Isavuconazole in the Treatment of Renally Impaired Aspergillosis and Rare Fungi

NCT ID: NCT00634049

Last Updated: 2024-12-11

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

149 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-04-22

Study Completion Date

2016-05-05

Brief Summary

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The purpose of this study is to investigate the efficacy and safety of isavuconazole in the treatment of renally impaired participants with invasive fungal infections caused by Aspergillus and participants with invasive fungal disease caused by rare fungi.

Detailed Description

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Acute invasive fungal infections caused by aspergillus, rare moulds, yeasts or dimorphic fungi are life threatening diseases. Early treatment with highly effective anti-fungals reduces mortality. This study investigates the safety and efficacy of isavuconazole in participants with aspergillosis and renal impairment, and in participants suffering from invasive infections from rare fungi.

Conditions

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Aspergillosis Invasive Fungal Infections

Keywords

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invasive fungal infections caused by rare molds, rare yeasts BAL8557 Isavuconazole Aspergillosis or by dimorphic fungi ASP9766

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Isavuconazole

Administration of isavuconazole 3 times a day in the vein (IV) or oral as a capsule for 2 days followed by daily administration of isavuconazole (IV) or oral

Group Type EXPERIMENTAL

isavuconazole

Intervention Type DRUG

Administration of 200 mg isavuconazole 3 times a day in the vein (IV) or oral as a capsule for 2 days, followed by daily administration of 200 mg isavuconazole (IV) or oral

Interventions

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isavuconazole

Administration of 200 mg isavuconazole 3 times a day in the vein (IV) or oral as a capsule for 2 days, followed by daily administration of 200 mg isavuconazole (IV) or oral

Intervention Type DRUG

Other Intervention Names

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BAL8557 ASP9766

Eligibility Criteria

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Inclusion Criteria

•Participants meeting EORTC/MSG (European Organization for the Research and Treatment of Cancer/Mycoses Study Group) definition of proven or culture positive probable IFD (invasive fungal disease) caused by rare moulds, yeasts, or dimorphic fungi (i.e. fungal pathogens other than Aspergillus fumigatus or Candida species) whether renally impaired or not (including dialysis) who require primary therapy for their IFD at the time of enrollment.

OR

•Participants who had proven or probable zygomycosis, whether renally impaired or not (including dialysis), who require primary therapy. Zygomycosis must be documented by culture or histology / cytology.

OR

•Participants meeting EORTC/MSG definition of proven or culture positive probable IFD caused by rare moulds, yeasts, or dimorphic fungi (i.e., fungal pathogens other than Aspergillus fumigatus or Candida species), whether RI or not (including dialysis), who were refractory to current treatment defined as,

* Clear documentation of progression of disease. Note: radiological progression only in association with white blood cell (WBC) count recovery was not acceptable.
* Failure to improve clinically despite receiving at least 7 days of standard antifungal regimen. Prior to enrolling patients who fell into this category, the Medical Monitor was contacted for approval.

OR

• Participants meeting EORTC/MSG definition of proven or culture positive probable IFD caused by rare moulds, yeasts, or dimorphic fungi (i.e., fungal pathogens other than Aspergillus fumigatus or Candida species), whether RI or not (including dialysis), who were intolerant to current treatment for example:

* Doubling of serum creatinine value to higher than the upper limit of normal (ULN) within 48 hours.
* Serum creatinine \> 2.0 mg/mL and current treatment with polyene or IV voriconazole.
* Other significant drug-related adverse reaction(s) to the current antifungal agent, resulting in discontinuation of the treatment, e.g., persistence of visual disturbance, allergic reaction, phototoxicity or severe infusion reaction (hypertensive crisis, severe chills or shock).
* Documented inability to achieve adequate blood levels of posaconazole, voriconazole or itraconazole.

Exclusion Criteria

* A known condition of the participants that may jeopardize adherence to the protocol requirements
* Participants who are unlikely to survive 30 days
* Participants with a body weight \< 40 kg
* Women who are pregnant or breastfeeding
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Basilea Pharmaceutica International Ltd

INDUSTRY

Sponsor Role collaborator

Astellas Pharma Inc

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Astellas Pharma Global Development

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

City Of Hope National Medical Center

Duarte, California, United States

Site Status

University of California Davis Health System

Sacramento, California, United States

Site Status

California Pacific Medical Center

San Francisco, California, United States

Site Status

University of California at San Francisco

San Francisco, California, United States

Site Status

Stanford University Hospital

Stanford, California, United States

Site Status

University Of Colorado Health Sciences Center

Aurora, Colorado, United States

Site Status

Emory Hospital

Atlanta, Georgia, United States

Site Status

University of Chicago, Division of Infectious Diseases

Chicago, Illinois, United States

Site Status

Indiana BMT

Beech Grove, Indiana, United States

Site Status

Infectious Disease of Indiana

Indianapolis, Indiana, United States

Site Status

Ochsner Clinic Foundation

New Orleans, Louisiana, United States

Site Status

Brigham & Womens Hospital

Boston, Massachusetts, United States

Site Status

UMASS Memorial Medical Center

Worcester, Massachusetts, United States

Site Status

Wayne State University School of Medicine

Detroit, Michigan, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Upstate Infectious Diseases Association LLP

Albany, New York, United States

Site Status

Cleveland Clinic

Cleveland, Ohio, United States

Site Status

Regional Infection Diseases Infusion Center Inc.

Lima, Ohio, United States

Site Status

Temple University Health Sciences

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh Medical Center Health System

Pittsburgh, Pennsylvania, United States

Site Status

University of Texas MD Anderson Cancer Center

Houston, Texas, United States

Site Status

Fred Hutchinson Cancer Research Center, Clinical Research

Seattle, Washington, United States

Site Status

Hospital Italiano de Buenos Aires

Ciudad Autonoma, , Argentina

Site Status

Instituto Medico Especializado Alexander Fleming

Ciudad Autonoma, , Argentina

Site Status

Hospital Nuestra Senora de la Misericordia

Córdoba, , Argentina

Site Status

Hospital San Roque

Córdoba, , Argentina

Site Status

Centro Polivalente de Asistencia e Investigación Clínica - CER San Juan

San Juan, , Argentina

Site Status

Mater Medical Centre

South Brisbane, , Australia

Site Status

Princess Alexandria Hospital

Woolloongabba, , Australia

Site Status

Institut Jules Bordet

Brussels, , Belgium

Site Status

Erasme Hospital

Brussels, , Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status

Universitaire Ziekenhuizen Leuven

Leuven, , Belgium

Site Status

Hospital Felicio Rocho

Belo Horizonte, , Brazil

Site Status

Santa Casa de Misericordia de Belo Horizonte

Belo Horizonte, , Brazil

Site Status

Hospital das Clinicas da UFPR

Curitiba, , Brazil

Site Status

Hospital de Clinicas da FMUSP - Ribeirao Preto

Ribeirão Preto, , Brazil

Site Status

Hospital Universitario Clementino Fraga Filho

Rio de Janeiro, , Brazil

Site Status

Hospital Universitario de Santa Maria

Santa Maria, , Brazil

Site Status

Hospital Professor Edmundo Vasconcelos

São Paulo, , Brazil

Site Status

Hamilton Health Sciences - Henderson Site

Hamilton, Ontario, Canada

Site Status

The Ottawa Hospital - General Campus

Ottawa, Ontario, Canada

Site Status

Hôpital Maisonneuve - Rosemont

Montreal, Quebec, Canada

Site Status

Hospital Clinico San Borja Arriaran

Santiago, , Chile

Site Status

Alexandria University Hospital

Alexandria, , Egypt

Site Status

National Cancer Institute

Cairo, , Egypt

Site Status

Nasser Institute

Cairo, , Egypt

Site Status

Hôpital Edouard Herriot

Lyon, , France

Site Status

Institut Paoli Calmette - Marseille

Marseille, , France

Site Status

Hotel Dieu

Nantes, , France

Site Status

Hôpital Saint-Louis

Paris, , France

Site Status

Hopital Hautepierre

Strasbourg, , France

Site Status

Hôpital de Brabois Adultes

Vandœuvre-lès-Nancy, , France

Site Status

Universitaetsklinikum Aachen

Aachen, , Germany

Site Status

Charite-Campus Benjamin Franklin

Berlin, , Germany

Site Status

Universitaet Koeln

Cologne, , Germany

Site Status

Klinikum Neuperlach

München, , Germany

Site Status

Medizinische Klinik und Polyklinik II

Würzburg, , Germany

Site Status

Medanta Medicity Hospital

Gurgaon, Haryan, India

Site Status

Shirdi Sai Baba Cancer Hospital K. M. C. Hospital

Manipal, Kama, India

Site Status

Tata Memorial Hopital, Department of Anesthesia

Mumbai, Mahara, India

Site Status

Deenanath Mangeshkar Hospital & Research Centre

Pune, Mahara, India

Site Status

Global Hospitals & Health City

Chennai, Tamilna, India

Site Status

Sterling Hospital

Ahmedabad, , India

Site Status

Apollo Hospitals

Hyderabad, , India

Site Status

Sahyadri Specialty Hospital

Pune, , India

Site Status

Rambam Health Care Campus

Haifa, , Israel

Site Status

Hadassah Universtiy Hospital - Ein Kerem

Jerusalem, , Israel

Site Status

Rabin MC

Petah Tikva, , Israel

Site Status

Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status

Sourasky MC Ichilov Hospital Tel Aviv

Tel Aviv, , Israel

Site Status

American University of Beirut Medical Center

Beirut, , Lebanon

Site Status

Clinique Dr. Rizk

Beirut, , Lebanon

Site Status

Rafik Hariri University Hospital

Beirut, , Lebanon

Site Status

Antiguo Hospital Civil de Guadalajara Fray Antonio Alcalde

Guadalajara, , Mexico

Site Status

Instituto Nacional de Ciencias Medicas y Nutricion Salvador

Mexico City, , Mexico

Site Status

Hospital Universitario Dr Jose Eleuterio Gonzalez

Monterrey, , Mexico

Site Status

Hospital Central Dr Ignacio Morones Prieto

San Luis Potosí City, , Mexico

Site Status

Samodzielny Publiczny Centralny Szpital Kliniczny

Warsaw, , Poland

Site Status

S.I. Russian Oncological Research Center n.a. N.N. Blokhin

Moscow, , Russia

Site Status

State Institution "Hematology Research Center" RAMS

Moscow, , Russia

Site Status

Republican Hospital named after V.A. Baranov

Petrozavodsk, , Russia

Site Status

St-Petersburg MA Postgraduate Education

Saint Petersburg, , Russia

Site Status

Private Practice

Lyttleton, Gauteng, South Africa

Site Status

Soonchunhyang University Bucheon Hospital

Buchon-si, , South Korea

Site Status

Gachon University Gil Hospital

Incheon, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

The Catholic University of Korea

Seoul, , South Korea

Site Status

Asan Medical Center

Seoul, , South Korea

Site Status

Songklanagarind Hospital

Hat Yai, , Thailand

Site Status

Maharat Nakhon Ratchasima Hospital

Muang, , Thailand

Site Status

Srinagarind Hospital

Muang, , Thailand

Site Status

Maharaj Nakorn Chiang Mai Hospital

Muang, , Thailand

Site Status

Ramathibodi Hospital

Ratchathewi, , Thailand

Site Status

Countries

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China Hungary Italy Malaysia New Zealand Philippines United Kingdom United States Argentina Australia Belgium Brazil Canada Chile Egypt France Germany India Israel Lebanon Mexico Poland Russia South Africa South Korea Thailand

References

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Hamed K, Engelhardt M, Kovanda LL, Huang JJ, Yan J, Aram JA. Post-hoc analysis of the safety and efficacy of isavuconazole in older patients with invasive fungal disease from the VITAL and SECURE studies. Sci Rep. 2023 Apr 25;13(1):6730. doi: 10.1038/s41598-023-31788-1.

Reference Type DERIVED
PMID: 37185921 (View on PubMed)

Kovanda LL, Desai AV, Lu Q, Townsend RW, Akhtar S, Bonate P, Hope WW. Isavuconazole Population Pharmacokinetic Analysis Using Nonparametric Estimation in Patients with Invasive Fungal Disease (Results from the VITAL Study). Antimicrob Agents Chemother. 2016 Jul 22;60(8):4568-76. doi: 10.1128/AAC.00514-16. Print 2016 Aug.

Reference Type DERIVED
PMID: 27185799 (View on PubMed)

Thompson GR 3rd, Rendon A, Ribeiro Dos Santos R, Queiroz-Telles F, Ostrosky-Zeichner L, Azie N, Maher R, Lee M, Kovanda L, Engelhardt M, Vazquez JA, Cornely OA, Perfect JR. Isavuconazole Treatment of Cryptococcosis and Dimorphic Mycoses. Clin Infect Dis. 2016 Aug 1;63(3):356-62. doi: 10.1093/cid/ciw305. Epub 2016 May 11.

Reference Type DERIVED
PMID: 27169478 (View on PubMed)

Marty FM, Ostrosky-Zeichner L, Cornely OA, Mullane KM, Perfect JR, Thompson GR 3rd, Alangaden GJ, Brown JM, Fredricks DN, Heinz WJ, Herbrecht R, Klimko N, Klyasova G, Maertens JA, Melinkeri SR, Oren I, Pappas PG, Racil Z, Rahav G, Santos R, Schwartz S, Vehreschild JJ, Young JH, Chetchotisakd P, Jaruratanasirikul S, Kanj SS, Engelhardt M, Kaufhold A, Ito M, Lee M, Sasse C, Maher RM, Zeiher B, Vehreschild MJGT; VITAL and FungiScope Mucormycosis Investigators. Isavuconazole treatment for mucormycosis: a single-arm open-label trial and case-control analysis. Lancet Infect Dis. 2016 Jul;16(7):828-837. doi: 10.1016/S1473-3099(16)00071-2. Epub 2016 Mar 9.

Reference Type DERIVED
PMID: 26969258 (View on PubMed)

Related Links

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https://astellasclinicalstudyresults.com/study.aspx?ID=51

Link to results on Astellas Clinical Study Results website

Other Identifiers

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WSA-CS-003

Identifier Type: OTHER

Identifier Source: secondary_id

2006-005003-33

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

9766-CL-0103

Identifier Type: -

Identifier Source: org_study_id