIVED
PMID: 26014298 (View on PubMed)

Chinot OL, Wick W, Mason W, Henriksson R, Saran F, Nishikawa R, Carpentier AF, Hoang-Xuan K, Kavan P, Cernea D, Brandes AA, Hilton M, Abrey L, Cloughesy T. Bevacizumab plus radiotherapy-temozolomide for newly diagnosed glioblastoma. N Engl J Med. 2014 Feb 20;370(8):709-22. doi: 10.1056/NEJMoa1308345.

Reference Type DERIVED
PMID: 24552318 (View on PubMed)

Chinot OL, Macdonald DR, Abrey LE, Zahlmann G, Kerloeguen Y, Cloughesy TF. Response assessment criteria for glioblastoma: practical adaptation and implementation in clinical trials of antiangiogenic therapy. Curr Neurol Neurosci Rep. 2013 May;13(5):347. doi: 10.1007/s11910-013-0347-2.

Reference Type DERIVED
PMID: 23529375 (View on PubMed)

Other Identifiers

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2008-006146-26

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

BO21990

Identifier Type: -

Identifier Source: org_study_id