Trial Outcomes & Findings for Sunitinib in Recurrent and Refractory Ovarian, Fallopian Tube and Peritoneal Carcinoma (NCT NCT00768144)

NCT ID: NCT00768144

Last Updated: 2018-08-24

Results Overview

Best response on treatment was based on RECIST 1.0 criteria with overall response defined as achieving partial response (PR) or complete response (CR). Per RECIST 1.0 for target lesions, CR is complete disappearance of all target lesions and PR is at least a 30% decrease in the sum of longest diameter (LD) of target lesions, taking as reference baseline sum LD. To be assigned a status of CR or PR, changes in tumor measurements must be confirmed by repeat assessments performed no fewer than 4 weeks after the response criteria are first met. PR or better overall response assumes at a minimum incomplete response/stable disease (SD) for the evaluation of non-target lesions and absence of new lesions.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

36 participants

Primary outcome timeframe

Clinical assessments were performed weekly for first 4 weeks and every 2 wks in subsequent cycles. Disease was evaluated radiologically at baseline, before each odd cycle and at end of trt.

Results posted on

2018-08-24

Participant Flow

Participants were recruited from the GYN Oncology clinics at the DFCI, MGH and BIDMC. Thirty six consenting participants were enrolled over a 19 month period.

Participant milestones

Participant milestones
Measure
Sunitinib
Patients received oral Sunitinib at the daily dose of 37.5 mg continuously over a 28- day treatment cycle. Treatment continued until clinical or radiological evidence of progressive disease or excessive toxicity.
Overall Study
STARTED
36
Overall Study
COMPLETED
0
Overall Study
NOT COMPLETED
36

Reasons for withdrawal

Reasons for withdrawal
Measure
Sunitinib
Patients received oral Sunitinib at the daily dose of 37.5 mg continuously over a 28- day treatment cycle. Treatment continued until clinical or radiological evidence of progressive disease or excessive toxicity.
Overall Study
Adverse Event
13
Overall Study
Progressive Disease
21
Overall Study
Patient or MD Decision to End Treatment
1
Overall Study
Pt Withdrew Consent
1

Baseline Characteristics

Sunitinib in Recurrent and Refractory Ovarian, Fallopian Tube and Peritoneal Carcinoma

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Sunitinib
n=36 Participants
Patients received oral Sunitinib at the daily dose of 37.5 mg continuously over a 28- day treatment cycle. Treatment continued until clinical or radiological evidence of progressive disease or excessive toxicity.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
26 Participants
n=5 Participants
Age, Categorical
>=65 years
10 Participants
n=5 Participants
Age, Continuous
61 years
STANDARD_DEVIATION 8.8 • n=5 Participants
Sex: Female, Male
Female
36 Participants
n=5 Participants
Sex: Female, Male
Male
0 Participants
n=5 Participants
Region of Enrollment
United States
36 participants
n=5 Participants
Histology
Papillary serous
23 participants
n=5 Participants
Histology
Endometrioid
2 participants
n=5 Participants
Histology
Clear cell
5 participants
n=5 Participants
Histology
Mixed Mullerian tumor
3 participants
n=5 Participants
Histology
Other (adenocarcinoma/mixed histology)
3 participants
n=5 Participants

PRIMARY outcome

Timeframe: Clinical assessments were performed weekly for first 4 weeks and every 2 wks in subsequent cycles. Disease was evaluated radiologically at baseline, before each odd cycle and at end of trt.

Population: The analysis dataset is comprised of all treated patients.

Best response on treatment was based on RECIST 1.0 criteria with overall response defined as achieving partial response (PR) or complete response (CR). Per RECIST 1.0 for target lesions, CR is complete disappearance of all target lesions and PR is at least a 30% decrease in the sum of longest diameter (LD) of target lesions, taking as reference baseline sum LD. To be assigned a status of CR or PR, changes in tumor measurements must be confirmed by repeat assessments performed no fewer than 4 weeks after the response criteria are first met. PR or better overall response assumes at a minimum incomplete response/stable disease (SD) for the evaluation of non-target lesions and absence of new lesions.

Outcome measures

Outcome measures
Measure
Sunitinib
n=36 Participants
Patients received oral Sunitinib at the daily dose of 37.5 mg continuously over a 28- day treatment cycle. Treatment continued until clinical or radiological evidence of progressive disease or excessive toxicity.
Overall Response Rate
.083 proportion of participants
Interval 0.024 to 0.21

SECONDARY outcome

Timeframe: Clinical assessments were performed weekly for first 4 weeks and every 2 weeks in subsequent cycles. Disease was evaluated radiologically at baseline, before each odd cycle and at end of treatment.

Population: The analysis dataset is comprised of all treated patients.

16-week progression-free survival is the probability of patients remaining alive and progression-free at 16-weeks from study entry estimated using Kaplan-Meier methods. Patients alive and progression-free at last follow-up are censored. Progressive disease (PD) based on RECIST 1.0 is at least a 20% increase in the sum of longest diameter (LD) of target lesions taking as reference the smallest sum LD recorded since the treatment started or the appearance of one or more new lesions. PD for the evaluation of non-target lesions is the appearance of one or more new lesions and/or equivocal progression of non-target lesions.

Outcome measures

Outcome measures
Measure
Sunitinib
n=36 Participants
Patients received oral Sunitinib at the daily dose of 37.5 mg continuously over a 28- day treatment cycle. Treatment continued until clinical or radiological evidence of progressive disease or excessive toxicity.
16-Week Progression-Free Survival
.36 probability
Interval 0.2 to 0.52

SECONDARY outcome

Timeframe: Clinical assessments were performed weekly for first 4 weeks and every 2 weeks in subsequent cycles. Disease was evaluated radiologically at baseline, before each odd cycle and at end of treatment.

Population: The analysis dataset is comprised of all treated patients.

Progression-free survival estimated using Kaplan-Meier methods is defined as the time from registration to the earlier of death or disease progression. Patients alive without disease progression are censored at the date of last disease evaluation. Progressive disease (PD) based on RECIST 1.0 is at least a 20% increase in the sum of longest diameter (LD) of target lesions taking as reference the smallest sum LD recorded since the treatment started or the appearance of one or more new lesions. Equivocal progression of non-target lesions also qualifies as PD.

Outcome measures

Outcome measures
Measure
Sunitinib
n=36 Participants
Patients received oral Sunitinib at the daily dose of 37.5 mg continuously over a 28- day treatment cycle. Treatment continued until clinical or radiological evidence of progressive disease or excessive toxicity.
Progression-Free Survival
9.9 weeks
Interval 7.1 to 16.4

Adverse Events

Sunitinib

Serious events: 7 serious events
Other events: 36 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Sunitinib
n=36 participants at risk
Sunitinib : Taken orally once a day in the evening
Metabolism and nutrition disorders
Hyperkalemia
2.8%
1/36 • Number of events 1 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Small bowel obstruction
5.6%
2/36 • Number of events 2 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Nervous system disorders
Cerebrovascular accident
2.8%
1/36 • Number of events 1 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Immune system disorders
Allergic reaction
2.8%
1/36 • Number of events 1 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Abdominal pain
2.8%
1/36 • Number of events 1 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
General disorders
Death due to progressive disease
2.8%
1/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.

Other adverse events

Other adverse events
Measure
Sunitinib
n=36 participants at risk
Sunitinib : Taken orally once a day in the evening
Vascular disorders
Hypertension
100.0%
36/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
General disorders
Fatigue
100.0%
36/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Vomiting
100.0%
36/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Blood and lymphatic system disorders
Anemia
22.2%
8/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Investigations
White blood cell increased
30.6%
11/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Investigations
Platelet count decreased
44.4%
16/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Investigations
Weight loss
5.6%
2/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Metabolism and nutrition disorders
Anorexia
11.1%
4/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Diarrhea
63.9%
23/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Nausea
100.0%
36/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Taste disturbance
30.6%
11/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Investigations
Alkaline phosphatase increased
11.1%
4/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Investigations
Neutrophil count decreased
33.3%
12/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Skin and subcutaneous tissue disorders
Palmar-plantar erythrodysesthesia syndrome
25.0%
9/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Constipation
22.2%
8/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Renal and urinary disorders
Proteinuria
100.0%
36/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Abdominal bloating
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Abdominal pain
25.0%
9/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Nervous system disorders
Headache
100.0%
36/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Investigations
Aspartate aminotransferase increased
33.3%
12/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Investigations
Creatinine increased
5.6%
2/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Metabolism and nutrition disorders
Hyperglycemia
19.4%
7/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Metabolism and nutrition disorders
Hypokalemia
11.1%
4/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Respiratory, thoracic and mediastinal disorders
Cough
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Respiratory, thoracic and mediastinal disorders
Dyspnea
11.1%
4/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Mucositis
61.1%
22/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Investigations
Bilirubin increased
5.6%
2/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Metabolism and nutrition disorders
Hyponatremia
19.4%
7/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Musculoskeletal and connective tissue disorders
Arthralgia
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Psychiatric disorders
Depression
5.6%
2/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Investigations
Alanine aminotransferase increased
22.2%
8/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Renal and urinary disorders
Urinary frequency
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Skin and subcutaneous tissue disorders
Alopecia
5.6%
2/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Dyspepsia
19.4%
7/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Respiratory, thoracic and mediastinal disorders
Epistaxis
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Metabolism and nutrition disorders
Hypomagnesemia
13.9%
5/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Metabolism and nutrition disorders
Hypophosphatemia
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Musculoskeletal and connective tissue disorders
Myalgia
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Metabolism and nutrition disorders
Dehydration
13.9%
5/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Skin and subcutaneous tissue disorders
Dry skin
16.7%
6/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Vascular disorders
CNS cerebrovascular ischemia
5.6%
2/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Investigations
White blood cell decreased
11.1%
4/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Nervous system disorders
Neuropathy
19.4%
7/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Gastrointestinal disorders
Dry mouth
5.6%
2/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Metabolism and nutrition disorders
Hypocalcemia
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Renal and urinary disorders
Urine color
5.6%
2/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Musculoskeletal and connective tissue disorders
Back pain
13.9%
5/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Skin and subcutaneous tissue disorders
Rash acneiform
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Musculoskeletal and connective tissue disorders
Pain in extremity
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.
Endocrine disorders
Hypothyroidism
8.3%
3/36 • Assessed each cycle throughout treatment from time of first dose and up to day 30 post-treatment.

Additional Information

Susana M. Campos, MD, MPH

Dana-Farber Cancer Institute

Phone: 617-632-5269

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place