Trial Outcomes & Findings for TARCEVA (Erlotinib) in Combination With Chemoradiation in Patients With Stage IIIA/B Non-Small Cell Lung Cancer (NSCLC) (NCT NCT00563784)

NCT ID: NCT00563784

Last Updated: 2019-11-20

Results Overview

Primary Endpoints is efficacy of concurrent erlotinib and chemoradiation as measured by time to progression. Progression is defined using Response Evaluation Criteria in Solid Tumors Criteria (RECIST v1.0), as a 20% increase in the sum of the longest diameter of target lesions. All patients will be evaluated by followed up one month after treatment, once a month until recovery from treatment related toxicities, then every 3 months for 2 years, then every 4 months for 2 years (total of 4 years), then annually up to 5 years.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

68 participants

Primary outcome timeframe

From date of registration until the date of first documented progression or death from any cause, or lost to follow up, whichever came first, assessed up to 5 years.

Results posted on

2019-11-20

Participant Flow

The recruitment period: Nov 20, 2007 to June 18,2010. Total 68 stage IIIA/IIIB Non-Small Cell Lung Cancer (NSCLC) patients registered in the study. Eligible criteria: stage III NSCLC, inoperable, Karnofsky score ≥ 80, weight loss ≤5% in 3 months, forced expiratory volume in 1 second ≥ 1.0 L, and adequate hematologic, hepatic, and renal function.

There were 20 patients off-study after enrollment due to screen failure. Two patients were taken off protocol: 1 for diarrhea unrelated to treatment and the other for chemotherapy-induced chest pain. Only 46 patients are evaluable for this study.

Participant milestones

Participant milestones
Measure
Phase II TARCEVA (Erlotinib) With Chemoradiation in Stage IIIA
TARCEVA (erlotinib) 150 mg, P.O., daily, except for chemotherapy. Paclitaxel, 45mg/m2; Carboplatin, AUC=2, weekly; RT: 63Gy/35 fractions/7 weeks
Overall Study
STARTED
68
Overall Study
COMPLETED
46
Overall Study
NOT COMPLETED
22

Reasons for withdrawal

Reasons for withdrawal
Measure
Phase II TARCEVA (Erlotinib) With Chemoradiation in Stage IIIA
TARCEVA (erlotinib) 150 mg, P.O., daily, except for chemotherapy. Paclitaxel, 45mg/m2; Carboplatin, AUC=2, weekly; RT: 63Gy/35 fractions/7 weeks
Overall Study
Withdrawal by Subject
2
Overall Study
Screen Failures
20

Baseline Characteristics

TARCEVA (Erlotinib) in Combination With Chemoradiation in Patients With Stage IIIA/B Non-Small Cell Lung Cancer (NSCLC)

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Phase II TARCEVA (Erlotinib) With Chemoradiation in Stage IIIA
n=48 Participants
TARCEVA (erlotinib) 150 mg, P.O., daily, except for chemotherapy. Paclitaxel, 45mg/m2; Carboplatin, AUC=2, weekly; RT: 63Gy/35 fractions/7 weeks
Age, Categorical
<=18 years
0 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
25 Participants
n=5 Participants
Age, Categorical
>=65 years
23 Participants
n=5 Participants
Age, Continuous
63.5 years
n=5 Participants
Sex: Female, Male
Female
18 Participants
n=5 Participants
Sex: Female, Male
Male
30 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Hispanic or Latino
3 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Not Hispanic or Latino
10 Participants
n=5 Participants
Ethnicity (NIH/OMB)
Unknown or Not Reported
35 Participants
n=5 Participants
Race (NIH/OMB)
American Indian or Alaska Native
0 Participants
n=5 Participants
Race (NIH/OMB)
Asian
2 Participants
n=5 Participants
Race (NIH/OMB)
Native Hawaiian or Other Pacific Islander
0 Participants
n=5 Participants
Race (NIH/OMB)
Black or African American
2 Participants
n=5 Participants
Race (NIH/OMB)
White
42 Participants
n=5 Participants
Race (NIH/OMB)
More than one race
0 Participants
n=5 Participants
Race (NIH/OMB)
Unknown or Not Reported
2 Participants
n=5 Participants
Region of Enrollment
United States
46 participants
n=5 Participants
Region of Enrollment
Mexico
1 participants
n=5 Participants
Region of Enrollment
United Arab Emirates
1 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Disease Stage IIIA
22 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Disease Stage IIIB
26 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Tumor Histology Adenocarcinoma
23 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Tumor Histology Squamous Cell Carcinoma
15 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Tumor Histology NSCLC Unspecified
9 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Karnofsky performance score (KPS) 100
3 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Karnofsky performance (KPS) score 90
32 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Karnofsky performance(KPS) score 80
13 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
EGFR status Wild-type
38 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
EGFR status- Mutated or deleted
4 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
EGFR status Unknown
6 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Smoking history Former
36 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Smoking history Current
6 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Smoking history Never
6 participants
n=5 Participants
Participants characteristic for completed treatment under the protocol and evaluable
Tumor HistologyLarge Cell Neuroendocrine Carcinoma
1 participants
n=5 Participants

PRIMARY outcome

Timeframe: From date of registration until the date of first documented progression or death from any cause, or lost to follow up, whichever came first, assessed up to 5 years.

Population: There were 46 out of 48 patients completed treatment under the protocol and evaluable for data analysis. 2 patients cannot complete the treatment and off-study. 1 for diarrhea unrelated to treatment and the other for chemotherapy-induced chest pain.

Primary Endpoints is efficacy of concurrent erlotinib and chemoradiation as measured by time to progression. Progression is defined using Response Evaluation Criteria in Solid Tumors Criteria (RECIST v1.0), as a 20% increase in the sum of the longest diameter of target lesions. All patients will be evaluated by followed up one month after treatment, once a month until recovery from treatment related toxicities, then every 3 months for 2 years, then every 4 months for 2 years (total of 4 years), then annually up to 5 years.

Outcome measures

Outcome measures
Measure
Phase II TARCEVA (Erlotinib) With Chemoradiation in Stage IIIA
n=46 Participants
TARCEVA (erlotinib) 150 mg, P.O., daily, except for chemotherapy. Paclitaxel, 45mg/m2; Carboplatin, AUC=2, weekly; RT: 63Gy/35 fractions/7 weeks
Time To First Disease Progression
14 Month
Interval 9.0 to 18.6

SECONDARY outcome

Timeframe: OS: From date of registration until the date of first documented death or lost to follow up, whichever came first, accessed up to 5 years. DLC: From date of registration until the date of first documented local disease recurrence, accessed up to 5 years.

Population: There were 46 out of 48 patients completed treatment under the protocol and evaluable for data analysis. 2 patients cannot complete the treatment and off-study. 1 for diarrhea unrelated to treatment and the other for chemotherapy-induced chest pain.

The Secondary Endpoints is Overall Survival (OS)and Disease Local Control (DLC)Rate. All patients will be followed up to evaluate Overall Survival and Disease Local Control by one month after treatment, once a month until recovery from treatment related toxicities, then every 3 months for 2 years, then every 4 months for 2 years (total of 4 years), then annually up to 5 years. CT scan of the chest/upper abdomen, MRI of brain or CT, and/or PET scan images are recommended to confirm the recurrence. Survival endpoints were estimated using the Kaplan-Meier method.

Outcome measures

Outcome measures
Measure
Phase II TARCEVA (Erlotinib) With Chemoradiation in Stage IIIA
n=46 Participants
TARCEVA (erlotinib) 150 mg, P.O., daily, except for chemotherapy. Paclitaxel, 45mg/m2; Carboplatin, AUC=2, weekly; RT: 63Gy/35 fractions/7 weeks
Overall Survival and Disease Local Control Rate
Local Regional Survival:5-year
55.8 percentage of participants
Overall Survival and Disease Local Control Rate
Overall Survival:5-year
35.9 percentage of participants
Overall Survival and Disease Local Control Rate
Disease Free Survival:5-year
25.8 percentage of participants
Overall Survival and Disease Local Control Rate
Distant Metastasis Free Survival:5-year
36.5 percentage of participants

Adverse Events

Phase II TARCEVA (Erlotinib) With Chemoradiation in Stage IIIA

Serious events: 10 serious events
Other events: 36 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Phase II TARCEVA (Erlotinib) With Chemoradiation in Stage IIIA
n=46 participants at risk
TARCEVA (erlotinib) 150 mg, P.O., daily, except for chemotherapy. Paclitaxel, 45mg/m2; Carboplatin, AUC=2, weekly; RT: 63Gy/35 fractions/7 weeks
Gastrointestinal disorders
Esophagitis
2.2%
1/46 • Number of events 1 • From the time of registration through study completion and follow up, assessed up to 5 years.
Respiratory, thoracic and mediastinal disorders
Pneumonititis
6.5%
3/46 • Number of events 3 • From the time of registration through study completion and follow up, assessed up to 5 years.
Skin and subcutaneous tissue disorders
Skin toxicity, any
13.0%
6/46 • Number of events 6 • From the time of registration through study completion and follow up, assessed up to 5 years.
Skin and subcutaneous tissue disorders
Acneform rash
4.3%
2/46 • Number of events 2 • From the time of registration through study completion and follow up, assessed up to 5 years.

Other adverse events

Other adverse events
Measure
Phase II TARCEVA (Erlotinib) With Chemoradiation in Stage IIIA
n=46 participants at risk
TARCEVA (erlotinib) 150 mg, P.O., daily, except for chemotherapy. Paclitaxel, 45mg/m2; Carboplatin, AUC=2, weekly; RT: 63Gy/35 fractions/7 weeks
Gastrointestinal disorders
Esophagitis
39.1%
18/46 • Number of events 18 • From the time of registration through study completion and follow up, assessed up to 5 years.
Respiratory, thoracic and mediastinal disorders
Pneumonitis
15.2%
7/46 • Number of events 7 • From the time of registration through study completion and follow up, assessed up to 5 years.
Skin and subcutaneous tissue disorders
Skin toxicity, any
21.7%
10/46 • Number of events 10 • From the time of registration through study completion and follow up, assessed up to 5 years.
Skin and subcutaneous tissue disorders
Acneform rash
60.9%
28/46 • Number of events 28 • From the time of registration through study completion and follow up, assessed up to 5 years.
General disorders
Fatigue
6.5%
3/46 • Number of events 3 • From the time of registration through study completion and follow up, assessed up to 5 years.

Additional Information

Dr. Steven H. Lin/Radiation Oncology

UT MD Anderson Cancer Center

Phone: 713-563-8490

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place