Trial Outcomes & Findings for Study of Sequential Administration of Oral 6-Thioguanine After Methotrexate in Patients With LCH (NCT NCT00588536)

NCT ID: NCT00588536

Last Updated: 2015-05-04

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

5 participants

Primary outcome timeframe

Conclusion of the study

Results posted on

2015-05-04

Participant Flow

Protocol Open to Accrual: 01/10/1995 Protocol Closed to Accrual: 07/25/2006 Primary Completion Date (if applicable): 06/09/2009 Recruitment Location is the medical clinic

Participant milestones

Participant milestones
Measure
MTX, 6-TG and Leucovorin
Methotrexate: MTX 30mg/m2 (or 1mg/kg for infants) orally, given in three equally divided doses at 0,8, and 16hrs 6-Thioguanine: 6-TG 300mg/m2 (or 10mg/kg for infants) orally, given in one dose. Leucovorin Calcium: 5mg orally at 36,48, and 60hrs (or 12 hrs after the dose of 6-TG and then every 12 hrs for a total of 3 doses)
Overall Study
STARTED
5
Overall Study
COMPLETED
5
Overall Study
NOT COMPLETED
0

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Study of Sequential Administration of Oral 6-Thioguanine After Methotrexate in Patients With LCH

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
MTX, 6-TG and Leucovorin
n=5 Participants
Methotrexate: MTX 30mg/m2 (or 1mg/kg for infants) orally, given in three equally divided doses at 0,8, and 16hrs 6-Thioguanine: 6-TG 300mg/m2 (or 10mg/kg for infants) orally, given in one dose. Leucovorin Calcium: 5mg orally at 36,48, and 60hrs (or 12 hrs after the dose of 6-TG and then every 12 hrs for a total of 3 doses)
Age, Categorical
<=18 years
4 Participants
n=93 Participants
Age, Categorical
Between 18 and 65 years
1 Participants
n=93 Participants
Age, Categorical
>=65 years
0 Participants
n=93 Participants
Sex: Female, Male
Female
3 Participants
n=93 Participants
Sex: Female, Male
Male
2 Participants
n=93 Participants
Region of Enrollment
United States
5 participants
n=93 Participants

PRIMARY outcome

Timeframe: Conclusion of the study

Outcome measures

Outcome measures
Measure
MTX, 6-TG and Leucovorin
n=5 Participants
Methotrexate: MTX 30mg/m2 (or 1mg/kg for infants) orally, given in three equally divided doses at 0,8, and 16hrs 6-Thioguanine: 6-TG 300mg/m2 (or 10mg/kg for infants) orally, given in one dose. Leucovorin Calcium: 5mg orally at 36,48, and 60hrs (or 12 hrs after the dose of 6-TG and then every 12 hrs for a total of 3 doses)
Determine the Incidence of Complete and Partial Response and the Duration of Response in Patients With Langerhans Cell Histiocytosis (LCH) Treated With Sequential Administration of Oral 6-TG After MTX.
Complete Response
2 participants
Determine the Incidence of Complete and Partial Response and the Duration of Response in Patients With Langerhans Cell Histiocytosis (LCH) Treated With Sequential Administration of Oral 6-TG After MTX.
Stable Disease
1 participants
Determine the Incidence of Complete and Partial Response and the Duration of Response in Patients With Langerhans Cell Histiocytosis (LCH) Treated With Sequential Administration of Oral 6-TG After MTX.
Progression of Disease
2 participants

Adverse Events

MTX, 6-TG and Leucovorin

Serious events: 2 serious events
Other events: 5 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
MTX, 6-TG and Leucovorin
n=5 participants at risk
Methotrexate: MTX 30mg/m2 (or 1mg/kg for infants) orally, given in three equally divided doses at 0,8, and 16hrs 6-Thioguanine: 6-TG 300mg/m2 (or 10mg/kg for infants) orally, given in one dose. Leucovorin Calcium: 5mg orally at 36,48, and 60hrs (or 12 hrs after the dose of 6-TG and then every 12 hrs for a total of 3 doses)
General disorders
Fever
20.0%
1/5 • Number of events 1
Investigations
Neutrophil count decreased
20.0%
1/5 • Number of events 1
Investigations
Platelet count decreased
20.0%
1/5 • Number of events 1

Other adverse events

Other adverse events
Measure
MTX, 6-TG and Leucovorin
n=5 participants at risk
Methotrexate: MTX 30mg/m2 (or 1mg/kg for infants) orally, given in three equally divided doses at 0,8, and 16hrs 6-Thioguanine: 6-TG 300mg/m2 (or 10mg/kg for infants) orally, given in one dose. Leucovorin Calcium: 5mg orally at 36,48, and 60hrs (or 12 hrs after the dose of 6-TG and then every 12 hrs for a total of 3 doses)
Gastrointestinal disorders
Abdominal pain/cramping
20.0%
1/5 • Number of events 1
Metabolism and nutrition disorders
Anorexia
20.0%
1/5 • Number of events 1
Investigations
Blood bilirubin increased
20.0%
1/5 • Number of events 1
Musculoskeletal and connective tissue disorders
Bone pain
20.0%
1/5 • Number of events 1
Respiratory, thoracic and mediastinal disorders
Sore throat
20.0%
1/5 • Number of events 2
Investigations
Creatinine increased
20.0%
1/5 • Number of events 1
Gastrointestinal disorders
Diarrhea
20.0%
1/5 • Number of events 1
Nervous system disorders
Headache
20.0%
1/5 • Number of events 1
Blood and lymphatic system disorders
Anemia
80.0%
4/5 • Number of events 10
Metabolism and nutrition disorders
Hypomagnesemia
20.0%
1/5 • Number of events 1
Investigations
White blood cell decreased
40.0%
2/5 • Number of events 4
Gastrointestinal disorders
Nausea
20.0%
1/5 • Number of events 1
Investigations
Neutrophil count decreased
20.0%
1/5 • Number of events 1
Investigations
Platelet count decreased
40.0%
2/5 • Number of events 9
Skin and subcutaneous tissue disorders
Rash desquamation
20.0%
1/5 • Number of events 1

Additional Information

Dr. Tanya Trippett

Memorial Sloan Kettering Cancer Center

Phone: 212-639-8267

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place