AMR PH GL 2007 CL001 Phase 3 Trial in Patients With Small Cell Lung Cancer After Failure of First-Line Chemotherapy

NCT ID: NCT00547651

Last Updated: 2019-11-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

637 participants

Study Classification

INTERVENTIONAL

Study Start Date

2007-09-01

Study Completion Date

2011-05-01

Brief Summary

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This study drug (Amrubicin) is believed to work by stopping the tumor cells in your body from growing. The purpose of this study is to evaluate the effect of amrubicin compared to topotecan in the treatment of small cell lung cancer.

Detailed Description

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Small cell lung cancer represents approximately 13% of the cancers of the lung and presents as extensive stage disease in 60% to 70% of patients. Sites of metastases include bone (35%), liver (25%), bone marrow (20%), brain (10%), extrathoracic lymph nodes (5%), and subcutaneous masses (5%). Small-cell lung cancer has prominent markers of neuroendocrine differentiation.

The staging classification for SCLC is the 2-stage Veterans Administration Lung Study Group system that categorizes patients as having limited or extensive disease. Limited stage SCLC is disease confined to 1 hemithorax with or without adjacent mediastinal and/or supraclavicular lymph node involvement, but without a pleural effusion. This extent of disease can be included in a tolerable radiation field. Extensive-disease SCLC is any disease beyond the definition of limited-stage disease.

There are few proven treatment options for SCLC patients who fail first-line chemotherapy. New treatment strategies must be evaluated. The need to discover active agents with better toxicity profiles continues to be of great importance. Amrubicin may be an effective treatment for this population.

Conditions

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Small Cell Lung Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Amrubicin

Amrubicin

Group Type EXPERIMENTAL

Amrubicin

Intervention Type DRUG

Amrubicin for injection is supplied as 50-mg vials. Patients will receive 40 mg/m2 amrubicin as a 5-minute infusion once daily for 3 consecutive days starting on Day 1 of a 21-day course

Topotecan

Topotecan

Group Type ACTIVE_COMPARATOR

Topotecan

Intervention Type DRUG

Topotecan for injection is supplied as 4-mg vials. Patients will receive 1.5 mg/m2 as a 30-minute infusion once daily for 5 consecutive days starting on Day 1 of a 21-day course

Interventions

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Amrubicin

Amrubicin for injection is supplied as 50-mg vials. Patients will receive 40 mg/m2 amrubicin as a 5-minute infusion once daily for 3 consecutive days starting on Day 1 of a 21-day course

Intervention Type DRUG

Topotecan

Topotecan for injection is supplied as 4-mg vials. Patients will receive 1.5 mg/m2 as a 30-minute infusion once daily for 5 consecutive days starting on Day 1 of a 21-day course

Intervention Type DRUG

Other Intervention Names

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amrubidin hydrochloride Calsed CNF3140 Topotecan hydrochloride Hycamtin

Eligibility Criteria

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Inclusion Criteria

* Histological or cytological diagnosis of SCLC at study entry according to the International Association for the Study of Lung Cancer (IASLC) histopathologic classification. Mixed or combined subtypes according to the IASLC are not allowed;
* SCLC that is either sensitive (defined as a response including stable disease to first-line platinum-based chemotherapy, with subsequent progression \>/= 90 days after completing first-line chemotherapy) or refractory (defined as best response to first-line platinum-based chemotherapy or progression \< 90 days after completing first-line chemotherapy);
* Extensive or limited disease; patients with limited disease who are candidates for local or regional salvage radiation therapy must have been offered such treatment prior to participation in this study;
* Radiographically documented progression after first-line treatment with platinum-based chemotherapy;
* No more than 1 prior chemotherapy regimen;
* At least 18 years of age;
* ECOG performance status of 0 - 1

Exclusion Criteria

* Chest radiotherapy with curative intent to the primary disease complex \</= 28 days prior to first dose; CNS radiotherapy \</= 21 days prior to first dose; radiotherapy to all other areas \</= 7 days prior to first dose;
* Prior anthracycline, topotecan, or irinotecan treatment.
* Prior anthracycline or topotecan treatment.
* Patients with know history of seropositive human immunodeficiency virus (HIV) or patients who are receiving immunosuppressive medications that would increase the risk of serious neutropenic complications
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Celgene

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Markus Renschler, M.D.

Role: STUDY_DIRECTOR

Celgene Corporation

Locations

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Northwest Alabama Cancer Center

Muscle Shoals, Alabama, United States

Site Status

Arizona Oncology Associates

Tucson, Arizona, United States

Site Status

Little Rock Hematology Oncology Associates

Little Rock, Arkansas, United States

Site Status

Cancer Care Associates of Fresno Medical Group, Inc.

Fresno, California, United States

Site Status

Cedars-Sinai Outpatient Cancer Center

Los Angeles, California, United States

Site Status

University of Colorado Health Science Centre

Aurora, Colorado, United States

Site Status

Rocky Mountain Cancer Center - Midtown (Main)

Denver, Colorado, United States

Site Status

Advanced Medical Specialties

Miami, Florida, United States

Site Status

Ocala Oncology Center

Ocala, Florida, United States

Site Status

Cancer Centers of Florida, P.A.

Ocoee, Florida, United States

Site Status

Florida Oncology Associates

Orange Park, Florida, United States

Site Status

Sacred Heart Medical Oncology

Pensacola, Florida, United States

Site Status

Medical Oncology Associates of Augusta

Augusta, Georgia, United States

Site Status

Joliet Oncology-Hematology Associates, Ltd.

Joliet, Illinois, United States

Site Status

Cancer & Hematology Specialists of Chicago (Main)

Niles, Illinois, United States

Site Status

Illinois Cancer Care

Peoria, Illinois, United States

Site Status

Cancer Care at Blessing Hospital

Quincy, Illinois, United States

Site Status

Central Indiana Cancer Centers

Indianapolis, Indiana, United States

Site Status

Hope Center

Terre Haute, Indiana, United States

Site Status

Kansas City Cancer Center (Main)

Overland Park, Kansas, United States

Site Status

Cancer Center of Kansas

Wichita, Kansas, United States

Site Status

Jayne Gurtler MD, Laura Brizn MD, Angelo Russo MD, and Janet Burroff MD, APMC

Metairie, Louisiana, United States

Site Status

Tulane University Health Sciences Center

New Orleans, Louisiana, United States

Site Status

Maine Center for Cancer Medicine and Blood Disorders

Scarborough, Maine, United States

Site Status

Sinai Hospital of Baltimore, Inc.

Baltimore, Maryland, United States

Site Status

Center for Cancer and Blood Disorders

Bethesda, Maryland, United States

Site Status

Alliance Hematology Oncology, P.A. (Main)

Westminster, Maryland, United States

Site Status

Kalamazoo Hematology and Oncology

Kalamazoo, Michigan, United States

Site Status

Michigan Hematology & Oncology Institute

Southgate, Michigan, United States

Site Status

University of Minnesota Medical Center, Cancer Center

Minneapolis, Minnesota, United States

Site Status

Missouri Cancer Associates

Columbia, Missouri, United States

Site Status

St. Joseph Oncology, Inc.

Saint Joseph, Missouri, United States

Site Status

Comprehensive Care Centers of Nevada (Main)

Las Vegas, Nevada, United States

Site Status

New York Oncology Hematology, P.C.

Latham, New York, United States

Site Status

SUNY Upstate Medical University - Regional Oncology Center

Syracuse, New York, United States

Site Status

Lineberger Comprehensive Cancer Center

Chapel Hill, North Carolina, United States

Site Status

Regional Cancer Care

Durham, North Carolina, United States

Site Status

Cancer Centers of North Carolina (Main)

Raleigh, North Carolina, United States

Site Status

Piedmont Hematology Oncology Associates

Winston-Salem, North Carolina, United States

Site Status

Gabrail Cancer Center

Canton, Ohio, United States

Site Status

Greater Dayton Cancer Center (Main)

Kettering, Ohio, United States

Site Status

Cancer Care Associates

Oklahoma City, Oklahoma, United States

Site Status

Cancer Care Associates

Tulsa, Oklahoma, United States

Site Status

Willamette Valley Cancer Center (Main)

Eugene, Oregon, United States

Site Status

Medical Oncology Associates

Kingston, Pennsylvania, United States

Site Status

Thomas Jefferson Memorial Hospital

Philadelphia, Pennsylvania, United States

Site Status

UPMC Cancer Pavilion

Pittsburgh, Pennsylvania, United States

Site Status

Cancer Centers of the Carolinas (Main)

Greenville, South Carolina, United States

Site Status

The Sarah Cannon Research Institute/TN Oncology

Nashville, Tennessee, United States

Site Status

Texas Oncology, P.A.

Amarillo, Texas, United States

Site Status

Coastal Bend Cancer Center

Corpus Christi, Texas, United States

Site Status

Texas Cancer Center at Medical City (Main)

Dallas, Texas, United States

Site Status

Texas Oncology, P.A. (Main)

Dallas, Texas, United States

Site Status

West Texas Cancer Center-Texas Oncology

Odessa, Texas, United States

Site Status

Texas Oncology, P.A.

Webster, Texas, United States

Site Status

Texoma Cancer Center

Wichita Falls, Texas, United States

Site Status

Fairfax Northern Virginia Hematology/Oncology

Fairfax, Virginia, United States

Site Status

Virginia Oncology Associates

Norfolk, Virginia, United States

Site Status

Blue Ridge Cancer Care

Roanoke, Virginia, United States

Site Status

Northwest Cancer Specialists - Vancouver (Main)

Vancouver, Washington, United States

Site Status

Marshfield Clinic

Marshfield, Wisconsin, United States

Site Status

Royal North Shore Hospital

St Leonards, New South Wales, Australia

Site Status

New South Wales Southern Medical Day Care Centre

Wollongong, New South Wales, Australia

Site Status

The Princess Alexandra Hospital, Dept of Respiratory Medicine

Woolloongabba, Queensland, Australia

Site Status

Flinders Medical Centre

Bedford Park, South Australia, Australia

Site Status

The Queen Elizabeth Hospital

Woodville South, , Australia

Site Status

Allgemeines Krankenhaus der Stadt Linz, Abteilung fur Atem und Lungenkrankheiten

Linz, , Austria

Site Status

Allegemeines Krankenhaus Wien, Univ. Klinik fur Innere, Medizin I

Vienna, , Austria

Site Status

Krankenhaus Hietzing, 5 Med. Abteilung mit Onkologie

Vienna, , Austria

Site Status

Klinikum Weis-Grieskirchen GmbH

Wels, , Austria

Site Status

UZ Brussel, Medical Oncology and Hematology

Brussels, , Belgium

Site Status

Centre Hospitalier Notre-Dame et Reine Fabiola

Charleroi, , Belgium

Site Status

Universitair Ziekenhuis Antwerpen, Dept. Respiratory Diseases

Edegem, , Belgium

Site Status

UZ Gasthuisberg, UZ Leuven

Leuven, , Belgium

Site Status

C.H.U. Sart-Tilman

Liège, , Belgium

Site Status

III-rd Internal Department, District Dispensary for Oncology diseases with stationary(DDOncDIU)

Plovdiv, , Bulgaria

Site Status

DDOncDIU Sofia District

Sofia, , Bulgaria

Site Status

MHAT "Tsaritsa Yoanna"

Sofia, , Bulgaria

Site Status

University Multiprofile Hospital for Active Treatment "Sveta Marina"

Varna, , Bulgaria

Site Status

Fraser Valley Cancer Centre-Surrey Memorial Hospital

Surrey, British Columbia, Canada

Site Status

London Regional Cancer Centre

London, Ontario, Canada

Site Status

Princess Margaret Hospital

Toronto, Ontario, Canada

Site Status

Humber River Regional Hospital

Weston, Ontario, Canada

Site Status

Royal Victoria Hospital

Montreal, Quebec, Canada

Site Status

Fakultni Nemocnice Ostrava

Ostrava-Poruba, , Czechia

Site Status

Fakultní Thomayerova nemocnice s poliklinikou

Prague, , Czechia

Site Status

Faculty Hospital Motol

Prague, , Czechia

Site Status

Masarykova nemocnice v Ústí nad Labem

Ústí nad Labem, , Czechia

Site Status

Rikshospitalet, Finsen Center

Copenhagen, , Denmark

Site Status

Herlev Hospital, Onkologisk afdeling R

Herlev, , Denmark

Site Status

Odense Universitetshospital,Onkologisk afdeling R

Odense C, , Denmark

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Centre François Baclesse

Caen, , France

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Hôpital de la Croix-Rousse

Lyon, , France

Site Status

CHU Montpellier - Unité de Cancérologie Thoracique

Montpellier, , France

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Institut Gustave Roussy

Villejuif, , France

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Zentralklinik Bad Berka GmbH

Bad Berka, , Germany

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Charité Universitätsmedizin Berlin

Berlin, , Germany

Site Status

Universitätsklinikum Essen Innere Klinik und Poliklinik

Essen, , Germany

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Asklepios Fachkliniken Muenchen Gauting

Gauting, , Germany

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Krankenhaus Grosshansdorf, Zentrum fur Pneumologie und Thoraxchirurgie

Großhansdorf, , Germany

Site Status

Staedtisches Krankenhaus Martha-Maria Halle-Doelau

Halle, , Germany

Site Status

Thoraxklinik am Universitätsklinikum Heidelberg AG

Heidelberg, , Germany

Site Status

St. Vincentius-Kliniken Karlsruhe, Hamatologie, Med Onkologie und Immunologie

Karlsruhe, , Germany

Site Status

Katholisches Klinikum Mainz, St. Hildegardis Krankenhaus

Mainz, , Germany

Site Status

Klinikum Mannheim GmbH, Chirugische Klinik, Thorakale Onkologie

Mannheim, , Germany

Site Status

Semmelweis University of Medicine

Budapest, , Hungary

Site Status

Országos Korányi Tbc és Pulmonológiai Intézet

Budapest, , Hungary

Site Status

DEODEC

Debrecen, , Hungary

Site Status

Matrai Gyogyintezet

Mátraháza, , Hungary

Site Status

County Hospital Baranya

Pécs, , Hungary

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Erzsébet Hospital Sopron

Sopron, , Hungary

Site Status

Policlinico di Modena - University of Modena & Reggio Emilia, Dept Oncology & Hematology

Modena, , Italy

Site Status

Ospedale S. Maria della Misericordia

Perugia, , Italy

Site Status

Azienda Ospedaliera San Camillo Forlanini

Roma, , Italy

Site Status

Ospedale S.S. Trinita

Sora, , Italy

Site Status

Nederlands Kanker Instituut - Antoni van Leeuwenhoek Ziekenhuis

Amsterdam, , Netherlands

Site Status

VU University Medical Center Amsterdam

Amsterdam, , Netherlands

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University Medical Center Groningen

Groningen, , Netherlands

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Elkerliek Ziekenhuis, Locatie Helmond

Helmond, , Netherlands

Site Status

Erasmus MC - Daniel den Hoed

Rotterdam, , Netherlands

Site Status

Specjalistyczny Zespol Chorob Pluc i Gruzlicy w Bystrej

Bystra, , Poland

Site Status

Akademickie Centrum Kliniczne

Gdansk, , Poland

Site Status

Zespol nr 1 Szpitala im. St. Leszczynskiego

Katowice, , Poland

Site Status

Klinika Nowotworow Ukladowych i Uogolnionych Centrum Onkologii, Instytut im. Marii Sklodowskiej-Curie

Krakow, , Poland

Site Status

Centrum Onkologii Ziemi Lubelskiej

Lublin, , Poland

Site Status

Wielkopolskie Centrum Pulmonologii i Tarakochirurgii Oddzial Onkologii Klinicznej z Pododdzialem Dziennej Chemioterapii

Poznan, , Poland

Site Status

Szpital Specjalistyczny w Prabutach

Prabuty, , Poland

Site Status

Wojewódzki Szpital Chorób Pluc im Alojzego Pawelca w Wodzislawiu Slaskim

Wodzisław Śląski, , Poland

Site Status

Hospital Universitario Germans Trias i Pujol

Barcelona, , Spain

Site Status

Duran i Reynals Institut Catala d'Oncologia

L'Hospitalet de Llobregat, , Spain

Site Status

Fundación Jiménez Díaz. Universidad Autónoma de Madrid

Madrid, , Spain

Site Status

Hospital Universitario Virgin de la Victoria

Málaga, , Spain

Site Status

Hospital General Universitario de Valencia

Valencia, , Spain

Site Status

Kantonsspital Aarau

Aarau, , Switzerland

Site Status

Kantonsspital Graubünden

Chur, , Switzerland

Site Status

Universitätsspital Zürich

Zurich, , Switzerland

Site Status

Edinburgh Cancer Research Centre

Edinburgh, , United Kingdom

Site Status

Beatson West of Scotland Cancer Centre

Glasgow, , United Kingdom

Site Status

Christie Hospital NHS Foundation Trust

Manchester, , United Kingdom

Site Status

The Royal Marsden NHS Foundation Trust

Surrey, , United Kingdom

Site Status

Countries

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United States Australia Austria Belgium Bulgaria Canada Czechia Denmark France Germany Hungary Italy Netherlands Poland Spain Switzerland United Kingdom

References

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von Pawel J, Jotte R, Spigel DR, O'Brien ME, Socinski MA, Mezger J, Steins M, Bosquee L, Bubis J, Nackaerts K, Trigo JM, Clingan P, Schutte W, Lorigan P, Reck M, Domine M, Shepherd FA, Li S, Renschler MF. Randomized phase III trial of amrubicin versus topotecan as second-line treatment for patients with small-cell lung cancer. J Clin Oncol. 2014 Dec 10;32(35):4012-9. doi: 10.1200/JCO.2013.54.5392. Epub 2014 Nov 10.

Reference Type BACKGROUND
PMID: 25385727 (View on PubMed)

Other Identifiers

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AMR PH GL 2007 CL001

Identifier Type: -

Identifier Source: org_study_id

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