Trial Outcomes & Findings for Phase 3 Clinical Study for the Treatment of Cold Sore (NCT NCT00769314)

NCT ID: NCT00769314

Last Updated: 2012-12-21

Results Overview

Healing was defined as the loss of crust (erythema may be present) as assessed by the investigator. TTH was the time from treatment initiation to healing as defined above and was assessed from the time of treatment initiation through Day 14. The primary vesicular lesion was the first developed lesion located on the lip and was not to have extended more than 1 cm outside the lip.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

1727 participants

Primary outcome timeframe

Assessed from time of treatment initiation through Day 14

Results posted on

2012-12-21

Participant Flow

Patients were screened beginning March 2007 and the last patient was treated in October 2008. The study was conducted at 47 sites in Australia, the Czech Republic, France, Germany, Poland, the United Kingdom and the United States.

Per protocol, a total of 1950 patients were to be randomized. Following randomization, patients were not to start treatment until a new labial herpes episode occurred. Thus, of those randomized, only 780 patients were planned to be treated (390 patients per treatment group) and 1170 patients were to be randomized, but not treated.

Participant milestones

Participant milestones
Measure
Acyclovir Lauriad Group
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
muco-adhesive buccal tablet with placebo
Overall Study
STARTED
378
397
Overall Study
COMPLETED
361
384
Overall Study
NOT COMPLETED
17
13

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Phase 3 Clinical Study for the Treatment of Cold Sore

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Acyclovir Lauriad Group
n=376 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet/Intent-to-Treat population
Placebo Group
n=395 Participants
muco-adhesive buccal tablet with placebo/Intent-to-Treat population
Total
n=771 Participants
Total of all reporting groups
Age Continuous
40 years
STANDARD_DEVIATION 12.97 • n=5 Participants
41.9 years
STANDARD_DEVIATION 13.33 • n=7 Participants
41.0 years
STANDARD_DEVIATION 13.18 • n=5 Participants
Sex: Female, Male
Female
258 Participants
n=5 Participants
271 Participants
n=7 Participants
529 Participants
n=5 Participants
Sex: Female, Male
Male
118 Participants
n=5 Participants
124 Participants
n=7 Participants
242 Participants
n=5 Participants
Region of Enrollment
United States
71 participants
n=5 Participants
72 participants
n=7 Participants
143 participants
n=5 Participants
Region of Enrollment
France
41 participants
n=5 Participants
49 participants
n=7 Participants
90 participants
n=5 Participants
Region of Enrollment
Czech Republic
47 participants
n=5 Participants
50 participants
n=7 Participants
97 participants
n=5 Participants
Region of Enrollment
Poland
74 participants
n=5 Participants
70 participants
n=7 Participants
144 participants
n=5 Participants
Region of Enrollment
Australia
53 participants
n=5 Participants
68 participants
n=7 Participants
121 participants
n=5 Participants
Region of Enrollment
Germany
79 participants
n=5 Participants
77 participants
n=7 Participants
156 participants
n=5 Participants
Region of Enrollment
United Kingdom
11 participants
n=5 Participants
9 participants
n=7 Participants
20 participants
n=5 Participants

PRIMARY outcome

Timeframe: Assessed from time of treatment initiation through Day 14

Population: The modified Intent-to-Treat (mITT) population was the population used for analysis of this endpoint. The mITT population included all randomized patients who received at least one dose of study medication and who reached the vesicular stage (ie, episodes that progressed through macula, papule, vesicle, crust and healing).

Healing was defined as the loss of crust (erythema may be present) as assessed by the investigator. TTH was the time from treatment initiation to healing as defined above and was assessed from the time of treatment initiation through Day 14. The primary vesicular lesion was the first developed lesion located on the lip and was not to have extended more than 1 cm outside the lip.

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=242 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=279 Participants
muco-adhesive buccal tablet with placebo
Time to Healing (TTH) of Vesicular Primary Lesion
7.00 Days
95% Confidence Interval 0.18 • Interval 6.75 to 7.31
7.32 Days
95% Confidence Interval 0.18 • Interval 6.97 to 7.92

SECONDARY outcome

Timeframe: Assessed from the time of treatment initiation through Day 14

Population: This endpoint was analyzed using the Intent-to-Treat (ITT) population, which consisted of all randomized patients who received at least one dose of study medication and who had complete information recorded for the application time.

Aborted lesions were defined as herpetic lesions preceded by prodromal symptoms that did not progress beyond the papule stage.

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=376 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=395 Participants
muco-adhesive buccal tablet with placebo
Abortion of Primary Lesions
Aborted Lesions = Yes
130 participants
109 participants
Abortion of Primary Lesions
Aborted Lesions = No
242 participants
279 participants
Abortion of Primary Lesions
Aborted Lesions = Missing
4 participants
7 participants

SECONDARY outcome

Timeframe: Assessed from the time of treatment initiation through Day 14

Population: This endpoint was analyzed using a subgroup of patients in the ITT population with non-primary lesions.

TTH of non-primary lesions was defined as the time from treatment initiation to healing of all non-primary vesicular lesions. Non-primary lesions were those that developed in addition to and/or in 1 or more days after the primary vesicular lesion and that were located at least 1 cm from the primary lesion. Aborted lesions were not included in this parameter. TTH was to be assessed by the investigator.

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=39 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=62 Participants
muco-adhesive buccal tablet with placebo
TTH of Non-primary Lesions (Aborted Lesions Excluded)
7.00 Days
Interval 5.53 to 8.7
9.08 Days
Interval 7.46 to 11.0

SECONDARY outcome

Timeframe: Assessed from initiation of treatment to Day 14

Population: This endpoint was analyzed using the ITT population.

For patients who experienced a vesicular lesion, DOE was defined as the time from treatment initiation to healing of primary and secondary vesicular lesions (loss of crust). For subjects whose primary and secondary lesions were not vesicular in nature, DOE was defied as the time from treatment initiation to return to normal skin or to cessation of symptoms, whichever came last.

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=373 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=395 Participants
muco-adhesive buccal tablet with placebo
Duration of Episode (DOE)
5.57 Days
Interval 5.03 to 6.01
6.38 Days
Interval 5.93 to 6.97

SECONDARY outcome

Timeframe: Assessed from time of treatment initiation through Day 14

Population: This endpoint was analyzed using the ITT population.

Time to cessation of symptoms was defined as the time from treatment initiation to cessation of all symptoms: pain, burning, itching, tingling, tenderness and discomfort. It was to be assessed by the investigator.

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=373 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=393 Participants
muco-adhesive buccal tablet with placebo
Time to Cessation of Symptoms
3.57 Days
Interval 3.04 to 4.01
4.16 Days
Interval 3.75 to 4.89

SECONDARY outcome

Timeframe: Assessed from time of treatment initiation through Day 14

Population: This endpoint was analyzed using the subgroup of patients within the ITT population with aborted lesions.

TTH of aborted primary lesions was defined as the time from treatment initiation to healing of the primary lesion (erythema or papule) or cessation of symptoms, whichever came last. It was to be assessed by the investigator.

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=108 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=85 Participants
muco-adhesive buccal tablet with placebo
TTH of Aborted Primary Lesions
2.57 Days
Interval 2.0 to 2.96
2.67 Days
Interval 2.1 to 3.04

SECONDARY outcome

Timeframe: From time of initial healing through the 9-month follow-up

Population: This endpoint was analyzed using the follow-up population, a subgroup of the ITT population who continued to the 9 month follow-up and had at least 1 diary assessment during that period. The follow-up population was defined as patients whose lesions were healed at the end of Day 14 and had no recurrence within 15 days of healing of all lesions.

Time to recurrence was the time from the healing of all lesions of the initial episode to the occurrence of new lesions.

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=232 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=246 Participants
muco-adhesive buccal tablet with placebo
Time to Recurrence of Non-aborted Lesions During 9-month Follow-up
205.0 Days
95% Confidence Interval 19.4 • Interval 163.0 to 287.0
165.0 Days
95% Confidence Interval 9.3 • Interval 136.0 to 203.0

SECONDARY outcome

Timeframe: From time of initial healing through the 9-month follow-up

Population: This endpoint was analyzed using the follow-up population, a subgroup of the ITT population who continued to the 9 month follow-up and had at least 1 diary assessment during that period. The follow-up population was defined as patients whose lesions were healed at the end of Day 14 and had no recurrence within 15 days of healing of all lesions.

Recurrence was the occurrence of new lesions and was evaluated in a subgroup of patients who agreed to record recurrences during the 9-month follow-up period.

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=267 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=270 Participants
muco-adhesive buccal tablet with placebo
Patient Incidence of Recurrence of Non-aborted Lesions During 9-month Follow-up
Recurrence during 9-month follow-up = yes
149 participants
181 participants
Patient Incidence of Recurrence of Non-aborted Lesions During 9-month Follow-up
Recurrence during 9-month follow-up = no
83 participants
65 participants
Patient Incidence of Recurrence of Non-aborted Lesions During 9-month Follow-up
Recurrence during 9-month follow-up = missing
35 participants
24 participants

SECONDARY outcome

Timeframe: Assessed on Days 1, 3, 5, 7 and 14 (or within 24 hours of healing)

Population: This endpoint was analyzed using the safety population, which consisted of all randomized patients who took at least 1 dose of study medication.

Patients were asked to place a tick mark on a 10 centimeter VAS indicating their symptom intensity. Scale ratings ranged from a minimum of 0 (none at all) to a maximum of 10 (worst possible). The location of the tick mark from "0" was measured in millimeters (0 - 100) and recorded.

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=378 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=397 Participants
muco-adhesive buccal tablet with placebo
Symptom Intensity (Visual Analogue Scale [VAS])
Day 1
30.5 units on a scale (0 - 100)
Standard Deviation 22.37
31.1 units on a scale (0 - 100)
Standard Deviation 22.07
Symptom Intensity (Visual Analogue Scale [VAS])
Day 3
21.2 units on a scale (0 - 100)
Standard Deviation 22.88
22.9 units on a scale (0 - 100)
Standard Deviation 22.60
Symptom Intensity (Visual Analogue Scale [VAS])
Day 5
12.7 units on a scale (0 - 100)
Standard Deviation 17.60
17.3 units on a scale (0 - 100)
Standard Deviation 20.70
Symptom Intensity (Visual Analogue Scale [VAS])
Day 7
8.2 units on a scale (0 - 100)
Standard Deviation 13.63
10.7 units on a scale (0 - 100)
Standard Deviation 18.48
Symptom Intensity (Visual Analogue Scale [VAS])
Day 14 (or within 24 hours of healing)
1.0 units on a scale (0 - 100)
Standard Deviation 5.14
0.9 units on a scale (0 - 100)
Standard Deviation 3.61

SECONDARY outcome

Timeframe: Assessed on Day 14 (or within 24 hours of healing)

Population: This endpoint was analyzed using the ITT population.

At the end of study (Day 14 \[or within 24 hours of healing\]), patients were asked whether they were satisfied with treatment (yes/no).

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=376 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=395 Participants
muco-adhesive buccal tablet with placebo
Patient Satisfaction With Treatment
Satisfied with treatment = yes
297 participants
275 participants
Patient Satisfaction With Treatment
Satisfied with treatment = no
66 participants
105 participants
Patient Satisfaction With Treatment
Missing
13 participants
15 participants

SECONDARY outcome

Timeframe: Assessed on Day 14 (or within 24 hours of healing)

Population: This endpoint was analyzed using the ITT population.

At the end of study (Day 14 \[ or within 24 hours of healing\]), patients were asked to rate efficacy of treatment using a 4-point scale (inactive, mildly active, moderately active, or very active).

Outcome measures

Outcome measures
Measure
Acyclovir Lauriad Group
n=376 Participants
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=395 Participants
muco-adhesive buccal tablet with placebo
Patient Assessment of Efficacy of the Treatment
Inactive
50 participants
79 participants
Patient Assessment of Efficacy of the Treatment
Midly active
49 participants
44 participants
Patient Assessment of Efficacy of the Treatment
Moderately active
100 participants
104 participants
Patient Assessment of Efficacy of the Treatment
Very active
154 participants
146 participants
Patient Assessment of Efficacy of the Treatment
Missing
23 participants
22 participants

Adverse Events

Acyclovir Lauriad Group

Serious events: 0 serious events
Other events: 20 other events
Deaths: 0 deaths

Placebo Group

Serious events: 1 serious events
Other events: 22 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Acyclovir Lauriad Group
n=378 participants at risk
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=397 participants at risk
muco-adhesive buccal tablet with placebo
Immune system disorders
Allergic reaction
0.00%
0/378 • Adverse events were recorded during the 14 day treatment period.
The safety population included all randomized patients who took at least 1 dose of study drug, including 378 patients in the acyclovir Lauriad group and 397 patients in the placebo group.
0.25%
1/397 • Number of events 1 • Adverse events were recorded during the 14 day treatment period.
The safety population included all randomized patients who took at least 1 dose of study drug, including 378 patients in the acyclovir Lauriad group and 397 patients in the placebo group.

Other adverse events

Other adverse events
Measure
Acyclovir Lauriad Group
n=378 participants at risk
Acyclovir Lauriad 50mg muco-adhesive tablet
Placebo Group
n=397 participants at risk
muco-adhesive buccal tablet with placebo
Nervous system disorders
headache
3.2%
12/378 • Number of events 12 • Adverse events were recorded during the 14 day treatment period.
The safety population included all randomized patients who took at least 1 dose of study drug, including 378 patients in the acyclovir Lauriad group and 397 patients in the placebo group.
3.0%
12/397 • Number of events 12 • Adverse events were recorded during the 14 day treatment period.
The safety population included all randomized patients who took at least 1 dose of study drug, including 378 patients in the acyclovir Lauriad group and 397 patients in the placebo group.
Infections and infestations
Nasopharyngitis
1.1%
4/378 • Number of events 4 • Adverse events were recorded during the 14 day treatment period.
The safety population included all randomized patients who took at least 1 dose of study drug, including 378 patients in the acyclovir Lauriad group and 397 patients in the placebo group.
0.76%
3/397 • Number of events 3 • Adverse events were recorded during the 14 day treatment period.
The safety population included all randomized patients who took at least 1 dose of study drug, including 378 patients in the acyclovir Lauriad group and 397 patients in the placebo group.
General disorders
Application Site Pain
1.1%
4/378 • Number of events 4 • Adverse events were recorded during the 14 day treatment period.
The safety population included all randomized patients who took at least 1 dose of study drug, including 378 patients in the acyclovir Lauriad group and 397 patients in the placebo group.
1.0%
4/397 • Number of events 4 • Adverse events were recorded during the 14 day treatment period.
The safety population included all randomized patients who took at least 1 dose of study drug, including 378 patients in the acyclovir Lauriad group and 397 patients in the placebo group.
Gastrointestinal disorders
nausea
0.26%
1/378 • Number of events 1 • Adverse events were recorded during the 14 day treatment period.
The safety population included all randomized patients who took at least 1 dose of study drug, including 378 patients in the acyclovir Lauriad group and 397 patients in the placebo group.
1.5%
6/397 • Number of events 6 • Adverse events were recorded during the 14 day treatment period.
The safety population included all randomized patients who took at least 1 dose of study drug, including 378 patients in the acyclovir Lauriad group and 397 patients in the placebo group.

Additional Information

Dr Pierre ATTALI

BioAlliance Pharma

Phone: +33145587600

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60