Trial Outcomes & Findings for Safety and Efficacy of Asacol 4.8 g/Day Versus Asacol 2.4 g/Day (ASCEND I) (NCT NCT00577473)

NCT ID: NCT00577473

Last Updated: 2011-09-16

Results Overview

Treatment Success - complete or partial response; Complete = complete resolution of clinical assessments (stool frequency, rectal bleeding, PFA \[patient's functional assessment\], sigmoidoscopy) and PGA (physician global assessment) = 0, Partial = improvement from baseline PGA score and improvement in at least 1 of the clinical assessments \[decrease of at least 1 on scale\] and no worsening \[no score increases\] of remaining clinical assessments. Each clinical assessment graded using scale 0/normal, better thru 3/severe, worse.

Recruitment status

COMPLETED

Study phase

PHASE3

Target enrollment

301 participants

Primary outcome timeframe

6 weeks

Results posted on

2011-09-16

Participant Flow

Screening began 9 Feb 2001

Participant milestones

Participant milestones
Measure
Asacol 2.4 g/Day
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Overall Study
STARTED
154
147
Overall Study
ITT Population
150
136
Overall Study
COMPLETED
133
123
Overall Study
NOT COMPLETED
21
24

Reasons for withdrawal

Reasons for withdrawal
Measure
Asacol 2.4 g/Day
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Overall Study
Protocol Violation
1
4
Overall Study
Adverse Event
8
5
Overall Study
Withdrawal by Subject
2
6
Overall Study
Physician Decision
2
2
Overall Study
Lack of Efficacy
8
7

Baseline Characteristics

Safety and Efficacy of Asacol 4.8 g/Day Versus Asacol 2.4 g/Day (ASCEND I)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Total
n=301 Participants
Total of all reporting groups
Age, Customized
18 - 64 years
141 Participants
n=5 Participants
133 Participants
n=7 Participants
274 Participants
n=5 Participants
Age, Customized
>= 65 years
13 Participants
n=5 Participants
14 Participants
n=7 Participants
27 Participants
n=5 Participants
Sex: Female, Male
Female
79 Participants
n=5 Participants
67 Participants
n=7 Participants
146 Participants
n=5 Participants
Sex: Female, Male
Male
75 Participants
n=5 Participants
80 Participants
n=7 Participants
155 Participants
n=5 Participants
Race/Ethnicity, Customized
Caucasian
122 Partcipants
n=5 Participants
116 Partcipants
n=7 Participants
238 Partcipants
n=5 Participants
Race/Ethnicity, Customized
Black or African American
18 Partcipants
n=5 Participants
18 Partcipants
n=7 Participants
36 Partcipants
n=5 Participants
Race/Ethnicity, Customized
Asian (Indian)
2 Partcipants
n=5 Participants
2 Partcipants
n=7 Participants
4 Partcipants
n=5 Participants
Race/Ethnicity, Customized
Asian (Oriental)
1 Partcipants
n=5 Participants
0 Partcipants
n=7 Participants
1 Partcipants
n=5 Participants
Race/Ethnicity, Customized
Hispanic
10 Partcipants
n=5 Participants
9 Partcipants
n=7 Participants
19 Partcipants
n=5 Participants
Race/Ethnicity, Customized
Multi-racial/other
1 Partcipants
n=5 Participants
2 Partcipants
n=7 Participants
3 Partcipants
n=5 Participants

PRIMARY outcome

Timeframe: 6 weeks

Population: ITT Population

Treatment Success - complete or partial response; Complete = complete resolution of clinical assessments (stool frequency, rectal bleeding, PFA \[patient's functional assessment\], sigmoidoscopy) and PGA (physician global assessment) = 0, Partial = improvement from baseline PGA score and improvement in at least 1 of the clinical assessments \[decrease of at least 1 on scale\] and no worsening \[no score increases\] of remaining clinical assessments. Each clinical assessment graded using scale 0/normal, better thru 3/severe, worse.

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=150 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=136 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Percentage of Patients Classified as Treatment Success at Week 6, ITT Population
51.3 Percentage of Participants
55.9 Percentage of Participants

SECONDARY outcome

Timeframe: 3 weeks

Population: ITT Population

Treatment Success - complete or partial response; Complete = complete resolution of clinical assessments (stool frequency, rectal bleeding, PFA \[patient's functional assessment\], sigmoidoscopy) and PGA (physician global assessment) = 0, Partial = improvement from baseline PGA score and improvement in at least 1 of the clinical assessments \[decrease of at least 1 on scale\] and no worsening \[no score increases\] of remaining clinical assessments. Each clinical assessment graded using scale 0/normal, better thru 3/severe, worse.

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=150 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=137 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Percentage of Patients Classified as Treatment Success at Week 3, ITT Population
42.0 Percentage of Participants
38.7 Percentage of Participants

SECONDARY outcome

Timeframe: Week 3

Population: All Randomized Patients

PGA - 0-quiescent disease activity (all 0's) , 1-mild (mostly 1's), 2-moderate (mostly 2's), 3-severe (mostly 3's) based upon on scoring for stool frequency, rectal bleeding, PFR (patient's functional assessment - 0-well, 1-fair, 2-poor, 3-terrible), sigmoidoscopy findings. Improvement defined as either complete response (remission, score = 0) or partial response (improvement on treatment). Scoring Scale: 0-good thru 3-worse.

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Physician's Global Assessment (PGA) Percentage of Patients Improved at Week 3, All Randomized Patients
49.3 Percentage of Participants
44.8 Percentage of Participants

SECONDARY outcome

Timeframe: Week 6

Population: All Randomized Patients

PGA - 0-quiescent disease activity (all 0's) , 1-mild (mostly 1's), 2-moderate (mostly 2's), 3-severe (mostly 3's) based upon on scoring for stool frequency, rectal bleeding, PFR (patient's functional assessment - 0-well, 1-fair, 2-poor, 3-terrible), sigmoidoscopy findings. Improvement defined as complete response (remission, score = 0) or partial response (improvement on treatment). Scoring Scale: 0-good thru 3-worse.

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Physician's Global Assessment (PGA) Percentage of Patients Improved at Week 6, All Randomized Patients
61.4 Percentage of Participants
64.8 Percentage of Participants

SECONDARY outcome

Timeframe: Week 3

Population: All Randomized Patients

0: normal stool frequency per day, 1: 1-2 stools greater than normal per day, 2: 3-4 stools greater than normal per day, 3: 5 or more stools greater than normal per day, Scoring Scale: 0-good thru 3-worse.

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Stool Frequency Improvement at Week 3, All Randomized Patients (Percentage)
46.7 Percentage of Participants
54.3 Percentage of Participants

SECONDARY outcome

Timeframe: Week 6

Population: All Randomized Patients

0: normal stool frequency per day, 1: 1-2 stools greater than normal per day, 2: 3-4 stools greater than normal per day, 3: 5 or more stools greater than normal per day, Scoring Scale: 0-good thru 3-worse.

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Stool Frequency Improvement at Week 6, All Randomized Patients (Percentage)
63.2 Percentage of Participants
66.7 Percentage of Participants

SECONDARY outcome

Timeframe: Week 3

Population: All Randomized Patients

0: no blood seen, 1: streaks of blood with stool less than half of the time, 2: obvious blood with stool most of the time, 3: blood alone passed, Scoring Scale: 0-good thru 3-worse.

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Rectal Bleeding Improvement at Week 3, All Randomized Patients (Percentage)
48.1 Percentage of Participants
59.1 Percentage of Participants

SECONDARY outcome

Timeframe: Week 6

Population: All Randomized Patients

0-no blood seen, 1- streaks of blood with stool less than half of the time, 2- obvious blood with stool most of the time, 3- blood alone passed. Scoring Scale: 0-good thru 3-worse.

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Rectal Bleeding Improvement at Week 6, All Randomized Patients (Percentage)
60.2 Percentage of Participants
71.5 Percentage of Participants

SECONDARY outcome

Timeframe: Week 3

Population: All Randomized Patients

0-generally well, 1-fair, 2-poor, 3-terrible

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Improvement in Patient's Functional Assessment (PFA) at Week 3, All Randomized Patients (Percentage)
42.2 Percentage of Participants
49.6 Percentage of Participants

SECONDARY outcome

Timeframe: Week 6

Population: All Randomized Patients

0-generally well, 1-fair, 2-poor, 3-terrible

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Improvement in Patient's Functional Assessment (PFA) at Week 6, All Randomized Patients (Percentage)
54.1 Percentage of Participants
60.7 Percentage of Participants

SECONDARY outcome

Timeframe: Week 3

Population: All Randomized Patients

0-normal (intact vascular pattern, no friability or granularity), 1-mild (erythema; diminished or absent vascular markings; mild granularity; friability), 2-moderate (marked erythema, granularity; absent vascular markings; bleeds with minimal trauma; no ulcerations), 3-severe (spontaneous bleeding, ulcerations). Scoring Scale: 0-good thru 3-worse.

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Improvement in Patient's Sigmoidoscopy Assessment Score at Week 3, All Randomized Patients (Percentage)
51.5 Percentage of Participants
52.0 Percentage of Participants

SECONDARY outcome

Timeframe: Week 6

Population: All Randomized Patients

0-normal (intact vascular pattern, no friability or granularity), 1-mild (erythema; diminished or absent vascular markings; mild granularity; friability), 2-moderate (marked erythema, granularity; absent vascular markings; bleeds with minimal trauma; no ulcerations), 3-severe (spontaneous bleeding, ulcerations). Scoring Scale: 0-good thru 3-worse.

Outcome measures

Outcome measures
Measure
Asacol 2.4 g/Day
n=154 Participants
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 Participants
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Improvement in Patient's Sigmoidoscopy Assessment Score at Week 6, All Randomized Patients (Percentage)
66.7 Percentage of Participants
73.2 Percentage of Participants

Adverse Events

Asacol 2.4 g/Day

Serious events: 3 serious events
Other events: 56 other events
Deaths: 0 deaths

Asacol 4.8 g/Day

Serious events: 1 serious events
Other events: 48 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Asacol 2.4 g/Day
n=154 participants at risk
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 participants at risk
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Reproductive system and breast disorders
Uterine Fibroids Exacerbation
0.65%
1/154 • Number of events 1 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.00%
0/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Reproductive system and breast disorders
Ovarian Cyst Exacerbation
0.65%
1/154 • Number of events 1 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.00%
0/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Worsening of Ulcerative Colitis
0.65%
1/154 • Number of events 1 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.00%
0/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Rectal Bleeding
0.65%
1/154 • Number of events 1 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.00%
0/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Diarrhea
0.65%
1/154 • Number of events 1 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.00%
0/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Vascular disorders
Abdominal Pain, Left Side
0.65%
1/154 • Number of events 1 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.00%
0/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Cholecystitis
0.65%
1/154 • Number of events 1 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.00%
0/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Nervous system disorders
Pain, Right Upper Quadrant
0.65%
1/154 • Number of events 1 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.00%
0/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Nervous system disorders
Epigastric Pain
0.00%
0/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.68%
1/147 • Number of events 1 • 6 week treatment period
Screening started February 2001, study completed November 2002

Other adverse events

Other adverse events
Measure
Asacol 2.4 g/Day
n=154 participants at risk
2 - 400 mg Asacol tablets and 2 placebo tablets (matching 800 mg Asacol tablet) 3 times daily for 6 weeks
Asacol 4.8 g/Day
n=147 participants at risk
2 - 800 mg Asacol tablets and 2 placebo tablets (matching 400 mg tablet) 3 times daily for 6 weeks
Nervous system disorders
Headache
5.8%
9/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
5.4%
8/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Nausea
1.3%
2/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
6.1%
9/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Abdominal Pain
4.5%
7/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
2.7%
4/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Infections and infestations
Infection
3.2%
5/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
3.4%
5/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Diarrhea
3.2%
5/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
2.7%
4/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Flatulence
1.9%
3/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
4.1%
6/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Colitis Ulcer
3.9%
6/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
1.4%
2/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Vomiting
0.65%
1/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
4.1%
6/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Skin and subcutaneous tissue disorders
Rash
1.9%
3/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
2.0%
3/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Respiratory, thoracic and mediastinal disorders
Cough
2.6%
4/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.68%
1/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Nervous system disorders
Dizziness
2.6%
4/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.68%
1/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Gastrointestinal disorders
Dyspepsia
1.3%
2/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
2.0%
3/147 • 6 week treatment period
Screening started February 2001, study completed November 2002
Infections and infestations
Flu Syndrome
3.2%
5/154 • 6 week treatment period
Screening started February 2001, study completed November 2002
0.00%
0/147 • 6 week treatment period
Screening started February 2001, study completed November 2002

Additional Information

Grexan Wulff, Manager Regulatory Affairs

Warner Chilcott

Phone: 973-442-3376

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60