Trial Outcomes & Findings for Invega (Paliperidone) for the Treatment of Mania in Children and Adolescents Ages 6-17 With Bipolar Disorder (NCT NCT00592358)

NCT ID: NCT00592358

Last Updated: 2012-07-04

Results Overview

The YMRS is an 11-item instrument used to assess the severity of mania in patients with a diagnosis of bipolar disorder. Four items are graded on a 0 to 8 scale (irritability, speech, thought content, and disruptive/aggressive behavior), while the remaining seven itemsare graded on a 0 to 4 scale. The maximum possible total score is 60 (worse outcome, severe symptoms), and the minimum possible total score is 0 (no symptoms).

Recruitment status

TERMINATED

Study phase

PHASE4

Target enrollment

17 participants

Primary outcome timeframe

Baseline and 8 weeks (or final study visit, if subjects completed the study before 8 weeks)

Results posted on

2012-07-04

Participant Flow

Participant milestones

Participant milestones
Measure
Paliperidone
Open label treatment with Invega (Paliperidone) once daily, with dosage of 3mg per day, titrated in 3mg increments to a maximum of 6mg per day based on subject age, weight and tolerance.
Overall Study
STARTED
17
Overall Study
COMPLETED
11
Overall Study
NOT COMPLETED
6

Reasons for withdrawal

Reasons for withdrawal
Measure
Paliperidone
Open label treatment with Invega (Paliperidone) once daily, with dosage of 3mg per day, titrated in 3mg increments to a maximum of 6mg per day based on subject age, weight and tolerance.
Overall Study
Withdrawal by Subject
2
Overall Study
Adverse Event
1
Overall Study
Lack of Efficacy
2
Overall Study
Inability to swallow pills
1

Baseline Characteristics

Invega (Paliperidone) for the Treatment of Mania in Children and Adolescents Ages 6-17 With Bipolar Disorder

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Paliperidone
n=17 Participants
Open label treatment with Invega (Paliperidone) once daily, with dosage of 3mg per day, titrated in 3mg increments to a maximum of 6mg per day based on subject age, weight and tolerance.
Age, Categorical
<=18 years
17 Participants
n=93 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=93 Participants
Age, Categorical
>=65 years
0 Participants
n=93 Participants
Age Continuous
9.88 years
STANDARD_DEVIATION 2.39 • n=93 Participants
Sex: Female, Male
Female
4 Participants
n=93 Participants
Sex: Female, Male
Male
13 Participants
n=93 Participants
Region of Enrollment
United States
17 participants
n=93 Participants

PRIMARY outcome

Timeframe: Baseline and 8 weeks (or final study visit, if subjects completed the study before 8 weeks)

Population: Participants exposed to study medication for a minimum of three weeks were included in analyses.

The YMRS is an 11-item instrument used to assess the severity of mania in patients with a diagnosis of bipolar disorder. Four items are graded on a 0 to 8 scale (irritability, speech, thought content, and disruptive/aggressive behavior), while the remaining seven itemsare graded on a 0 to 4 scale. The maximum possible total score is 60 (worse outcome, severe symptoms), and the minimum possible total score is 0 (no symptoms).

Outcome measures

Outcome measures
Measure
Paliperidone
n=15 Participants
Open-label treatment with Paliperidone.
Change in Symptoms Measured by Young Mania Rating Scale (YMRS)
Baseline
32.8 units on a scale
Standard Deviation 6.1
Change in Symptoms Measured by Young Mania Rating Scale (YMRS)
Endpoint
14.1 units on a scale
Standard Deviation 11.2

SECONDARY outcome

Timeframe: Baseline and 8 weeks (or final study visit, if subjects completed the study before 8 weeks)

Population: All participants for whom the mania checklist was available at both baseline and endpoint (8-weeks) were included in analyses.

A 13-item clinician-rated symptom checklist developed by Massachusetts General Hospital to measure symptoms of mania. Each item is given a rating for frequency (1=less than 4 days, 2=greater than or equal to 4 days, 3=daily) and intensity (1=mild, 2=moderate, 3=severe), which are combined to yield a composite severity score ranging from 0 (least severe) to 3 (most severe). The composite severity scores from all 13 items are summed to yield a total measure score, with a minimum score of 0 (least severe) and a maximum score of 39 (most severe).

Outcome measures

Outcome measures
Measure
Paliperidone
n=8 Participants
Open-label treatment with Paliperidone.
Change in Symptoms Measured by DSM-IV Mania Symptoms Checklist
Baseline
18.5 units on a scale
Standard Deviation 5.6
Change in Symptoms Measured by DSM-IV Mania Symptoms Checklist
Endpoint
10.9 units on a scale
Standard Deviation 6.3

Adverse Events

Paliperidone

Serious events: 0 serious events
Other events: 14 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
Paliperidone
n=15 participants at risk
Open label treatment with Invega (Paliperidone) once daily, with dosage of 3mg per day, titrated in 3mg increments to a maximum of 6mg per day based on subject age, weight and tolerance.
Skin and subcutaneous tissue disorders
Plaque-like skin lesion
6.7%
1/15 • Number of events 1
Skin and subcutaneous tissue disorders
Superficial scratches on arm
6.7%
1/15 • Number of events 1
Skin and subcutaneous tissue disorders
Acne
6.7%
1/15 • Number of events 1
Eye disorders
Blurred vision
20.0%
3/15 • Number of events 4
Respiratory, thoracic and mediastinal disorders
Bronchospasm
6.7%
1/15 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Cold symptoms
26.7%
4/15 • Number of events 6
Gastrointestinal disorders
Diarrhea
6.7%
1/15 • Number of events 1
Renal and urinary disorders
Enuresis
6.7%
1/15 • Number of events 1
General disorders
Mild extrapyrimidal symptoms
6.7%
1/15 • Number of events 1
Skin and subcutaneous tissue disorders
Erythema
6.7%
1/15 • Number of events 2
Eye disorders
Eye twitching
6.7%
1/15 • Number of events 2
General disorders
Flu like symptoms
20.0%
3/15 • Number of events 3
General disorders
Headache
20.0%
3/15 • Number of events 7
Metabolism and nutrition disorders
Increased appetite
40.0%
6/15 • Number of events 15
General disorders
insomnia
33.3%
5/15 • Number of events 6
Gastrointestinal disorders
Nausea
6.7%
1/15 • Number of events 3
Cardiac disorders
Heart palpitation
6.7%
1/15 • Number of events 1
Skin and subcutaneous tissue disorders
Rash
13.3%
2/15 • Number of events 6
Respiratory, thoracic and mediastinal disorders
Seasonal allergies
6.7%
1/15 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Sore throat
20.0%
3/15 • Number of events 3
General disorders
Strep throat
13.3%
2/15 • Number of events 4
Gastrointestinal disorders
Vomiting
13.3%
2/15 • Number of events 2
Metabolism and nutrition disorders
Weight gain
6.7%
1/15 • Number of events 1
Psychiatric disorders
Worsening of anxiety and depressive symptoms
6.7%
1/15 • Number of events 1
Metabolism and nutrition disorders
Low appetite
13.3%
2/15 • Number of events 3

Additional Information

Janet Wozniak, MD

Massachusetts General Hospital

Phone: (617)503-1038

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place