Trial Outcomes & Findings for Lenalidomide in Chronic Lymphocytic Leukemia (CLL) Patients With Residual Disease (NCT NCT00632359)

NCT ID: NCT00632359

Last Updated: 2020-02-10

Results Overview

To evaluate ability of lenalidomide to improve quality of remission (e.g. from partial remission (PR) to complete remission (CR)), disease status assessed at start \& end of Lenalidomide consolidation. NCI Working Group Response Criteria: Participants who began therapy in PR, improvement of status to nodular partial remission (nPR) or CR; Participants in nPR (otherwise CR, bone marrow nodules identified histologically), improvement of status to CR. Participants in CR, resolution of measurable disease in blood \&/or bone marrow per immuno flow cytometry or PCR testing. Progressive Disease (PD): One or more of following: \>50% increase in sum of products of =/\>2 lymph nodes on 2 consecutive examinations; One+ node must be \>2 cm or appearance of new enlarged lymph nodes; \>50% increase in liver \&/or spleen as determined by physical examination/appearance of splenomegaly not previously present; \>50% increase in circulating lymphocytes with absolute count \>10,000.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

33 participants

Primary outcome timeframe

Baseline to 12 Months, Disease status assessed at Start/End of Lenalidomide Consolidation

Results posted on

2020-02-10

Participant Flow

Recruitment Period: February 28, 2008 to January 7, 2015. All recruitment done at The University of Texas MD Anderson Cancer Center.

Participant milestones

Participant milestones
Measure
Lenalidomide
Lenalidomide 10 mg daily given for 12 months.
Overall Study
STARTED
33
Overall Study
COMPLETED
31
Overall Study
NOT COMPLETED
2

Reasons for withdrawal

Reasons for withdrawal
Measure
Lenalidomide
Lenalidomide 10 mg daily given for 12 months.
Overall Study
Withdrawal by Subject
2

Baseline Characteristics

Lenalidomide in Chronic Lymphocytic Leukemia (CLL) Patients With Residual Disease

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Lenalidomide
n=33 Participants
Lenalidomide 10 mg daily given for 12 months.
Age, Continuous
59 years
n=5 Participants
Sex: Female, Male
Female
11 Participants
n=5 Participants
Sex: Female, Male
Male
22 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
0 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
0 Participants
n=5 Participants
Race (NIH/OMB)
White
32 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
1 Participants
n=5 Participants
Region of Enrollment
United States
33 participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline to 12 Months, Disease status assessed at Start/End of Lenalidomide Consolidation

Population: Of the three participants registered, two were not evaluable for response.

To evaluate ability of lenalidomide to improve quality of remission (e.g. from partial remission (PR) to complete remission (CR)), disease status assessed at start \& end of Lenalidomide consolidation. NCI Working Group Response Criteria: Participants who began therapy in PR, improvement of status to nodular partial remission (nPR) or CR; Participants in nPR (otherwise CR, bone marrow nodules identified histologically), improvement of status to CR. Participants in CR, resolution of measurable disease in blood \&/or bone marrow per immuno flow cytometry or PCR testing. Progressive Disease (PD): One or more of following: \>50% increase in sum of products of =/\>2 lymph nodes on 2 consecutive examinations; One+ node must be \>2 cm or appearance of new enlarged lymph nodes; \>50% increase in liver \&/or spleen as determined by physical examination/appearance of splenomegaly not previously present; \>50% increase in circulating lymphocytes with absolute count \>10,000.

Outcome measures

Outcome measures
Measure
Lenalidomide
n=31 Participants
Lenalidomide 10 mg daily given for 12 months.
Improvement in Quality of Remission: Number of Participants With Response Versus No Response by NCI Working Group Criteria Disease Status Change at Start/End of Lenalidomide Consolidation
Response
10 participants
Improvement in Quality of Remission: Number of Participants With Response Versus No Response by NCI Working Group Criteria Disease Status Change at Start/End of Lenalidomide Consolidation
No Response
21 participants

PRIMARY outcome

Timeframe: 12 Months, Disease status assessed at the End of Lenalidomide Consolidation

Population: Of the 33 participants who were treated, two Participants were not evaluable.

Complete remission (CR), requiring absence of peripheral blood clonal lymphocytes by immunophenotyping, absence of lymphadenopathy, absence of hepatomegaly or splenomegaly, absence of constitutional symptoms and satisfactory blood counts; positive or negative minimal residual disease (MRD); Partial remission (PR), defined as ≥ 50% fall in lymphocyte count, ≥ 50% reduction in lymphadenopathy or ≥ 50% reduction in liver or spleen, together with improvement in peripheral blood counts; Nodular Partial Remission (nPR) is CR with bone marrow nodules identified histologically. Progressive disease (PD), defined as ≥ 50% rise in lymphocyte count to \> 5 x109/L, ≥ 50% increase in lymphadenopathy, ≥ 50% increase in liver or spleen size, Richter's transformation, or new cytopenias due to CLL; Stable disease, defined as not meeting criteria for CR, PR or PD.

Outcome measures

Outcome measures
Measure
Lenalidomide
n=31 Participants
Lenalidomide 10 mg daily given for 12 months.
Response Assessments: Disease Status at the End of Lenalidomide Consolidation Per International Workshop on Chronic Lymphocytic Leukemia (IWCLL) Response Criteria
CR, MRD Positive or Negative
13 participants
Response Assessments: Disease Status at the End of Lenalidomide Consolidation Per International Workshop on Chronic Lymphocytic Leukemia (IWCLL) Response Criteria
PR
8 participants
Response Assessments: Disease Status at the End of Lenalidomide Consolidation Per International Workshop on Chronic Lymphocytic Leukemia (IWCLL) Response Criteria
nPR
7 participants
Response Assessments: Disease Status at the End of Lenalidomide Consolidation Per International Workshop on Chronic Lymphocytic Leukemia (IWCLL) Response Criteria
PD
1 participants

PRIMARY outcome

Timeframe: From baseline to 12 months

Population: Of the 33 participants treated, two were not evaluable for outcome assessment due to early departure from study.

Time from the start of study drug therapy to the first documentation of disease progression. Progressive disease characterized by at least one of the following: \>50% increase in the sum of products of at least 2 lymph nodes on 2 consecutive examinations. At least one node larger than 2 cm. Or, appearance of new enlarged lymph nodes. \>50% increase in size of liver and/or spleen as determined by physical examination or appearance of splenomegaly which was not previously present. \>50% increase in number of circulating lymphocytes with absolute count of at least 10,000.

Outcome measures

Outcome measures
Measure
Lenalidomide
n=31 Participants
Lenalidomide 10 mg daily given for 12 months.
Time to Progression
8 Months
Interval 6.6 to 9.4

Adverse Events

Lenalidomide

Serious events: 8 serious events
Other events: 27 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Lenalidomide
n=33 participants at risk
Lenalidomide 10 mg daily given for 12 months.
Blood and lymphatic system disorders
Neutropenia
24.2%
8/33 • Number of events 8 • Adverse event collection for 12 months of treatment.
Blood and lymphatic system disorders
Thrombocytopenia
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Respiratory, thoracic and mediastinal disorders
Pulmonary Embolus
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Infections and infestations
Infections, Respiratory syncytial virus (RSV)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Respiratory, thoracic and mediastinal disorders
PNEUMONITIS
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Vascular disorders
THROMBOSIS/THROMBUS/EMBOLISM
6.1%
2/33 • Number of events 2 • Adverse event collection for 12 months of treatment.

Other adverse events

Other adverse events
Measure
Lenalidomide
n=33 participants at risk
Lenalidomide 10 mg daily given for 12 months.
Investigations
ALKALINE PHOSPHATASE INCREASE
3.0%
1/33 • Number of events 2 • Adverse event collection for 12 months of treatment.
Respiratory, thoracic and mediastinal disorders
ALLERGIC RHINITIS
6.1%
2/33 • Number of events 3 • Adverse event collection for 12 months of treatment.
Investigations
Alanine aminotransferase Increased (ALT, SGPT)
6.1%
2/33 • Number of events 7 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
ANOREXIA
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Musculoskeletal and connective tissue disorders
ARTHRITIS
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Investigations
Aspartate aminotransferase increased (AST, SGOT)
6.1%
2/33 • Number of events 5 • Adverse event collection for 12 months of treatment.
Cardiac disorders
ATRIAL FIBRILLATION
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Ear and labyrinth disorders
AUDITORY/EAR (OTHER)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Blood and lymphatic system disorders
BILIRUBIN INCREASED
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Cardiac disorders
CARDIAC ISCHEMIA/INFARCTION
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Gastrointestinal disorders
CONSTIPATION
18.2%
6/33 • Number of events 6 • Adverse event collection for 12 months of treatment.
Respiratory, thoracic and mediastinal disorders
COUGH
24.2%
8/33 • Number of events 8 • Adverse event collection for 12 months of treatment.
Investigations
CREATININE INCREASED
18.2%
6/33 • Number of events 8 • Adverse event collection for 12 months of treatment.
Skin and subcutaneous tissue disorders
DERMATOLOGY/SKIN (OTHER)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
DIABETES (Hyperglycemia)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Gastrointestinal disorders
DIARRHEA
27.3%
9/33 • Number of events 11 • Adverse event collection for 12 months of treatment.
General disorders
DISTENSION/BLOATING
9.1%
3/33 • Number of events 3 • Adverse event collection for 12 months of treatment.
Nervous system disorders
DIZZINESS
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Skin and subcutaneous tissue disorders
DRY SKIN
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Respiratory, thoracic and mediastinal disorders
DYSPNEA
6.1%
2/33 • Number of events 2 • Adverse event collection for 12 months of treatment.
Endocrine disorders
ENDOCRINE (OTHER: adrenal difference)
6.1%
2/33 • Number of events 2 • Adverse event collection for 12 months of treatment.
Skin and subcutaneous tissue disorders
ERYTHEMA MULTIFORME
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
General disorders
FATIGUE
48.5%
16/33 • Number of events 17 • Adverse event collection for 12 months of treatment.
Blood and lymphatic system disorders
FEBRILE NEUTROPENIA
6.1%
2/33 • Number of events 2 • Adverse event collection for 12 months of treatment.
Gastrointestinal disorders
FLATULENCE
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
General disorders
FLU-LIKE SYNDROME
6.1%
2/33 • Number of events 2 • Adverse event collection for 12 months of treatment.
Gastrointestinal disorders
GASTRITIS
6.1%
2/33 • Number of events 2 • Adverse event collection for 12 months of treatment.
Gastrointestinal disorders
GASTROINTESTINAL (OTHER)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Ear and labyrinth disorders
HEARING CHANGE (WITHOUT MONITORING)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Investigations
HEMOGLOBIN INCREASED
54.5%
18/33 • Number of events 22 • Adverse event collection for 12 months of treatment.
Renal and urinary disorders
HEMORRHAGE, Genitourinary
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Respiratory, thoracic and mediastinal disorders
HEMORRHAGE, PULMONARY (NOSE)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Reproductive system and breast disorders
HOT FLASHES
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
HYPERGLYCEMIA
12.1%
4/33 • Number of events 6 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
HYPERNATREMIA
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
HYPERTENSION
6.1%
2/33 • Number of events 2 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
HYPERURICEMIA
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
HYPOALBUMINEMIA
3.0%
1/33 • Number of events 2 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
HYPOCALCEMIA
6.1%
2/33 • Number of events 3 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
HYPOMAGNESEMIA
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
HYPONATREMIA
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Infections and infestations
INFECTION
12.1%
4/33 • Number of events 4 • Adverse event collection for 12 months of treatment.
Psychiatric disorders
INSOMNIA
9.1%
3/33 • Number of events 3 • Adverse event collection for 12 months of treatment.
Blood and lymphatic system disorders
Leukocytosis
39.4%
13/33 • Number of events 16 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
MAGNESIUM, SERUM-HIGH
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Metabolism and nutrition disorders
METABOLIC/LABORATORY (OTHER)
30.3%
10/33 • Number of events 16 • Adverse event collection for 12 months of treatment.
Psychiatric disorders
MOOD ALTERATION (AGITATION)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Psychiatric disorders
MOOD ALTERATION (ANXIETY)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Psychiatric disorders
MOOD ALTERATION (DEPRESSION)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Musculoskeletal and connective tissue disorders
MOTOR SKILLS, AFFECTED
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Gastrointestinal disorders
NAUSEA
15.2%
5/33 • Number of events 5 • Adverse event collection for 12 months of treatment.
Nervous system disorders
NEUROPATHY: SENSORY
6.1%
2/33 • Number of events 2 • Adverse event collection for 12 months of treatment.
Blood and lymphatic system disorders
Neutrophils, AGC (absolute granulocyte counts) Increased
51.5%
17/33 • Number of events 31 • Adverse event collection for 12 months of treatment.
Renal and urinary disorders
OBSTRUCTION, GU (BLADDER)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Eye disorders
OCULAR/VISUAL (OTHER)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Infections and infestations
PHLEBITIS
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Investigations
Platelet count decreased
36.4%
12/33 • Number of events 16 • Adverse event collection for 12 months of treatment.
Respiratory, thoracic and mediastinal disorders
PNEUMONITIS
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Skin and subcutaneous tissue disorders
PRURITUS
6.1%
2/33 • Number of events 3 • Adverse event collection for 12 months of treatment.
Respiratory, thoracic and mediastinal disorders
PULMONARY (OTHER)
9.1%
3/33 • Number of events 3 • Adverse event collection for 12 months of treatment.
Respiratory, thoracic and mediastinal disorders
PULMONARY EMBOLISM
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Skin and subcutaneous tissue disorders
RASH/DESQUAMATION
24.2%
8/33 • Number of events 11 • Adverse event collection for 12 months of treatment.
Renal and urinary disorders
RENAL FAILURE
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Renal and urinary disorders
RENAL/GENITOURINARY (OTHER)
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Respiratory, thoracic and mediastinal disorders
RESPIRATORY SYMPTOMS
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
General disorders
RIGORS/CHILLS
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Cardiac disorders
SUPRAVENTRICULAR TACHYCARDIA
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Skin and subcutaneous tissue disorders
SWEATING
6.1%
2/33 • Number of events 3 • Adverse event collection for 12 months of treatment.
Vascular disorders
THROMBOSIS/THROMBUS/EMBOLISM
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Ear and labyrinth disorders
TINNITUS
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
Investigations
TUMOR FLARE REACTION
12.1%
4/33 • Number of events 4 • Adverse event collection for 12 months of treatment.
Nervous system disorders
VOICE CHANGES
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.
General disorders
PAIN
24.2%
8/33 • Number of events 8 • Adverse event collection for 12 months of treatment.
General disorders
FEVER
3.0%
1/33 • Number of events 1 • Adverse event collection for 12 months of treatment.

Additional Information

Alessandra Ferrajoli, Professor, Leukemia

The University of Texas (UT) MD Anderson Cancer Center

Phone: 713-792-7734

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place