Trial Outcomes & Findings for Follow-Up Study for Exubera (NCT NCT00734591)

NCT ID: NCT00734591

Last Updated: 2012-10-23

Results Overview

Reported deaths from primary lung cancer were adjudicated and classified into 4 categories: highly likely (clinical, radiographic, and/or histological data consistent with primary lung cancer); likely (some information may have been missing for definite diagnosis); unlikely; insufficient information. Highly likely and likely cases used to report rate and rate ratio of primary lung cancer mortality. Includes events from the start of the original trial to the end of FUSE.

Recruitment status

COMPLETED

Target enrollment

7439 participants

Primary outcome timeframe

Baseline from original trial up to Year 2 of this study

Results posted on

2012-10-23

Participant Flow

This study had retrospective and prospective components. Individuals who participated in Exubera-controlled trials that were still active in 2003 or later participated in the retrospective part of this study (Follow-Up Study for Exubera; FUSE). Individuals from sites participating in the prospective part of FUSE were eligible.

Participant milestones

Participant milestones
Measure
Previously Randomized to Exubera
Participants randomized to Exubera® (inhalable form of recombinant human \[rh\] insulin) per protocol in a prior Exubera-controlled clinical trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Previously Randomized to Comparator
Participants randomized to comparator (Type 1 or Type 2 diabetes mellitus treatments such as injected insulin or oral agent therapy) in a prior Exubera-controlled trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Retrospective Period
STARTED
3875
3564
Retrospective Period
COMPLETED
3875
3564
Retrospective Period
NOT COMPLETED
0
0
Screening for Prospective Period
STARTED
3875
3564
Screening for Prospective Period
COMPLETED
1358
1273
Screening for Prospective Period
NOT COMPLETED
2517
2291
Prospective Period
STARTED
1358
1273
Prospective Period
COMPLETED
1307
1229
Prospective Period
NOT COMPLETED
51
44

Reasons for withdrawal

Reasons for withdrawal
Measure
Previously Randomized to Exubera
Participants randomized to Exubera® (inhalable form of recombinant human \[rh\] insulin) per protocol in a prior Exubera-controlled clinical trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Previously Randomized to Comparator
Participants randomized to comparator (Type 1 or Type 2 diabetes mellitus treatments such as injected insulin or oral agent therapy) in a prior Exubera-controlled trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Screening for Prospective Period
Site did not participate
1604
1488
Screening for Prospective Period
Patient at partic. site not enrolled
913
803
Prospective Period
Withdrawal by Subject
11
9
Prospective Period
Lost to Follow-up
37
33
Prospective Period
Study Terminated
1
0
Prospective Period
Other
2
2

Baseline Characteristics

Follow-Up Study for Exubera

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Previously Randomized to Exubera
n=3875 Participants
Participants randomized to Exubera® (inhalable form of recombinant human \[rh\] insulin) per protocol in a prior Exubera-controlled clinical trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Previously Randomized to Comparator
n=3564 Participants
Participants randomized to comparator (Type 1 or Type 2 diabetes mellitus treatments such as injected insulin or oral agent therapy) in a prior Exubera-controlled trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Total
n=7439 Participants
Total of all reporting groups
Age Continuous
54.8 years
STANDARD_DEVIATION 12.1 • n=5 Participants
54.7 years
STANDARD_DEVIATION 12.6 • n=7 Participants
54.8 years
STANDARD_DEVIATION 12.4 • n=5 Participants
Sex: Female, Male
Female
1677 Participants
n=5 Participants
1557 Participants
n=7 Participants
3234 Participants
n=5 Participants
Sex: Female, Male
Male
2198 Participants
n=5 Participants
2007 Participants
n=7 Participants
4205 Participants
n=5 Participants
Smoking status
Never-smoker
2194 participants
n=5 Participants
2031 participants
n=7 Participants
4225 participants
n=5 Participants
Smoking status
Ever-smoker
1681 participants
n=5 Participants
1533 participants
n=7 Participants
3214 participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline from original trial up to Year 2 of this study

Population: Entire study population: all randomized participants (retrospective).

Reported deaths from primary lung cancer were adjudicated and classified into 4 categories: highly likely (clinical, radiographic, and/or histological data consistent with primary lung cancer); likely (some information may have been missing for definite diagnosis); unlikely; insufficient information. Highly likely and likely cases used to report rate and rate ratio of primary lung cancer mortality. Includes events from the start of the original trial to the end of FUSE.

Outcome measures

Outcome measures
Measure
Previously Randomized to Exubera
n=3875 Participants
Participants randomized to Exubera® (inhalable form of recombinant human \[rh\] insulin) per protocol in a prior Exubera-controlled clinical trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Previously Randomized to Comparator
n=3654 Participants
Participants randomized to comparator (Type 1 or Type 2 diabetes mellitus treatments such as injected insulin or oral agent therapy) in a prior Exubera-controlled trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Rate of Primary Lung Cancer Mortality
0.48 Deaths per 1000 patient years (PY)
Interval 0.17 to 1.04
0.17 Deaths per 1000 patient years (PY)
Interval 0.02 to 0.61

SECONDARY outcome

Timeframe: Baseline from original trial up to Year 2 of this study

Population: Subset of the entire study population who were former smokers.

Reported deaths from primary lung cancer were adjudicated and classified into 4 categories: highly likely (clinical, radiographic, and/or histological data consistent with primary lung cancer); likely (some information may have been missing for definite diagnosis); unlikely; insufficient information. Highly likely and likely cases used to report rate and rate ratio of primary lung cancer mortality. Includes events from the start of the original trial to the end of FUSE.

Outcome measures

Outcome measures
Measure
Previously Randomized to Exubera
n=1681 Participants
Participants randomized to Exubera® (inhalable form of recombinant human \[rh\] insulin) per protocol in a prior Exubera-controlled clinical trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Previously Randomized to Comparator
n=1533 Participants
Participants randomized to comparator (Type 1 or Type 2 diabetes mellitus treatments such as injected insulin or oral agent therapy) in a prior Exubera-controlled trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Rate of Primary Lung Cancer Mortality Among Former Smokers
0.94 Deaths per 1000 PY
Interval 0.3 to 2.18
0.41 Deaths per 1000 PY
Interval 0.05 to 1.48

SECONDARY outcome

Timeframe: Baseline from original trial up to Year 2 of this study

Population: Entire study population

The rate and rate ratio of all-cause mortality that occurred anytime from the start of the original trial to the end of FUSE.

Outcome measures

Outcome measures
Measure
Previously Randomized to Exubera
n=3875 Participants
Participants randomized to Exubera® (inhalable form of recombinant human \[rh\] insulin) per protocol in a prior Exubera-controlled clinical trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Previously Randomized to Comparator
n=3564 Participants
Participants randomized to comparator (Type 1 or Type 2 diabetes mellitus treatments such as injected insulin or oral agent therapy) in a prior Exubera-controlled trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Rate of All-cause Mortality
6.03 Deaths per 1000 PY
Interval 4.75 to 7.55
7.37 Deaths per 1000 PY
Interval 5.9 to 9.09

SECONDARY outcome

Timeframe: Baseline from original trial up to Year 2 of this study

Population: Entire study population

The rate and rate ratio of lung cancer adjudicated as highly likely (clinical, radiographic, and/or histological data consistent with primary lung cancer) or likely (some information may have been missing for definite diagnosis) to be newly diagnosed primary lung cancer that occurred anytime from the start of the original trial to the end of FUSE.

Outcome measures

Outcome measures
Measure
Previously Randomized to Exubera
n=3875 Participants
Participants randomized to Exubera® (inhalable form of recombinant human \[rh\] insulin) per protocol in a prior Exubera-controlled clinical trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Previously Randomized to Comparator
n=3564 Participants
Participants randomized to comparator (Type 1 or Type 2 diabetes mellitus treatments such as injected insulin or oral agent therapy) in a prior Exubera-controlled trial. There was no active study medication used in FUSE. During prospective follow-up all participants received treatment for diabetes mellitus per routine clinical practice.
Rate of Primary Lung Cancer Diagnosis
1.07 Lung Cancer per 1000 PY
Interval 0.55 to 1.87
0.29 Lung Cancer per 1000 PY
Interval 0.06 to 0.84

Adverse Events

Previously Randomized to Exubera

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Previously Randomized to Comparator

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Pfizer ClinicalTrials.gov Call Center

Pfizer, Inc.

Phone: 1-800-718-1021

Results disclosure agreements

  • Principal investigator is a sponsor employee Pfizer has the right to review disclosures, requesting a delay of less than 60 days. Investigator will postpone single center publications until after disclosure of pooled data (all sites), less than 12 months from study completion/termination at all participating sites. Investigator may not disclose previously undisclosed confidential information other than study results.
  • Publication restrictions are in place

Restriction type: OTHER