Trial Outcomes & Findings for Phase II Trial Of ZK-EPO (ZK 219477) (Sagopilone) In Metastatic Melanoma (NCT NCT00598507)

NCT ID: NCT00598507

Last Updated: 2013-12-11

Results Overview

Objective tumor response according to Response Evaluation Criteria In Solid Tumors (RECIST). Complete Response (CR): Disappearance of all target lesions. Any pathological lymph nodes (whether target or non-target) must have reduction in short axis to \<10 mm. Partial Response (PR): At least a 30% decrease in the sum of the diameters of target lesions, taking as reference the baseline sum diameters. Stable Disease (SD): Stable disease is measured from the start of the treatment until the criteria for progression are met, taking as reference the smallest measurements recorded since the treatment started, including the baseline measurements. Progressive Disease (PD): At least a 20% increase in the sum of the diameters of target lesions, taking as reference the smallest sum on study (this includes the baseline sum if that is the smallest on study).

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

35 participants

Primary outcome timeframe

Up to 5 years

Results posted on

2013-12-11

Participant Flow

Accrual began in May 2007 at Moffitt Cancer Center and was completed in October 2008.

Participant milestones

Participant milestones
Measure
Chemotherapy - ZK-EPO
ZK-EPO (ZK 219477) (Sagopilone), 16 mg/m\^2, was administered intravenously over 3-hours every 21 days until progression or unacceptable toxicity.
Overall Study
STARTED
35
Overall Study
COMPLETED
35
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Phase II Trial Of ZK-EPO (ZK 219477) (Sagopilone) In Metastatic Melanoma

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Chemotherapy - ZK-EPO
n=35 Participants
ZK-EPO (ZK 219477) (Sagopilone), 16 mg/m\^2, was administered intravenously over 3-hours every 21 days until progression or unacceptable toxicity.
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
12 Participants
n=5 Participants
Age, Categorical
>=65 years
23 Participants
n=5 Participants
Age Continuous
68.7 years
STANDARD_DEVIATION 1.7 • n=5 Participants
Sex: Female, Male
Female
11 Participants
n=5 Participants
Sex: Female, Male
Male
24 Participants
n=5 Participants
Region of Enrollment
United States
35 participants
n=5 Participants

PRIMARY outcome

Timeframe: Up to 5 years

Population: All participants

Objective tumor response according to Response Evaluation Criteria In Solid Tumors (RECIST). Complete Response (CR): Disappearance of all target lesions. Any pathological lymph nodes (whether target or non-target) must have reduction in short axis to \<10 mm. Partial Response (PR): At least a 30% decrease in the sum of the diameters of target lesions, taking as reference the baseline sum diameters. Stable Disease (SD): Stable disease is measured from the start of the treatment until the criteria for progression are met, taking as reference the smallest measurements recorded since the treatment started, including the baseline measurements. Progressive Disease (PD): At least a 20% increase in the sum of the diameters of target lesions, taking as reference the smallest sum on study (this includes the baseline sum if that is the smallest on study).

Outcome measures

Outcome measures
Measure
Chemotherapy - ZK-EPO
n=35 Participants
ZK-EPO (ZK 219477) (Sagopilone), 16 mg/m\^2, was administered intravenously over 3-hours every 21 days until progression or unacceptable toxicity.
Response Rate (RR)
Confirmed Complete Response
1 participants
Response Rate (RR)
Confirmed Partial Response
2 participants
Response Rate (RR)
Unconfirmed Partial Response
1 participants
Response Rate (RR)
Stable Disease for at Least 12 Weeks
8 participants

SECONDARY outcome

Timeframe: Up to 5 years

Population: All participants

PFS: the duration of time from start of treatment to time of progression or death, whichever occurs first. Progressive Disease (PD)according to modified Response Evaluation Criteria in Solid Tumors (RECIST) Criteria: At least a 20% increase in the sum of the diameters of target lesions, taking as reference the smallest sum on study (this includes the baseline sum if that is the smallest on study).

Outcome measures

Outcome measures
Measure
Chemotherapy - ZK-EPO
n=35 Participants
ZK-EPO (ZK 219477) (Sagopilone), 16 mg/m\^2, was administered intravenously over 3-hours every 21 days until progression or unacceptable toxicity.
Median Progression Free Survival (PFS)
7.5 weeks
Interval 6.4 to 8.7

SECONDARY outcome

Timeframe: Up to 5 years

Population: All participants

Median OS: the time (expressed in months or years) when half the patients are expected to be alive.

Outcome measures

Outcome measures
Measure
Chemotherapy - ZK-EPO
n=35 Participants
ZK-EPO (ZK 219477) (Sagopilone), 16 mg/m\^2, was administered intravenously over 3-hours every 21 days until progression or unacceptable toxicity.
Median Overall Survival (OS)
31 weeks
Interval 14.9 to 47.1

SECONDARY outcome

Timeframe: Up to 5 years

Population: All participants

Number of participants with Grade 3 or higher adverse events, attributable to treatment with sagopilone.

Outcome measures

Outcome measures
Measure
Chemotherapy - ZK-EPO
n=35 Participants
ZK-EPO (ZK 219477) (Sagopilone), 16 mg/m\^2, was administered intravenously over 3-hours every 21 days until progression or unacceptable toxicity.
Occurrence of Attributable Serious Adverse Events (SAEs)
0 participants

Adverse Events

Chemotherapy - ZK-EPO

Serious events: 5 serious events
Other events: 35 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Chemotherapy - ZK-EPO
n=35 participants at risk
ZK-EPO (ZK 219477) (Sagopilone), 16 mg/m\^2, was administered intravenously over 3-hours every 21 days until progression or unacceptable toxicity.
General disorders
Confusion
2.9%
1/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Metabolism and nutrition disorders
Creatinine - high
2.9%
1/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Death not associated with CTCAE term - Death NOS
2.9%
1/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Gastrointestinal disorders
Dehydration
2.9%
1/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Fever in the absence of neutropenia
2.9%
1/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Infections and infestations
Infection with normal ANC or Grade 1 or 2 neutrophils - Lung (pneumonia)
2.9%
1/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Cardiac disorders
Pulmonary hypertension
2.9%
1/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Respiratory, thoracic and mediastinal disorders
Pulmonary/Upper Respiratory - Other
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Syncope (fainting)
2.9%
1/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.

Other adverse events

Other adverse events
Measure
Chemotherapy - ZK-EPO
n=35 participants at risk
ZK-EPO (ZK 219477) (Sagopilone), 16 mg/m\^2, was administered intravenously over 3-hours every 21 days until progression or unacceptable toxicity.
Nervous system disorders
Neuropathy: sensory
54.3%
19/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Nervous system disorders
Neuropathy: motor
22.9%
8/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Confusion
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Blood and lymphatic system disorders
Hemoglobin - low
31.4%
11/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Blood and lymphatic system disorders
Leukocytes (total WBC) - low
22.9%
8/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Blood and lymphatic system disorders
Neutrophils/granulocytes (ANC/AGC) - low
14.3%
5/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Blood and lymphatic system disorders
Platelets - low
14.3%
5/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Fatigue (asthenia, lethargy, malaise)
37.1%
13/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Fever (in the absence of neutropenia)
8.6%
3/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Constitutional Symptoms - Other
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Pain - Extremity-limb
20.0%
7/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Pain - Joint
20.0%
7/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Pain - Muscle
14.3%
5/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Pain - Back
8.6%
3/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Pain - Bone
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
General disorders
Pain - Head/headache
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Metabolism and nutrition disorders
Glucose, serum-high (hyperglycemia)
28.6%
10/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Metabolism and nutrition disorders
Sodium, serum-low (hyponatremia)
14.3%
5/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Metabolism and nutrition disorders
Potassium, serum-high (hyperkalemia)
11.4%
4/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Metabolism and nutrition disorders
Alkaline phosphatase
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Metabolism and nutrition disorders
ALT, SGPT (serum glutamic pyruvic transaminase) - high
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Metabolism and nutrition disorders
AST, SGOT(serum glutamic oxaloacetic transaminase) - high
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Metabolism and nutrition disorders
Calcium, serum-low (hypocalcemia)
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Gastrointestinal disorders
Nausea
31.4%
11/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Gastrointestinal disorders
Anorexia
22.9%
8/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Gastrointestinal disorders
Constipation
17.1%
6/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Gastrointestinal disorders
Vomiting
11.4%
4/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Gastrointestinal disorders
Dehydration
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Gastrointestinal disorders
Diarrhea
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Respiratory, thoracic and mediastinal disorders
Cough
20.0%
7/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Respiratory, thoracic and mediastinal disorders
Dyspnea (shortness of breath)
20.0%
7/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Respiratory, thoracic and mediastinal disorders
Pulmonary/Upper Respiratory - Other
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Skin and subcutaneous tissue disorders
Hair loss/alopecia (scalp or body)
11.4%
4/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Skin and subcutaneous tissue disorders
Rash/desquamation
11.4%
4/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Cardiac disorders
Hypotension
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Infections and infestations
Infection with normal ANC or Grade 1 or 2 neutrophils - Lymphatic
5.7%
2/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.
Blood and lymphatic system disorders
Edema: limb
14.3%
5/35 • Up to 5 years
Participants treated with at least one dose of sagopilone.

Additional Information

Ronald DeConti, M.D., Principal Investigator

H. Lee Moffitt Cancer Center and Research Institute

Phone: 813-745-8466

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place