Trial Outcomes & Findings for A Multicenter, Placebo-controlled, Double-blind Investigative Extension Trial of the Safety and Efficacy of Aripiprazole in the Treatment of Patients With Bipolar Disorder Experiencing a Manic or Mixed Episode (NCT NCT00606177)

NCT ID: NCT00606177

Last Updated: 2014-02-12

Results Overview

Using LOCF datasets, descriptive statistics of actual values for changes of YMRS total scores from baseline (Day 1 of preceding study) to endpoint (Day 154) was calculated for each treatment group. YMRS is composed of 11 evaluation items with 5 rating levels each. Items rated on a scale of 0 to 4 (comprising 5 rating levels of one point each) are 1) levated mood, 2) increased motor activity/energy, 3) sexual interest, 4) sleep, 7) language-thought disorder, 10) appearance, and 11) insight. Items rated on a scale of 0 to 8 (comprising 5 rating levels of two points each) are 5) irritability, 6) speech (rate and amount), 8) content, and 9) disruptive-aggressive behavior. YMRS ranges from 0 (best possible outcome) to 60 (worst possible outcome).

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

99 participants

Primary outcome timeframe

Baseline (Day 1 of preceding study) , Day 154 or at discontinuation

Results posted on

2014-02-12

Participant Flow

Participant milestones

Participant milestones
Measure
Aripiprazole
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered 24 ,12, or 30 mg/day of aripiprazole once daily for 154 days.
Placebo
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered placebo once daily for 154 days.
Overall Study
STARTED
55
44
Overall Study
COMPLETED
28
19
Overall Study
NOT COMPLETED
27
25

Reasons for withdrawal

Reasons for withdrawal
Measure
Aripiprazole
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered 24 ,12, or 30 mg/day of aripiprazole once daily for 154 days.
Placebo
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered placebo once daily for 154 days.
Overall Study
Adverse Event
9
5
Overall Study
Lack of Efficacy
3
7
Overall Study
Physician Decision
1
0
Overall Study
Protocol Violation
1
4
Overall Study
Withdrawal by Subject
5
6
Overall Study
Progression to depressive phase
6
1
Overall Study
Diabetic blood glucose level/ High HbA1c
1
1
Overall Study
Change of residence or other commitments
1
1

Baseline Characteristics

A Multicenter, Placebo-controlled, Double-blind Investigative Extension Trial of the Safety and Efficacy of Aripiprazole in the Treatment of Patients With Bipolar Disorder Experiencing a Manic or Mixed Episode

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Aripiprazole
n=54 Participants
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered 24 ,12, or 30 mg/day of aripiprazole once daily for 154 days.
Placebo
n=42 Participants
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered placebo once daily for 154 days.
Total
n=96 Participants
Total of all reporting groups
Age, Continuous
38.7 years
STANDARD_DEVIATION 11.95 • n=5 Participants
37.8 years
STANDARD_DEVIATION 11.67 • n=7 Participants
38.3 years
STANDARD_DEVIATION 11.78 • n=5 Participants
Age, Categorical
<=18 years
0 Participants
n=5 Participants
1 Participants
n=7 Participants
1 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
54 Participants
n=5 Participants
41 Participants
n=7 Participants
95 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Sex: Female, Male
Female
29 Participants
n=5 Participants
24 Participants
n=7 Participants
53 Participants
n=5 Participants
Sex: Female, Male
Male
25 Participants
n=5 Participants
18 Participants
n=7 Participants
43 Participants
n=5 Participants
Region of Enrollment
Taiwan
4 participants
n=5 Participants
9 participants
n=7 Participants
13 participants
n=5 Participants
Region of Enrollment
China
9 participants
n=5 Participants
9 participants
n=7 Participants
18 participants
n=5 Participants
Region of Enrollment
Japan
22 participants
n=5 Participants
10 participants
n=7 Participants
32 participants
n=5 Participants
Region of Enrollment
Malaysia
4 participants
n=5 Participants
6 participants
n=7 Participants
10 participants
n=5 Participants
Region of Enrollment
Indonesia
5 participants
n=5 Participants
2 participants
n=7 Participants
7 participants
n=5 Participants
Region of Enrollment
Philippines
10 participants
n=5 Participants
6 participants
n=7 Participants
16 participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline (Day 1 of preceding study) , Day 154 or at discontinuation

Population: FAS: The FAS consisted of subjects who had received at least one dose of investigational product and for whom the post-dosing efficacy parameter data had been obtained. Cases of GCP violation were excluded from analysis.

Using LOCF datasets, descriptive statistics of actual values for changes of YMRS total scores from baseline (Day 1 of preceding study) to endpoint (Day 154) was calculated for each treatment group. YMRS is composed of 11 evaluation items with 5 rating levels each. Items rated on a scale of 0 to 4 (comprising 5 rating levels of one point each) are 1) levated mood, 2) increased motor activity/energy, 3) sexual interest, 4) sleep, 7) language-thought disorder, 10) appearance, and 11) insight. Items rated on a scale of 0 to 8 (comprising 5 rating levels of two points each) are 5) irritability, 6) speech (rate and amount), 8) content, and 9) disruptive-aggressive behavior. YMRS ranges from 0 (best possible outcome) to 60 (worst possible outcome).

Outcome measures

Outcome measures
Measure
Aripiprazole
n=54 Participants
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered 24 ,12, or 30 mg/day of aripiprazole once daily for 154 days.
Placebo
n=42 Participants
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered placebo once daily for 154 days.
Young Mania Rating Scale (YMRS)
-22.6 scores on a scale
Standard Deviation 11.08
-15.4 scores on a scale
Standard Deviation 12.90

SECONDARY outcome

Timeframe: Baseline (Day 1 of preceding study), Day 154 or at discontinuation

Population: FAS: The FAS consisted of subjects who had received at least one dose of investigational product and for whom the post-dosing efficacy parameter data had been obtained. Cases of GCP violation were excluded from analysis.

Using LOCF datasets, descriptive statistics of actual values for change of CGI-BP severity of illness score (mania) from baseline (Day 1 of preceding study) to endpoint (Day 154) were calculated for each treatment group. CGI-BP severity of illness is a scale for overall evaluation of the severity of bipolar disorder; it comprises 3 components-mania, depression, and overall bipolar illness. CGI-BP severity of illness score (mania) ranges form 1 (normal, not ill) to 7 (very severely ill).

Outcome measures

Outcome measures
Measure
Aripiprazole
n=54 Participants
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered 24 ,12, or 30 mg/day of aripiprazole once daily for 154 days.
Placebo
n=42 Participants
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered placebo once daily for 154 days.
Clinical Global Impression - Bipolar Version (CGI-BP) Severity of Illness (Mania)
-2.9 scores on scale
Standard Deviation 1.45
-1.9 scores on scale
Standard Deviation 1.70

Adverse Events

Aripiprazole

Serious events: 7 serious events
Other events: 46 other events
Deaths: 0 deaths

Placebo

Serious events: 4 serious events
Other events: 26 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Aripiprazole
n=54 participants at risk
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered 24 ,12, or 30 mg/day of aripiprazole once daily for 154 days.
Placebo
n=42 participants at risk
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered placebo once daily for 154 days.
Injury, poisoning and procedural complications
Clavicle Fracture
1.9%
1/54 • Number of events 1 • 22 weeks
0.00%
0/42 • 22 weeks
Nervous system disorders
Akathisia
1.9%
1/54 • Number of events 1 • 22 weeks
0.00%
0/42 • 22 weeks
Nervous system disorders
Stupor
0.00%
0/54 • 22 weeks
2.4%
1/42 • Number of events 1 • 22 weeks
Psychiatric disorders
Depression
3.7%
2/54 • Number of events 2 • 22 weeks
2.4%
1/42 • Number of events 1 • 22 weeks
Psychiatric disorders
Bipolar I Disorder
1.9%
1/54 • Number of events 1 • 22 weeks
2.4%
1/42 • Number of events 1 • 22 weeks
Psychiatric disorders
Mania
1.9%
1/54 • Number of events 1 • 22 weeks
2.4%
1/42 • Number of events 1 • 22 weeks
Psychiatric disorders
Bipolar Disorder
1.9%
1/54 • Number of events 1 • 22 weeks
0.00%
0/42 • 22 weeks
Psychiatric disorders
Delusion of Grandeur
1.9%
1/54 • Number of events 1 • 22 weeks
0.00%
0/42 • 22 weeks

Other adverse events

Other adverse events
Measure
Aripiprazole
n=54 participants at risk
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered 24 ,12, or 30 mg/day of aripiprazole once daily for 154 days.
Placebo
n=42 participants at risk
Patients who had completed the preceding study and demonstrated drug efficacy were the target. Subjects were administered placebo once daily for 154 days.
Gastrointestinal disorders
Constipation
11.1%
6/54 • Number of events 6 • 22 weeks
7.1%
3/42 • Number of events 4 • 22 weeks
Gastrointestinal disorders
Diarrhoea
7.4%
4/54 • Number of events 5 • 22 weeks
9.5%
4/42 • Number of events 6 • 22 weeks
Gastrointestinal disorders
Salivary Hypersecretion
11.1%
6/54 • Number of events 7 • 22 weeks
4.8%
2/42 • Number of events 2 • 22 weeks
Gastrointestinal disorders
Vomiting
3.7%
2/54 • Number of events 2 • 22 weeks
9.5%
4/42 • Number of events 5 • 22 weeks
Gastrointestinal disorders
Nausea
0.00%
0/54 • 22 weeks
14.3%
6/42 • Number of events 11 • 22 weeks
Gastrointestinal disorders
Toothache
5.6%
3/54 • Number of events 5 • 22 weeks
4.8%
2/42 • Number of events 3 • 22 weeks
Gastrointestinal disorders
Abdominal Discomfort
1.9%
1/54 • Number of events 1 • 22 weeks
7.1%
3/42 • Number of events 3 • 22 weeks
Hepatobiliary disorders
Hepatic Function Abnormal
1.9%
1/54 • Number of events 1 • 22 weeks
7.1%
3/42 • Number of events 3 • 22 weeks
Infections and infestations
Nasopharyngitis
9.3%
5/54 • Number of events 6 • 22 weeks
11.9%
5/42 • Number of events 6 • 22 weeks
Infections and infestations
Upper Respiratory Tract Infection
5.6%
3/54 • Number of events 4 • 22 weeks
11.9%
5/42 • Number of events 5 • 22 weeks
Injury, poisoning and procedural complications
Excoriation
5.6%
3/54 • Number of events 4 • 22 weeks
2.4%
1/42 • Number of events 1 • 22 weeks
Investigations
Weight Increased
16.7%
9/54 • Number of events 9 • 22 weeks
2.4%
1/42 • Number of events 1 • 22 weeks
Investigations
Blood Creatine Phosphokinase Increased
5.6%
3/54 • Number of events 3 • 22 weeks
0.00%
0/42 • 22 weeks
Musculoskeletal and connective tissue disorders
Muscle Rigidity
7.4%
4/54 • Number of events 5 • 22 weeks
4.8%
2/42 • Number of events 2 • 22 weeks
Musculoskeletal and connective tissue disorders
Back Pain
1.9%
1/54 • Number of events 1 • 22 weeks
7.1%
3/42 • Number of events 4 • 22 weeks
Musculoskeletal and connective tissue disorders
Myalgia
1.9%
1/54 • Number of events 1 • 22 weeks
7.1%
3/42 • Number of events 3 • 22 weeks
Musculoskeletal and connective tissue disorders
Musculoskeletal Stiffness
5.6%
3/54 • Number of events 4 • 22 weeks
2.4%
1/42 • Number of events 1 • 22 weeks
Nervous system disorders
Akathisia
31.5%
17/54 • Number of events 20 • 22 weeks
16.7%
7/42 • Number of events 8 • 22 weeks
Nervous system disorders
Tremor
18.5%
10/54 • Number of events 11 • 22 weeks
9.5%
4/42 • Number of events 7 • 22 weeks
Nervous system disorders
Headache
3.7%
2/54 • Number of events 2 • 22 weeks
11.9%
5/42 • Number of events 6 • 22 weeks
Nervous system disorders
Dizziness
3.7%
2/54 • Number of events 2 • 22 weeks
9.5%
4/42 • Number of events 6 • 22 weeks
Nervous system disorders
Bradykinesia
9.3%
5/54 • Number of events 6 • 22 weeks
0.00%
0/42 • 22 weeks
Nervous system disorders
Dyskinesia
5.6%
3/54 • Number of events 4 • 22 weeks
2.4%
1/42 • Number of events 1 • 22 weeks
Nervous system disorders
Somnolence
5.6%
3/54 • Number of events 4 • 22 weeks
2.4%
1/42 • Number of events 2 • 22 weeks
Psychiatric disorders
Insomnia
13.0%
7/54 • Number of events 7 • 22 weeks
16.7%
7/42 • Number of events 13 • 22 weeks
Psychiatric disorders
Mania
1.9%
1/54 • Number of events 1 • 22 weeks
7.1%
3/42 • Number of events 3 • 22 weeks

Additional Information

Director of Clinical Research and Development

Otsuka Pharmaceutical Co., Ltd.

Phone: +81-3-6361-7366

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place