A Multi-Center Controlled Screening Trial of Safety and Efficacy of Lithium Carbonate in Subjects With Amyotrophic Lateral Sclerosis (ALS)

NCT ID: NCT00790582

Last Updated: 2020-10-30

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

109 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-05-31

Study Completion Date

2010-03-31

Brief Summary

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This is a Phase II screening study of lithium carbonate in ALS. The purpose of this study is to find out if lithium carbonate is safe to be used in people with ALS and if it can slow the progression of the disease. Since there is no placebo in this study, all patients will be taking lithium carbonate.

Detailed Description

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This is a Phase II Screening study. There is no placebo (inactive or 'fake' drug) in this study, meaning that all participants will be taking lithium carbonate. The purpose of this study is to find out if lithium carbonate is safe to be used in people with ALS and if it can slow the progression of the disease.

A recent article was published in a highly regarded medical journal that showed a positive effect of lithium carbonate on an ALS type mouse. The researchers then studied a very small number of people with ALS, giving 16 people lithium carbonate with riluzole and giving 28 people only riluzole. The people who took lithium remained stronger for a considerably longer period of time. However, the study was very small and we cannot really tell if lithium works unless a larger study is performed. It is not well understood why lithium carbonate might be helpful but it is believed that it may play a role in protecting the motor nerves from the damage of ALS.

If you choose to participate, you will need to go to your study clinic for research study visits 7 times in one year and you will have 4 telephone interviews during that time. These visits and phone calls could take up to 17 hours in total.

Caution: Lithium is an FDA approved drug used for some psychiatric disorders. It is not FDA approved for ALS. Lithium has many potentially serious side effects and must only be taken under close supervision of your physician.

Conditions

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Amyotrophic Lateral Sclerosis

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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lithium carbonate

Group Type EXPERIMENTAL

lithium carbonate

Intervention Type DRUG

The dosage of lithium carbonate will be adjusted for each individual. The maximum dose is 450mg/day.

Interventions

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lithium carbonate

The dosage of lithium carbonate will be adjusted for each individual. The maximum dose is 450mg/day.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of laboratory-supported probable, probable, or definite ALS
* Vital capacity of at least 75% of predicted
* Onset of weakness within 3 years prior to enrollment
* If patients are on riluzole, they must be on a stable dose for at least 30 days prior to baseline visit
* Women of childbearing potential must be surgically sterile or using an effective method of birth control and have a negative pregnancy test
* Willing and able to give informed consent

Exclusion Criteria

* Diagnosis of other neurodegenerative disease
* Need tracheotomy ventilation or non-invasive ventilation 23 or more hours/day
* Clinically significant history of any unstable medical condition in past 30 days
* History of renal
* History of liver disease
* Current pregnancy or lactation
* Use of lithium within thirty days of enrollment
* Significantly limited mental capacity
* History of recent drug or alcohol abuse
* Use of any investigational drug within 30 days prior to enrollment
Minimum Eligible Age

21 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Muscular Dystrophy Association

OTHER

Sponsor Role collaborator

Forbes Norris MDA/ALS Research Center

OTHER

Sponsor Role lead

Responsible Party

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Dr. Robert Miller

Director

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Robert G Miller, MD

Role: STUDY_DIRECTOR

California Pacific Medical Center

Locations

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Mayo Clinic

Scottsdale, Arizona, United States

Site Status

UCLA Neuromuscular Research Center

Los Angeles, California, United States

Site Status

UC Irvine MDA/ALS & Neuromuscular Center

Orange, California, United States

Site Status

California Pacific Medical Center

San Francisco, California, United States

Site Status

Kansas University Medical Center

Kansas City, Kansas, United States

Site Status

Washington University Department of Neurology

St Louis, Missouri, United States

Site Status

Providence ALS Clinic

Portland, Oregon, United States

Site Status

University of Pennsylvania Neurological Institute

Philadelphia, Pennsylvania, United States

Site Status

Methodist Neurological Institute

Houston, Texas, United States

Site Status

University of Utah Clinical Neurosciences Center

Salt Lake City, Utah, United States

Site Status

Countries

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United States

References

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Fornai F, Longone P, Cafaro L, Kastsiuchenka O, Ferrucci M, Manca ML, Lazzeri G, Spalloni A, Bellio N, Lenzi P, Modugno N, Siciliano G, Isidoro C, Murri L, Ruggieri S, Paparelli A. Lithium delays progression of amyotrophic lateral sclerosis. Proc Natl Acad Sci U S A. 2008 Feb 12;105(6):2052-7. doi: 10.1073/pnas.0708022105. Epub 2008 Feb 4.

Reference Type BACKGROUND
PMID: 18250315 (View on PubMed)

Other Identifiers

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28.013

Identifier Type: -

Identifier Source: org_study_id