Trial Outcomes & Findings for Study to Asses Pharmacodynamics, Pharmacokinetics, Safety and Tolerability of AZD0328 in Patients With Schizophrenia (NCT NCT00669903)

NCT ID: NCT00669903

Last Updated: 2010-08-06

Results Overview

The GMLT and OCLT standardized change composite score will be calculated as the mean of the GMLT and OCLT standardized change from baseline scores. Least square means were derived using a mixed effects repeated measures model with protocol scheduled assessment day, treatment group, baseline score, and assessment day-by-treatment interaction as fixed factors, center as a random factor, and baseline score as a covariate. Scale range from negative infinity (worst value) to positive infinity (best value).

Recruitment status

TERMINATED

Study phase

PHASE2

Target enrollment

100 participants

Primary outcome timeframe

Baseline and Day 14

Results posted on

2010-08-06

Participant Flow

A total of two US centers were inititated with first patient enrolled on 2 April 2008 and last patient completed on 4 November 2008. A total of 158 patients were enrolled with 100 patients allocated to randomized treatment.

Patients were to receive a stable dose of an antipsychotic for the 4 weeks prior to randomization, have stable psychotic symptoms without a hospitalization for the 8 weeks prior to randomization, and were to be smoking an average of \>=10 cigarettes per day. Enrolled patients who no longer met entry criteria at randomization were not randomized.

Participant milestones

Participant milestones
Measure
AZD0328 Low Dose Group
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
Placebo
Overall Study
STARTED
23
37
18
22
Overall Study
Completed Treatment Period
23
33
13
19
Overall Study
COMPLETED
22
32
13
18
Overall Study
NOT COMPLETED
1
5
5
4

Reasons for withdrawal

Reasons for withdrawal
Measure
AZD0328 Low Dose Group
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
Placebo
Overall Study
Adverse Event
0
1
3
1
Overall Study
Withdrawal by Subject
0
2
2
2
Overall Study
Lost to Follow-up
1
1
0
1
Overall Study
Protocol Violation
0
1
0
0

Baseline Characteristics

Study to Asses Pharmacodynamics, Pharmacokinetics, Safety and Tolerability of AZD0328 in Patients With Schizophrenia

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
AZD0328 Low Dose Group
n=23 Participants
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
n=37 Participants
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
n=18 Participants
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
n=22 Participants
Placebo
Total
n=100 Participants
Total of all reporting groups
Race/Ethnicity, Customized
Caucasian
4 Participants
n=5 Participants
3 Participants
n=7 Participants
1 Participants
n=5 Participants
2 Participants
n=4 Participants
10 Participants
n=21 Participants
Age Continuous
38.5 Years
STANDARD_DEVIATION 11.2 • n=5 Participants
41.7 Years
STANDARD_DEVIATION 9.2 • n=7 Participants
38.3 Years
STANDARD_DEVIATION 9.8 • n=5 Participants
40.0 Years
STANDARD_DEVIATION 9.8 • n=4 Participants
40.0 Years
STANDARD_DEVIATION 9.9 • n=21 Participants
Sex: Female, Male
Female
1 Participants
n=5 Participants
4 Participants
n=7 Participants
3 Participants
n=5 Participants
2 Participants
n=4 Participants
10 Participants
n=21 Participants
Sex: Female, Male
Male
22 Participants
n=5 Participants
33 Participants
n=7 Participants
15 Participants
n=5 Participants
20 Participants
n=4 Participants
90 Participants
n=21 Participants
Race/Ethnicity, Customized
Black
18 Participants
n=5 Participants
33 Participants
n=7 Participants
17 Participants
n=5 Participants
18 Participants
n=4 Participants
86 Participants
n=21 Participants
Race/Ethnicity, Customized
Other
1 Participants
n=5 Participants
1 Participants
n=7 Participants
0 Participants
n=5 Participants
2 Participants
n=4 Participants
4 Participants
n=21 Participants
Baseline Positive and Negative Syndrome Scale (PANSS) total score
67.9 Points of PANSS score
STANDARD_DEVIATION 10.3 • n=5 Participants
71.8 Points of PANSS score
STANDARD_DEVIATION 12.0 • n=7 Participants
72.1 Points of PANSS score
STANDARD_DEVIATION 12.2 • n=5 Participants
69.5 Points of PANSS score
STANDARD_DEVIATION 13.2 • n=4 Participants
70.4 Points of PANSS score
STANDARD_DEVIATION 11.9 • n=21 Participants

PRIMARY outcome

Timeframe: Baseline and Day 14

The GMLT and OCLT standardized change composite score will be calculated as the mean of the GMLT and OCLT standardized change from baseline scores. Least square means were derived using a mixed effects repeated measures model with protocol scheduled assessment day, treatment group, baseline score, and assessment day-by-treatment interaction as fixed factors, center as a random factor, and baseline score as a covariate. Scale range from negative infinity (worst value) to positive infinity (best value).

Outcome measures

Outcome measures
Measure
AZD0328 Low Dose Group
n=23 Participants
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
n=32 Participants
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
n=13 Participants
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
n=19 Participants
Placebo
CogState Groton Maze Learning Task (GMLT) and One Card Learning Task (OCLT) Standardized Composite Score at Day 14
0.234 units on a scale
Standard Error 0.122 • Interval 0.122 to
0.240 units on a scale
Standard Error 0.072 • Interval 0.072 to
0.194 units on a scale
Standard Error 0.216 • Interval 0.216 to
0.266 units on a scale
Standard Error 0.099 • Interval 0.099 to

SECONDARY outcome

Timeframe: Baseline and Day 14

GMLT score is defined as the -log10 transform of the sum of the number of errors made during GMLT trials. Mean GMLT score was calculated as the average of the 2 hour, 5 hour, and 8 hour scores. The GMLT standardized change score was calculated as the change from baseline in the mean GMLT score divided by the within subject standard deviation. Scale range from negative infinity (worst value) to positive infinity (best value).

Outcome measures

Outcome measures
Measure
AZD0328 Low Dose Group
n=23 Participants
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
n=32 Participants
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
n=13 Participants
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
n=19 Participants
Placebo
CogState Groton Maze Learning Task (GMLT) Standardized Change Score at Day 14
0.313 units on a scale
Standard Error 0.163 • Interval 0.163 to
0.360 units on a scale
Standard Error 0.104 • Interval 0.104 to
0.281 units on a scale
Standard Error 0.249 • Interval 0.249 to
0.235 units on a scale
Standard Error 0.124 • Interval 0.124 to

SECONDARY outcome

Timeframe: Baseline and Day 14

OCLT score is defined as the arcsine transform of the proportion of correct responses during OCLT trials. Mean OCLT score was calculated as the average of the 2 hour, 5 hour, and 8 hour scores. The OCLT standardized change score was calculated as the change from baseline in the mean OCLT score divided by the within-subject standard deviation. Scale range from negative infinity (worst value) to positive infinity (best value).

Outcome measures

Outcome measures
Measure
AZD0328 Low Dose Group
n=23 Participants
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
n=33 Participants
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
n=13 Participants
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
n=19 Participants
Placebo
CogState One Card Learning Task (OCLT) Standardized Change Score at Day 14
0.150 units on a scale
Standard Error 0.126 • Interval 0.126 to
0.102 units on a scale
Standard Error 0.100 • Interval 0.1 to
0.094 units on a scale
Standard Error 0.232 • Interval 0.232 to
0.316 units on a scale
Standard Error 0.152 • Interval 0.152 to

SECONDARY outcome

Timeframe: Baseline and Day 14

DT score is defined as -1 times the mean of log10 transformed reaction times for all correct responses. Mean DT score was calculated as the average of the 2 hour, 5 hour, and 8 hour scores. The DT standardized change score will be calculated as the change from baseline in the mean DT score divided by the within-subject standard deviation. Score range from negative infinity (worst value) to positive infinity (best value).

Outcome measures

Outcome measures
Measure
AZD0328 Low Dose Group
n=23 Participants
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
n=33 Participants
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
n=13 Participants
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
n=19 Participants
Placebo
CogState Detection Task (DT) Standardized Change Score at Day 14
0.116 units on a scale
Standard Error 0.116 • Interval 0.116 to
-0.014 units on a scale
Standard Error 0.115 • Interval 0.115 to
-0.095 units on a scale
Standard Error 0.158 • Interval 0.158 to
0.098 units on a scale
Standard Error 0.095 • Interval 0.095 to

SECONDARY outcome

Timeframe: Baseline and Day 14

IT score defined as 1 times the mean of log10 transformed reaction times for all correct responses. Mean IT score calculated as the average of the 2 hour, 5 hour, and 8 hour scores. The IT standardized change score will be calculated as the change from baseline in the mean IT score divided by the within-subject standard dev. Least square means were derived using a mixed effects repeated measures model with protocol scheduled assessment day, treatment group, baseline score, and assessment day-by-treatment interaction as fixed factors, center as a random factor, and baseline score as a covariate

Outcome measures

Outcome measures
Measure
AZD0328 Low Dose Group
n=23 Participants
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
n=33 Participants
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
n=13 Participants
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
n=19 Participants
Placebo
CogState Identification Task (IT) Standardized Change Score at Day 14
-0.145 unit on a scale
Standard Error 0.177 • Interval 0.177 to
-0.049 unit on a scale
Standard Error 0.121 • Interval 0.121 to
-0.173 unit on a scale
Standard Error 0.136 • Interval 0.136 to
-0.103 unit on a scale
Standard Error 0.132 • Interval 0.132 to

SECONDARY outcome

Timeframe: Baseline and Day 14

GMRT score defined as the -log10 transform of the sum of the number of errors made during GMRT trials. Mean GMRT score calculated as the average of the 2 hour, 5 hour, and 8 hour scores. The GMRT standardized change score was calculated as change from baseline in mean GMRT score divided by the within subject standard deviation. Least square means were derived using a mixed effects repeated measures model with protocol scheduled assessment day, treatment group, baseline score, assessment day-by-treatment interaction as fixed factors, center as random factor, and baseline score as a covariate

Outcome measures

Outcome measures
Measure
AZD0328 Low Dose Group
n=23 Participants
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
n=33 Participants
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
n=13 Participants
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
n=19 Participants
Placebo
CogState Groton Maze Recall Task (GMRT) Standardized Change Score at Day 14
0.213 unit on a scale
Standard Error 0.139 • Interval 0.139 to
0.406 unit on a scale
Standard Error 0.112 • Interval 0.112 to
0.467 unit on a scale
Standard Error 0.263 • Interval 0.263 to
0.409 unit on a scale
Standard Error 0.183 • Interval 0.183 to

Adverse Events

AZD0328 Low Dose Group

Serious events: 0 serious events
Other events: 17 other events
Deaths: 0 deaths

AZD0328 Optimal Dose Group

Serious events: 0 serious events
Other events: 22 other events
Deaths: 0 deaths

AZD0328 High Dose Group

Serious events: 0 serious events
Other events: 11 other events
Deaths: 0 deaths

Placebo

Serious events: 1 serious events
Other events: 11 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
AZD0328 Low Dose Group
n=23 participants at risk
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
n=37 participants at risk
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
n=18 participants at risk
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
n=22 participants at risk
Placebo
Respiratory, thoracic and mediastinal disorders
Pulmonary Embolism
0.00%
0/23
0.00%
0/37
0.00%
0/18
4.5%
1/22

Other adverse events

Other adverse events
Measure
AZD0328 Low Dose Group
n=23 participants at risk
AZD0328 Low dose group (0.00093 to 0.0028 mg oral solution)
AZD0328 Optimal Dose Group
n=37 participants at risk
AZD0328 Optimal dose group (0.0048 to 0.0329 mg oral solution)
AZD0328 High Dose Group
n=18 participants at risk
AZD0328 High dose group (0.075 to 0.675 mg oral solution)
Placebo
n=22 participants at risk
Placebo
Gastrointestinal disorders
DYSPEPSIA
39.1%
9/23
27.0%
10/37
27.8%
5/18
18.2%
4/22
Nervous system disorders
HEADACHE
26.1%
6/23
10.8%
4/37
33.3%
6/18
18.2%
4/22
Musculoskeletal and connective tissue disorders
MYALGIA
4.3%
1/23
13.5%
5/37
5.6%
1/18
4.5%
1/22
Gastrointestinal disorders
NAUSEA
4.3%
1/23
5.4%
2/37
22.2%
4/18
0.00%
0/22
Gastrointestinal disorders
CONSTIPATION
13.0%
3/23
8.1%
3/37
0.00%
0/18
4.5%
1/22
Psychiatric disorders
INSOMNIA
0.00%
0/23
8.1%
3/37
11.1%
2/18
0.00%
0/22
Nervous system disorders
LETHARGY
0.00%
0/23
10.8%
4/37
5.6%
1/18
0.00%
0/22
Nervous system disorders
SEDATION
4.3%
1/23
5.4%
2/37
11.1%
2/18
4.5%
1/22
Psychiatric disorders
ANXIETY
0.00%
0/23
5.4%
2/37
11.1%
2/18
4.5%
1/22
Respiratory, thoracic and mediastinal disorders
COUGH
4.3%
1/23
8.1%
3/37
0.00%
0/18
0.00%
0/22
Respiratory, thoracic and mediastinal disorders
NASAL CONGESTION
8.7%
2/23
2.7%
1/37
5.6%
1/18
0.00%
0/22
Gastrointestinal disorders
TOOTHACHE
13.0%
3/23
2.7%
1/37
0.00%
0/18
0.00%
0/22

Additional Information

Gerard Lynch

AstraZeneca

Results disclosure agreements

  • Principal investigator is a sponsor employee No publication or presentation of results until the earlier of the publication of the first multi-center publication and the second anniversary of the completion of the multi-center study at all sites. Sponsor must receive a copy of proposed manuscript for review and comment at least 60 days prior to its submission for publication or presentation.
  • Publication restrictions are in place

Restriction type: OTHER