VA NEPHRON-D: Diabetes iN Nephropathy Study

NCT ID: NCT00555217

Last Updated: 2015-05-29

Study Results

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

1448 participants

Study Classification

INTERVENTIONAL

Study Start Date

2008-07-31

Study Completion Date

2014-10-31

Brief Summary

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Diabetes is the leading cause of end-stage renal disease (ESRD) in the United States. The overall rate of ESRD secondary to diabetes has risen 68% since 1992. Medications that block the renin angiotensin system have been shown to decrease the progression of diabetic nephropathy. The use of an angiotensin receptor blocker (ARB) has been shown to decrease the risk of progression of kidney disease in two studies of individuals with Type 2 diabetes and proteinuria. Despite the use of an ARB, the incidence of renal failure remained high in the treated group in both studies. The combination of an angiotensin converting enzyme inhibitor (ACEI) and ARB can lead to more complete blockade of the renin angiotensin system. In diabetic kidney disease, combination therapy has been shown to decrease proteinuria in short-term studies. Although there are encouraging results for improvement in proteinuria there are no data on progression of kidney disease for the use of combination of ACEI and ARB therapy in patients with diabetes. In addition, there could be an increased risk of serious hyperkalemia in individuals with diabetes who receive combination ACEI and ARB. The investigators therefore propose a randomized double blind multi-center clinical trial to assess the effect of combination of ACEI and ARB in patients with diabetes and proteinuria on progression of kidney disease.

Detailed Description

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Primary Hypothesis:

To evaluate the combination of an angiotensin converting enzyme inhibitor (ACEI) with an angiotensin receptor blocker (ARB) vs. standard treatment with angiotensin receptor blocker on the progression of kidney disease in individuals with Type 2 diabetes and overt nephropathy.

The primary outcome is a composite endpoint of reduction in estimated GFR of 30 ml/min/1.73m\*m in individuals with an estimated baseline GFR greater than or equal to 60 ml/min/1.73m\*m; reduction in estimated GFR of greater than 50% in individuals with an estimated baseline GFR less than 60 mL/min/1.73m\*m; progression to end-stage renal disease (defined as need for dialysis, renal transplant or an eGFR less than 15 ml/min/1.73m\*m) or death.

Secondary outcome: a renal composite endpoint, defined as; reduction in estimated GFR of more than 50% (for individuals with a baseline estimated GFR less than 60 ml/min/1.73m\*m); reduction in estimated GFR of more than 30 ml/min/1.73m\*m (for individuals with a baseline estimated GFR greater than or equal to 60 ml/min/1.73m\*m) or progression to end-stage renal disease (defined as need for dialysis, renal transplant or an eGFR of less than 15 ml/min/1.73m\*m).

Tertiary outcomes are cardiovascular events (cardiovascular mortality, myocardial infarction, cerebrovascular accident, admission for heart failure), change in albuminuria at 12 months and decline in slope of kidney function.

Study Abstract:

The study is a multi-center, prospective, randomized, parallel group trial to test the efficacy of the combination of an angiotensin converting enzyme inhibitor (ACEI) with an angiotension receptor blocker (ARB) vs. standard treatment with angiotension receptor blocker on the combined end-point. The primary outcome is a composite endpoint of reduction in estimated GFR of 30 ml/min/1.73m\*m in individuals with an estimated GFR greater than or equal to 60 ml/min/1.73m\*m; reduction in estimated GFR of greater than 50% in individuals with an estimated GFR less than 60 ml/min/1.73m\*m; progression to end-stage renal disease (defined as need for dialysis, renal transplant or en eGFR less than 15 ml/min/1.73m\*m)or death. The study population is individuals with type 2 diabetes and overt nephropathy.

Eligible subjects who consent to participate will be randomized into either the combination therapy arm or the mono therapy arm. The randomization will be stratified by site and within sites by baseline albuminuria (\< 1 vs. greater than or equal to 1 gram/gram creatinine) and eGFR (\< 60 vs. greater than or equal to 60 ml/min/1.73m\*m). All participants will receive open label therapy with losartan, an ARB, as standard of care. Patients not treated with an ACEI or ARB will be initiated on losartan; patients treated with an ACEI or ARB other than losartan (the study ARB) will be converted to losartan (the study ARB) and the dose titrated to 100 mg/day. Individuals who tolerate ARB 100mg/day criteria will be randomized in a 1:1 ratio to the addition of blinded lisinopril (the study ACEI) or placebo. The medication (lisinopril or placebo) will be titrated from an initial dose of 10 mg/day to a target dose of 40 mg/day. After each adjustment in dose, serum chemistries will be evaluated for kidney function and potassium levels. Subjects will be enrolled over a period of 4.25 years and the maximum length of follow-up is 6.25 years. The planned study duration is 6.25 years with 4.25 years of accrual and 6.25 years of follow-up for all enrolled patients. The intervention was stopped on November 7, 2012 for safety concerns after an interim analysis. Patients are still under passively follow-up without intervention.

Conditions

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Kidney Disease Nephropathy Type 2 Diabetes

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Caregivers

Study Groups

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Combination of ARB and ACEI

Combination of an angiotensin converting enzyme inhibitor (ACEI) with an angiotensin receptor blocker (ARB)

Group Type EXPERIMENTAL

losartan

Intervention Type DRUG

50 or 100mg/day

lisinopril

Intervention Type DRUG

10, 20 or 40 mg/day

Monotherapy ARB

Mono therapy arm. Standard treatment with angiotensin receptor blocker (ARB)

Group Type ACTIVE_COMPARATOR

losartan

Intervention Type DRUG

50 or 100mg/day

Interventions

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losartan

50 or 100mg/day

Intervention Type DRUG

lisinopril

10, 20 or 40 mg/day

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Type 2 diabetes
* Albuminuria \>300mg/gram creatinine
* Stage 2 or 3 CKD (eGFR 30 to \<90 mg/min/1.73m\*2 )
* Able to give informed consent
* Telephone contact available

Exclusion Criteria

* History of intolerance to ACEI or ARB
* Serum potassium level \>5.5 meq/L
* Receiving sodium polystyrene sulfonate (Kayexalate)
* Pregnancy, breast feeding, planning to become pregnant or sexually active and not using birth control
* Renal transplant recipient
* Suspected non-diabetic kidney disease
* Inability to discontinue current use of ACEI/ARB combination
* Current use of Lithium
* Severe (end-stage) comorbid disease
* Prisoner
* Age \<18
* Estimated glomerular filtration rate (GFR) \<30 or \>=90 ml/min/1.73m\*m
* HbA1c \>10.5%
* Patient refusal
* Participation in a concurrent interventional study
* Blood pressure \>180/95
* Unwilling to stop any proscribed medications after enrollment
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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US Department of Veterans Affairs

FED

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Linda Fried, MD MPH

Role: STUDY_CHAIR

VA Pittsburgh Healthcare System University Drive Division, Pittsburgh, PA

Locations

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Carl T. Hayden VA Medical Center

Phoenix, Arizona, United States

Site Status

Central Arkansas VHS Eugene J. Towbin Healthcare Ctr, Little Rock

Little Rock, Arkansas, United States

Site Status

VA Medical Center, Loma Linda

Loma Linda, California, United States

Site Status

VA Palo Alto Health Care System

Palo Alto, California, United States

Site Status

VA Connecticut Health Care System (West Haven)

West Haven, Connecticut, United States

Site Status

North Florida/South Georgia Veterans Health System

Gainesville, Florida, United States

Site Status

VA Medical Center, Miami

Miami, Florida, United States

Site Status

James A. Haley Veterans Hospital, Tampa

Tampa, Florida, United States

Site Status

Edward Hines, Jr. VA Hospital

Hines, Illinois, United States

Site Status

Richard Roudebush VA Medical Center, Indianapolis

Indianapolis, Indiana, United States

Site Status

VA Medical Center, Iowa City

Iowa City, Iowa, United States

Site Status

VA Maryland Health Care System, Baltimore

Baltimore, Maryland, United States

Site Status

VA Medical Center, Minneapolis

Minneapolis, Minnesota, United States

Site Status

VA Medical Center, Kansas City MO

Kansas City, Missouri, United States

Site Status

VA Medical Center, St Louis

St Louis, Missouri, United States

Site Status

VA Medical Center, Omaha

Omaha, Nebraska, United States

Site Status

VA New Jersey Health Care System, East Orange

East Orange, New Jersey, United States

Site Status

New Mexico VA Health Care System, Albuquerque

Albuquerque, New Mexico, United States

Site Status

VA Western New York Healthcare System at Buffalo

Buffalo, New York, United States

Site Status

VA Medical Center, Durham

Durham, North Carolina, United States

Site Status

VA Medical Center, Cleveland

Cleveland, Ohio, United States

Site Status

VA Medical Center, Portland

Portland, Oregon, United States

Site Status

VA Pittsburgh Healthcare System University Drive Division, Pittsburgh, PA

Pittsburgh, Pennsylvania, United States

Site Status

Ralph H Johnson VA Medical Center, Charleston

Charleston, South Carolina, United States

Site Status

WJB Dorn Veterans Hospital, Columbia

Columbia, South Carolina, United States

Site Status

VA Medical Center, Memphis

Memphis, Tennessee, United States

Site Status

VA Medical Center

Nashville, Tennessee, United States

Site Status

VA North Texas Health Care System, Dallas

Dallas, Texas, United States

Site Status

Hunter Holmes McGuire VA Medical Center

Richmond, Virginia, United States

Site Status

Zablocki VA Medical Center, Milwaukee

Milwaukee, Wisconsin, United States

Site Status

VA Medical Center, San Juan

San Juan, , Puerto Rico

Site Status

Countries

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United States Puerto Rico

References

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Fried LF, Duckworth W, Zhang JH, O'Connor T, Brophy M, Emanuele N, Huang GD, McCullough PA, Palevsky PM, Seliger S, Warren SR, Peduzzi P; VA NEPHRON-D Investigators. Design of combination angiotensin receptor blocker and angiotensin-converting enzyme inhibitor for treatment of diabetic nephropathy (VA NEPHRON-D). Clin J Am Soc Nephrol. 2009 Feb;4(2):361-8. doi: 10.2215/CJN.03350708. Epub 2008 Dec 31.

Reference Type BACKGROUND
PMID: 19118120 (View on PubMed)

Fried LF, Emanuele N, Zhang JH, Brophy M, Conner TA, Duckworth W, Leehey DJ, McCullough PA, O'Connor T, Palevsky PM, Reilly RF, Seliger SL, Warren SR, Watnick S, Peduzzi P, Guarino P; VA NEPHRON-D Investigators. Combined angiotensin inhibition for the treatment of diabetic nephropathy. N Engl J Med. 2013 Nov 14;369(20):1892-903. doi: 10.1056/NEJMoa1303154. Epub 2013 Nov 9.

Reference Type RESULT
PMID: 24206457 (View on PubMed)

Fried LF, Emanuele N, Zhang JH. Combined angiotensin inhibition in diabetic nephropathy. N Engl J Med. 2014 Feb 20;370(8):779. doi: 10.1056/NEJMc1315504. No abstract available.

Reference Type RESULT
PMID: 24552328 (View on PubMed)

Chen SS, Seliger SL, Fried LF. Complete inhibition of the renin-angiotensin-aldosterone system; where do we stand? Curr Opin Nephrol Hypertens. 2014 Sep;23(5):449-55. doi: 10.1097/MNH.0000000000000043.

Reference Type RESULT
PMID: 25014549 (View on PubMed)

Zimering MB, Zhang JH, Guarino PD, Emanuele N, McCullough PA, Fried LF; Investigators for the VA NEPHRON-D. Endothelial cell autoantibodies in predicting declining renal function, end-stage renal disease, or death in adult type 2 diabetic nephropathy. Front Endocrinol (Lausanne). 2014 Aug 11;5:128. doi: 10.3389/fendo.2014.00128. eCollection 2014.

Reference Type RESULT
PMID: 25157242 (View on PubMed)

Tamargo CL, Coca SG, Thiessen Philbrook H, Hu DG, Ix JH, Shlipak MG, Fried LF, Gutierrez OM, Waikar SS, Schrauben SJ, Schelling JR, Ganz P, Kimmel PL, Greenberg JH, Deo R, Takakura A, Vasan RS, Bonventre JV, Parikh CR. The distal nephron biomarkers associate with diabetic kidney disease progression. JCI Insight. 2025 Jun 23;10(12):e186836. doi: 10.1172/jci.insight.186836. eCollection 2025 Jun 23.

Reference Type DERIVED
PMID: 40548378 (View on PubMed)

Natale P, Palmer SC, Navaneethan SD, Craig JC, Strippoli GF. Angiotensin-converting-enzyme inhibitors and angiotensin receptor blockers for preventing the progression of diabetic kidney disease. Cochrane Database Syst Rev. 2024 Apr 29;4(4):CD006257. doi: 10.1002/14651858.CD006257.pub2.

Reference Type DERIVED
PMID: 38682786 (View on PubMed)

Huang Y, Fried LF, Kyriakides TC, Johnson GR, Chiu S, Mcdonald L, Zhang JH. Automated safety event monitoring using electronic medical records in a clinical trial setting: Validation study using the VA NEPHRON-D trial. Clin Trials. 2019 Feb;16(1):81-89. doi: 10.1177/1740774518813121. Epub 2018 Nov 16.

Reference Type DERIVED
PMID: 30445841 (View on PubMed)

Other Identifiers

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565

Identifier Type: -

Identifier Source: org_study_id

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