Belinostat in Relapsed or Refractory Peripheral T-Cell Lymphoma

NCT ID: NCT00865969

Last Updated: 2021-10-29

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

129 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-12-15

Study Completion Date

2014-10-27

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to assess efficacy and safety of belinostat in participants with relapsed or refractory peripheral T-cell lymphoma (PTCL), who failed at least one prior systemic therapy.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

This is an open-label, multicenter, single arm efficacy and safety study in participants with relapsed or refractory peripheral T-cell lymphoma, who have failed at least one prior systemic therapy.

Approximately 120 participants will be enrolled. Participants will be treated with 1000 mg/m\^2 belinostat administered as a 30-minute IV infusion on Days 1-5 of every 3-week cycle until there is disease progression or unmanageable treatment-related toxicities.

The primary study endpoint is objective response rate (ORR) based on the International Harmonization Project (IHP) revision International Working Group (IWG) criteria. Safety will be evaluated during the study and for 30 days after the last administration of study drug. Adverse events and laboratory studies will be graded according to National Cancer Institute - Common Terminology Criteria for Adverse Events (NCI-CTCAE) v. 3.0.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Peripheral T-cell Lymphoma

Keywords

Explore important study keywords that can help with search, categorization, and topic discovery.

Belinostat Peripheral T-cell lymphoma PXD101 PTCL HDAC inhibitor Histone deacetylase inhibitor

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Belinostat

Belinostat 1000 mg/m\^2 administered as a 30 minute IV infusion on Days 1-5 of every 3-week cycle until disease progression or unmanageable treatment-related toxicities.

Group Type EXPERIMENTAL

Belinostat

Intervention Type DRUG

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Belinostat

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

PXD101

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* A histologically confirmed diagnosis of PTCL
* Participants must have relapsed or refractory disease after at least one prior systemic anticancer regimen. Systemic anticancer therapy is defined as chemotherapy or immunotherapy administered systemically.
* Participants must have at least one site of disease measurable in two dimensions by computed tomography (CT).
* Age ≥ 18 years.
* Adequate bone marrow, liver, and renal functions.
* Eastern Cooperative Oncology Group (ECOG) performance status 0-2.
* Negative pregnancy test for women of childbearing potential.

Exclusion Criteria

* Relapse within 100 days of autologous or allogeneic bone marrow transplant.
* Prior histone deacetylase (HDAC) inhibitor therapy.
* Co-existing active infection or any medical condition likely to interfere with trial procedures.
* Severe cardiovascular disease.
* Clinically significant central nervous system disorders with altered mental status or psychiatric disorders precluding understanding of the informed consent process and/or completion of the necessary studies.
* Active concurrent malignancy (except adequately treated non-melanoma skin cancer or carcinoma in situ of the cervix).
* Symptomatic or untreated central nervous system (CNS) metastases.
* Pregnant or breast-feeding women.
* Known infection with human immunodeficiency virus (HIV), hepatitis B or hepatitis C.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Valerio Therapeutics

INDUSTRY

Sponsor Role collaborator

Spectrum Pharmaceuticals, Inc

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Peter Brown, MD

Role: PRINCIPAL_INVESTIGATOR

H:S Rigshospitalet, Department of Hematology, Denmark

Pier L Zinzani, MD

Role: PRINCIPAL_INVESTIGATOR

Università di Bologna, Italy

André Bosly, MD

Role: PRINCIPAL_INVESTIGATOR

Cliniques Universitaires UCL Mont Godinne, Belgium

Georges Fillet, MD

Role: PRINCIPAL_INVESTIGATOR

University of Liege, Belgium

Eric van den Neste, MD

Role: PRINCIPAL_INVESTIGATOR

Clinique Universitaier Saint Luc, Belgium

Nicolas Monier, MD

Role: PRINCIPAL_INVESTIGATOR

Hôpital de l'Archet 1 Centre Hospitalier Universitaire (CHU) de Nice, France

Elisabeth Perez, MD

Role: PRINCIPAL_INVESTIGATOR

Groupe Hospitalier Sud Réunion, France

Maria Delioukina, MD

Role: PRINCIPAL_INVESTIGATOR

City of Hope National Medical Center, USA

Adam Lerner, MD

Role: PRINCIPAL_INVESTIGATOR

Boston Medical Center, USA

Lydia Dreosti, MD

Role: PRINCIPAL_INVESTIGATOR

Pretoria Academic Hospital, South Africa

D. Moodley, MD

Role: PRINCIPAL_INVESTIGATOR

Drs Pirjol, Szpak and Moodley Inc, Durban, South Africa

Hanneke C. Kluin-Nelemans, MD

Role: PRINCIPAL_INVESTIGATOR

University Medical Center Groningen UMCG, The Netherlands

G. Sissolak, MD

Role: PRINCIPAL_INVESTIGATOR

Tygerberg Hospital, Cape Town, South Africa

L. Verdonk, MD

Role: PRINCIPAL_INVESTIGATOR

Isala Clinics, Zwolle, The Netherlands

O. Visser, MD

Role: PRINCIPAL_INVESTIGATOR

VU Medical Center, Amsterdam, The Netherlands

Owen A. O'Connor, MD

Role: PRINCIPAL_INVESTIGATOR

New York University Cancer Institute, USA

Sarit Assouline, MD

Role: PRINCIPAL_INVESTIGATOR

McGill University, Department of Oncology Clinical Research Program, Montreal, Canada

Juan Manuel Sancho Cia, MD

Role: PRINCIPAL_INVESTIGATOR

ICO Hospital Germans Trias i Pujol, Badalona, Spain

Consolación Rayon, MD

Role: PRINCIPAL_INVESTIGATOR

Hospital Universitario Central de Asturias, Oviedo, Spain

Sonia Gonzales, MD

Role: PRINCIPAL_INVESTIGATOR

Hospital Clinico Universitario de Santiago, Santiago de Compostella, Spain

Lorenz Trümper, MD

Role: PRINCIPAL_INVESTIGATOR

Universität Göttingen, Abteilung Hämatologie und Onkologie, Göttingen, Germany

Andreas Viardot, MD

Role: PRINCIPAL_INVESTIGATOR

Universitätsklinikum Ulm, Ulm, Germany

Georg Hess, MD

Role: PRINCIPAL_INVESTIGATOR

Universitätsmedizin der Johannes Gutenberg-Universität Mainz, Mainz, Germany

Hans-Heinrich Wolf, MD

Role: PRINCIPAL_INVESTIGATOR

Universitätsklinikum (AöR) der Martin-Luther-Universität Halle-Wittenberg, Halle, Germany

Andreas Neubauer, MD

Role: PRINCIPAL_INVESTIGATOR

University Hospital Marburg, Marburg, Germany

Michele Frank, MD

Role: PRINCIPAL_INVESTIGATOR

Cascade Cancer Center

Madeleine Duvic, MD

Role: PRINCIPAL_INVESTIGATOR

UT - M. D. Anderson Cancer Center

Andrei Shustov, MD

Role: PRINCIPAL_INVESTIGATOR

Fred Hutchinson Cancer Research Center - Seattle Cancer Care Alliance

Melissa Runge-Morris, MD

Role: PRINCIPAL_INVESTIGATOR

Barbara Ann Karmanos Cancer Institute

Nalini Janakiraman, MD

Role: PRINCIPAL_INVESTIGATOR

Henry Ford Health System

Amanda Cashen, MD

Role: PRINCIPAL_INVESTIGATOR

Wasington University School of Medicine- Division of Oncology

Beata Holkova, MD

Role: PRINCIPAL_INVESTIGATOR

Massey Cancer Center

Mohammad Tirgan, MD

Role: PRINCIPAL_INVESTIGATOR

Hematology Associates

Bernard Poiesz, MD

Role: PRINCIPAL_INVESTIGATOR

Upstate Medical Univeristy Syracuse

Charles Farber, MD

Role: PRINCIPAL_INVESTIGATOR

Morristown Memorial Hospital

Zale Bernstein, MD

Role: PRINCIPAL_INVESTIGATOR

Erie County Medical Center (Roswell Park)

Ralph Boccia, MD

Role: PRINCIPAL_INVESTIGATOR

Center for Cancers and Blood Disorders

David Grinblatt, MD

Role: PRINCIPAL_INVESTIGATOR

Kellogg Cancer Care Center

Laura Blakely, MD

Role: PRINCIPAL_INVESTIGATOR

Accelerated Community Oncology Reseaerch Network, Inc. (ACORN)

David Dennis, MD

Role: PRINCIPAL_INVESTIGATOR

Boca Raton Clinical Research Associates

Fernando Camacho, MD

Role: PRINCIPAL_INVESTIGATOR

Bronx River Medical Associates, PC

Eliot Epner, MD

Role: PRINCIPAL_INVESTIGATOR

Penn State Hershey Cancer Institute

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

City of Hope National Medical Center

Duarte, California, United States

Site Status

Wilshire Oncology Medical Group, Inc

La Verne, California, United States

Site Status

Comprehensive Cancer Center

Palm Springs, California, United States

Site Status

Yale Cancer Center-Section of Medical Oncology

New Haven, Connecticut, United States

Site Status

Oncology Associates of Bridgeport

Trumbull, Connecticut, United States

Site Status

Boca Raton Clinical Research Associates

Boca Raton, Florida, United States

Site Status

Georgia Health Sciences University

Augusta, Georgia, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Rush University Medical Center

Chicago, Illinois, United States

Site Status

Kellogg Cancer Care Center

Evanston, Illinois, United States

Site Status

Illinois Cancer Specialists/Cancer Care & Hematology Specialists of Chicagoland

Niles, Illinois, United States

Site Status

Illinois CancerCare, P.C.

Peoria, Illinois, United States

Site Status

Center for Cancers and Blood Disorders

Bethesda, Maryland, United States

Site Status

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Boston University Medical Center

Boston, Massachusetts, United States

Site Status

Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status

Henry Ford Health System

Detroit, Michigan, United States

Site Status

Saint Louis University

St Louis, Missouri, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Northern New Jersey Cancer Associates

Hackensack, New Jersey, United States

Site Status

Morristown Memorial Hospital

Morristown, New Jersey, United States

Site Status

Erie County Medical Center (Roswell Park)

Buffalo, New York, United States

Site Status

Monter Cancer Center

Lake Success, New York, United States

Site Status

New York University Cancer Institute

New York, New York, United States

Site Status

New York University

New York, New York, United States

Site Status

Memorial Sloan-Kettering Cancer Center

New York, New York, United States

Site Status

Upstate Medical Univeristy Syracuse

Syracuse, New York, United States

Site Status

Bronx River Medical Associates, PC

The Bronx, New York, United States

Site Status

Duke University Medical Center

Durham, North Carolina, United States

Site Status

Hematology Associates

Bedford, Ohio, United States

Site Status

St Luke's Cancer Center

Bethlehem, Pennsylvania, United States

Site Status

Penn State Hershey Cancer Institute

Hershey, Pennsylvania, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Avera Cancer Center

Sioux Falls, South Dakota, United States

Site Status

Associates In Oncology and Hematology

Chattanooga, Tennessee, United States

Site Status

University of Tennessee Cancer Institute

Knoxville, Tennessee, United States

Site Status

Accelerated Community Oncology Reseaerch Network, Inc. (ACORN)

Memphis, Tennessee, United States

Site Status

UT - M. D. Anderson Cancer Center

Houston, Texas, United States

Site Status

The UT Health Science Centre at San Antonio

San Antonio, Texas, United States

Site Status

Massey Cancer Center

Richmond, Virginia, United States

Site Status

Cascade Cancer Center

Kirkland, Washington, United States

Site Status

Fred Hutchinson Cancer Research Center - Seattle Cancer Care Alliance

Seattle, Washington, United States

Site Status

ZNA Middelheim

Antwerp, , Belgium

Site Status

ZNA Stuivenberg

Antwerp, , Belgium

Site Status

AZ St. Jan

Bruges, , Belgium

Site Status

Clinique Universitaire Saint Luc, Service Hématologie

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status

University of Liege, Divisions of Hematology and Medical Oncology

Liège, , Belgium

Site Status

Cliniques Universitaires UCL Mont Godinne, Service Hématologie

Yvoir, , Belgium

Site Status

University of British Columbia

Vancouver, British Columbia, Canada

Site Status

CHA Hôpital de l'Enfant-Jésus

Québec, Quebec, Canada

Site Status

McGill University

Montreal, , Canada

Site Status

CHC Split Clinic of Internal Diseases

Split, , Croatia

Site Status

CHC Zagreb Clinic of Internal Diseases

Zagreb, , Croatia

Site Status

UH Dubrava Clinic of Internal Diseases

Zagreb, , Croatia

Site Status

CHC Rijeka, Clinic of Internal Diseases

Zagreb, , Croatia

Site Status

H:S Rigshospitalet, The Finsen Centre, KAT, Haematology Department 4241

Copenhagen, , Denmark

Site Status

Hôpital de l'Archet, Centre Hospitalier Universitaire (CHU) de Nice, Hématologie Clinique

Nice, , France

Site Status

Groupe Hospitalier Sud Réunion, Site Saint-Pierre

Saint-Pierre, , France

Site Status

Klinik Essen Süd, Evangelisches Krankenhaus

Essen, , Germany

Site Status

Leitender Oberarzt/Klinik für Onkologie und Hämatologie

Frankfurt, , Germany

Site Status

Universität Göttingen, Abteilung Hämatologie und Onkologie

Göttingen, , Germany

Site Status

Universitätsklinikum (AöR) der Martin-Luther-Universität Halle-Wittenberg

Halle, , Germany

Site Status

Asklepios Klinik St. Georg

Hamburg, , Germany

Site Status

Universitätsklinikum des Saarlandes

Homburg/Saar, , Germany

Site Status

Universitätsklinikum Leipzig AöR

Leipzig, , Germany

Site Status

Universitätsmedizin der johannes Gutenberg -Universität Mainz

Mainz, , Germany

Site Status

University Hospital Marburg

Marburg, , Germany

Site Status

Münchner Studienzentrum Klinikum Rechts der Isar

München, , Germany

Site Status

Klinikum Nuernberg Nord

Nuremberg, , Germany

Site Status

Universitätsklinikum Rostock

Rostock, , Germany

Site Status

Universitätsklinikum Ulm

Ulm, , Germany

Site Status

Szt István és Szt. Laszlo

Budapest, , Hungary

Site Status

Belgyógyászati Klinika

Debrecen, , Hungary

Site Status

Belgyógyászati Klinika Györ

Győr, , Hungary

Site Status

Belgyógyászati Klinika es Kardiologial Központ

Szeged, , Hungary

Site Status

The Soroka University Medical Center

Beersheba, , Israel

Site Status

Rambam Medical Center Department of Hematology

Haifa, , Israel

Site Status

Hadassah University Hospital Sharet Building Department of Hematology

Jerusalem, , Israel

Site Status

Rabin Medical Center Belinson Campus

Petah Tikva, , Israel

Site Status

Ospedale Sant'Orsola, Instituto di Ematologia e Oncologia Medica

Bologna, , Italy

Site Status

Ospedale Policlinico Careggi

Florence, , Italy

Site Status

VU Medical Center, Department of Haematology

Amsterdam, , Netherlands

Site Status

University Medical Center Groningen UMCG, Department of Haematologie

Groningen, , Netherlands

Site Status

Erasmus University Medical Center

Rotterdam, , Netherlands

Site Status

Isala Clinics, Department of Haematololgy

Zwolle, , Netherlands

Site Status

Klinika Nowotworów Ukladu Chlonnego Centrum Onkologii Instytut Marii Sklodowskiej-Curie

Warsaw, Masovian Voivodeship, Poland

Site Status

Uniwersyteckie Centrum Kliniczne Klinika Hematologii i Transplantologii

Gdansk, , Poland

Site Status

Małopolskie Centrum Medyczne

Krakow, , Poland

Site Status

Wojewódzki Szpital Specjalistyczny im M. Kopernika w Łodzi Oddział Hematologii - Klinika Hematologii

Lodz, , Poland

Site Status

Szpital Wojewódzki w Opolu/Oddział Hematologii

Opole, , Poland

Site Status

MTZ Clinical Research Sp z o.o.

Warsaw, , Poland

Site Status

Instytut Hematologii i Transfuzjologii Klinika Hematologii

Warsaw, , Poland

Site Status

Wojskowy Instytut Medyczny Klinika Chorób/Wewnętrznych i Hematologii Centralnego Szpitala

Warsaw, , Poland

Site Status

State Therapeutical and Prophylactic Institution Chelyabinsk Regional Clinical Oncology Dispensary

Chelyabinsk, , Russia

Site Status

Russian Cancer Research Centre named after N.N. Blokhin of Russian Academy of Medical Sciences

Moscow, , Russia

Site Status

Research Center of Haematology

Moscow, , Russia

Site Status

Narodny Onkologicky Ustav (NOU)

Bratislava, , Slovakia

Site Status

Klinika Hematologie a Onkohematologie FNLP a LF UPJS

Košice, , Slovakia

Site Status

Tygerberg Hospital, Department of Radiation Oncology

Bellville, , South Africa

Site Status

Drs pirjol, Szpak and Moodley Inc.

Durban, , South Africa

Site Status

Medical Oncology 2nd Floor Radiotherapy building Steve Biko Academic Hospital

Pretoria, , South Africa

Site Status

Pretoria Academic Hospital, Department of Radiation Oncology

Pretoria, , South Africa

Site Status

Complexo Hospitalario a Coruna

A Coruña, , Spain

Site Status

Hospital Clinico Universitario de Santiago

A Coruña, , Spain

Site Status

ICO Hospital Germans Trias i Pujol

Badalona, , Spain

Site Status

Hospital Duran i Reinals

Barcelona, , Spain

Site Status

Hospital Universitario Virgen de la Arrixaca

El Palmar, , Spain

Site Status

Hospital General Universitario Gregorio Maranón

Madrid, , Spain

Site Status

Hospital Universitario Morales Meseguer

Murcia, , Spain

Site Status

Hospital Universitario Central de Asturias

Oviedo, , Spain

Site Status

St James's Institute of Oncology Bexley Wing

Leeds, , United Kingdom

Site Status

Leicester Royal Infirmary

Leicester, , United Kingdom

Site Status

Institute of Cancer/ Centre for Medical Oncology/Barts and The London School of Medicine and Dentistry

London, , United Kingdom

Site Status

The Christie NHS Foundation Trust, The Christie Hospital,

Manchester, , United Kingdom

Site Status

Northern Centre for Cancer Care, Freeman Hospital

Newcastle upon Tyne, , United Kingdom

Site Status

The Royal Marsden Haemato-Oncology Wards

Sutton, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Belgium Canada Croatia Denmark France Germany Hungary Israel Italy Netherlands Poland Russia Slovakia South Africa Spain United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Campbell P, Thomas CM. Belinostat for the treatment of relapsed or refractory peripheral T-cell lymphoma. J Oncol Pharm Pract. 2017 Mar;23(2):143-147. doi: 10.1177/1078155216634178. Epub 2016 Jun 23.

Reference Type RESULT
PMID: 26921086 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2008-005843-40

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

PXD101-CLN-19

Identifier Type: -

Identifier Source: org_study_id