Trial Outcomes & Findings for Topical Imiquimod Cream in Combination With Cryotherapy for the Treatment of Actinic Keratoses (NCT NCT00774787)

NCT ID: NCT00774787

Last Updated: 2016-11-07

Results Overview

Percent change = \[(actinic keratoses count at 4-8 weeks post-treatment)-(actinic keratoses count at baseline)\]/(actinic keratoses count at baseline)\]\*100%. Data from one patient, lost to follow-up immediately after cryotherapy, not included in these analyses. Actinic keratoses at 4-8 weeks post-treatment visit includes all actinic keratoses in each respective treatment area, baseline and new.

Recruitment status

COMPLETED

Study phase

PHASE4

Target enrollment

27 participants

Primary outcome timeframe

Baseline, 4-8 weeks post-treatment

Results posted on

2016-11-07

Participant Flow

First patient enrolled - 08 Oct 08; last patient enrolled - 07 Jul 09; last patient completed: 09 Sep 09; Setting - private practice clinics

Participant milestones

Participant milestones
Measure
Cryotherapy Followed by Imiquimod 5% Cream or Observation
Split-face study of cryotherapy of all actinic keratoses in target treatment area (bilaterally symmetrical area on face or balding scalp) followed by random assignment to treatment of half of treatment area with imiquimod 5% cream and of other half to no treatment
Overall Study
STARTED
27
Overall Study
COMPLETED
26
Overall Study
NOT COMPLETED
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Cryotherapy Followed by Imiquimod 5% Cream or Observation
Split-face study of cryotherapy of all actinic keratoses in target treatment area (bilaterally symmetrical area on face or balding scalp) followed by random assignment to treatment of half of treatment area with imiquimod 5% cream and of other half to no treatment
Overall Study
Lost to Follow-up
1

Baseline Characteristics

Topical Imiquimod Cream in Combination With Cryotherapy for the Treatment of Actinic Keratoses

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Cryotherapy Followed by Imiquimod 5% Cream or Observation
n=27 Participants
Split-face study of cryotherapy of all actinic keratoses in target treatment area (bilaterally symmetrical area on face or balding scalp) followed by random assignment to treatment of half of treatment area with imiquimod 5% cream and of other half to no treatment
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
10 Participants
n=5 Participants
Age, Categorical
>=65 years
17 Participants
n=5 Participants
Age, Continuous
67.8 years
STANDARD_DEVIATION 9.2 • n=5 Participants
Sex: Female, Male
Female
1 Participants
n=5 Participants
Sex: Female, Male
Male
26 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
26 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
Region of Enrollment
United States
27 participants
n=5 Participants
Actinic keratoses, total
17.3 Lesions
STANDARD_DEVIATION 4.1 • n=5 Participants
Actinic keratoses, Imiquimod side
8.7 Lesions
STANDARD_DEVIATION 2.2 • n=5 Participants
Actinic keratoses, Observation Side
8.5 Lesions
STANDARD_DEVIATION 2.3 • n=5 Participants

PRIMARY outcome

Timeframe: Baseline, 4-8 weeks post-treatment

Population: Patients who had end of study visit with count of actinic keratoses. Change not calculated for one patient who was lost to follow-up immediately after baseline visit, and had no post-treatment data. Actinic keratoses at 4-8 weeks post-treatment visit includes all actinic keratoses in each respective treatment area, baseline or new.

Percent change = \[(actinic keratoses count at 4-8 weeks post-treatment)-(actinic keratoses count at baseline)\]/(actinic keratoses count at baseline)\]\*100%. Data from one patient, lost to follow-up immediately after cryotherapy, not included in these analyses. Actinic keratoses at 4-8 weeks post-treatment visit includes all actinic keratoses in each respective treatment area, baseline and new.

Outcome measures

Outcome measures
Measure
Cryotherapy Followed by Imiquimod 5% Cream or Observation
n=26 Participants
Split-face study of cryotherapy of all actinic keratoses in target treatment area (bilaterally symmetrical area on face or balding scalp) followed by random assignment to treatment of half of treatment area with imiquimod 5% cream and of other half to no treatment
Change From Baseline in Actinic Keratoses Count at 4-8 Weeks Post-treatment
Change from baseline, imiquimod side
-73.2 Percent change
Standard Deviation 27.1
Change From Baseline in Actinic Keratoses Count at 4-8 Weeks Post-treatment
Change from baseline, observation side
-62.0 Percent change
Standard Deviation 30.3

SECONDARY outcome

Timeframe: 4-8 weeks post-treatment

Population: Patients who had end of study visit with cosmetic appearance assessment. Cosmetic appearance score, by treatment area, not included for one patient who was lost to follow-up immediately after baseline visit, and had no post-treatment data.

Cosmetic appearance score, based recall comparison to appearance at baseline. Seven point scale: +3 = treatment area is much better appearing; +2 = treatment area is moderately better appearing; + 1 = treatment area is slightly better appearing; 0 = treatment area appears same; -1 = treatment area is slightly worse appearing; -2 = treatment area is moderately worse appearing; -3 = treatment area is much worse appearing. Data from one patient, lost to follow-up immediately after cryotherapy, not included in these analyses.

Outcome measures

Outcome measures
Measure
Cryotherapy Followed by Imiquimod 5% Cream or Observation
n=26 Participants
Split-face study of cryotherapy of all actinic keratoses in target treatment area (bilaterally symmetrical area on face or balding scalp) followed by random assignment to treatment of half of treatment area with imiquimod 5% cream and of other half to no treatment
Cosmetic Appearance Score at 4-8 Weeks Post-treatment
Investigator assessed, imiquimod side
2.1 Scores on a scale
Standard Deviation 1.1
Cosmetic Appearance Score at 4-8 Weeks Post-treatment
Investigator assessed, observation side
1.6 Scores on a scale
Standard Deviation 1.1
Cosmetic Appearance Score at 4-8 Weeks Post-treatment
Patient assessed, imiquimod side
2.6 Scores on a scale
Standard Deviation 1.0
Cosmetic Appearance Score at 4-8 Weeks Post-treatment
Patient assessed, observation side
1.2 Scores on a scale
Standard Deviation 1.3

POST_HOC outcome

Timeframe: 4-8 weeks post-treatment

Population: All patients enrolled.

Complete clearance (actinic keratosis count of 0) in each respective area at 4-8 weeks post-treatment. Actinic keratoses at 4-8 weeks post-treatment visit includes all actinic keratoses in each respective treatment area, baseline and new.

Outcome measures

Outcome measures
Measure
Cryotherapy Followed by Imiquimod 5% Cream or Observation
n=27 Treatment areas
Split-face study of cryotherapy of all actinic keratoses in target treatment area (bilaterally symmetrical area on face or balding scalp) followed by random assignment to treatment of half of treatment area with imiquimod 5% cream and of other half to no treatment
Complete Clearance of Actinic Keratoses at 4-8 Weeks Post-treatment
Completely cleared, observation side
5 Participants
Complete Clearance of Actinic Keratoses at 4-8 Weeks Post-treatment
Completely cleared, imiquimod side
8 Participants

OTHER_PRE_SPECIFIED outcome

Timeframe: Post baseline to end of study (4-8 weeks post-treatment)

Population: One patient not included who was lost to follow-up immediately after baseline visit, and had no post-treatment data.

Mean maximum post-baseline intensity of investigator assessed local skin reactions (erythema, edema, weeping/exudate, flaking/scaling/dryness, scabbing/crusting, erosion/ulceration) by treatment area. 0 = none, 1 = mild, 2 = moderate, 3 = severe. Data from one patient, lost to follow-up immediately after cryotherapy, not included in these analyses.

Outcome measures

Outcome measures
Measure
Cryotherapy Followed by Imiquimod 5% Cream or Observation
n=26 Participants
Split-face study of cryotherapy of all actinic keratoses in target treatment area (bilaterally symmetrical area on face or balding scalp) followed by random assignment to treatment of half of treatment area with imiquimod 5% cream and of other half to no treatment
Local Skin Reactions
Erythema, imiquimod side
1.5 Scores on a scale
Standard Deviation 0.7
Local Skin Reactions
Erythema, observation side
1.3 Scores on a scale
Standard Deviation 0.5
Local Skin Reactions
Edema, imiquimod side
0.2 Scores on a scale
Standard Deviation 0.4
Local Skin Reactions
Edema, observation side
0.1 Scores on a scale
Standard Deviation 0.3
Local Skin Reactions
Weeping/exudate, imiquimod side
0.3 Scores on a scale
Standard Deviation 0.7
Local Skin Reactions
Weeping/exudate, observation side
0.0 Scores on a scale
Standard Deviation 0.0
Local Skin Reactions
Flaking/scaling/dryness, imiquimod side
1.4 Scores on a scale
Standard Deviation 0.6
Local Skin Reactions
Flaking/scaling/dryness, observation side
1.2 Scores on a scale
Standard Deviation 0.6
Local Skin Reactions
Scabbing/crusting, imiquimod side
0.9 Scores on a scale
Standard Deviation 1.1
Local Skin Reactions
Scabbing/crusting, observation side
0.6 Scores on a scale
Standard Deviation 0.7
Local Skin Reactions
Erosion/ulceration, imiquimod side
0.4 Scores on a scale
Standard Deviation 0.7
Local Skin Reactions
Erosion/ulceration, observation side
0.1 Scores on a scale
Standard Deviation 0.4

Adverse Events

Cryotherapy Followed by Imiquimod 5% Cream or Observation

Serious events: 0 serious events
Other events: 3 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Cryotherapy Followed by Imiquimod 5% Cream or Observation
n=27 participants at risk
Split-face study of cryotherapy of all actinic keratoses in target treatment area (bilaterally symmetrical area on face or balding scalp) followed by random assignment to treatment of half of treatment area with imiquimod 5% cream and of other half to no treatment
Skin and subcutaneous tissue disorders
Systemic interferon reaction on areas with previous sun exposure; arms, thighs, upper chest, upper b
3.7%
1/27 • Number of events 1 • 8-12 weeks: from baseline cryotherapy visit to end of study (4-8 weeks post completion of imiquimod treatment).
General disorders
Weakness
3.7%
1/27 • Number of events 1 • 8-12 weeks: from baseline cryotherapy visit to end of study (4-8 weeks post completion of imiquimod treatment).
Gastrointestinal disorders
Decreased appetite
3.7%
1/27 • Number of events 1 • 8-12 weeks: from baseline cryotherapy visit to end of study (4-8 weeks post completion of imiquimod treatment).
Infections and infestations
Cold
3.7%
1/27 • Number of events 1 • 8-12 weeks: from baseline cryotherapy visit to end of study (4-8 weeks post completion of imiquimod treatment).

Additional Information

Darrell Rigel

Rigel Dermatology

Phone: 212-684-5964

Results disclosure agreements

  • Principal investigator is a sponsor employee PIs must agree on communication of complete results, but may discuss individual site results. Collaborator can review complete results communications prior to public release and can embargo communications regarding trial results, if patents are to be pursued, for a period that is more than 60 days but less than or equal to 180 days from the time submitted to the collaborator for review. The collaborator cannot require changes to the communication and cannot extend the embargo.
  • Publication restrictions are in place

Restriction type: OTHER