Randomized, Controlled Study Evaluating CERE-110 in Subjects With Mild to Moderate Alzheimer's Disease

NCT ID: NCT00876863

Last Updated: 2020-12-21

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

49 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-11-30

Study Completion Date

2015-08-13

Brief Summary

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The purpose of this study is to evaluate the potential benefits of CERE-110 in the treatment of Alzheimer's disease. CERE-110 is an experimental drug that is designed to help nerve cells in the brain function better. CERE-110 uses a virus to transfer a gene that makes Nerve Growth Factor (NGF), a protein that may make nerve cells in the brain healthier and protect them from dying. The virus used in CERE-110 does not cause disease in people. CERE-110 has been carefully studied in laboratory animals and is in the early stages of being tested in people.

Fifty patients with mild to moderate Alzheimer's disease will participate in this study. Half of the study subjects will have CERE-110 injected into the brain during a surgical procedure, while the other half will undergo a "placebo" surgery where no medication will be injected. All study participants will be followed for at least two years after surgery.

Detailed Description

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Conditions

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Alzheimer's Disease

Keywords

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Alzheimer's disease Dementia Memory loss Cognitive impairment Nerve growth factor NGF Neurotrophic factors Gene therapy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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CERE-110

CERE-110: Adeno-Associated Virus Delivery of NGF

Group Type EXPERIMENTAL

CERE-110: Adeno-Associated Virus injection Surgery

Intervention Type DRUG

Injecting CERE-110 2.0 X 10\^11 vg into brain during surgical procedure.

Placebo

Placebo Surgery

Group Type SHAM_COMPARATOR

Placebo Surgery

Intervention Type PROCEDURE

Placebo Surgery

Interventions

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CERE-110: Adeno-Associated Virus injection Surgery

Injecting CERE-110 2.0 X 10\^11 vg into brain during surgical procedure.

Intervention Type DRUG

Placebo Surgery

Placebo Surgery

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of mild to moderate Alzheimer's disease
* Approved medications for Alzheimer's disease may be taken if the dose has been stable for 3 months
* A study partner who can attend all study visits
* Good general health
* Medically able to undergo neurosurgery

Exclusion Criteria

* Significant neurological disease other than Alzheimer's disease
* Significant depression or other psychiatric disorder
* Unstable medical conditions
Minimum Eligible Age

55 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Alzheimer's Disease Cooperative Study (ADCS)

OTHER

Sponsor Role collaborator

Sangamo Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Paul S. Aisen, M.D.

Role: STUDY_DIRECTOR

Alzheimer's Disease Cooperative Study (ADCS)

Locations

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University of Alabama

Birmingham, Alabama, United States

Site Status

University of California, Los Angeles

Los Angeles, California, United States

Site Status

University of California, San Diego

San Diego, California, United States

Site Status

Georgetown University

Washington D.C., District of Columbia, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

Mount Sinai School of Medicine

New York, New York, United States

Site Status

Duke University

Durham, North Carolina, United States

Site Status

Case Western Reserve University

Cleveland, Ohio, United States

Site Status

Medical University of South Carolina

North Charleston, South Carolina, United States

Site Status

University of Utah

Salt Lake City, Utah, United States

Site Status

Countries

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United States

References

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Rafii MS, Tuszynski MH, Thomas RG, Barba D, Brewer JB, Rissman RA, Siffert J, Aisen PS; AAV2-NGF Study Team. Adeno-Associated Viral Vector (Serotype 2)-Nerve Growth Factor for Patients With Alzheimer Disease: A Randomized Clinical Trial. JAMA Neurol. 2018 Jul 1;75(7):834-841. doi: 10.1001/jamaneurol.2018.0233.

Reference Type DERIVED
PMID: 29582053 (View on PubMed)

Other Identifiers

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NIH Grant 1R01AG030048-01A1

Identifier Type: -

Identifier Source: secondary_id

CERE-110-03

Identifier Type: -

Identifier Source: org_study_id