Trial Outcomes & Findings for Ketoconazole, Hydrocortisone and Dutasteride in Asymptomatic Hormone Refractory Prostate Cancer (NCT NCT00673127)

NCT ID: NCT00673127

Last Updated: 2015-04-22

Results Overview

PSA decline of 50% from baseline confirmed by a PSA at least 4 weeks later.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

57 participants

Primary outcome timeframe

From treatment initiation until treatment cessation. Maximum 32 months. Median treament duration 8 months.

Results posted on

2015-04-22

Participant Flow

Medical oncology clinics

Required 6 week washout for any AR antagonists

Participant milestones

Participant milestones
Measure
KHAD
KHAD; ketoconazole, hydrocortisone and dutasteride for CRPC
Overall Study
STARTED
57
Overall Study
COMPLETED
57
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Ketoconazole, Hydrocortisone and Dutasteride in Asymptomatic Hormone Refractory Prostate Cancer

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
KHAD
n=57 Participants
Ketoconazole, Hydrocortisone and Dutasteride
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
32 Participants
n=5 Participants
Age, Categorical
>=65 years
25 Participants
n=5 Participants
Age, Continuous
62 years
STANDARD_DEVIATION 7 • n=5 Participants
Sex: Female, Male
Female
0 Participants
n=5 Participants
Sex: Female, Male
Male
57 Participants
n=5 Participants
Region of Enrollment
United States
49 participants
n=5 Participants
Region of Enrollment
Canada
8 participants
n=5 Participants

PRIMARY outcome

Timeframe: From treatment initiation until treatment cessation. Maximum 32 months. Median treament duration 8 months.

PSA decline of 50% from baseline confirmed by a PSA at least 4 weeks later.

Outcome measures

Outcome measures
Measure
KHAD
n=57 Participants
Ketoconazole, Hydrocortisone and Dutasteride
PSA Response
56 percentage of participants
Interval 42.4 to 69.3

SECONDARY outcome

Timeframe: Duration of time from treatment initiation until documented progression. Maximum 32 months

Duration of time from treatment initiation until documented progression (PSA or Disease progression)

Outcome measures

Outcome measures
Measure
KHAD
n=57 Participants
Ketoconazole, Hydrocortisone and Dutasteride
Time to Progression
14.5 months
Interval 11.0 to 17.0

Adverse Events

KHAD

Serious events: 1 serious events
Other events: 56 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
KHAD
n=57 participants at risk
Ketoconazole, Hydrocortisone and Dutasteride
Vascular disorders
grade 4 thrombosis
1.8%
1/57 • Number of events 1

Other adverse events

Other adverse events
Measure
KHAD
n=57 participants at risk
Ketoconazole, Hydrocortisone and Dutasteride
Blood and lymphatic system disorders
Hemoglobin
40.4%
23/57
Blood and lymphatic system disorders
Hematologic-other
1.8%
1/57
Cardiac disorders
Cardiomyopathy, restrictive
1.8%
1/57
Cardiac disorders
Cardiac-other
1.8%
1/57
Ear and labyrinth disorders
Tinnitus
1.8%
1/57
Endocrine disorders
Endocrine-other
1.8%
1/57
Eye disorders
Cataract
1.8%
1/57
Eye disorders
Dry eye syndrome
5.3%
3/57
Eye disorders
Vision-blurred
3.5%
2/57
Eye disorders
Tearing
1.8%
1/57
Eye disorders
Ocular-other
3.5%
2/57
Gastrointestinal disorders
Constipation
8.8%
5/57
Gastrointestinal disorders
Diarrhea w/o prior colostomy
7.0%
4/57
Gastrointestinal disorders
Distention/bloating, abdominal
1.8%
1/57
Gastrointestinal disorders
Dry mouth
7.0%
4/57
Gastrointestinal disorders
Esophagitis
1.8%
1/57
Gastrointestinal disorders
Flatulence
1.8%
1/57
Gastrointestinal disorders
Gastritis
1.8%
1/57
Gastrointestinal disorders
Dyspepsia
10.5%
6/57
Gastrointestinal disorders
Incontinence, anal
1.8%
1/57
Gastrointestinal disorders
Nausea
24.6%
14/57
Gastrointestinal disorders
Vomiting
7.0%
4/57
Gastrointestinal disorders
GI-other
8.8%
5/57
General disorders
Fatigue
36.8%
21/57
General disorders
Fever w/o neutropenia
1.8%
1/57
General disorders
Constitutional, other
10.5%
6/57
General disorders
Edema head and neck
1.8%
1/57
General disorders
Edema limb
17.5%
10/57
General disorders
Pain-other
8.8%
5/57
Infections and infestations
Infection Gr0-2 neut, sinus
1.8%
1/57
Infections and infestations
Infection-other
1.8%
1/57
Injury, poisoning and procedural complications
Bruising
3.5%
2/57
Investigations
Lymphopenia
5.3%
3/57
Investigations
Weight gain
3.5%
2/57
Investigations
Alkaline phosphatase
10.5%
6/57
Investigations
ALT, SGPT
47.4%
27/57
Investigations
AST, SGOT
50.9%
29/57
Investigations
Bilirubin
5.3%
3/57
Investigations
Creatinine
26.3%
15/57
Investigations
Metabolic/Laboratory-other
3.5%
2/57
Metabolism and nutrition disorders
Pancreatic glucose intolerance
1.8%
1/57
Metabolism and nutrition disorders
Hypoalbuminemia
1.8%
1/57
Metabolism and nutrition disorders
Hypocalcemia
1.8%
1/57
Metabolism and nutrition disorders
Hyperglycemia
36.8%
21/57
Metabolism and nutrition disorders
Hypoglycemia
7.0%
4/57
Metabolism and nutrition disorders
Hypomagnesemia
1.8%
1/57
Metabolism and nutrition disorders
Hyperkalemia
3.5%
2/57
Metabolism and nutrition disorders
Hypokalemia
10.5%
6/57
Metabolism and nutrition disorders
Hyponatremia
1.8%
1/57
Metabolism and nutrition disorders
Hyperuricemia
3.5%
2/57
Musculoskeletal and connective tissue disorders
Nonneuropathic lower extr muscle weak
3.5%
2/57
Musculoskeletal and connective tissue disorders
Nonneuropathic generalized weakness
1.8%
1/57
Musculoskeletal and connective tissue disorders
Back, pain
1.8%
1/57
Musculoskeletal and connective tissue disorders
Extremity-limb, pain
1.8%
1/57
Nervous system disorders
Taste disturbance
10.5%
6/57
Nervous system disorders
Cognitive disturbance
1.8%
1/57
Nervous system disorders
Dizziness
3.5%
2/57
Nervous system disorders
Memory impairment
1.8%
1/57
Nervous system disorders
Neuropathy-sensory
1.8%
1/57
Nervous system disorders
Neurologic-other
5.3%
3/57
Nervous system disorders
Head/headache
7.0%
4/57
Psychiatric disorders
Insomnia
8.8%
5/57
Psychiatric disorders
Agitation
5.3%
3/57
Psychiatric disorders
Anxiety
1.8%
1/57
Psychiatric disorders
Depression
5.3%
3/57
Psychiatric disorders
Personality
1.8%
1/57
Renal and urinary disorders
Cystitis
1.8%
1/57
Renal and urinary disorders
Incontinence urinary
3.5%
2/57
Renal and urinary disorders
Urinary frequency/urgency
10.5%
6/57
Renal and urinary disorders
Urinary retention
1.8%
1/57
Reproductive system and breast disorders
Erectile impotence
3.5%
2/57
Reproductive system and breast disorders
Gynecomastia
3.5%
2/57
Respiratory, thoracic and mediastinal disorders
Nose, hemorrhage
5.3%
3/57
Respiratory, thoracic and mediastinal disorders
Cough
3.5%
2/57
Respiratory, thoracic and mediastinal disorders
Dyspnea
7.0%
4/57
Respiratory, thoracic and mediastinal disorders
Nasal cavity/paranasal sinus reaction
5.3%
3/57
Respiratory, thoracic and mediastinal disorders
Voice changes/dysarthria
1.8%
1/57
Respiratory, thoracic and mediastinal disorders
Pulmonary/Upper Respiratory-other
1.8%
1/57
Skin and subcutaneous tissue disorders
Sweating
3.5%
2/57
Skin and subcutaneous tissue disorders
Dry skin
15.8%
9/57
Skin and subcutaneous tissue disorders
Alopecia
3.5%
2/57
Skin and subcutaneous tissue disorders
Hyperpigmentation
1.8%
1/57
Skin and subcutaneous tissue disorders
Nail changes
8.8%
5/57
Skin and subcutaneous tissue disorders
Pruritus/itching
1.8%
1/57
Skin and subcutaneous tissue disorders
Rash/desquamation
14.0%
8/57
Skin and subcutaneous tissue disorders
Rash: acne/acneiform
1.8%
1/57
Skin and subcutaneous tissue disorders
Skin-other
12.3%
7/57
Vascular disorders
Hypertension
21.1%
12/57
Vascular disorders
Hypotension
1.8%
1/57
Vascular disorders
Flushing
1.8%
1/57
Vascular disorders
Hot flashes
17.5%
10/57

Additional Information

Steven Balk

Beth Israel Deaconess

Phone: 617-735-2065

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place