A Safety and Efficacy Trial of Stannsoporfin in Neonates With Hyperbilirubinemia

NCT ID: NCT00850993

Last Updated: 2019-10-30

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

58 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-08-31

Study Completion Date

2012-05-31

Brief Summary

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It is a normal process in the human body for red blood cells to die, which makes bilirubin.

Bilirubin is cleared away through the liver.

Some babies are born with livers that don't work well enough yet, or their red blood cells are dying too fast, so the baby looks yellow (jaundice).

This means there is too much bilirubin in the body. It can be dangerous if a baby's bilirubin gets too high.

Phototherapy is what they call the lights they shine on newborn babies to help the liver get rid of bilirubin.

This study tests an experimental drug to see if it can reduce how much bilirubin is being made in the first place.

Detailed Description

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The purpose of this study is to determine if an experimental drug, stannsoporfin, is safe and effective in the treatment of hyperbilirubinemia in hemolyzing neonates.

Conditions

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Hyperbilirubinemia, Neonatal

Keywords

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Hemolysis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Sequential experimental cohorts are run in parallel with placebo controls.
Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators
Clinical personnel at the site (including investigator, study coordinator and central cardiologist) were blinded to treatment group.

The research pharmacy and the health care provider responsible for giving the injection to patients knew what the treatment was (they were not blinded).

Study Groups

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Cohort 1: Stannsoporfin 1.5 mg/kg

Participants receive a single dose of 1.5 mg/kg by intramuscular (IM) injection, along with PhotoTherapy (PT) if and when needed.

Group Type EXPERIMENTAL

Stannsoporfin

Intervention Type DRUG

Stannsoporfin administered as a single IM injection

PhotoTherapy (as needed)

Intervention Type OTHER

PT standard care administered as needed, based on bilirubin levels throughout the treatment period

Cohort 2: Stannsoporfin 3.0 mg/kg

Participants receive a single dose of 3.0 mg/kg by intramuscular (IM) injection, along with PT if and when needed.

Group Type EXPERIMENTAL

Stannsoporfin

Intervention Type DRUG

Stannsoporfin administered as a single IM injection

PhotoTherapy (as needed)

Intervention Type OTHER

PT standard care administered as needed, based on bilirubin levels throughout the treatment period

Cohort 3: Stannsoporfin 4.5 mg/kg

Participants receive a single dose of 4.5 mg/kg by intramuscular (IM) injection, along with PT if and when needed.

Group Type EXPERIMENTAL

Stannsoporfin

Intervention Type DRUG

Stannsoporfin administered as a single IM injection

PhotoTherapy (as needed)

Intervention Type OTHER

PT standard care administered as needed, based on bilirubin levels throughout the treatment period

Cohort 4: Placebo

Participants receive a single dose of placebo (sterile saline solution) by IM injection, along with PT if and when needed.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Placebo (sterile saline solution) administered as a single IM injection

PhotoTherapy (as needed)

Intervention Type OTHER

PT standard care administered as needed, based on bilirubin levels throughout the treatment period

Interventions

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Stannsoporfin

Stannsoporfin administered as a single IM injection

Intervention Type DRUG

Placebo

Placebo (sterile saline solution) administered as a single IM injection

Intervention Type OTHER

PhotoTherapy (as needed)

PT standard care administered as needed, based on bilirubin levels throughout the treatment period

Intervention Type OTHER

Other Intervention Names

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Experimental product Saline PT

Eligibility Criteria

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Inclusion Criteria

Babies may only participate if they meet all the following criteria:

* Is a term or late preterm baby
* Is at risk for protocol-defined hemolytic disease
* Weighs at least 2500 g (5.5 lbs)
* Has total serum bilirubin (TSB) a specified amount lower than the phototherapy threshold for the age
* Has parents/guardians who are willing to follow light precautions and sign informed consent

Exclusion Criteria

The following criteria will make a baby not eligible to participate:

* Needs medications that may prolong the QT interval
* Has family history or risk factors for Long QT Syndrome, Sudden Infant Death Syndrome, or Porphyrias
* Has an Apgar score of 6 or below at age 5 minutes
* Has abnormalities or infections (in mother or child) that per protocol or in the opinion of the investigator may compromise the safety and well-being of the baby or analysis of study results
Minimum Eligible Age

1 Minute

Maximum Eligible Age

48 Hours

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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InfaCare Pharmaceuticals Corporation, a Mallinckrodt Company

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Team Leader

Role: STUDY_DIRECTOR

Mallinckrodt

Locations

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Arrowhead Regional Med Center

Colton, California, United States

Site Status

UCSD Medical Center

San Diego, California, United States

Site Status

Kapi'olani Medical Center for Women and Children

Honolulu, Hawaii, United States

Site Status

University of Louisville

Louisville, Kentucky, United States

Site Status

Westchester Medical Center

Valhalla, New York, United States

Site Status

ECU Brody School of Medicine

Greenville, North Carolina, United States

Site Status

St. Vincent Mercy Children's Hospital

Toledo, Ohio, United States

Site Status

Drexel University College of Medicine, Clinical Research Group

Philadelphia, Pennsylvania, United States

Site Status

Albert Einstein Medical Center

Philadelphia, Pennsylvania, United States

Site Status

Jan Bizel University Hospital No. 2; Department of Neonatal, Preemies and Neonatal Intensive Care

Bydgoszcz, , Poland

Site Status

Research Institute of Polish Mother's Health Center

Lodz, , Poland

Site Status

Neonatal Department Warsaw Medical University

Warsaw, , Poland

Site Status

Complejo Hospitalario Universitario A Coruña

A Coruña, , Spain

Site Status

Hospital Vall D´Hebrón

Barcelona, , Spain

Site Status

Hospital Clinic i Provincial

Barcelona, , Spain

Site Status

Hospital Doce de Octubre

Madrid, , Spain

Site Status

Hospital La Paz

Madrid, , Spain

Site Status

University Hospital Santiago de Compostela-L Coruna

Santiago de Compostela, , Spain

Site Status

Municipal Medical Institution "Regional pediatric clinical hospital #1", Department of pathology of the newborns; Bukovynian State Medical University, Department of Pediatrics and Children's Infectious Diseases

Chernivtsi, , Ukraine

Site Status

National Pediatric Specialized Hospital "OHMATDYT".

Kiev, , Ukraine

Site Status

State Institution "Institute of Pediatrics, Obstetrics and Gynecology of the Academy of Medical Science of the Ukraine", Neonatology Department

Kiev, , Ukraine

Site Status

Municipal Institution "Odessa regional clinical hospital", Department of pathology of the newborns and premature infants; Odessa State Medical University; Chair of Pediatrics #1 and Neonatology

Odesa, , Ukraine

Site Status

Vinnytsia regional pediatric hospital, Department of pathology of the newborns, Vinnytsia National Medical University named after M.I.Pirogov, Chair of Pediatrics #1

Vinnitsa, , Ukraine

Site Status

Countries

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United States Poland Spain Ukraine

Other Identifiers

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2009-017434-45

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

64,185-202

Identifier Type: -

Identifier Source: org_study_id