Autologous Bone Marrow Transplant for Children With Acute Myelogenous Leukemia (AML) in First Complete Remission

NCT ID: NCT00667927

Last Updated: 2008-04-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

17 participants

Study Classification

INTERVENTIONAL

Study Start Date

1991-03-31

Study Completion Date

2008-01-31

Brief Summary

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This study proposes to transfer marker genes (detectable genetic traits or segments of DNA that can be identified and tracked) into aliquots of marrow obtained for Bone Marrow Transplant (BTM) in patients in remission of Acute Myelogenous Leukemia (AML).

Detailed Description

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The primary objective of this study was to estimate the continuous complete remission rate at 2 years post transplant for children with AML in first complete remission treated with autologous BMT.

Secondary objectives used transduction of marker genes into autologous marrow to determine the following:

1. whether the source of relapse after BMT for AML is residual malignant cells in the harvested marrow or in the patient, and whether marrow purging is therefore rational.
2. whether the majority of AML, which lack genetic markers, represent abnormalities in a multi-lineage progenitor cell, and whether therefore, auto grafting/intensified chemotherapy is ever likely to augment the cure rate.
3. the mechanisms of autologous reconstitution, and the effects of stimuli which modify the process.

Conditions

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Acute Myeloid Leukemia

Keywords

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Autologous bone marrow transplant gene marking

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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1

Group Type OTHER

Busulfan

Intervention Type DRUG

See Detailed Description section for description of treatment plan.

Cyclophosphamide

Intervention Type DRUG

See Detailed Description section for description of treatment plan.

Mesna

Intervention Type DRUG

See Detailed Description section for description of treatment plan.

Interventions

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Busulfan

See Detailed Description section for description of treatment plan.

Intervention Type DRUG

Cyclophosphamide

See Detailed Description section for description of treatment plan.

Intervention Type DRUG

Mesna

See Detailed Description section for description of treatment plan.

Intervention Type DRUG

Other Intervention Names

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Myleran Cytoxan, CTX MESNCX

Eligibility Criteria

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Inclusion Criteria

* Patients aged between 1 and 18 years at diagnosis with acute nonlymphocytic leukemia in first remission are eligible for this protocol.
* Patients enrolled on the AML-87 study in second or subsequent remission are eligible for this protocol.

Exclusion Criteria

* Has an HLA-matched, MLC-compatible donor(unless parents and/or patient refuses transplant.
* Diagnosis of FAB M3 or FAB M3v (acute progranulocytic leukemia)
* Life expectancy limited by disease other than leukemia
* Significant cardiac disease (echo shortening fraction \<25% or MUGA scan \<50%)
* Severe renal dysfunction, i.e., creatinine clearance less than 60cc/1.73 m2/min
* Severe restrictive pulmonary disease (FCV less than 40% of predicted)
* Severe hepatic disease (bilirubin greater than 3 mg/dl or SGPT greater than 500IU)
* Severe personality disorder or mental illness
* Previous severe cystitis from cyclophosphamide
* Previous total dose of anthracyclines of \>450 mg/m2
* Sever infection that on evaluation by the PI precludes ablative chemotherapy or successful transplantation
* Previous autologous transplant
* HIV reactivity
* Karnofsky score \<70%
Minimum Eligible Age

1 Year

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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St. Jude Children's Research Hospital

OTHER

Sponsor Role lead

Responsible Party

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St. Jude Children's Research Hospital

Principal Investigators

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Gregory A Hale, MD

Role: PRINCIPAL_INVESTIGATOR

St. Jude Children's Research Hospital

Locations

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St. Jude Children's Research Hospital

Memphis, Tennessee, United States

Site Status

Countries

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United States

Related Links

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Other Identifiers

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AMLREM

Identifier Type: -

Identifier Source: org_study_id