Trial Outcomes & Findings for Phase I Study of Intravenous Lipotecan® (TLC388 HCl for Injection) in Patients With Advanced Solid Tumors (NCT NCT00747474)

NCT ID: NCT00747474

Last Updated: 2019-11-18

Results Overview

MTD is the highest dose of drug that did not cause an unacceptable side effect (= Dose Limiting Toxicity (DLT)). A 3+3 study design was used to determine MTD. The MTD was the highest dose level at which 0 of 3 or 1 of 6 patients experience a DLT, with the next higher dose having at least 2 of 3 or 2 of 6 patients experiencing a DLT.

Recruitment status

COMPLETED

Study phase

PHASE1

Target enrollment

54 participants

Primary outcome timeframe

First treatment to toxicity up to 42 days

Results posted on

2019-11-18

Participant Flow

The study recruitment period was from Sep 2008 to Dec 2010. Patients were recruited from three US clinical sites and one Taiwan site.

Patients will attend the clinic for a screening visit up to 28 days before receiving, if eligible, the first dose of Lipotecan®.

Participant milestones

Participant milestones
Measure
Cohort 1 (1.5 mg/m^2)
Participants received 1.5 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 2 (3 mg/m^2)
Participants received 3 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 3 (6 mg/m^2)
Participants received 6 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 4 (9 mg/m^2)
Participants received 9 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 5 (13.5 mg/m^2)
Participants received 13.5 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 6 (20 mg/m^2)
Participants received 20 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 7 (30 mg/m^2)
Participants received 30 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 8 (40 mg/m^2)
Participants received 40 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 9 (35 mg/m^2)
Participants received 35 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 10 (40 mg/m^2)
Participants received 40 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 11 (50 mg/m^2)
Participants received 50 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 12 (60 mg/m^2)
Participants received 60 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 1 (1.5 mg/m^2) Period
STARTED
3
0
0
0
0
0
0
0
0
0
0
0
Cohort 1 (1.5 mg/m^2) Period
COMPLETED
3
0
0
0
0
0
0
0
0
0
0
0
Cohort 1 (1.5 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0
Cohort 2 (3 mg/m^2) Period
STARTED
0
4
0
0
0
0
0
0
0
0
0
0
Cohort 2 (3 mg/m^2) Period
COMPLETED
0
4
0
0
0
0
0
0
0
0
0
0
Cohort 2 (3 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0
Cohort 3 (6 mg/m^2) Period
STARTED
0
0
3
0
0
0
0
0
0
0
0
0
Cohort 3 (6 mg/m^2) Period
COMPLETED
0
0
3
0
0
0
0
0
0
0
0
0
Cohort 3 (6 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0
Cohort 4 (9 mg/m^2) Period
STARTED
0
0
0
4
0
0
0
0
0
0
0
0
Cohort 4 (9 mg/m^2) Period
COMPLETED
0
0
0
4
0
0
0
0
0
0
0
0
Cohort 4 (9 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0
Cohort 5 (13.5 mg/m^2) Period
STARTED
0
0
0
0
4
0
0
0
0
0
0
0
Cohort 5 (13.5 mg/m^2) Period
COMPLETED
0
0
0
0
4
0
0
0
0
0
0
0
Cohort 5 (13.5 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0
Cohort 6 (20 mg/m^2) Period
STARTED
0
0
0
0
0
4
0
0
0
0
0
0
Cohort 6 (20 mg/m^2) Period
COMPLETED
0
0
0
0
0
4
0
0
0
0
0
0
Cohort 6 (20 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0
Cohort 7 (30 mg/m^2) Period
STARTED
0
0
0
0
0
0
4
0
0
0
0
0
Cohort 7 (30 mg/m^2) Period
COMPLETED
0
0
0
0
0
0
4
0
0
0
0
0
Cohort 7 (30 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0
Cohort 8 (40 mg/m^2) Period
STARTED
0
0
0
0
0
0
0
6
0
0
0
0
Cohort 8 (40 mg/m^2) Period
COMPLETED
0
0
0
0
0
0
0
5
0
0
0
0
Cohort 8 (40 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
1
0
0
0
0
Cohort 9 (35 mg/m^2) Period
STARTED
0
0
0
0
0
0
0
0
4
0
0
0
Cohort 9 (35 mg/m^2) Period
COMPLETED
0
0
0
0
0
0
0
0
4
0
0
0
Cohort 9 (35 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0
Cohort 10 (40 mg/m^2) Period
STARTED
0
0
0
0
0
0
0
0
0
7
0
0
Cohort 10 (40 mg/m^2) Period
COMPLETED
0
0
0
0
0
0
0
0
0
7
0
0
Cohort 10 (40 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0
Cohort 11 (50 mg/m^2) Period
STARTED
0
0
0
0
0
0
0
0
0
0
5
0
Cohort 11 (50 mg/m^2) Period
COMPLETED
0
0
0
0
0
0
0
0
0
0
5
0
Cohort 11 (50 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0
Cohort 12 (60 mg/m^2) Period
STARTED
0
0
0
0
0
0
0
0
0
0
0
6
Cohort 12 (60 mg/m^2) Period
COMPLETED
0
0
0
0
0
0
0
0
0
0
0
6
Cohort 12 (60 mg/m^2) Period
NOT COMPLETED
0
0
0
0
0
0
0
0
0
0
0
0

Reasons for withdrawal

Reasons for withdrawal
Measure
Cohort 1 (1.5 mg/m^2)
Participants received 1.5 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 2 (3 mg/m^2)
Participants received 3 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 3 (6 mg/m^2)
Participants received 6 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 4 (9 mg/m^2)
Participants received 9 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 5 (13.5 mg/m^2)
Participants received 13.5 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 6 (20 mg/m^2)
Participants received 20 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 7 (30 mg/m^2)
Participants received 30 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 8 (40 mg/m^2)
Participants received 40 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 9 (35 mg/m^2)
Participants received 35 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 10 (40 mg/m^2)
Participants received 40 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 11 (50 mg/m^2)
Participants received 50 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 12 (60 mg/m^2)
Participants received 60 mg/m\^2/dose, given as a 30 minute IV infusion on Days 1, 8 and 15 of a 28 day cycle. Each 28 day (4 week) period will constitute one cycle of treatment. Dose escalation of Lipotecan® will be based upon the safety and tolerability data from the first treatment cycle in each patient and determined by Safety Review Committee (SRC) for this study.
Cohort 8 (40 mg/m^2) Period
with efficacy and continued treatment
0
0
0
0
0
0
0
1
0
0
0
0

Baseline Characteristics

Phase I Study of Intravenous Lipotecan® (TLC388 HCl for Injection) in Patients With Advanced Solid Tumors

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Overall Population
n=54 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
32 Participants
n=5 Participants
Age, Categorical
>=65 years
22 Participants
n=5 Participants
Age, Continuous
60.5 years
STANDARD_DEVIATION 11.6 • n=5 Participants
Sex: Female, Male
Female
22 Participants
n=5 Participants
Sex: Female, Male
Male
32 Participants
n=5 Participants
Region of Enrollment
United States
41 participants
n=5 Participants
Region of Enrollment
Taiwan
13 participants
n=5 Participants

PRIMARY outcome

Timeframe: First treatment to toxicity up to 42 days

Population: Patients received at least one dose of Lipotecan.

MTD is the highest dose of drug that did not cause an unacceptable side effect (= Dose Limiting Toxicity (DLT)). A 3+3 study design was used to determine MTD. The MTD was the highest dose level at which 0 of 3 or 1 of 6 patients experience a DLT, with the next higher dose having at least 2 of 3 or 2 of 6 patients experiencing a DLT.

Outcome measures

Outcome measures
Measure
All Participants
n=54 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Maximum Tolerated Dose (MTD) of Lipotecan
50 mg/m^2

PRIMARY outcome

Timeframe: an average of 6 months

Population: Patients received at least one dose of Lipotecan

Number of participants with AEs that occurred during treatment and follow-up period (30 days after last treatment). Drug-related AEs and SAEs were followed until resolved or stabilized. AEs were classified by the investigator according to severity graded using CTCAE version 3.0 and relationship to study drug. The severity scale is: Grade 1= Mild, Grade 2= Moderate, Grade 3= Severe, Grade 4= Life-threatening or disabling, Grade 5= Death related to AE

Outcome measures

Outcome measures
Measure
All Participants
n=54 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Number of Participants With Adverse Events
54 participants

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Maximum Observed Dose-normalized Plasma Concentration (Cmax) of S,R-TLC388
1.39 ng/mL
Standard Deviation 3.21

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Maximum Observed Dose-normalized Plasma Concentration (Cmax) of S,S-TLC388
2.21 ng/mL
Standard Deviation 5.12

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Maximum Observed Dose-normalized Plasma Concentration (Cmax) of Topotecan
0.82 ng/mL
Standard Deviation 0.44

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Maximum Observed Dose-normalized Plasma Concentration (Cmax) of TLC-U1
5.01 ng/mL
Standard Deviation 1.91

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1h, 1h30m, 2h, 4h, 8h

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Maximum Observed Dose-normalized Plasma Concentration (Cmax) of TLC-U2
1.40 ng/mL
Standard Deviation 0.48

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Time to Reach Maximum Observed Plasma Concentration (Tmax) of S,R-TLC388
0.47 hour
Standard Deviation 0.30

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Time to Reach Maximum Observed Plasma Concentration (Tmax) of S,S-TLC388
0.47 hour
Standard Deviation 0.30

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Time to Reach Maximum Observed Plasma Concentration (Tmax) of Topotecan
0.93 hour
Standard Deviation 0.82

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Time to Reach Maximum Observed Plasma Concentration (Tmax) of TLC-U1
0.45 hour
Standard Deviation 0.17

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Time to Reach Maximum Observed Plasma Concentration (Tmax) of TLC-U2
0.47 hour
Standard Deviation 0.14

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Dose-normalized Area Under the Curve From Time Zero to Last Quantifiable Concentration [AUC (0-t)] of S,R-TLC388
0.70 hr*ng/mL
Standard Deviation 1.63

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Dose-normalized Area Under the Curve From Time Zero to Last Quantifiable Concentration [AUC (0-t)] of S,S-TLC388
1.04 hr*ng/mL
Standard Deviation 2.44

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Dose-normalized Area Under the Curve From Time Zero to Last Quantifiable Concentration [AUC (0-t)] of Topotecan
3.59 hr*ng/mL
Standard Deviation 1.30

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Dose-normalized Area Under the Curve From Time Zero to Last Quantifiable Concentration [AUC (0-t)] of TLC-U1
7.15 hr*ng/mL
Standard Deviation 2.20

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Dose-normalized Area Under the Curve From Time Zero to Last Quantifiable Concentration [AUC (0-t)] of TLC-U2
2.00 hr*ng/mL
Standard Deviation 0.66

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Plasma Decay Half-Life (t1/2) of S,R-TLC388
1.08 hour
Standard Deviation 1.77

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Plasma Decay Half-Life (t1/2) of S,S-TLC388
0.75 hour
Standard Deviation 1.18

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Plasma Decay Half-Life (t1/2) of Topotecan
6.05 hour
Standard Deviation 2.71

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Plasma Decay Half-Life (t1/2) of TLC-U1
3.13 hour
Standard Deviation 1.27

PRIMARY outcome

Timeframe: 0, 15m, 29m, 33m, 40m, 50m, 1 h, 1h 30m, 2h, 4h, 8h post-dose

Population: Patients complete cycle 1 and 2 treatments without major protocol deviation.

Drug product Lipotecan consists of TLC388 diastereomers (S,S-TLC388 and S,R-TLC388 in 2:1 ratio). Three metabolites as TLC-U1, TLC-U2 and topotecan were identified in rats, dogs and human.

Outcome measures

Outcome measures
Measure
All Participants
n=48 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Plasma Decay Half-Life (t1/2) of TLC-U2
2.58 hour
Standard Deviation 0.62

SECONDARY outcome

Timeframe: From start of treatment assessed every 2 cycles up to 2.5 years

Population: Patients received at least one dose of Lipotecan.

Patients were evaluated by tumor assessment using RECIST guidelines. Possible evaluations include: Complete Response (CR): disappearance of all target lesions. Partial Response (PR): at least a 30% decrease in the size of target lesions. Progressive Disease (PD): at least a 20% increase in the size of target lesions. Stable Disease (SD): neither sufficient shrinkage to qualify for PR nor sufficient increase to qualify for PD.

Outcome measures

Outcome measures
Measure
All Participants
n=54 Participants
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle according to the dose assigned.
Anti-tumor Activity
Complete Response (CR)
0 participants
Anti-tumor Activity
Partitial Response (PR)
0 participants
Anti-tumor Activity
Stable Disease (SD)
21 participants
Anti-tumor Activity
Progression Disease (PD)
20 participants
Anti-tumor Activity
No assessment
13 participants

Adverse Events

Overall Population

Serious events: 11 serious events
Other events: 54 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Overall Population
n=54 participants at risk
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle.
Gastrointestinal disorders
ABDOMINAL PAIN
1.9%
1/54 • Number of events 1 • 32 months
Cardiac disorders
ACUTE MYOCARDIAL INFARCTION
1.9%
1/54 • Number of events 1 • 32 months
Blood and lymphatic system disorders
ANAEMIA
3.7%
2/54 • Number of events 3 • 32 months
General disorders
ASTHENIA
1.9%
1/54 • Number of events 1 • 32 months
Cardiac disorders
CARDIO-RESPIRATORY ARREST
1.9%
1/54 • Number of events 1 • 32 months
Nervous system disorders
CEREBROVASCULAR ACCIDENT
3.7%
2/54 • Number of events 2 • 32 months
Infections and infestations
CYSTITIS KLEBSIELLA
1.9%
1/54 • Number of events 1 • 32 months
Metabolism and nutrition disorders
DEHYDRATION
1.9%
1/54 • Number of events 1 • 32 months
Gastrointestinal disorders
DIARRHOEA
1.9%
1/54 • Number of events 1 • 32 months
Gastrointestinal disorders
ENTEROVESICAL FISTULA
1.9%
1/54 • Number of events 1 • 32 months
Infections and infestations
ESCHERICHIA URINARY TRACT INFECTION
1.9%
1/54 • Number of events 1 • 32 months
Blood and lymphatic system disorders
FEBRILE NEUTROPENIA
1.9%
1/54 • Number of events 1 • 32 months
Musculoskeletal and connective tissue disorders
FLANK PAIN
1.9%
1/54 • Number of events 1 • 32 months
Renal and urinary disorders
HAEMATURIA
1.9%
1/54 • Number of events 1 • 32 months
Vascular disorders
HYPERTENSION
1.9%
1/54 • Number of events 1 • 32 months
Metabolism and nutrition disorders
HYPONATRAEMIA
3.7%
2/54 • Number of events 2 • 32 months
Infections and infestations
INFECTIVE EXACERBATION OF CHRONIC OBSTRUCTIVE AIRWAYS DISEASE
1.9%
1/54 • Number of events 1 • 32 months
Blood and lymphatic system disorders
LEUKOPENIA
1.9%
1/54 • Number of events 2 • 32 months
Blood and lymphatic system disorders
NEUTROPENIA
1.9%
1/54 • Number of events 1 • 32 months
Infections and infestations
PYELONEPHRITIS
1.9%
1/54 • Number of events 1 • 32 months
Blood and lymphatic system disorders
THROMBOCYTOPENIA
3.7%
2/54 • Number of events 3 • 32 months
Infections and infestations
URINARY TRACT INFECTION
3.7%
2/54 • Number of events 2 • 32 months

Other adverse events

Other adverse events
Measure
Overall Population
n=54 participants at risk
Lipotecan was administered intravenously on day 1, 8 and 15 of a 28-day cycle.
Gastrointestinal disorders
ABDOMINAL DISTENSION
5.6%
3/54 • Number of events 4 • 32 months
Gastrointestinal disorders
ABDOMINAL PAIN
18.5%
10/54 • Number of events 19 • 32 months
Gastrointestinal disorders
ABDOMINAL PAIN UPPER
11.1%
6/54 • Number of events 7 • 32 months
Investigations
ALANINE AMINOTRANSFERASE INCREASED
5.6%
3/54 • Number of events 3 • 32 months
Skin and subcutaneous tissue disorders
ALOPECIA
7.4%
4/54 • Number of events 4 • 32 months
Blood and lymphatic system disorders
ANAEMIA
63.0%
34/54 • Number of events 106 • 32 months
Musculoskeletal and connective tissue disorders
ARTHRALGIA
9.3%
5/54 • Number of events 6 • 32 months
Musculoskeletal and connective tissue disorders
BACK PAIN
11.1%
6/54 • Number of events 8 • 32 months
Investigations
BLOOD ALKALINE PHOSPHATASE INCREASED
5.6%
3/54 • Number of events 4 • 32 months
Gastrointestinal disorders
CONSTIPATION
25.9%
14/54 • Number of events 20 • 32 months
Respiratory, thoracic and mediastinal disorders
COUGH
13.0%
7/54 • Number of events 7 • 32 months
Metabolism and nutrition disorders
DECREASED APPETITE
22.2%
12/54 • Number of events 17 • 32 months
Gastrointestinal disorders
DIARRHOEA
27.8%
15/54 • Number of events 25 • 32 months
Nervous system disorders
DIZZINESS
14.8%
8/54 • Number of events 8 • 32 months
Respiratory, thoracic and mediastinal disorders
DYSPNOEA
7.4%
4/54 • Number of events 5 • 32 months
General disorders
FATIGUE
40.7%
22/54 • Number of events 48 • 32 months
Musculoskeletal and connective tissue disorders
FLANK PAIN
5.6%
3/54 • Number of events 3 • 32 months
Metabolism and nutrition disorders
HYPERCALCAEMIA
5.6%
3/54 • Number of events 3 • 32 months
Metabolism and nutrition disorders
HYPOALBUMINAEMIA
13.0%
7/54 • Number of events 7 • 32 months
Metabolism and nutrition disorders
HYPOCALCAEMIA
13.0%
7/54 • Number of events 9 • 32 months
Metabolism and nutrition disorders
HYPOKALAEMIA
7.4%
4/54 • Number of events 4 • 32 months
Metabolism and nutrition disorders
HYPONATRAEMIA
13.0%
7/54 • Number of events 7 • 32 months
Metabolism and nutrition disorders
HYPOPHOSPHATAEMIA
5.6%
3/54 • Number of events 3 • 32 months
Vascular disorders
HYPOTENSION
5.6%
3/54 • Number of events 5 • 32 months
Psychiatric disorders
INSOMNIA
9.3%
5/54 • Number of events 5 • 32 months
Investigations
INTERNATIONAL NORMALISED RATIO INCREASED
5.6%
3/54 • Number of events 3 • 32 months
Blood and lymphatic system disorders
LEUKOPENIA
24.1%
13/54 • Number of events 23 • 32 months
Musculoskeletal and connective tissue disorders
MUSCLE SPASMS
9.3%
5/54 • Number of events 8 • 32 months
Musculoskeletal and connective tissue disorders
MUSCULOSKELETAL PAIN
9.3%
5/54 • Number of events 5 • 32 months
Gastrointestinal disorders
NAUSEA
37.0%
20/54 • Number of events 30 • 32 months
Blood and lymphatic system disorders
NEUTROPENIA
27.8%
15/54 • Number of events 54 • 32 months
General disorders
OEDEMA PERIPHERAL
16.7%
9/54 • Number of events 9 • 32 months
Musculoskeletal and connective tissue disorders
PAIN IN EXTREMITY
7.4%
4/54 • Number of events 4 • 32 months
Skin and subcutaneous tissue disorders
PRURITUS
7.4%
4/54 • Number of events 8 • 32 months
General disorders
PYREXIA
7.4%
4/54 • Number of events 4 • 32 months
Blood and lymphatic system disorders
THROMBOCYTOPENIA
24.1%
13/54 • Number of events 31 • 32 months
Infections and infestations
URINARY TRACT INFECTION
9.3%
5/54 • Number of events 5 • 32 months
Gastrointestinal disorders
VOMITING
25.9%
14/54 • Number of events 24 • 32 months
Investigations
WEIGHT DECREASED
5.6%
3/54 • Number of events 3 • 32 months

Additional Information

Shu Chi Hsu

Taiwan Liposome Company, Ltd.

Phone: 650-872-8816

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: GT60