Trial Outcomes & Findings for Pilot and Feasibility Study for the Treatment of Pre-diabetes in Patients With Cystic Fibrosis (NCT NCT00763412)

NCT ID: NCT00763412

Last Updated: 2017-06-05

Results Overview

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

31 participants

Primary outcome timeframe

2 year/end of study

Results posted on

2017-06-05

Participant Flow

Participant milestones

Participant milestones
Measure
Placebo
1 pill before each meal 3-4 times a day for 2 years. placebo: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with placebo by taking 1 pill before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
2. Repaglinide
repaglinide 0.5 mg before each meal 3-4 times a day for 2 years. repaglinide: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with repaglinide 0.5 mg before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
Overall Study
STARTED
8
8
Overall Study
COMPLETED
4
4
Overall Study
NOT COMPLETED
4
4

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Pilot and Feasibility Study for the Treatment of Pre-diabetes in Patients With Cystic Fibrosis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Patients Who Received Repaglinide
n=4 Participants
All participants were receiving ADEK vitamins and pancreatic enzyme replacement. Patients were required to be clinically stable, without evidence of deterioration from previous pulmonary function tests (PFTs) for 3-months prior to the study and without CF exacerbation or hospitalization for 2-months prior to the study. Additionally, patients were required to have maintained stable weight within 5% variance for 3-months prior to participation. Exclusion criteria included fasting blood glucose levels \>126 mg/dL on study day, IV antibiotic or systemic steroid use within two months, oral corticosteroid usage for more than 28-days over the past 6-months, history of lung or liver transplant, elevated transaminases, allergic bronchopulmonary aspergillosis, or the inability to perform spirometry.
Total
n=8 Participants
Total of all reporting groups
Patients Who Received Placebo
n=4 Participants
All participants were receiving ADEK vitamins and pancreatic enzyme replacement. Patients were required to be clinically stable, without evidence of deterioration from previous pulmonary function tests (PFTs) for 3-months prior to the study and without CF exacerbation or hospitalization for 2-months prior to the study. Additionally, patients were required to have maintained stable weight within 5% variance for 3-months prior to participation. Exclusion criteria included fasting blood glucose levels \>126 mg/dL on study day, IV antibiotic or systemic steroid use within two months, oral corticosteroid usage for more than 28-days over the past 6-months, history of lung or liver transplant, elevated transaminases, allergic bronchopulmonary aspergillosis, or the inability to perform spirometry.
Age, Categorical
<=18 years
3 Participants
n=7 Participants
6 Participants
n=5 Participants
3 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
1 Participants
n=7 Participants
2 Participants
n=5 Participants
1 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=7 Participants
0 Participants
n=5 Participants
0 Participants
n=5 Participants
Age, Continuous
15 years
n=7 Participants
15.5 years
n=5 Participants
16 years
n=5 Participants
Sex: Female, Male
Female
3 Participants
n=7 Participants
5 Participants
n=5 Participants
2 Participants
n=5 Participants
Sex: Female, Male
Male
1 Participants
n=7 Participants
3 Participants
n=5 Participants
2 Participants
n=5 Participants
Region of Enrollment
United States
8 participants
n=7 Participants
16 participants
n=5 Participants
8 participants
n=5 Participants
BMI
18.38 Kg/m^2
n=7 Participants
18.94 Kg/m^2
n=5 Participants
19.45 Kg/m^2
n=5 Participants
Wt Z score
-0.29 Z score
n=7 Participants
-0.7 Z score
n=5 Participants
-1.11 Z score
n=5 Participants
Fat %
22.06 % Fat mass
n=7 Participants
21.2 % Fat mass
n=5 Participants
20.34 % Fat mass
n=5 Participants
Lean %
75 % Lean mass
n=7 Participants
75.9 % Lean mass
n=5 Participants
76.71 % Lean mass
n=5 Participants
Tanner stage
3.25 units on a scale
n=7 Participants
3.5 units on a scale
n=5 Participants
3.75 units on a scale
n=5 Participants
FEV 1
92.75 % of lung function
n=7 Participants
95.25 % of lung function
n=5 Participants
97.75 % of lung function
n=5 Participants
Fasting Glucose
100 mg/dl
n=7 Participants
99.6 mg/dl
n=5 Participants
99.1 mg/dl
n=5 Participants
2 hour glucose
183 mg/dl
n=7 Participants
182.7 mg/dl
n=5 Participants
182.4 mg/dl
n=5 Participants
Fasting C-Peptide
1.7 mg/dl
n=7 Participants
1.45 mg/dl
n=5 Participants
1.2 mg/dl
n=5 Participants
2 hour c-peptide
9.5 mg/dl
n=7 Participants
9.6 mg/dl
n=5 Participants
9.7 mg/dl
n=5 Participants
Inflammatory marker
IL1
0.9 pg/ml
n=7 Participants
0.5 pg/ml
n=5 Participants
0.1 pg/ml
n=5 Participants
Inflammatory marker
IL6
12.6 pg/ml
n=7 Participants
10.5 pg/ml
n=5 Participants
8.3 pg/ml
n=5 Participants
Inflammatory marker
IL8
8.5 pg/ml
n=7 Participants
7.75 pg/ml
n=5 Participants
7 pg/ml
n=5 Participants
Inflammatory marker
TNF Alpha
4.5 pg/ml
n=7 Participants
5.9 pg/ml
n=5 Participants
7.3 pg/ml
n=5 Participants
CRP
2.1 mg/L
n=7 Participants
1.95 mg/L
n=5 Participants
1.8 mg/L
n=5 Participants

PRIMARY outcome

Timeframe: 2 year/end of study

Outcome measures

Outcome measures
Measure
1 Placebo
n=4 Participants
1 pill before each meal 3-4 times a day for 2 years. placebo: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with placebo by taking 1 pill before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
2. Repaglinide
n=4 Participants
repaglinide 0.5 mg before each meal 3-4 times a day for 2 years. repaglinide: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with repaglinide 0.5 mg before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
BMI
19.63 Kg/m^2
Interval 15.56 to 22.64
21.19 Kg/m^2
Interval 20.78 to 21.8

PRIMARY outcome

Timeframe: 2 year/end of study

Reporting % of Fat and Lean body mass

Outcome measures

Outcome measures
Measure
1 Placebo
n=4 Participants
1 pill before each meal 3-4 times a day for 2 years. placebo: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with placebo by taking 1 pill before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
2. Repaglinide
n=4 Participants
repaglinide 0.5 mg before each meal 3-4 times a day for 2 years. repaglinide: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with repaglinide 0.5 mg before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
Body Composition
Fat
19.82 % body mass
Interval 12.0 to 37.8
26.21 % body mass
Interval 8.78 to 34.26
Body Composition
Lean
77.15 % body mass
Interval 59.54 to 87.84
70.83 % body mass
Interval 62.82 to 87.8

PRIMARY outcome

Timeframe: 2 year/end of study

Outcome measures

Outcome measures
Measure
1 Placebo
n=4 Participants
1 pill before each meal 3-4 times a day for 2 years. placebo: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with placebo by taking 1 pill before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
2. Repaglinide
n=4 Participants
repaglinide 0.5 mg before each meal 3-4 times a day for 2 years. repaglinide: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with repaglinide 0.5 mg before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
CRP
9.6 mg/L
Interval 0.7 to 27.5
2 mg/L
Interval 0.6 to 3.7

SECONDARY outcome

Timeframe: 2-year

We completed the OGTT at the 2 year/end of study visit.

Outcome measures

Outcome measures
Measure
1 Placebo
n=4 Participants
1 pill before each meal 3-4 times a day for 2 years. placebo: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with placebo by taking 1 pill before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
2. Repaglinide
n=4 Participants
repaglinide 0.5 mg before each meal 3-4 times a day for 2 years. repaglinide: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with repaglinide 0.5 mg before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
Glucose Tolerance
2 hour glucose
185.75 mg/dl
Interval 145.0 to 258.0
184 mg/dl
Interval 123.0 to 266.0
Glucose Tolerance
fasting glucose
101.5 mg/dl
Interval 91.0 to 121.0
94.5 mg/dl
Interval 85.0 to 108.0

SECONDARY outcome

Timeframe: 2 year/end of study

Outcome measures

Outcome measures
Measure
1 Placebo
n=4 Participants
1 pill before each meal 3-4 times a day for 2 years. placebo: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with placebo by taking 1 pill before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
2. Repaglinide
n=4 Participants
repaglinide 0.5 mg before each meal 3-4 times a day for 2 years. repaglinide: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with repaglinide 0.5 mg before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
Inflammatory Markers
IL1
0.14 pg/ml
Interval 0.13 to 0.17
0.34 pg/ml
Interval 0.13 to 1.0
Inflammatory Markers
IL6
10.4 pg/ml
Interval 0.54 to 28.6
6 pg/ml
Interval 2.2 to 11.9
Inflammatory Markers
IL8
5.8 pg/ml
Interval 3.59 to 10.79
5.2 pg/ml
Interval 3.1 to 8.33
Inflammatory Markers
TNF alpha
5.1 pg/ml
Interval 2.05 to 7.5
3.6 pg/ml
Interval 1.99 to 5.3

SECONDARY outcome

Timeframe: 2 year/end of study

Outcome measures

Outcome measures
Measure
1 Placebo
n=4 Participants
1 pill before each meal 3-4 times a day for 2 years. placebo: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with placebo by taking 1 pill before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
2. Repaglinide
n=4 Participants
repaglinide 0.5 mg before each meal 3-4 times a day for 2 years. repaglinide: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with repaglinide 0.5 mg before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
Wt Z Score
-1.21 Z score
Interval -1.94 to 0.08
-0.26 Z score
Interval -0.31 to 0.72

SECONDARY outcome

Timeframe: 2 year/end of study

Puberty scale measuring 1-5, 1 being least development, 5 being most development.

Outcome measures

Outcome measures
Measure
1 Placebo
n=4 Participants
1 pill before each meal 3-4 times a day for 2 years. placebo: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with placebo by taking 1 pill before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
2. Repaglinide
n=4 Participants
repaglinide 0.5 mg before each meal 3-4 times a day for 2 years. repaglinide: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with repaglinide 0.5 mg before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
Tanner Stage
4.25 units on a scale
Interval 4.0 to 5.0
5 units on a scale
Interval 5.0 to 5.0

SECONDARY outcome

Timeframe: 2 year/end of study

% of lung function

Outcome measures

Outcome measures
Measure
1 Placebo
n=4 Participants
1 pill before each meal 3-4 times a day for 2 years. placebo: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with placebo by taking 1 pill before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
2. Repaglinide
n=4 Participants
repaglinide 0.5 mg before each meal 3-4 times a day for 2 years. repaglinide: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with repaglinide 0.5 mg before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
FEV 1
90.5 % lung function
Interval 71.0 to 99.0
91.5 % lung function
Interval 74.0 to 108.0

SECONDARY outcome

Timeframe: 2 year

Outcome measures

Outcome measures
Measure
1 Placebo
n=4 Participants
1 pill before each meal 3-4 times a day for 2 years. placebo: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with placebo by taking 1 pill before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
2. Repaglinide
n=4 Participants
repaglinide 0.5 mg before each meal 3-4 times a day for 2 years. repaglinide: CF pancreatic insufficient patients with prediabetes by OGTT will be treated with repaglinide 0.5 mg before each meal that contains more than 20 grams of carbohydrate 3-4 times a day for 2 years.
C-Peptide
fasting
1.5 pg/ml
Interval 0.8 to 2.3
1.6 pg/ml
Interval 0.6 to 2.5
C-Peptide
2 hour
7.5 pg/ml
Interval 5.0 to 8.7
7.7 pg/ml
Interval 4.2 to 11.9

Adverse Events

Placebo

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Repaglinide

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Ana Maria Arbelaez

Washington University in St Louis

Phone: 314-286-1138

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place