Efficacy and Safety Study of DP-b99 in Treating Acute Ischemic Stroke

NCT ID: NCT00893867

Last Updated: 2012-10-24

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

446 participants

Study Classification

INTERVENTIONAL

Study Start Date

2009-12-31

Study Completion Date

2012-04-30

Brief Summary

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The purpose of this trial is to determine if intravenous administration of the metal ion trapping agent DP-b99 up to 9 hours following acute ischemic stroke onset, and then for 3 additional days (4 consecutive days in total) is effective in improving long term outcome. Patients will be followed up for 3 months after the stroke.

Detailed Description

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This will be a randomized, double-blind, placebo-controlled, multicenter, multi-national, parallel-arm, pivotal study comparing a placebo group to a DP-b99 group treated with intravenous 1.0 mg/kg/d for 4 consecutive days, in acute ischemic stroke patients with an entry National Institutes of Health Stroke Scale (NIHSS) score of 10-16 and a clinical syndrome that includes at least 1 of the following: language dysfunction, visual field defect or Extinction and Inattention (formerly Neglect) (as reflected by at least 1 point on any of the corresponding items of the NIHSS: 9, 3 or 11). An interim analysis for futility will be performed after Day 90 (or last available observation) primary endpoint data have been collected on about 45% of subjects planned to be enrolled. Clinical trial material (CTM) will be administered within 9 hours after the onset of acute ischemic stroke symptoms. Subjects will be randomized at a ratio of 1:1 to receive either DP-b99 or placebo. A data and safety monitoring board (DSMB) will assess the accumulating safety data periodically and will oversee the interim futility analysis.

Conditions

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Acute Ischemic Stroke

Keywords

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acute ischemic stroke neuroprotective agent

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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DP-b99

Group Type EXPERIMENTAL

DP-b99

Intervention Type DRUG

1mg/kg/day over 4 consecutive days given intravenously and initiated up to 9 hours following acute stroke onset.

Mannitol

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

1mg/kg/day over 4 consecutive days given intravenously and initiated up to 9 hours following acute stroke onset.

Interventions

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DP-b99

1mg/kg/day over 4 consecutive days given intravenously and initiated up to 9 hours following acute stroke onset.

Intervention Type DRUG

Placebo

1mg/kg/day over 4 consecutive days given intravenously and initiated up to 9 hours following acute stroke onset.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. M or F age 18 - 85, inclusive
2. Suffered an acute, likely hemispheric, ischemic stroke, defined as acute, focal, neurological deficit(s), secondary to a presumed vascular event, which must include at least one of the following components (as reflected by at least 1 point on any of the corresponding items of the NIHSS: 3, 9 or 11):

* Visual
* Best Language
* Extinction and Inattention (formerly Neglect)
3. Suffered the onset of an acute ischemic stroke that can be evaluated and treatment initiated within 9 hours after the onset of acute ischemic stroke symptoms.
4. Screening NIHSS score of 10 to 16, inclusive
5. Readily accessible peripheral venous access for clinical trial material (CTM) administration and blood sampling
6. Ability to understand the requirements of the study and be willing to provide written informed consent as evidenced by signature on an informed consent document approved by an institutional review board or independent ethics committee, and agree to abide by the study restrictions and return for the required assessments.
7. Provided written authorization for use and disclosure of protected health information in accordance with the Health Insurance Portability and Accountability Act in the United States and the Personal Information Protection and Electronic Documents Act in Canada

Exclusion Criteria

1. An intracerebral or subarachnoid hemorrhage per screening/baseline computerized tomography scan or susceptibility-weighted magnetic resonance imaging
2. A candidate for either:

1. thrombolytic therapy, or have been treated with thrombolytic therapy for the current stroke
2. mechanical thromboembolectomy, or have been treated with mechanical thromboembolectomy for the current stroke
3. Delirious, comatose or stuporous or demented, or having a mental impairment that in the investigator's opinion renders the subject incapable to participate in the study
4. Have seizure(s) anytime from stroke onset to screening/baseline NIHSS evaluation
5. Neurological or non-neurological comorbidities that in the investigator's opinion may lead, independent of the current stroke, to further deterioration in the subject's neurological status during the trial period, or may render the study's neurological assessments inconclusive for the purpose of evaluating solely the stroke's effects
6. Likely to undergo a procedure involving cardiopulmonary bypass during the study period
7. Suffered a myocardial infarction in the last 90 days
8. Any medical condition that in the investigator's opinion may threaten the subject's ability to complete the study (e.g., concurrent significant or life-threatening diseases, such as malignancies or end stage organ failure)
9. Rapid spontaneous improvement of neurological signs during screening/baseline assessments
10. Premorbid neurological deficits and functional limitations assessed by a pre-stroke Modified Rankin Scale score of \> 1
11. Suffered a stroke within 90 days of the screening/baseline assessments that is either diagnostically confirmed or assumed to be in the same cerebral territory as is the current acute stroke
12. Either severe hypertension or hypotension, as measured by at least 2 consecutive supine measurements taken 10 minutes apart prior to randomization.
13. Significant current renal or hepatic disease(s): a serum creatinine concentration of \>2.5 mg/dL; alanine aminotransferase, aspartate aminotransferase, or gamma-glutamyl transferase values that are three times greater than the upper limit of normal.
14. Have a platelet count of \<100,000/mm3 or, for patients on oral anticoagulants at study entry, INR of \>4
15. Female of childbearing potential who is not willing to use adequate and effective birth control measures for the duration of the trial. Effective birth control measures include hormonal contraception, a barrier method such as a diaphragm, intrauterine device and/or condom with spermicide
16. Positive urine pregnancy test at screening/baseline or be a lactating female
17. Currently dependent on, or abusing, alcohol or one or more of the following: sympathomimetic amines, cannabis, cocaine, hallucinogens, inhalants, opioids, phencyclidine, sedatives and hypnotics
18. Received an investigational drug or product or participated in an investigational drug study within a period of 30 days prior to receiving study medication or have previously participated in a clinical trial involving DP-b99
19. Severe anemia as measured by a hemoglobin value of \< 7 g/dl.
20. In a dependent relationship with the physician or the study sponsor.
21. Known hypersensitivity to any component of the investigational product.
Minimum Eligible Age

18 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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D-Pharm Ltd.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Ashfaq Shuaib, MD

Role: PRINCIPAL_INVESTIGATOR

University of Alberta Hospital, Edmonton, Canada

Vasco Salgado, MD

Role: PRINCIPAL_INVESTIGATOR

Hospital Professor Doutor Fernando Fonseca, EPE, Amadora, Portugal

Philippe Lyrer, Prof. Dr.

Role: PRINCIPAL_INVESTIGATOR

Universitätsspital Basel, Neurologie, Basel, Switzerland

Tobien Schreuder, MD

Role: PRINCIPAL_INVESTIGATOR

Atrium MC Parkstad, Heerlen, Netherlands

Maria S Rocha, MD

Role: PRINCIPAL_INVESTIGATOR

Hospital Santa Marcelina, Sao Paulo, Brasil

Hugues Chabriat, Prof.

Role: PRINCIPAL_INVESTIGATOR

Hôpital Lariboisière - Service Neurologie, Paris, France

Locations

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University Hospital Nitra

Nitra, , Slovakia

Site Status

Hospital un Poliklinic

Spišská Nová Ves, , Slovakia

Site Status

Faculty Hospital Trnava

Trnava, , Slovakia

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Research Center of Southern California

Oceanside, California, United States

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Associated Neurologists, P.C.

Danbury, Connecticut, United States

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Memorial Health University Medical Center

Savannah, Georgia, United States

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The University of Kentucky The Methodist Hospital

Lexington, Kentucky, United States

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University of Louisville, Kentucky Neuroscience Research

Louisville, Kentucky, United States

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Tufts Medical Center

Boston, Massachusetts, United States

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Capital Health Regional Medical Center Neuroscience Institute

Trenton, New Jersey, United States

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Presbitarian Hospital

Charlotte, North Carolina, United States

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St. Elizabeth's Medical Center

Youngstown, Ohio, United States

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Legacy Meridian Park Medical Center

Tualatin, Oregon, United States

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Thomas Jefferson University

Philadelphia, Pennsylvania, United States

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The Methodist Hospital

Houston, Texas, United States

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Carilion Clinic

Roanoke, Virginia, United States

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Medizinische Universität Innsbruck

Innsbruck, , Austria

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Landeskrankenhaus Klagenfurt

Klagenfurt, , Austria

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Abt. Neurologie und Psychiatrie

Linz, , Austria

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LKH St. Pölten Department of Neurology

Sankt Pölten, , Austria

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Santa Casa de Misericordia de Belo Horizonte Departamento de Neurologia

Belo Horizonte, , Brazil

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Hospital de Clinicas de Porto Alegre

Porto Alegre, , Brazil

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Hospital Moinhos de Vento

Porto Alegre, , Brazil

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Hospital Mãe de Deus

Porto Alegre, , Brazil

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Santa Casa de Misericórdia de Porto Alegre Policlinica Santa Clara Sala de Neurologia

Porto Alegre, , Brazil

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Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto Unidade de Emergência Centro de Estudos

Ribeirão Preto, , Brazil

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Hospital São José de Joinville

Santa Catarina, , Brazil

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Hospital Santa Marcelina

São Paulo, , Brazil

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UNIFESP

São Paulo, , Brazil

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Hamilton Health Sciences Centre

Hamilton, Ontario, Canada

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Grey Nun's Community Hospital

Edmonton, , Canada

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University of Alberta Hospital

Edmonton, , Canada

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Hamilton Health Sciences Centre

Hamilton, , Canada

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Kingston General Hospital

Kingston, , Canada

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Chinook Regional Hospital

Lethbridge, , Canada

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CHA- Hôpital de l'Enfant-Jésus

Québec, , Canada

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University Hospital Brno

Brno, , Czechia

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University Hospital Hradec Kralove, Clinic of Neurology

Hradec Králové, , Czechia

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Hospital Jihlava Clinic of Neurology

Jihlava, , Czechia

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Hospital Vítkovice Clinic of Neurology

Ostrava, , Czechia

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County Hospital Pardubice Clinic of Neurology

Pardubice, , Czechia

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Clinic of Neurology, Stroke Center, Charles University

Prague, , Czechia

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University Hospital Kralovske Vinohrady

Prague, , Czechia

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University Hospital Motol Clinic of Neurology

Prague, , Czechia

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CHU Jean Minjoz Besançon

Besançon, , France

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Hopital Pellegrin-Tripode

Bordeaux, , France

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CHU Henri Mondor

Créteil, , France

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Hopital Gui de Chauliac

Montpellier, , France

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Hôpital Bichat

Paris, , France

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Hôpital Lariboisière - Service Neurologie

Paris, , France

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Hôpital Saint Jean

Perpignan, , France

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Ärztlicher Direktor Neurologische Klinik, Neurologische Klink GmbH der Rhoen-Klinikum AG

Bad Neustadt / Saale, , Germany

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Marien-Krankenhaus gGmbH, Abteilung für Neurologie

Bergisch Gladbach, , Germany

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DRK Kliniken Berlin, Klinik fuer Neurologie

Berlin, , Germany

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Vivantes Klinikum Neukölln, Klinik für Neurologie, Stroke Unit

Berlin, , Germany

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Klinikum Bremen-Mitte

Bremen, , Germany

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Klinikum Bremerhaven-Reinkenheide gGmbH, Neurologische Klinik

Bremerhaven, , Germany

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Klinikum Chemnitz GmbH Chefarzt Klinik für Neurologie

Chemnitz, , Germany

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Klinikum Köln Merheim, Department of Neurology

Cologne, , Germany

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Helios Klinikum Erfurt GmbH

Erfurt, , Germany

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Universitätsklinikum Erlangen, Neurologische klinik

Erlangen, , Germany

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Universitätsklinikum Essen, Klinik und Poliklinik für Neurologie

Essen, , Germany

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Neurologische Universitätsklinik Freiburg, Neurozentrum

Freiburg im Breisgau, , Germany

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Klinikum Fulda, Neurologische Klinik

Fulda, , Germany

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Evangelische Kliniken Gelsenkirchen GmbH Klinik für Neurologie und Klinische Neurophysiologie

Gelsenkirchen, , Germany

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Georg-August-Universitat Gottingen Neurologische Klinik

Göttingen, , Germany

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Ernst Moritz Arndt University

Grifswald, , Germany

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Askepios Klinik Altona

Hamburg, , Germany

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Askepios Klinik Heidberg

Hamburg, , Germany

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Universitätsklinikum Leipzig AöR, Klinik und Poliklinik für Neurologie

Leipzig, , Germany

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Klinikum der Otto-von-Guericke-Universität Magdeburg, Neurologische Universitätsklinik

Magdeburg, , Germany

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Johannes Gutenberg Universitat, Klinik und Poliklinik fur Neurologie

Mainz, , Germany

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Klinikum 1 Minden, Neurologische Klinik

Minden, , Germany

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Universität Rostock Chefarzt Abteilung Neurologie

Rostock, , Germany

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ASKLEPIOS Fachklinikum Teupitz

Teupitz, , Germany

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Krankenhaus der Bramherzigen Brüder

Trier, , Germany

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Universitätsklinikum Ulm, Abteilung für Neurologie im RKU

Ulm, , Germany

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Heinrich Braun Klinikum Zwickau

Zwickau, , Germany

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Fővárosi Önkormányzat Péterfy Sándor utcai Kórház- Rendelőintézet és Baleseti Központ

Budapest, , Hungary

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Állami Egészségügyi Központ

Budapest, , Hungary

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Kenezy Korhaz Rendelointezet Egezsegugyi Szolgaltato Nonprofit Kft.

Debrecen, , Hungary

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University of Debrecen, Medical and Health Science Center

Debrecen, , Hungary

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Aladár Petz County Teaching Hospital

Győr, , Hungary

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PM Flór Ferenc County Hospital

Kistarcsa, , Hungary

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Borsod-Abaúj-Zemplén County Hospital Miskolc

Miskolc, , Hungary

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Pécsi Tudományegyetem Klinikai Központ

Pécs, , Hungary

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Zala Megyei Kórház

Zalaegerszeg, , Hungary

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Bnai Zion Medical Center

Haifa, , Israel

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Neurological Dept. Edith Wolfson Medical Center

Holon, , Israel

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Meir Medical Center

Kfar Saba, , Israel

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Sourasky Medical Center

Tel Aviv, , Israel

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Chaim Sheba Medical Center

Tel Litwinsky, , Israel

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Ospedale Regionale Valle d'Aosta

Aosta, , Italy

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Dipartimento di Neuroscienze, Ospedale di Brotzu

Cagliari, , Italy

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Ospedale di Circolo di Varese

Lombardia, , Italy

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Istituto Scientifico San Raffaele - Stroke Unit

Milan, , Italy

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Istituto Neurologico C. Mondino

Pavia, , Italy

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Università di Perugia, Division of Internal and Cardiovascular Medicine - Stroke Unit

Perugia, , Italy

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Presidio Ospedaliero di Piacenza

Piacenza, , Italy

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Azienda Ospedaliera Sant'Andrea, Stroke Unit

Rome, , Italy

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Istituto Patologia Generale U.C.S.C

Rome, , Italy

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U.O.C. Stroke Unit

Rome, , Italy

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Università di Roma "La Sapienza" - Stroke Unit

Rome, , Italy

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Azienda Ospedaliera Universitaria "Santa Maria della Misericordia" Stroke Unit

Udine, , Italy

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Catharina Ziekenhuis Neurologie

Eindhoven, , Netherlands

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Medisch Spectrum Twente Hoofd Afdeling Vasculaire Neurologie

Enschede, , Netherlands

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Atrium MC Parkstad

Heerlen, , Netherlands

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Isala Klinieken Ploikliniek Neurologie

Zwolle, , Netherlands

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Pomerania Traumatology Center, Regional Specialist Hospital im. Nicolaus Copernicus

Gdansk, , Poland

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Medical University of Lublin, Department of Neurology, Stroke Unit

Lublin, , Poland

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Samodzielny Publiczny Zespol Zakladow Opieki Zdrowotnej w Sandomierzu

Sandomierz, , Poland

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Szpital Powiatowy im. Marii Curie - Skłodowskiej w Skarżysku-Kamiennej

Skarżysko-Kamienna, , Poland

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Wojewodzki Szpital Specjalistyczny Nr 1 im. Prof. Jozefa Gasinskiego

Tychy, , Poland

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Instytut Psychiatrii i Neurologii Oddział Neurologiczny z Pododdziałem Udarowym

Warsaw, , Poland

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Medical University of Warsaw, Department of Neurology

Warsaw, , Poland

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Szpital Wolski im. dr Anny Gostyńskiej Samodzielny Publiczny Zakład Opieki Zdrowotnej, Oddział Neurologii

Warsaw, , Poland

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Wojskowy Instytut Medyczny, Oddział Neurologii

Warsaw, , Poland

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Hospital Professor Doutor Fernando Fonseca, EPE

Amadora, , Portugal

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Centro Hospitalar de Coimbra EPE

Coimbra, , Portugal

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Hospitais da Universidadde de Coimbra, EPE

Coimbra, , Portugal

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Centro de Estudos Egas Moniz - Hospital de Santa Maria

Lisbon, , Portugal

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Hospital de São Sebastião, EPE

Santa Maria da Feira, , Portugal

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Neurology Clinic, Faculty Hospital in Martin

Martin, , Slovakia

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Neurology dept.,Hospital Zilina

Žilina, , Slovakia

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Fichmed

Bloemfontein, , South Africa

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Constantiaberg Medi-clinic

Cape Town, , South Africa

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Union Hospital

Gauteng, , South Africa

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Helderberg Research Institute

Western Cape, , South Africa

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Triervlei Trial Centre

Western Cape, , South Africa

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Clinical Projects Research

Worcester, , South Africa

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Dong-A Medical Center

Busan, , South Korea

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Inje University BUSAN Paik Hospital

Busan, , South Korea

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Inje University ILSAN Paik Hospital

Goyang, , South Korea

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Chonnam National University Hospital

Gwangju, , South Korea

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Inha University Hospital

Incheon, , South Korea

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Seoul National University Bundang Hospital

Seongnam, , South Korea

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ASAN Medical Center

Seoul, , South Korea

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Severance Hospital

Seoul, , South Korea

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The Catholic University of Korea Seoul St. Mary's hospital

Seoul, , South Korea

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Hospital Universitario de Albacete

Albacete, , Spain

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Hospital De La Santa Ta Creu i Sant Pau

Barcelona, , Spain

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Hospital del Mar

Barcelona, , Spain

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Hospital Germans Triasy Pujol

Barcelona, , Spain

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Hospital Vall D'hebron

Barcelona, , Spain

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Hospital Gregorio Maranon

Madrid, , Spain

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Hospital La Princesa

Madrid, , Spain

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Hospital Ramon y Cajal

Madrid, , Spain

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Hospital Universitario Clinico San Carlos

Madrid, , Spain

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Hospital Universitario La Paz

Madrid, , Spain

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Hospital Clinico Universitario de Santiago

Santiago de Compostela, , Spain

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Consorcio Hospital General Universitario Valencia

Valencia, , Spain

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Hospital Clinico Universitario De Valladolid

Valladolid, , Spain

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Universitätsspital Basel, Neurologie

Basel, , Switzerland

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Universitätsspital Zürich, Klinik für Neurologie

Zurich, , Switzerland

Site Status

Countries

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United States Austria Brazil Canada Czechia France Germany Hungary Israel Italy Netherlands Poland Portugal Slovakia South Africa South Korea Spain Switzerland

References

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Diener HC, Schneider D, Lampl Y, Bornstein NM, Kozak A, Rosenberg G. DP-b99, a membrane-activated metal ion chelator, as neuroprotective therapy in ischemic stroke. Stroke. 2008 Jun;39(6):1774-8. doi: 10.1161/STROKEAHA.107.506378. Epub 2008 Apr 10.

Reference Type BACKGROUND
PMID: 18403736 (View on PubMed)

Rosenberg G, Angel I, Kozak A. Clinical pharmacology of DP-b99 in healthy volunteers: first administration to humans. Br J Clin Pharmacol. 2005 Jul;60(1):7-16. doi: 10.1111/j.1365-2125.2005.02378.x.

Reference Type BACKGROUND
PMID: 15963088 (View on PubMed)

Barkalifa R, Hershfinkel M, Friedman JE, Kozak A, Sekler I. The lipophilic zinc chelator DP-b99 prevents zinc induced neuronal death. Eur J Pharmacol. 2009 Sep 15;618(1-3):15-21. doi: 10.1016/j.ejphar.2009.07.019. Epub 2009 Jul 19.

Reference Type BACKGROUND
PMID: 19622352 (View on PubMed)

Rosenberg G, Bornstein N, Diener HC, Gorelick PB, Shuaib A, Lees K; MACSI investigators. The Membrane-Activated Chelator Stroke Intervention (MACSI) Trial of DP-b99 in acute ischemic stroke: a randomized, double-blind, placebo-controlled, multinational pivotal phase III study. Int J Stroke. 2011 Aug;6(4):362-7. doi: 10.1111/j.1747-4949.2011.00608.x. Epub 2011 Jun 6.

Reference Type BACKGROUND
PMID: 21645269 (View on PubMed)

Rosenberg G, Marshall LS, Caraco Y. The neuroprotective agent DP-b99 does not interact with s-warfarin in vivo despite significant CYP2C9 inhibition in vitro. Basic Clin Pharmacol Toxicol. 2011 Apr;108(4):289-92. doi: 10.1111/j.1742-7843.2010.00654.x. Epub 2010 Dec 16. No abstract available.

Reference Type BACKGROUND
PMID: 21414144 (View on PubMed)

Other Identifiers

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Ptcl-01373

Identifier Type: -

Identifier Source: org_study_id